A Study to Evaluate the Efficacy and Safety of CC-93538 in Adult and Adolescent Participants With Eosinophilic Esophagitis

NCT ID: NCT04753697

Last Updated: 2025-03-13

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

430 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-02-22

Study Completion Date

2024-08-29

Brief Summary

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Study CC-93538-EE-001 is a Phase 3, multicenter, multinational, randomized, double-blind, placebo-controlled induction and maintenance study to evaluate the efficacy and safety of CC- 93538 in adult and adolescent participants with eosinophilic esophagitis (EoE). The study will incorporate a 24-week Induction Phase followed by a 24-week Maintenance Phase.

Participants will be randomized at the beginning of the study into 3 treatment arms:

* Placebo for Induction and Maintenance
* CC-93538 360 mg Subcutaneous (SC) once weekly for Induction followed by 360 mg SC once every other week for Maintenance
* CC-93538 360 mg SC once weekly for Induction and Maintenance

Detailed Description

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Conditions

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Eosinophilic Esophagitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Administration of CC-93538

CC-93538 360 mg Subcutaneously (SC) once weekly for 24 weeks followed by CC-93538 360 mg SC once weekly for 24 weeks

Group Type EXPERIMENTAL

CC-93538

Intervention Type DRUG

Subcutaneous

Administration of CC-93538 and Placebo

CC-93538 360 mg SC once weekly for 24 weeks followed by CC-93538 360 mg SC once every other week for 24 weeks.

During the Maintenance Phase, matching placebo will be administered once every other week on alternate weeks to maintain the blind.

Group Type EXPERIMENTAL

CC-93538

Intervention Type DRUG

Subcutaneous

Placebo

Intervention Type OTHER

Subcutaneous

Administration of Placebo

Matching placebo SC once weekly for 24 weeks followed by matching placebo SC once weekly for 24 weeks

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Subcutaneous

Interventions

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CC-93538

Subcutaneous

Intervention Type DRUG

Placebo

Subcutaneous

Intervention Type OTHER

Other Intervention Names

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RPC4046

Eligibility Criteria

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Inclusion Criteria

Participants must satisfy the following criteria to be enrolled in the study:

1. Male or female patients aged ≥ 12 and ≤ 75 years, with a body weight of \> 40 kg.
2. Histologic evidence of eosinophilic esophagitis, defined as a peak count of ≥ 15 eosinophils/high-power field at 2 levels of the esophagus.

3 Participant-reported history of 4 or more Dysphagia Days within 2 consecutive weeks prior to end of screening.

4\. Lack of complete response to an adequate trial of proton pump inhibitor (8 weeks). Participants on a proton pump inhibitor must have been on a stable dose for at least 4 weeks prior to first Screening Visit and agree to continue the same dose throughout the study.

5\. Participants currently receiving inhaled corticosteroids, leukotriene receptor antagonists, or mast cell stabilizers for indications other than EoE, or medium potency topical corticosteroids for dermatologic conditions, must maintain stable doses for at least 4 weeks prior to the first Screening Visit and throughout the duration of the study.

6\. Participants must agree to maintain a stable diet (including any food elimination diet for the treatment of food allergy or eosinophilic esophagitis) and not introduce any changes in their diet from the first Screening Visit to the end of the study.

7\. Females of childbearing potential must have 2 negative pregnancy tests as verified by the Investigator prior to starting study therapy and agree to practice a highly effective method of contraception until 5 months after the last dose.

Exclusion Criteria

The presence of any of the following will exclude a participant from enrollment:

1. Clinical or endoscopic evidence of other diseases that may affect the histologic, endoscopic, and clinical symptom evaluation for this study.
2. Other gastrointestinal disorders such as active Helicobacter pylori infection, esophageal varices, gastritis, colitis, celiac disease, Mendelian disorder associated with eosinophilic esophagitis, liver function impairment, or a known hereditary fructose intolerance.
3. Evidence of a severe endoscopic structural abnormality in the esophagus.
4. Esophageal dilation for symptom relief within 8 weeks prior to first Screening Visit or during the Screening Period, or if esophageal dilation is anticipated within 48 weeks of dosing during the study.
5. Evidence of immunosuppression, or of having received systemic immunosuppressive or immunomodulating drugs within 5 drug half-lives prior to the first Screening Visit.
6. Treatment with a high potency topical corticosteroid for dermatologic use, or a systemic corticosteroid within 8 weeks of the first Screening Visit.
7. Treatment with a swallowed topical corticosteroid, leukotriene receptor antagonist, or mast cell stabilizer for EoE, within 4 weeks of the first Screening Visit.
8. Treatment with oral or sublingual immunotherapy within 6 months of the first Screening Visit (any use will be prohibited during the study). Subcutaneous immunotherapy may be allowed if on stable doses for at least 3 months prior to the first Screening Visit and during the study.
9. Actively successful dietary modification adherence (e.g. food elimination diet), resulting in a complete response to EoE.
10. Prior treatment with CC-93538 during a Phase 1 or 2 clinical study.
11. Receipt of a live attenuated vaccine within 4 weeks of the first Screening Visit.
12. Any disease that would affect the conduct of the protocol or interpretation of the study results, or would put a patient at risk by participating in the study (e.g. severe uncontrolled asthma, infection causing eosinophilia, hypereosinophilic syndrome, or cardiovascular condition, or neurologic disorder or psychiatric illness that compromises the Participant's ability to accurately document symptoms of eosinophilic esophagitis).
13. Active or ongoing infections including parasitic/helminthic, hepatitis, tuberculosis, or human immunodeficiency virus.
14. Severe acute respiratory syndrome coronavirus 2 (SARS-CoV-2) infection within 4 weeks of the first Screening Visit.
15. Females who are pregnant or lactating.
Minimum Eligible Age

