Safety Evaluation Study for Patients With Polycythemia Vera

NCT ID: NCT05074550

Last Updated: 2023-07-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE1

Total Enrollment

6 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-08-24

Study Completion Date

2024-03-31

Brief Summary

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This is PhaseI Dose-Escalation Study to Evaluate the Safety and Pharmacokinetics of PPMX-T003 in Polycythemia Vera

Detailed Description

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Conditions

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Polycythemia Vera

Study Design

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Allocation Method

NA

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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PPMX-T003

This drug should be administered within 48 hours after the phlebotomy. In addition, as a dose escalation design, 4 doses of 0.25 mg/kg, 0.4 mg/kg, 0.64 mg/kg, and 1 mg/kg are administered to the same subject, when the next phlebotomy required during observation period after the 1st administration.

Group Type EXPERIMENTAL

PPMX-T003

Intervention Type DRUG

As an observation and evaluation method, for each dose, in principle, inpatient observation is performed for 1 week from the day before administration, and then safety and pharmacodynamic tests are evaluated by visiting the hospital every 2 weeks.

Interventions

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PPMX-T003

As an observation and evaluation method, for each dose, in principle, inpatient observation is performed for 1 week from the day before administration, and then safety and pharmacodynamic tests are evaluated by visiting the hospital every 2 weeks.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Confirmed diagnosis of PV according to either the 2008 or 2016 WHO classification criteria
* PV patients being only treated with phlebotomy and the interval is 4-9 weeks

Exclusion Criteria

* Patients administrated drugs for PV treatment such as hydroxyurea or ruxolitinib (aspirin is excluded)
Minimum Eligible Age

20 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Perseus Proteomics Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Kansai Medical University Hospital

Hirakata, Osaka, Japan

Site Status RECRUITING

Shimane University Hospital

Izumo, Shimane, Japan

Site Status RECRUITING

Osaka City University Hospital

Osaka, , Japan

Site Status RECRUITING

Countries

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Japan

Central Contacts

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Tadashi Matsuura

Role: CONTACT

+81-3-5738-1705

Hiroko Akiyoshi

Role: CONTACT

+81-3-5738-1705

References

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Gorak EJ, Otterstatter M, Al Baghdadi T, Gillis N, Foran JM, Liu JJ, Bejar R, Gore SD, Kroft SH, Harrington A, Saber W, Starczynowski D, Rollison DE, Zhang L, Moscinski L, Wilson S, Thompson J, Borchert C, Sherman S, Hebert D, Walker ME, Padron E, DeZern AE, Sekeres MA. Discordant pathologic diagnoses of myelodysplastic neoplasms and their implications for registries and therapies. Blood Adv. 2023 Oct 24;7(20):6120-6129. doi: 10.1182/bloodadvances.2023010061.

Reference Type DERIVED
PMID: 37552083 (View on PubMed)

Other Identifiers

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PPMX-T003-CT102

Identifier Type: -

Identifier Source: org_study_id

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