Efficacy and Safety of Tozorakimab in Symptomatic Chronic Obstructive Pulmonary Disease With a History of Exacerbations

NCT ID: NCT06040086

Last Updated: 2025-12-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

1454 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-09-22

Study Completion Date

2026-05-22

Brief Summary

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The purpose of this Phase III study is to evaluate the efficacy and safety of tozorakimab administered subcutaneously (SC) in adult participants with symptomatic COPD with a history of ≥ 2 moderate or ≥ 1 severe exacerbations of COPD in the 12 months prior to enrolment. Participants should be receiving optimised treatment with inhaled maintenance therapy (ICS/LABA/LAMA triple therapy, or dual therapy if triple is not considered appropriate) throughout at least the last 3 months prior to enrolment.

Detailed Description

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Conditions

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Chronic Obstructive Pulmonary Disease (COPD)

Keywords

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Chronic Obstructive Pulmonary Disease COPD tozorakimab MEDI3506 exacerbations ICS LABA/LAMA Biologic Biologic Treatment

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Tozorakimab

Dosing subcutaneously tozorakimab

Group Type EXPERIMENTAL

Tozorakimab

Intervention Type DRUG

Administered subcutaneously tozorakimab and placebo throughout the study.

Placebo

Dosing subcutaneously with equivalent volume to tozorakimab

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo administered subcutaneously, equivalent volume to tozorakimab throughout the study.

Interventions

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Placebo

Placebo administered subcutaneously, equivalent volume to tozorakimab throughout the study.

Intervention Type DRUG

Tozorakimab

Administered subcutaneously tozorakimab and placebo throughout the study.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Participant must be ≥ 40 years of age and capable of giving signed informed consent.
2. Documented diagnosis of COPD for at least one year prior to enrolment.
3. Post BD FEV1/FVC \< 0.70 and post-BD FEV1 \>20% of predicted normal value
4. Documented history of ≥ 2 moderate or ≥ 1 severe COPD exacerbations within 12 months prior to enrolment.
5. Documented optimised inhaled dual or triple therapy for at least 3 months prior to enrolment.
6. Smoking history of ≥ 10 pack-years.
7. CAT total score ≥ 10, with each of the phlegm (sputum) and cough items with a score ≥ 2

Exclusion Criteria

1. Clinically important pulmonary disease other than COPD.
2. Radiological findings suggestive of a respiratory disease other than COPD that is significantly contributing to the participant's respiratory symptoms. Radiological findings of pulmonary nodules suspicious for lung cancer, as per applicable guidances, without appropriate follow up prior to randomisation. Radiological findings suggestive of acute infection.
3. Current diagnosis of asthma, prior history of asthma, or asthma-COPD overlap. Childhood history of asthma is allowed and defined as asthma diagnosed and resolved before the age of 18
4. Any unstable disorder, including, but not limited to, cardiovascular, gastrointestinal, hepatic, renal, neurological, musculoskeletal, infectious, endocrine, metabolic, haematological, psychiatric disorder, major physical and/or cognitive impairment that could affect safety, study findings or participants ability to complete the study.
5. COPD exacerbation, within 2 weeks prior to randomization, that was treated with systemic corticosteroids and/or antibiotics, and/or led to hospitalization.
6. Active significant infection within the 4 weeks prior to randomization, pneumonia within 6 weeks prior to randomization, or medical condition that predisposes the participant to infection.
7. Suspicion of, or confirmed, ongoing SARS-CoV-2 infection.
8. Significant COVID-19 illness within the 6 months prior to enrolment.
9. Unstable cardiovascular disorder.
10. Diagnosis of cor pulmonale, pulmonary arterial hypertension and/or right ventricular failure.
11. History of active severe inflammatory bowel disease or colitis within one year prior to enrolment, or unexplained diarrhoea within the 4 weeks prior to randomisation.
12. History of known immunodeficiency disorder, including a positive test for HIV-1 or HIV 2.
13. History of positive test or treatment for hepatitis B or hepatitis C (except for cured hepatitis C)
14. Evidence of active liver disease, including jaundice during screening.
15. Malignancy, current or within the past 5 years, except for adequately treated non-invasive basal cell and squamous cell carcinoma of the skin and cervical carcinoma-in-situ treated with apparent success more than one year prior to enrolment. Suspected malignancy or undefined neoplasms.
16. Participants who have evidence of active TB.
17. History of partial or total lung resection.
18. Scheduled major surgical procedure during the course of the study.
19. Participants that have previously received tozorakimab.
20. Any clinically significant abnormal findings in physical examination, vital signs, ECG, or laboratory testing during the screening period, which in the opinion of the investigator may put the participant at risk because of their participation in the study, or may influence the results of the study, or the participant's ability to complete the entire duration of the study.
Minimum Eligible Age

