Efficacy and Safety of Calcifediol vs Placebo in Subjects With Vitamin D Deficiency

NCT ID: NCT04735926

Last Updated: 2023-09-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

674 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-12-23

Study Completion Date

2023-04-25

Brief Summary

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This is a randomised, double-blind, double-dummy, multicentre, dose-ranging clinical trial in subjects with vitamin D deficiency or insufficiency. Its general objective is to determine the efficacy and safety of different doses of calcifediol soft gelatin capsules (SGCs) compared to placebo.

Detailed Description

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Conditions

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Vitamin D Deficiency Vitamin D Insufficiency

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Group 1A

Subjects corresponding to Cohort 1 (25-OH-D baseline level \> 10 to \< 20 ng/mL)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Soft gelatin capsule. Oral administration once per week.

Placebo

Intervention Type OTHER

Soft gelatin capsule. Oral administration once per week.

Group 1B

Subjects corresponding to Cohort 1 (25-OH-D baseline level \> 10 to \< 20 ng/mL)

Group Type EXPERIMENTAL

Calcifediol 75mcg

Intervention Type DRUG

Soft gelatin capsule. Oral administration once per week

Placebo

Intervention Type OTHER

Soft gelatin capsule. Oral administration once per week.

Group 1C

Subjects corresponding to Cohort 1 (25-OH-D baseline level \> 10 to \< 20 ng/mL)

Group Type EXPERIMENTAL

Calcifediol 100mcg

Intervention Type DRUG

Soft gelatin capsule. Oral administration once per week

Placebo

Intervention Type OTHER

Soft gelatin capsule. Oral administration once per week.

Group 2A

Subjects corresponding to Cohort 2 (25-OH-D baseline level ≤ 10 ng/mL)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Soft gelatin capsule. Oral administration once per week.

Placebo

Intervention Type OTHER

Soft gelatin capsule. Oral administration once per week.

Group 2B

Subjects corresponding to Cohort 2 (25-OH-D baseline level ≤ 10 ng/mL)

Group Type EXPERIMENTAL

Calcifediol 100mcg

Intervention Type DRUG

Soft gelatin capsule. Oral administration once per week

Placebo

Intervention Type OTHER

Soft gelatin capsule. Oral administration once per week.

Group 2C

Subjects corresponding to Cohort 2 (25-OH-D baseline level ≤ 10 ng/mL)

Group Type EXPERIMENTAL

Calcifediol 125mcg

Intervention Type DRUG

Soft gelatin capsule. Oral administration once per week.

Placebo

Intervention Type OTHER

Soft gelatin capsule. Oral administration once per week.

Interventions

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Calcifediol 75mcg

Soft gelatin capsule. Oral administration once per week

Intervention Type DRUG

Calcifediol 100mcg

Soft gelatin capsule. Oral administration once per week

Intervention Type DRUG

Calcifediol 125mcg

Soft gelatin capsule. Oral administration once per week.

Intervention Type DRUG

Placebo

Soft gelatin capsule. Oral administration once per week.

Intervention Type OTHER

Placebo

Soft gelatin capsule. Oral administration once per week.

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Male or female subjects ≥ 18 years of age.
* Evidence of serum 25-OH-D levels \< 20 ng/mL or ≤ 10 ng/mL, for each cohort.
* Written informed consent.
* For females of childbearing potential only: willing to perform pregnancy tests, must agree to use highly effective methods of birth control throughout the study.

Exclusion Criteria

* Subjects receiving any treatment with calcifediol, vitamin D analogues, vitamin complexes or vitamin D supplements.
* Subjects taking drugs that could modify vitamin D levels.
* Subjects taking calcium supplements.
* Uncorrected hypercalcaemia, known hypercalciuria or nephrolithiasis.
* Severe renal impairment.
* Subjects diagnosed with liver or biliary failure, congestive heart failure, malabsorption, primary hyperparathyroidism, hypothyroidism, prolonged immobilisation, sarcoidosis, tuberculosis or other granulomatous diseases or hyperthyroidism.
* Any present or previous malignancy.
* Known contraindications or sensitivities to the use of the IP or any of its components.
* Pregnant woman, breastfeeding woman or woman planning a pregnancy.
* Subject has received an IP within 30 days before the start of the screening or is currently enrolled in an investigational interventional study.
* Any condition that may jeopardise the clinical trial conduct according to the protocol.
* Employees of the investigator or clinical trial site, as well as family members of the employees or the principal investigator.
* Person committed to an institution by virtue of an order issued either by judicial or other authorities.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Faes Farma, S.A.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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MC-1-Sevlievo Ltd.

Sevlievo, , Bulgaria

Site Status

Diagnostic & Consultative Center "Sveta Anna" EOOD

Sofia, , Bulgaria

Site Status

Individual Practice Ambulatory for Specialized Medical Care - Cardiology, Obstetrics and Gynecology

Sofia, , Bulgaria

Site Status

IV MHAT - Sofia

Sofia, , Bulgaria

Site Status

Lora - Medical center Sofia

Sofia, , Bulgaria

Site Status

Medical Centre Asklepion - Research in human medicine

Sofia, , Bulgaria

Site Status

Medical Centre Salvebis

Sofia, , Bulgaria

Site Status

Alergologie Němcová, s.r.o.

Brno, , Czechia

Site Status

Poliklinika Choceň - Neurologická ambulance

Choceň, , Czechia

Site Status

MUDr. Eva Richterová - HK, s.r.o.

