MGTA-145 + Plerixafor in the Mobilization of HSCs for Allogeneic Transplant in Hematologic Malignancies

NCT ID: NCT04762875

Last Updated: 2024-11-06

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

7 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-06-16

Study Completion Date

2022-03-14

Brief Summary

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This research study tests a new medicine for mobilizing stem cells so they can be collected and used for allogeneic stem cell transplant for treatment of hematological malignancies. MGTA-145, the new medicine, will be given with plerixafor.

Detailed Description

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This is a Phase II, open-label, multicenter, prospective study of MGTA-145 + plerixafor mobilized HLA-matched sibling and matched unrelated donor allografts for myeloablative hematopoietic stem cell transplantation (HSCT) in recipients with hematological malignancies. Donors will undergo 1 or 2 days of mobilization and apheresis.

Conditions

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Related Donors Donating PBSC to a Family Member Healthy Donors Acute Myelogenous Leukemia Acute Lymphoblastic Leukemia Myelodysplastic Syndrome

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Single dose MGTA-145 plus plerixafor followed by apheresis

MGTA-145 in combination with plerixafor followed by apheresis on one or two consecutive days

Group Type EXPERIMENTAL

MGTA-145

Intervention Type BIOLOGICAL

MGTA-145 will be be administered as an IV infusion

Plerixafor

Intervention Type BIOLOGICAL

240 µg/kg subcutaneously

Interventions

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MGTA-145

MGTA-145 will be be administered as an IV infusion

Intervention Type BIOLOGICAL

Plerixafor

240 µg/kg subcutaneously

Intervention Type BIOLOGICAL

Other Intervention Names

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Mozobil

Eligibility Criteria

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Inclusion Criteria

* Donor medical suitability and eligibility will be determined following Institution or NMDP/Be The Match standards
* Age 18-65 years old at the time of signing informed consent
* 8/8 (HLA- A, B, C, and DRB1) HLA-matched sibling or volunteer unrelated donor
* Fulfill Institution or NMDP/Be The Match criteria to serve as a mobilized blood cell donor
* Serum creatinine \< 1.5 x institution upper limit of normal (ULN) or estimated creatinine clearance (CRCL) \> 50 mL/min using the Modification of Diet in Renal Disease Study (MDRD) equation or similar method


* At least 18 years old at the time of signing informed consent
* Has an available 8/8 (HLA- A, B, C, and DRB1) HLA-matched sibling or volunteer unrelated donor willing to donate peripheral blood stem cells (PBSC) for transplant
* Fulfill additional individual Transplant Center Criteria for transplant beyond NMDP/Be The Match criteria
* One of the following diagnoses:

* Acute myelogenous leukemia (AML) in 1st remission or beyond with ≤ 5% marrow blasts and no circulating blasts. Documentation of bone marrow assessment will be accepted within 45 days prior to the date of consent.
* Acute lymphoblastic leukemia (ALL) in 1st remission or beyond with ≤ 5% marrow blasts and no circulating blasts. Documentation of bone marrow assessment will be accepted within 45 days prior to the date of consent.
* Patients with myelodysplasia (MDS) with no circulating blasts and with less than 10% blasts in the bone marrow (higher blast percentage allowed in MDS due to lack of differences in outcomes with \< 5% or 5-10% blasts in MDS). Documentation of bone marrow assessment will be accepted within 45 days prior to the date of consent.
* Cardiac function: Left ventricular ejection fraction at least 45% based on most recent echocardiogram or MUGA results obtained via standard of care
* Estimated creatinine clearance acceptable per local institutional guidelines
* Pulmonary function: diffusing capacity of the lungs for carbon monoxide (DLCO) corrected for hemoglobin at least 50% and forced expiratory volume in first second (FEV1) predicted at least 50% based on most recent DLCO results obtained via standard of care
* Liver function acceptable per local institutional guidelines
* Karnofsky performance status (KPS) of 70% or greater
* Hematopoietic Cell Transplantation-Comorbidity Index (HCT-CI) score of 4 or less

Exclusion Criteria

* Donor unwilling or unable to give informed consent, or unable to comply with the protocol including required follow-up and testing
* Donor already enrolled on another investigational agent study
* Pregnant or breastfeeding females, sexually active female and male donors not willing or able to use adequate contraception, or males who do not agree to refrain from donating sperm, from the time of consent through 3 months after treatment with MGTA-145 + plerixafor


* Subject unwilling or unable to give informed consent, or unable to comply with the protocol including required follow-up and testing
* Subject whose donor does not meet the eligibility criteria and is a screen fail
* Subjects with a prior allogeneic transplant
* Subjects with active, uncontrolled infection at the time of the transplant preparative regimen
* Pregnant or breastfeeding females, sexually active female or male subjects not willing or able to use adequate contraception, or males who do not agree to refrain from donating sperm, from the time of consent through 3 months after PBSC infusion
* Subjects with clinical evidence of active Central Nervous System (CNS) tumor involvement as evidenced by documented disease on examination of spinal fluid or MRI within 45 days of start of conditioning
* A condition, which, in the opinion of the clinical investigator, would interfere with the evaluation of primary and secondary endpoints
* Planned treatment with a new investigational agent from the time of transplant through 30 days post-transplant
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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National Marrow Donor Program

OTHER

Sponsor Role collaborator

Ensoma

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Steven Devine, MD

Role: STUDY_CHAIR

National Marrow Donor Program

Locations

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City of Hope National Medical Center

Duarte, California, United States

Site Status

Stanford Health Care

Stanford, California, United States

Site Status

Emory University Hospital

Atlanta, Georgia, United States

Site Status

Mayo Clinic Rochester

Rochester, Minnesota, United States

Site Status

Roswell Park Cancer Institute

Buffalo, New York, United States

Site Status

Ohio State Medical Center, James Cancer Center

Columbus, Ohio, United States

Site Status

M.D. Anderson Cancer Center

Houston, Texas, United States

Site Status

Be The Match Collection Center Seattle

Seattle, Washington, United States

Site Status

Countries

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United States

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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145-ADS-202

Identifier Type: -

Identifier Source: org_study_id

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