40 Years

Maximum Eligible Age

130 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Research Site

Birmingham, Alabama, United States

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Decatur, Alabama, United States

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Sheffield, Alabama, United States

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Phoenix, Arizona, United States

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Tucson, Arizona, United States

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Yuma, Arizona, United States

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Los Angeles, California, United States

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Newport Beach, California, United States

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San Francisco, California, United States

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Westminster, California, United States

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Aurora, Colorado, United States

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Boulder, Colorado, United States

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Washington D.C., District of Columbia, United States

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Boynton Beach, Florida, United States

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Cape Coral, Florida, United States

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Lakeland, Florida, United States

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Lakeland, Florida, United States

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Naples, Florida, United States

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Ocala, Florida, United States

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Ormond Beach, Florida, United States

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Atlanta, Georgia, United States

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Lithonia, Georgia, United States

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Champaign, Illinois, United States

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Chicago, Illinois, United States

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Chicago, Illinois, United States

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Andover, Kansas, United States

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Bowling Green, Kentucky, United States

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Lexington, Kentucky, United States

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Towson, Maryland, United States

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Detroit, Michigan, United States

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Minneapolis, Minnesota, United States

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Chesterfield, Missouri, United States

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Chesterfield, Missouri, United States

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Hannibal, Missouri, United States

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Papillion, Nebraska, United States

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Las Vegas, Nevada, United States

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Toms River, New Jersey, United States

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The Bronx, New York, United States

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Charlotte, North Carolina, United States

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Greenville, North Carolina, United States

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Huntersville, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Dayton, Ohio, United States

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Lima, Ohio, United States

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Grants Pass, Oregon, United States

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Gaffney, South Carolina, United States

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Union, South Carolina, United States

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Chattanooga, Tennessee, United States

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Elizabethton, Tennessee, United States

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Jackson, Tennessee, United States

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Dallas, Texas, United States

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El Paso, Texas, United States

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Houston, Texas, United States

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McKinney, Texas, United States

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San Antonio, Texas, United States

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Roy, Utah, United States

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Kenosha, Wisconsin, United States

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Buenos Aires, , Argentina

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CABA, , Argentina

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CABA, , Argentina

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Ciudad de Buenos Aires, , Argentina

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Córdoba, , Argentina

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La Plata, , Argentina

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Mar del Plata, , Argentina

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Mar del Plata, , Argentina

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Mendoza, , Argentina

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Quilmes, , Argentina

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San Fernando, , Argentina

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San Juan Bautista, , Argentina

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San Miguel de Tucumán, , Argentina

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Brussels, , Belgium

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Edegem, , Belgium

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Ghent, , Belgium

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Kortrijk, , Belgium

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Leuven, , Belgium

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Mechelen, , Belgium

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Namur, , Belgium

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Roeselare, , Belgium

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Barretos, , Brazil

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Belo Horizonte, , Brazil

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Blumenau, , Brazil

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Campina Grande do Sul, , Brazil

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Campinas, , Brazil

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São José do Rio Preto, , Brazil

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São Paulo, , Brazil

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Valinhos, , Brazil

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Dupnitsa, , Bulgaria

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Haskovo, , Bulgaria

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Panagyurishte, , Bulgaria

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Plovdiv, , Bulgaria

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Sofia, , Bulgaria

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Veliko Tanovo, , Bulgaria

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Yambol, , Bulgaria

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Calgary, Alberta, Canada

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Kelowna, British Columbia, Canada

