Induction Therapy for Patients With FLT3 Mutated Acute Myeloid Leukemia

NCT ID: NCT04982354

Last Updated: 2024-10-01

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

WITHDRAWN

Clinical Phase

PHASE1/PHASE2

Study Classification

INTERVENTIONAL

Study Start Date

2022-07-05

Study Completion Date

2032-08-01

Brief Summary

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This is a pilot study designed to identify the effect of daunorubicin-cytarabine liposome (CPX-351) in combination with a FLT3-inhibitor (midostaurin) as induction and consolidation therapy for patients with high-risk FLT3 mutated acute myeloid leukemia (AML) and subsequent CD34+-selected allogeneic stem cell transplant from HLA compatible related or unrelated donors.

Detailed Description

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Conditions

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Acute Myeloid Leukemia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Investigational Treatment

Daunorubicin-cytarabine liposome (CPX-351) Plus FLT3-inhibitor (Midostaurin) Induction Therapy followed by Busulfan/Melphalan/Fludarabine Conditioning therapy and CD34+-selected allografts.

Group Type EXPERIMENTAL

CPX-351

Intervention Type DRUG

For this trial, patients will be treated with CPX-351 100 (daunorubicin 44 mg/m2 and cytarabine 100 mg/m2) for 3 doses on days 1, 3 and 5 of one and on days 1 + 3 of a second cycle of induction therapy, depending on response obtained following the first induction. Thereafter, up to 2 cycles of consolidation therapy of 2 doses on days 1 and 3 of daunorubicin 29 mg/m2 and cytarabine 65 mg/m2 will be administered to the patients.

Midostaurin

Intervention Type DRUG

The FLT3 directed inhibitor, midostaurin, will be given at a dose of 50mg twice daily, starting on day 8 through day 21 of each cycle of CPX-351 until admission for allogeneic stem cell transplant.

Busulfan

Intervention Type DRUG

0.8 mg/kg/dose every six hours x 12 doses administered intravenously

Melphalan

Intervention Type DRUG

70 mg/m2/day x 2 doses administered intravenously

Fludarabine

Intervention Type DRUG

25 mg/m2/day x 5 doses administered intravenously

CD34+ selected allogeneic stem cell transplant from an HLA-compatible donor

Intervention Type BIOLOGICAL

Allogeneic stem cell transplant infused intravenously

Interventions

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CPX-351

For this trial, patients will be treated with CPX-351 100 (daunorubicin 44 mg/m2 and cytarabine 100 mg/m2) for 3 doses on days 1, 3 and 5 of one and on days 1 + 3 of a second cycle of induction therapy, depending on response obtained following the first induction. Thereafter, up to 2 cycles of consolidation therapy of 2 doses on days 1 and 3 of daunorubicin 29 mg/m2 and cytarabine 65 mg/m2 will be administered to the patients.

Intervention Type DRUG

Midostaurin

The FLT3 directed inhibitor, midostaurin, will be given at a dose of 50mg twice daily, starting on day 8 through day 21 of each cycle of CPX-351 until admission for allogeneic stem cell transplant.

Intervention Type DRUG

Busulfan

0.8 mg/kg/dose every six hours x 12 doses administered intravenously

Intervention Type DRUG

Melphalan

70 mg/m2/day x 2 doses administered intravenously

Intervention Type DRUG

Fludarabine

25 mg/m2/day x 5 doses administered intravenously

Intervention Type DRUG

CD34+ selected allogeneic stem cell transplant from an HLA-compatible donor

Allogeneic stem cell transplant infused intravenously

Intervention Type BIOLOGICAL

Other Intervention Names

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Rydapt Myleran Alkeran Fludara

Eligibility Criteria

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Inclusion Criteria

* Patients must have a Karnofsky (adult) Performance Status of at least 70%.
* Patients must have adequate organ function

Exclusion Criteria

* Female patients who are pregnant or breast-feeding
* Active viral, bacterial or fungal infection
* Patient seropositive for Human Immunodeficiency Virus (HIV-I /II); Human T-Cell Lymphotrophic Virus (HTLV -I /II)
* Presence of leukemia in the Central Nervous System (CNS).
Minimum Eligible Age

18 Years

Maximum Eligible Age

74 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Jazz Pharmaceuticals

INDUSTRY

Sponsor Role collaborator

Guenther Koehne

OTHER

Sponsor Role lead

Responsible Party

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Guenther Koehne

Deputy Director and Chief of Blood and Marrow Transplant, Hematologic Oncology and Benign Hematology

Responsibility Role SPONSOR_INVESTIGATOR

Principal Investigators

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Guenther Koehne, MD. PhD

Role: PRINCIPAL_INVESTIGATOR

Miami Cancer Institute at Baptist Health of South Florida

Locations

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Miami Cancer Institute at Baptist Health of South Florida

Miami, Florida, United States

Site Status

Countries

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United States

Related Links

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http://baptisthealth.net/cancer-care/home

Miami Cancer Institute Website

Other Identifiers

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2019-KOE-003

Identifier Type: -

Identifier Source: org_study_id

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