Individual Patient Compassionate Use of Mirdametinib

NCT ID: NCT05028166

Last Updated: 2024-03-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

AVAILABLE

Study Classification

EXPANDED_ACCESS

Brief Summary

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This program is being offered on a patient by patient basis and will require company, Institutional Review Board/Independent Ethics Committee, and applicable competent authority approval.

Detailed Description

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Conditions

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Neurofibromatosis Type 1-Associated Plexiform Neurofibromas Histiocytic Neoplasm Other MAP-K Pathway Driven Diseases

Interventions

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Mirdametinib (MEK Inhibitor)

Patients will receive oral mirdametinib.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patient has a serious, debilitating or life-threatening medical condition that cannot be treated satisfactorily with an authorized medicinal product or other available standard treatment options, or all other treatment options have been exhausted.
* Patient does not qualify to participate in an ongoing clinical trial.
Minimum Eligible Age

2 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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SpringWorks Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Central Contacts

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SpringWorks Medical Information

Role: CONTACT

(888) 400-7989

Other Identifiers

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MEK-NF1-701

Identifier Type: -

Identifier Source: org_study_id

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