Hradec Králové, , Czechia

Site Status

MUDr. Tomáš Edelsberger

Krnov, , Czechia

Site Status

G-CENTRUM Olomouc s.r.o.

Olomouc, , Czechia

Site Status

Centrum gynekologické rehabilitace s.r.o.

Písek, , Czechia

Site Status

Centrum pro diagnostiku a léčbu myasthenia gravis - Neurologická klinika 1. LF UK a VFN v Praze

Prague, , Czechia

Site Status

MediCel, s.r.o.

Prague, , Czechia

Site Status

Milan Kvapil s.r.o.

Prague, , Czechia

Site Status

RS centrum - Neurologická klinika 1.LF UK a VFN v Praze

Prague, , Czechia

Site Status

Ordinace MediFem, s.r.o.

Teplice, , Czechia

Site Status

CHU Bordeaux, Hôpital Pellegrin

Bordeaux, , France

Site Status

CHR Orléans, Service Rhumatologie

Orléans, , France

Site Status

CHU Saint Etienne, Hôpital Nord

Saint-Etienne, , France

Site Status

CHU Purpan

Toulouse, , France

Site Status

Fondazione IRCCS Cà Granda - Ospedale Maggiore Policlinico -UOC Endocrinologia e Malattie Metaboliche

Milan, , Italy

Site Status

IRCCS Ospedale San Raffaele /Unità di Endocrinologia

Milan, , Italy

Site Status

Azienda Ospedaliero Universitaria - Università degli Studi della Campania Luigi Vanvitelli - UOC di Medicina Fisica e Riabilitazione

Napoli, , Italy

Site Status

UOC di Riabilitazione -Azienda Ospedaliero Universitaria Paolo Giaccone Palermo

Palermo, , Italy

Site Status

AOU Pisana - Centro di Farmacologia Clinica per la Sperimentazione dei Farmaci

Pisa, , Italy

Site Status

Fondazione PTV -Policlinico Ospedaliero Universitario Tor Vergata - U.O.C. Ortopedia e Traumatologia

Roma, , Italy

Site Status

Institut za reumatologiju

Belgrade, , Serbia

Site Status

Klinički centar Kragujevac, Centar za reumatologiju, alergologiju i kliničku imunologiju, Odeljenje za reumatologiju

Kragujevac, , Serbia

Site Status

Institut za lečenje i rehabilitaciju "Niška Banja" Niš, Klinika za reumatologiju

Niška Banja, , Serbia

Site Status

Klinički centar Vojvodine, Klinika za endokrinologiju, dijabetes i bolesti metabolizma

Novi Sad, , Serbia

Site Status

Specijalna bolnica za reumatske bolesti Novi Sad

Novi Sad, , Serbia

Site Status

Opšta bolnica "Đorđe Joanović" Zrenjanin, Odeljenje za reumatologiju

Zrenjanin, , Serbia

Site Status

IN MEDIC s.r.o., Neurologická ambulancia

Bardejov, , Slovakia

Site Status

ALERGO H2B, s.r.o., Ambulancia klinickej imunológie a alergológie

Komárno, , Slovakia

Site Status

ALERSA, s.r.o., Ambulancia klinickej imunológie a alergológie

Košice, , Slovakia

Site Status

Endomed, s.r.o. - Gastroenterologická ambulancia

Košice, , Slovakia

Site Status

DANIMED, s.r.o., Ambulancia klinickej imunológie a alergológie

Levice, , Slovakia

Site Status

KARDIO 1, s.r.o., Kardiologická ambulancia

Lučenec, , Slovakia

Site Status

Elte HU, s.r.o., Chirurgická ambulancia

Rimavská Sobota, , Slovakia

Site Status

Kardioamb, s.r.o., Kardiologická a interná ambulancia

Rimavská Sobota, , Slovakia

Site Status

MEDILEX, s.r.o., Ambulancia vnútorného lekárstva

Rimavská Sobota, , Slovakia

Site Status

Zoll-Med, s.r.o., Ambulancia klinickej imunológie a alergológie

Rimavská Sobota, , Slovakia

Site Status

Pľúcna ambulancia Hrebenár, s.r.o. - Pneumologicko-ftizeologická ambulancia

Spišská Nová Ves, , Slovakia

Site Status

ANA JJ, s.r.o., Ambulancia klinickej imunológie a alergológie

Topoľčany, , Slovakia

Site Status

KK Neuro, s.r.o., Neurologická ambulancia

Žilina, , Slovakia

Site Status

Clínica Sagrada Familia

Barcelona, , Spain

Site Status

EAP Sardenya

Barcelona, , Spain

Site Status

Hospital del Mar

Barcelona, , Spain

Site Status

Hospital Quirónsalud Barcelona

Barcelona, , Spain

Site Status

Hospital Universitario Quirónsalud Madrid

Pozuelo de Alarcón, , Spain

Site Status

Complejo Asistencial Universitario de Salamanca

Salamanca, , Spain

Site Status

Hospital Universitario Marqués de Valdecilla

Santander, , Spain

Site Status

Hospital Universitario Rio Hortega

Valladolid, , Spain

Site Status

Countries

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Bulgaria Czechia France Italy Serbia Slovakia Spain

Other Identifiers

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HIDR-0320/DR

Identifier Type: -

Identifier Source: org_study_id

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