New Horizons for the Treatment of Cardiomyopathy in Children

NCT ID: NCT04893629

Last Updated: 2025-02-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

NA

Total Enrollment

22 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-05-20

Study Completion Date

2024-11-30

Brief Summary

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Collecting mono nuclear cells from the patient's blood after a course of granulocyte stimulation then injecting them into the weak heart muscle measuring the heart function at the beginning and after 2.4.6 months to assess the improvement due to this procedure, by comparing these patients to patients with the same condition treated the classic way.

Detailed Description

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Dilated cardiomyopathy in children has high morbidity and mortality, current treatment doesn't improve the prognosis and the only cure available is heart transplantation which is limited, has long waiting list (if available), high cost, and has many side effects, leading to the need of novel effective, less costly therapeutic alternatives.

Stem cell therapy has proven to improve the cardiac function, reverse the pathologic histological changes, decrease the morbidity and mortality, offering a possible replacement to heart transplantation, different reports proved the safety and efficacy of this therapy using different types of cells and different routs of application in cardiomyopathy and acute myocardial infarction in children and adults, and in congenital heart disease, but the published cases of this therapy conducted on children with dilated cardiomyopathy are scanty .

Conditions

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Cardiomyopathy

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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intervention group

children diagnosed with dilated cardiomyopathy , will undergo trans endocardium injection of mono nuclear cells

Group Type EXPERIMENTAL

mono nuclear cells injection

Intervention Type BIOLOGICAL

trans endocardium injection of autologous mono nuclear cells for the intervention group and classic treatment for the control group

control group

children diagnosed with dilated cardiomyopathy ,will continue the classic medical treatment

Group Type ACTIVE_COMPARATOR

Digoxin+furosemide+captopril

Intervention Type DRUG

classical heart failure medical treatment

Interventions

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mono nuclear cells injection

trans endocardium injection of autologous mono nuclear cells for the intervention group and classic treatment for the control group

Intervention Type BIOLOGICAL

Digoxin+furosemide+captopril

classical heart failure medical treatment

Intervention Type DRUG

Other Intervention Names

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lasix,capoten

Eligibility Criteria

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Inclusion Criteria

* Dilated cardiomyopathy diagnosed and treated at least 6 mo. Ago
* LVEF less than 40%
* Use of I.V inotropes

Exclusion Criteria

* Acute infection
* Severe organ failure (other than the heart)
Minimum Eligible Age

6 Months

Maximum Eligible Age

14 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Damascus University

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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samir srour, prof

Role: STUDY_CHAIR

membership of the French society of the pediatric cardiology

Locations

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Children'S Hospital

Damascus, , Syria

Site Status

Countries

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Syria

References

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Selem SM, Kaushal S, Hare JM. Stem cell therapy for pediatric dilated cardiomyopathy. Curr Cardiol Rep. 2013 Jun;15(6):369. doi: 10.1007/s11886-013-0369-z.

Reference Type BACKGROUND
PMID: 23666883 (View on PubMed)

Zeinaloo A, Zanjani KS, Bagheri MM, Mohyeddin-Bonab M, Monajemzadeh M, Arjmandnia MH. Intracoronary administration of autologous mesenchymal stem cells in a critically ill patient with dilated cardiomyopathy. Pediatr Transplant. 2011 Dec;15(8):E183-6. doi: 10.1111/j.1399-3046.2010.01366.x. Epub 2010 Sep 29.

Reference Type BACKGROUND
PMID: 20880092 (View on PubMed)

Vrtovec B, Poglajen G, Lezaic L, Sever M, Domanovic D, Cernelc P, Socan A, Schrepfer S, Torre-Amione G, Haddad F, Wu JC. Effects of intracoronary CD34+ stem cell transplantation in nonischemic dilated cardiomyopathy patients: 5-year follow-up. Circ Res. 2013 Jan 4;112(1):165-73. doi: 10.1161/CIRCRESAHA.112.276519. Epub 2012 Oct 12.

Reference Type BACKGROUND
PMID: 23065358 (View on PubMed)

Abdel-Latif A, Bolli R, Tleyjeh IM, Montori VM, Perin EC, Hornung CA, Zuba-Surma EK, Al-Mallah M, Dawn B. Adult bone marrow-derived cells for cardiac repair: a systematic review and meta-analysis. Arch Intern Med. 2007 May 28;167(10):989-97. doi: 10.1001/archinte.167.10.989.

Reference Type BACKGROUND
PMID: 17533201 (View on PubMed)

Mozid AM, Arnous S, Sammut EC, Mathur A. Stem cell therapy for heart diseases. Br Med Bull. 2011;98:143-59. doi: 10.1093/bmb/ldr014. Epub 2011 May 19.

Reference Type BACKGROUND
PMID: 21596713 (View on PubMed)

Related Links

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https://doi.org/10.1186/s13287-019-1238-5

-Wang et al. Stem Cell Research \& Therapy (2019) 10:137

http://dx.doi.org/10.21037/tp.2019.03.01

I. M-Behnke et al. Regenerative therapies in young hearts with structural or congenital heart disease

Other Identifiers

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UDMS-Cardio-01-2021

Identifier Type: -

Identifier Source: org_study_id

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