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Ajax, Ontario, Canada

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Burlington, Ontario, Canada

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Toronto, Ontario, Canada

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Winchester, Ontario, Canada

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Lévis, Quebec, Canada

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Québec, Quebec, Canada

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Saint-Charles-Borromée, Quebec, Canada

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Chile, , Chile

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Concepción, , Chile

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Quillota, , Chile

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Santiago, , Chile

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Viña del Mar, , Chile

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Beijing, , China

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Changsha, , China

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Chengdu, , China

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Chongqing, , China

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Guangzhou, , China

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Guangzhou, , China

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Hefei, , China

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Hohhot, , China

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Huizhou, , China

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Jinan, , China

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Lanzhou, , China

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Liaocheng, , China

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Linhai, , China

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Nanchang, , China

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Nanchong, , China

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Nanjing, , China

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Nanjing, , China

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Nanning, , China

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Ningbo, , China

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Pingxiang, , China

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Xuzhou, , China

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Yinchuan, , China

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Zigong, , China

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Aalborg, , Denmark

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Aarhus, , Denmark

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Hvidovre, , Denmark

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København NV, , Denmark

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Næstved, , Denmark

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Roskilde, , Denmark

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Vejle, , Denmark

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Aix-en-Provence, , France

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Brest, , France

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Colmar, , France

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Epagny Metz-Tessy, , France

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La Tronche, , France

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Lyon, , France

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Marseille, , France

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Montpellier, , France

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Quimper, , France

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Reims, , France

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Villefranche-sur-Saône, , France

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Augsburg, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Cologne, , Germany

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Darmstadt, , Germany

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Essen, , Germany

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Frankfurt, , Germany

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Frankfurt am Main, , Germany

