A Study of the Safety and Tolerability in Participants With PIK3CA-related Overgrowth Spectrum or Proteus Syndrome Who Are Being Treated With Miransertib (MK-7075) in Other Studies (MK-7075-006)

NCT ID: NCT04980872

Last Updated: 2025-02-07

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

60 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-11-02

Study Completion Date

2030-02-07

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This is a study of the safety and tolerability of oral miransertib (MK-7075) administered to participants at least 2 years of age with phosphatidylinositol-4,5-bisphosphate 3-kinase catalytic subunit alpha (PIK3CA)-related overgrowth spectrum (PROS) or Proteus Syndrome (PS). This is an extension of other miransertib studies (MK-7075-002 \[NCT03094832\] or ArQule CU/EAP \[NCT03317366\]), and may also enroll participants who are approved for MK-7075-002 but have not yet started miransertib therapy.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

PIK3CA-Related Overgrowth Spectrum (PROS)/Proteus Syndrome (PS)

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NA

Intervention Model

SINGLE_GROUP

Multicenter
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

None (Open-label)

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Miransertib

Participants with either PROS or PS receive miransertib orally once daily between 5 and 35 mg/m\^2 based on prior approved dosing for up to 96 cycles. A cycle is 28 days long.

Group Type EXPERIMENTAL

Miransertib

Intervention Type DRUG

Miransertib capsules administered orally either 1 hour before or 2 hours after a meal.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Miransertib

Miransertib capsules administered orally either 1 hour before or 2 hours after a meal.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

MK-7075 ARQ 092

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Has PROS or PS and has been screened in Study MK-7075-002 (or has been approved by the Sponsor to screen for MK-7075-002) or is currently being treated with miransertib as part of Study MK-7075-002 (NCT03094832) or ArQule's CU/EAP (NCT03317366)
* For males, agrees to be abstinent from heterosexual intercourse or use contraception unless confirmed to be azoospermic during the study period and for ≥90 days after the last dose of study intervention
* For females, is not pregnant or breastfeeding, and is either not a participant of childbearing potential (POCBP) or is a POCBP and is abstinent or uses a highly effective method of contraception

Exclusion Criteria

* Has previously discontinued miransertib due to related SAEs or other intolerance of miransertib
* Has received other investigational agents, if any, that were administered between leaving Study MK-7075-02 or ArQule's CU/EAP and entering this trial
* Is receiving systemic inhibitors of the mechanistic target of rapamycin (mTOR) pathway (eg, sirolimus, everolimus)
* Is receiving immunosuppressive therapies
* Is receiving continuous high dose steroids
Minimum Eligible Age

2 Years

Maximum Eligible Age

120 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Medical Director

Role: STUDY_DIRECTOR

Merck Sharp & Dohme LLC

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Children's Healthcare of Atlanta - Egleston Hospital ( Site 0107)

Atlanta, Georgia, United States

Site Status

Boston Children's Hospital ( Site 0089)

Boston, Massachusetts, United States

Site Status

Cincinnati Children's Hospital Medical Center-Hematology ( Site 0102)

Cincinnati, Ohio, United States

Site Status

Texas Children's Hospital ( Site 0104)

Houston, Texas, United States

Site Status

Seattle Children's Hospital ( Site 0103)

Seattle, Washington, United States

Site Status

John Hunter Hospital ( Site 0203)

Newcastle, New South Wales, Australia

Site Status

Bundaberg Base Hospital ( Site 0202)

Bundaberg, Queensland, Australia

Site Status

Hospital Araújo Jorge ( Site 0801)

Goiânia, Goiás, Brazil

Site Status

Fondazione Policlinico Universitario Agostino Gemelli ( Site 0052)

Rome, Lazio, Italy

Site Status

Ospedale Pediatrico Bambino Gesù-Centro Trials ( Site 0087)

Rome, Roma, Italy

Site Status

Great Ormond Street Hospital ( Site 0701)

London, London, City of, United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Brazil Italy United Kingdom

Related Links

Access external resources that provide additional context or updates about the study.

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

MK-7075-006

Identifier Type: OTHER

Identifier Source: secondary_id

2022-500689-87-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

2021-001369-19

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

7075-006

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.