Effect of Sodium Zirconium Cyclosilicate on Arrythmia-related Cardiovascular Outcomes in Participants on Chronic Hemodialysis With Recurrent Hyperkalemia (DIALIZE-Outcomes)

NCT ID: NCT04847232

Last Updated: 2025-06-18

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

2690 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-04-30

Study Completion Date

2024-03-07

Brief Summary

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The purpose of this study is to evaluate the effect of Sodium Zirconium Cyclosilicate (SZC) on arrhythmia-related cardiovascular outcomes in participants on chronic hemodialysis with recurrent hyperkalemia.

Detailed Description

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This is an international, multicenter, event-driven, randomized, double-blind, parallel group, placebo-controlled study, evaluating the utility of SZC versus placebo to reduce the incidence of sudden cardiac death (SCD), stroke, and arrhythmia-related hospitalizations, interventions, and emergency department (ED) visits in participants on chronic hemodialysis with recurrent hyperkalemia.

Conditions

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Hyperkalemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Sodium Zirconium Cyclosilicate

Group Type EXPERIMENTAL

Sodium Zirconium Cyclosilicate (SZC)

Intervention Type DRUG

Powder for oral suspension in a sachet. A dose is titrated in 5 g increments during a period of 4 weeks from 5 g up to 15 g qd on non-dialysis days. Afterward, the dose is adjusted monthly (or more frequent based on clinical judgment) depending on the current potassium value as measured after the long interdialytic interval (LIDI).

Placebo

Group Type PLACEBO_COMPARATOR

SZC Placebo

Intervention Type DRUG

Powder for oral suspension in a sachet. A dose is titrated in 5 g increments during a period of 4 weeks from 5 g up to 15 g qd on non-dialysis days. Afterward, the dose is adjusted monthly (or more frequent based on clinical judgment) depending on the current potassium value as measured after the LIDI.

Interventions

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Sodium Zirconium Cyclosilicate (SZC)

Powder for oral suspension in a sachet. A dose is titrated in 5 g increments during a period of 4 weeks from 5 g up to 15 g qd on non-dialysis days. Afterward, the dose is adjusted monthly (or more frequent based on clinical judgment) depending on the current potassium value as measured after the long interdialytic interval (LIDI).

Intervention Type DRUG

SZC Placebo

Powder for oral suspension in a sachet. A dose is titrated in 5 g increments during a period of 4 weeks from 5 g up to 15 g qd on non-dialysis days. Afterward, the dose is adjusted monthly (or more frequent based on clinical judgment) depending on the current potassium value as measured after the LIDI.

Intervention Type DRUG

Other Intervention Names

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Lokelma TM

Eligibility Criteria

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Inclusion Criteria

1. Capable of giving signed informed consent which includes compliance with the requirements and restrictions listed in the ICF and in this protocol
2. Provision of signed and dated, written ICF prior to any mandatory study specific procedures, sampling, and analyses
3. Must be ≥ 18 years of age, at the time of signing the ICF.
4. Receiving hemodialysis (or hemodiafiltration) 3 times a week for treatment of ESRD for ≥ 4 months before enrollment
5. Must have hemodialysis access consisting of an arteriovenous fistula, arteriovenous graft, or tunneled (permanent) catheter which is expected to remain in place for the entire duration of the study
6. At least 2 out of 3 pre-dialysis S K ≥ 5.5 mmol/L after the LIDI during screening
7. Negative pregnancy test for female participants of childbearing potential
8. Female participants must be 1 year postmenopausal, surgically sterile, or using one highly effective form of birth control (defined as one that can achieve a failure rate of less than 1% per year when used consistently and correctly). They should have been stable on their chosen method of birth control for a minimum of 3 months before entering the study and willing to remain on the birth control until 12 weeks after the last dose

Exclusion Criteria

1. Pseudohyperkalemia secondary to hemolyzed blood specimen (this situation is not considered screening failure, sampling or full screening can be postponed to a later time as applicable)
2. Presence of cardiac arrhythmias or conduction defects that require immediate treatment
3. Participants who have a pacemaker or implantable cardiac defibrillator
4. Any medical condition, including active, clinically significant infection or liver disease, that in the opinion of the investigator or sponsor may pose a safety risk to a participant in this study, confound safety or efficacy assessment and jeopardize the quality of the data, or interfere with study participation, or any other restrictions or contraindications in the local prescribing information for SZC
5. History of QT prolongation associated with other medications that required discontinuation of that medication
6. Congenital long QT syndrome
7. QTcF \> 550 msec
8. Atrial fibrillation requiring immediate/urgent intervention at screening or randomizations
9. Treated with sodium polystyrene sulfonate (SPS, Kayexalate, Resonium), calcium polystyrene sulfonate (CPS Resonium Calcium), patiromer (Veltassa), or SZC (Lokelma) within 7 days before screening or anticipated requiring chronic use of any of these agents during the study. If participant requires rescue therapy (potassium binder or dialysate S-K change during screening period), the participant will be screen failed
10. Participation in another clinical study with an investigational product, device, or non-standard hemodialysis procedure administered within one month before screening
11. Involvement in the planning and/or conduct of the study (applies to both AstraZeneca staff and/or staff at the study site)
12. Judgment by the investigator that the participant should not participate in the study if the participant is unlikely to comply with study procedures, restrictions, and requirements
13. Previous randomization in the present study
14. Females who are pregnant (confirmed with positive pregnancy test or a uterine ultrasound if pregnancy test result is questionable), breastfeeding, or planning to become pregnant during the study
15. Known hypersensitivity or previous anaphylaxis to SZC or to components thereof
16. Scheduled date for living donor kidney transplant
17. Sustained Ventricular Tachycardia \> 30 seconds requiring assessment / intervention
Minimum Eligible Age

