Effects of FT011 in Systemic Sclerosis

NCT ID: NCT04647890

Last Updated: 2023-12-20

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

30 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-07-19

Study Completion Date

2022-11-16

Brief Summary

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FT011 is an anti-fibrotic drug that is being tested as a treatment for scleroderma. This study is being conducted to see what the body does to the drug (pharmacokinetics), and what the drug does to the body (pharmacodynamics).

Detailed Description

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Conditions

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Scleroderma, Systemic Scleroderma, Diffuse Sclerosis, Systemic

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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FT011 200mg

200mg once daily for 12 weeks

Group Type EXPERIMENTAL

FT011

Intervention Type DRUG

Two x 100mg capsules once daily for 12 weeks

FT011 400mg

400mg once daily for 12 weeks

Group Type EXPERIMENTAL

FT011

Intervention Type DRUG

Two x 200mg capsules once daily for 12 weeks

Placebo

Placebo once daily for 12 weeks

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Two placebo capsules once daily for 12 weeks

Interventions

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FT011

Two x 100mg capsules once daily for 12 weeks

Intervention Type DRUG

FT011

Two x 200mg capsules once daily for 12 weeks

Intervention Type DRUG

Placebo

Two placebo capsules once daily for 12 weeks

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Provide written informed consent prior to any study procedures and who agree to adhere to all protocol requirements.
2. Aged 18 to 75 years inclusive at the time of consent.
3. Have a classification of systemic sclerosis, as defined by American College of Rheumatology (ACR) and European League Against Rheumatism (EULAR) criteria with disease duration ≤10 years from first non-Raynaud phenomenon manifestation.
4. Have a diagnosis of diffuse cutaneous SSc defined as systemic sclerosis with skin thickening on the upper arms proximal to the elbows, on the upper legs proximal to the knees, or on the trunk.
5. Have skin thickening in a body area suitable for repeat biopsy.
6. Have a mRSS at Screening of ≥15 to ≤40.
7. FVC ≥50% of predicted at Screening.
8. If on azathioprine, mycophenolate mofetil, or hydroxychloroquine, have been on a stable dose for at least 2 months prior to baseline.
9. Women of childbearing potential (WOCPB) and males with partners of child-bearing potential must agree to use highly effective contraception (a failure rate of \<1%), for the duration of the study and until three months after their last dose of IMP.

Exclusion Criteria

1. Pregnant or breast-feeding, or plan to become pregnant during the study.
2. Have received any IMP within 30 days or 5 half-lives prior to randomisation (4 months if the previous drug was a new chemical entity), whichever is longer.
3. Have known or suspected contraindications to the IMP.
4. Have severe or unstable SSc or end-stage organ involvement as evidenced by:

1. On an organ transplantation list or has received an organ transplant including autologous stem cell transplant.
2. Renal crisis within 1 year prior to Baseline.
5. Interstitial lung disease or pulmonary hypertension requiring constant oxygen therapy. This excludes oxygen used to aid sleep or exercise.
6. Gastrointestinal dysmotility requiring total parenteral nutrition or requiring hospitalisation within the 6 months prior to Baseline.
7. Concomitant inflammatory myositis, rheumatoid arthritis, or systemic lupus erythematosus when definite classification criteria for those diseases are met (Bohan and Peter criteria for polymyositis and dermatomyositis)
8. SSc-like illnesses related to exposures or ingestions
9. The use of the following drugs within the specified periods:

1. Methotrexate in the 2 weeks prior to Day 1
2. Other anti-fibrotic agents including D-penicillamine or tyrosine kinase inhibitors (nilotinib, imatinib, dasatinib) in the month prior to Screening.
3. Biologic drugs such as tumour necrosing factor (TNF) inhibitors, tocilizumab, or Janus kinase (JAK) inhibitors, in the 3 months prior to Screening.
4. Rituximab in the 6 months prior to Screening.
5. Cyclophosphamide oral or IV in the 3 months prior to Screening.
6. Oral prednisolone \>10 mg per day or IV steroids in the month prior to Screening.
10. Have any malignancy not considered cured (except basal cell or squamous cell carcinoma of the skin, or carcinoma in situ of the cervix); a subject is considered cured if there has been no evidence of cancer recurrence for the 6 years prior to randomisation.
11. Have aspartate transaminase (AST), alanine transaminase (ALT), gamma-glutamyl transferase (GGT), lactate dehydrogenase (LDH), or bilirubin values above the upper limit of normal (ULN) at Screening or Baseline, or evidence of hepatic disease as determined by any one of the following: history of hepatic encephalopathy, history of oesophageal varices, or history of portacaval shunt.
12. Estimated glomerular filtration rate (eGFR) \<60mL/min, urinary albumin/creatinine ratio \>30mg/g.
13. Haemoglobin \< 80 g/L, platelets \< 90 x 109/L, or neutrophil count \< 1.4 x 109/L
14. Other than SSc, have any other medical condition or significant co-morbidities, clinically relevant social or psychiatric conditions, or any finding during Screening, which in the investigator's opinion may put the subject at risk or interfere with the study objectives.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Certa Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Darren Kelly, PhD

Role: STUDY_DIRECTOR

Certa Therapeutics Pty Ltd

Locations

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Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

St Vincent's Hospital Melbourne

Fitzroy, Victoria, Australia

Site Status

Certa SSc trial site

Nijmegen, , Netherlands

Site Status

Certa SSc trial site

Bydgoszcz, , Poland

Site Status

Certa SSc trial site

Krakow, , Poland

Site Status

Certa SSc trial site

Malbork, , Poland

Site Status

Certa SSc trial site

Warsaw, , Poland

Site Status

Certa SSc trial site

Barcelona, , Spain

Site Status

Certa SSc trial site

Kyiv, , Ukraine

Site Status

Certa SSc trial site

Poltava, , Ukraine

Site Status

Countries

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Australia Netherlands Poland Spain Ukraine

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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CER-FT011-SSc01

Identifier Type: -

Identifier Source: org_study_id