12 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Celgene

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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Local Institution - 144

Birmingham, Alabama, United States

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Tuscaloosa, Alabama, United States

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Phoenix, Arizona, United States

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Phoenix, Arizona, United States

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Scottsdale, Arizona, United States

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Tucson, Arizona, United States

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North Little Rock, Arkansas, United States

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Lancaster, California, United States

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Los Angeles, California, United States

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Oakland, California, United States

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San Diego, California, United States

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Aurora, Colorado, United States

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Colorado Springs, Colorado, United States

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Denver, Colorado, United States

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Littleton, Colorado, United States

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Wheat Ridge, Colorado, United States

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Bristol, Connecticut, United States

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Farmington, Connecticut, United States

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Hamden, Connecticut, United States

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Clearwater, Florida, United States

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Inverness, Florida, United States

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Jacksonville, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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North Miami Beach, Florida, United States

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Orlando, Florida, United States

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Orlando, Florida, United States

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Orlando, Florida, United States

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Pinellas Park, Florida, United States

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Plantation, Florida, United States

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Port Orange, Florida, United States

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Sweetwater, Florida, United States

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Atlanta, Georgia, United States

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Atlanta, Georgia, United States

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Atlanta, Georgia, United States

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Macon, Georgia, United States

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Idaho Falls, Idaho, United States

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Chicago, Illinois, United States

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Gurnee, Illinois, United States

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Indianapolis, Indiana, United States

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Clive, Iowa, United States

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Iowa City, Iowa, United States

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Kansas City, Kansas, United States

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Florence, Kentucky, United States

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Louisville, Kentucky, United States

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Baton Rouge, Louisiana, United States

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Metairie, Louisiana, United States

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Metairie, Louisiana, United States

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Baltimore, Maryland, United States

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Catonsville, Maryland, United States

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Columbia, Maryland, United States

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Glen Burnie, Maryland, United States

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Hagerstown, Maryland, United States

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Boston, Massachusetts, United States

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Boston, Massachusetts, United States

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Framingham, Massachusetts, United States

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South Dartmouth, Massachusetts, United States

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Springfield, Massachusetts, United States

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Worcester, Massachusetts, United States

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Troy, Michigan, United States

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Wyoming, Michigan, United States

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Plymouth, Minnesota, United States

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Rochester, Minnesota, United States

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Flowood, Mississippi, United States

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Kansas City, Missouri, United States

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St Louis, Missouri, United States

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Omaha, Nebraska, United States

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Lebanon, New Hampshire, United States

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Albuquerque, New Mexico, United States

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Great Neck, New York, United States

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New York, New York, United States

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New York, New York, United States

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Syracuse, New York, United States

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Syracuse, New York, United States

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Chapel Hill, North Carolina, United States

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Charlotte, North Carolina, United States

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Durham, North Carolina, United States

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Greensboro, North Carolina, United States

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Kinston, North Carolina, United States

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Beavercreek, Ohio, United States

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Cincinnati, Ohio, United States

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Cincinnati, Ohio, United States

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Cincinnati, Ohio, United States

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Cleveland, Ohio, United States

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Columbus, Ohio, United States

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Columbus, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Hershey, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pottsville, Pennsylvania, United States

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Providence, Rhode Island, United States

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Anderson, South Carolina, United States

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Greenville, South Carolina, United States

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Chattanooga, Tennessee, United States

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Nashville, Tennessee, United States

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Cedar Park, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Rockwell, Texas, United States

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San Antonio, Texas, United States

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Southlake, Texas, United States

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Tyler, Texas, United States

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Draper, Utah, United States

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Ogden, Utah, United States

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Salt Lake City, Utah, United States

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Leesburg, Virginia, United States

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Lynchburg, Virginia, United States

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Richmond, Virginia, United States

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Roanoke, Virginia, United States