18 Years

Maximum Eligible Age

130 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Steven Fishbane, Professor, MD

Role: PRINCIPAL_INVESTIGATOR

North Shore University Hospital, 300 Community Drive, Manhasset, NY 11030

Locations

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Huntsville, Alabama, United States

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Mesa, Arizona, United States

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Bakersfield, California, United States

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Glendale, California, United States

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Granada Hills, California, United States

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Lynwood, California, United States

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San Diego, California, United States

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Vacaville, California, United States

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Victorville, California, United States

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Denver, Colorado, United States

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Bloomfield, Connecticut, United States

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Middlebury, Connecticut, United States

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Newark, Delaware, United States

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Fort Lauderdale, Florida, United States

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Tampa, Florida, United States

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Columbus, Georgia, United States

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Lawrenceville, Georgia, United States

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Statesboro, Georgia, United States

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Nampa, Idaho, United States

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Iowa City, Iowa, United States

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Baton Rouge, Louisiana, United States

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Detroit, Michigan, United States

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Kalamazoo, Michigan, United States

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Roseville, Michigan, United States

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Minneapolis, Minnesota, United States

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Brookhaven, Mississippi, United States

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Columbus, Mississippi, United States

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Tupelo, Mississippi, United States

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Kansas City, Missouri, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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Las Vegas, Nevada, United States

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Las Vegas, Nevada, United States

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Jersey City, New Jersey, United States

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Manhasset, New York, United States

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The Bronx, New York, United States

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Charlotte, North Carolina, United States

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New Bern, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Bethlehem, Pennsylvania, United States

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Providence, Rhode Island, United States

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Spartanburg, South Carolina, United States

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St. George, Utah, United States

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Norfolk, Virginia, United States

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Virginia Beach, Virginia, United States

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Milwaukee, Wisconsin, United States

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Córdoba, , Argentina

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Junín, , Argentina

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Mar del Plata, , Argentina

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Pergamino, , Argentina

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Graz, , Austria

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Blagoevgrad, , Bulgaria

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Gotse Delchev, , Bulgaria

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Haskovo, , Bulgaria

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Pleven, , Bulgaria

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Plovdiv, , Bulgaria

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Saint John, New Brunswick, Canada

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Halifax, Nova Scotia, Canada

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Sydney, Nova Scotia, Canada

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Oshawa, Ontario, Canada

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Beijing, , China

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Changchun, , China

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Changsha, , China

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Changzhou, , China

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Guiyang, , China

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Yinchuan, , China

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Zhengzhou, , China

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Zhuzhou, , China

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České Budějovice, , Czechia

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Havlíčkův Brod, , Czechia

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Jilemnice, , Czechia

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Klatovy, , Czechia

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Liberec, , Czechia

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Nové Město na Moravě, , Czechia

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Pilsen, , Czechia

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Prague, , Czechia

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Tábor, , Czechia

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Třebíč, , Czechia

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Cloppenburg, , Germany

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Düsseldorf, , Germany

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Hanover, , Germany

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Minden, , Germany

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Potsdam, , Germany

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Stuttgart, , Germany

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Villingen-Schwenningen, , Germany

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Baja, , Hungary

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Budapest, , Hungary

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Kaposvár, , Hungary

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Karcag, , Hungary

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Kistarcsa, , Hungary

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Miskolc, , Hungary

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Nagykanizsa, , Hungary

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Szombathely, , Hungary

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Ahmedabad, , India

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Chennai, , India

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Dhanvantari Nagar, , India

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Nadiād, , India

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Pune, , India

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Bassano del Grappa, , Italy

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Bergamo, , Italy

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Bologna, , Italy

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Caserta, , Italy

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Milan, , Italy

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Monza, , Italy

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Pavia, , Italy

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Pesaro, , Italy

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Roma, , Italy

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San Giovanni Rotondo, , Italy