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Großhansdorf, , Germany

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Halle, , Germany

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Halle, , Germany

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Hanover, , Germany

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Leipzig, , Germany

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Marburg, , Germany

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Moers, , Germany

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München, , Germany

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München-Pasing, , Germany

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Nuremberg, , Germany

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Peine, , Germany

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Solingen, , Germany

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Athens, , Greece

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Athens, , Greece

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Heraklion, , Greece

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Thessaloniki, , Greece

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Budapest, , Hungary

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Debrecen, , Hungary

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Edelény, , Hungary

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Encs, , Hungary

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Gödöllő, , Hungary

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Hajdúnánás, , Hungary

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Mosonmagyaróvár, , Hungary

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Pécs, , Hungary

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Százhalombatta, , Hungary

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Szolnok, , Hungary

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Ajmer, , India

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Calicut, , India

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Dehradun, , India

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Delhi, , India

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Dwārka, , India

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Hyderabad, , India

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Hyderabad, , India

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Jaipur, , India

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Jaipur, , India

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Kolkata, , India

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Nagpur, , India

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Vijayawada, , India

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Visakhapatnam, , India

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Cork, , Ireland

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Dublin, , Ireland

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Galway, , Ireland

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Moneymore, , Ireland

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Cona, , Italy

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Foggia, , Italy

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Modena, , Italy

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Napoli, , Italy

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Padua, , Italy

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Pavia, , Italy

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Pisa, , Italy

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Roma, , Italy

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Aomori, , Japan

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Asahikawa-shi, , Japan

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Chikushino-shi, , Japan

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Chūōku, , Japan

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Fujieda-shi, , Japan

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Fukuoka, , Japan

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Ginowan-shi, , Japan

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Habikino-shi, , Japan

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Hakodate-shi, , Japan

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Hamamatsu, , Japan

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Iizuka-shi, , Japan

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Itabashi-ku, , Japan

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Izumi-shi, , Japan

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Kagoshima, , Japan

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Kasuga-shi, , Japan

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Kasugai-shi, , Japan

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Kawachinagano-shi, , Japan

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Kitakyushu-shi, , Japan

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Kiyose-shi, , Japan

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Kobe, , Japan

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Kumamoto, , Japan

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Kusatsu-shi, , Japan

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Kyoto, , Japan

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Matsusaka-shi, , Japan

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Minoh, , Japan

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Minokamo Shi, , Japan

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Mizunami-shi, , Japan

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Morioka, , Japan

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Nagoya, , Japan

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Nankoku-shi, , Japan

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Ogaki-shi, , Japan

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Okinawa-shi, , Japan

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Omuta-shi, , Japan

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Osaka, , Japan

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Sagamihara-shi, , Japan

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Sagamihara-shi, , Japan

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Sakaide-shi, , Japan

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Sakaishi, , Japan

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Sapporo, , Japan

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Sapporo, , Japan

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Sapporo, , Japan

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Sapporo, , Japan

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Sendai, , Japan

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Shizuoka, , Japan

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Tachikawa-shi, , Japan

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Toon-shi, , Japan

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Toride-shi, , Japan

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Toshima-ku, , Japan

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Toyonaka-shi, , Japan

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Ube, , Japan

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Ueda-shi, , Japan

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Urasoe-shi, , Japan

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Yanagawa-shi, , Japan

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Yokohama, , Japan

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Yokohama, , Japan

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Yokohama, , Japan

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Yokohama, , Japan

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Alor Star, , Malaysia

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Kajang, , Malaysia

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Kota Bharu, , Malaysia

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Kuala Lumpur, , Malaysia

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Kuantan, , Malaysia

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Seremban, , Malaysia

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Mexico City, , Mexico

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's-Hertogenbosch, , Netherlands

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Arnhem, , Netherlands

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Breda, , Netherlands

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Heerlen, , Netherlands

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Roermond, , Netherlands

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Rotterdam, , Netherlands

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Rotterdam, , Netherlands

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Zutphen, , Netherlands

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Piura, , Peru

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Santa Beatriz, , Peru

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Bialystok, , Poland

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Bydgoszcz, , Poland

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Chrzanów, , Poland

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Kielce, , Poland

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Krakow, , Poland

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Krakow, , Poland

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Pruszków, , Poland

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Płock, , Poland

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Rzeszów, , Poland

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Anyang-si, , South Korea

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Daegu, , South Korea

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Incheon, , South Korea

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Jeonju, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Wŏnju, , South Korea

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Badalona(Barcelona), , Spain

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Barcelona, , Spain

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Cáceres, , Spain

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Madrid, , Spain

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Málaga, , Spain

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Mérida, , Spain

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Santander, , Spain

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Zaragoza, , Spain

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Hat Yai, , Thailand

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Khlong Luang, , Thailand

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Muang, , Thailand

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Muang, , Thailand

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Mueang, , Thailand

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Nakhon Ratchasima, , Thailand

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Adana, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Mersin, , Turkey (Türkiye)

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Chernivtsi, , Ukraine

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Ivano-Frankivsk, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Tarasove Village, , Ukraine

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Ternopil, , Ukraine

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Uzhhorod, , Ukraine

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Vinnytsia, , Ukraine

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Vinnytsia, , Ukraine

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Zhytomyr, , Ukraine

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Bradford, , United Kingdom

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Cottingham, , United Kingdom

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Glasgow, , United Kingdom

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Leeds, , United Kingdom

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Liverpool, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Macclesfield, , United Kingdom

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Newcastle upon Tyne, , United Kingdom

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Portsmouth, , United Kingdom

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Wakefield, , United Kingdom

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Hanoi, , Vietnam

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Hanoi, , Vietnam

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Hà Nội, , Vietnam

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Ho Chi Minh City, , Vietnam

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Ho Chi Minh City, , Vietnam

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Hochiminh, , Vietnam

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Countries

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United States Argentina Belgium Brazil Bulgaria Canada Chile China Denmark France Germany Greece Hungary India Ireland Italy Japan Malaysia Mexico Netherlands Peru Poland South Korea Spain Thailand Turkey (Türkiye) Ukraine United Kingdom Vietnam

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

D9180C00012

Identifier Type: -

Identifier Source: org_study_id

2023-505543-39-00

Identifier Type: REGISTRY

Identifier Source: secondary_id