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Spokane, Washington, United States

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Vancouver, Washington, United States

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Milwaukee, Wisconsin, United States

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Milwaukee, Wisconsin, United States

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Casper, Wyoming, United States

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Buenos Aires, , Argentina

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Mar del Plata, , Argentina

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Quilmes, , Argentina

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Concord, New South Wales, Australia

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Liverpool, New South Wales, Australia

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Westmead, New South Wales, Australia

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Maroorchydore, Queensland, Australia

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South Brisbane, Queensland, Australia

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Woolloongabba, Queensland, Australia

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Adelaide, South Australia, Australia

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Elizabeth Vale, South Australia, Australia

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Clayton, Victoria, Australia

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Footscray, Victoria, Australia

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Melbourne, Victoria, Australia

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Murdoch, Western Australia, Australia

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Fitzroy, , Australia

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Western Australia, , Australia

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Burgenland, , Austria

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Graz, , Austria

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Linz, , Austria

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Brussels, , Belgium

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Kortrijk, , Belgium

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Leuven, , Belgium

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West-Vlaanderen, , Belgium

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Calgary, Alberta, Canada

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Edmonton, Alberta, Canada

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Edmonton, Alberta, Canada

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Vancouver, British Columbia, Canada

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Victoria, British Columbia, Canada

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Ottawa, Ontario, Canada

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Vaughan, Ontario, Canada

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Bayern, , Germany

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Brandenburg, , Germany

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Frankfurt am Main, , Germany

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Hamburg, , Germany

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Leipzig, , Germany

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Leipzig, , Germany

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München, , Germany

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München, , Germany

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Haifa, , Israel

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Holon, , Israel

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Jerusalem, , Israel

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Jerusalem, , Israel

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Tel Aviv, , Israel

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Ẕerifin, , Israel

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Genova, , Italy

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Milan, , Italy

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Padua, , Italy

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Pisa, , Italy

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Rome, , Italy

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Nishinomiya, Hyōgo, Japan

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Bunkyo-ku, Tokyo, Japan

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Setagaya-ku, Tokyo, Japan

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Akita, , Japan

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Isehara City, Kanagawa, , Japan

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Kobe, , Japan

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Maebashi, , Japan

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Nagoya, , Japan

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Nagoya, , Japan

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Niigata, , Japan

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Okayama, , Japan

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Osaka, , Japan

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Shibukawa, , Japan

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Shinjuku-Ku, , Japan

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Tokyo, , Japan

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Toyoake, , Japan

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Yamagata, , Japan

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Bydgoszcz, , Poland

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Częstochowa, , Poland

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Gdansk, , Poland

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Katowice, , Poland

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Lódz, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Wroclaw, , Poland

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Wroclaw, , Poland

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Lisbon, , Portugal

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Lisbon, , Portugal

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Porto, , Portugal

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Porto, , Portugal

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Barcelona, , Spain

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Córdoba, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Marbella, , Spain

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Seville, , Spain

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Lausanne, , Switzerland

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Belfast Northern Ireland, , United Kingdom

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Birmingham, , United Kingdom

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Cardiff, , United Kingdom

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Chorley, , United Kingdom

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Hexam, , United Kingdom

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Liverpool, , United Kingdom

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Local Institution - 237

Manchester, , United Kingdom

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Local Institution - 226

Southampton, , United Kingdom

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Countries

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United States Argentina Australia Austria Belgium Canada Germany Israel Italy Japan Poland Portugal Spain Switzerland United Kingdom

References

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Dellon ES, Charriez CM, Zhang S, Falk GW, Oliva S, Ma C, Siffledeen J, Schroeder S, Philpott H, Vanuytsel T, Abe Y, Li K, Zema CL, Venkatasamy A, Yeshokumar AK, Oh YS, Schoepfer A. Cendakimab in Adults and Adolescents with Eosinophilic Esophagitis. NEJM Evid. 2025 Oct;4(10):EVIDoa2500095. doi: 10.1056/EVIDoa2500095. Epub 2025 Sep 23.

Reference Type DERIVED
PMID: 40985784 (View on PubMed)

Charriez CM, Zhang S, de Oliveira CHMC, Patel V, Oh YS, Hirano I, Schoepfer A, Dellon ES. Design of a phase 3, randomized, double-blind, placebo-controlled, 48-week study to evaluate the efficacy and safety of cendakimab in adult and adolescent patients with eosinophilic esophagitis. Contemp Clin Trials. 2024 Dec;147:107708. doi: 10.1016/j.cct.2024.107708. Epub 2024 Oct 9.

Reference Type DERIVED
PMID: 39384067 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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U1111-1263-4351

Identifier Type: REGISTRY

Identifier Source: secondary_id

2020-004336-16

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CC-93538-EE-001

Identifier Type: -

Identifier Source: org_study_id

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