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Verona, , Italy

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Fujisawa-shi, , Japan

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Fukuoka, , Japan

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Hamamatsu, , Japan

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Kawasaki-shi, , Japan

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Kumagaya-shi, , Japan

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Kumamoto, , Japan

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Kyoto, , Japan

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Moriya-shi, , Japan

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Nagano, , Japan

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Nagasaki, , Japan

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Nakagami-gun, , Japan

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Okinawa-shi, , Japan

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Ōmihachiman, , Japan

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Sashima-gun, , Japan

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Setagaya-ku, , Japan

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Shiroishi-shi, , Japan

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Tamanashi, , Japan

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Toride-shi, , Japan

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Tsukuba, , Japan

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Ushiku-shi, , Japan

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Yatomi-shi, , Japan

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Batu Caves, , Malaysia

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Ipoh, , Malaysia

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Malacca, , Malaysia

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Seri Manjung, , Malaysia

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Chihuahua City, , Mexico

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Culiacán, , Mexico

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D.F, , Mexico

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Mazatlán, , Mexico

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Mexico City, , Mexico

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Monterrey, , Mexico

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Morelia, , Mexico

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San Luis Potosí City, , Mexico

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Veracruz, , Mexico

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Xalapa, , Mexico

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Zapopan, , Mexico

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Cusco, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Piura, , Peru

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Gdansk, , Poland

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Leżajsk, , Poland

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Lodz, , Poland

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Lodz, , Poland

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Lublin, , Poland

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Oleśnica, , Poland

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Olkusz, , Poland

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Pszczyna, , Poland

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Słupsk, , Poland

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Tczew, , Poland

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Wołomin, , Poland

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Żory, , Poland

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Żyrardów, , Poland

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Kemerovo, , Russia

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Mytischi, , Russia

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Novosibirsk, , Russia

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Omsk, , Russia

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Penza, , Russia

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Saint Petersburg, , Russia

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Yaroslavl, , Russia

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Bratislava, , Slovakia

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Košice, , Slovakia

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Lučenec, , Slovakia

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Púchov, , Slovakia

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Žilina, , Slovakia

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Alcalá de Henares, , Spain

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Barcelona, , Spain

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Pamplona, , Spain

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Valencia, , Spain

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Kaohsiung City, , Taiwan

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Keelung, , Taiwan

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Linkou District, , Taiwan

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New Taipei City, , Taiwan

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New Taipei City, , Taiwan

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Taichung, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Bangkok, , Thailand

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Chiang Mai, , Thailand

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Hat Yai, , Thailand

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Ratchathewi, , Thailand

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Adapazarı, , Turkey (Türkiye)

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Ankara, , Turkey (Türkiye)

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Gaziantep, , Turkey (Türkiye)

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Kahramanmaraş, , Turkey (Türkiye)

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Kayseri, , Turkey (Türkiye)

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Kocaeli, , Turkey (Türkiye)

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Chernivtsі, , Ukraine

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Dnipro, , Ukraine

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Ivano-Frankivsk, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Odesa, , Ukraine

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Ternopil, , Ukraine

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Uzhhorod, , Ukraine

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Vinnytsia, , Ukraine

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Zaporizhzhia, , Ukraine

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Zaporizhzhia, , Ukraine

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Bristol, , United Kingdom

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Leicester, , United Kingdom

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Liverpool, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Preston, , United Kingdom

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Salford, , United Kingdom

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Swansea, , United Kingdom

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Wolverhampton, , United Kingdom

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Biên Hòa, , Vietnam

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Da Nang, , Vietnam

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Hanoi, , Vietnam

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Hanoi, , Vietnam

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Ho Chi Minh City, , Vietnam

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Ho Chi Minh City, , Vietnam

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Ho Chi Minh City, , Vietnam

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Huế, , Vietnam

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Countries

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United States Argentina Austria Brazil Bulgaria Canada China Czechia Germany Hungary India Italy Japan Malaysia Mexico Peru Poland Russia Slovakia Spain Taiwan Thailand Turkey (Türkiye) Ukraine United Kingdom Vietnam

References

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Fishbane S, Dember LM, Jadoul M, Kovesdy CP, Guzman N, Kordzakhia G, Lisovskaja V, Sekar P, Wessman P, Al-Shurbaji A, Herzog CA. The randomized DIALIZE-Outcomes trial evaluated sodium zirconium cyclosilicate in hemodialysis. Kidney Int. 2025 Oct;108(4):686-694. doi: 10.1016/j.kint.2025.06.016. Epub 2025 Jul 4.

Reference Type DERIVED
PMID: 40618849 (View on PubMed)

Fishbane S, Jadoul M, Dember L, Kovesdy CP, Al-Shurbaji A, Lisovskaja V, Sekar P, Katona B, Guzman N, Herzog C. Evaluation of the effect of sodium zirconium cyclosilicate on arrhythmia-related cardiovascular outcomes in patients receiving chronic haemodialysis with hyperkalaemia: protocol for the multicentre, randomised, controlled DIALIZE-Outcomes study. BMJ Open. 2023 May 25;13(5):e071309. doi: 10.1136/bmjopen-2022-071309.

Reference Type DERIVED
PMID: 37230521 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2020-005561-14

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

D9487C00001

Identifier Type: -

Identifier Source: org_study_id

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