A Trial to Evaluate the Efficacy, Durability, and Safety of KSI-301 Compared to Aflibercept in Participants With Diabetic Macular Edema (DME)

NCT ID: NCT04611152

Last Updated: 2024-08-22

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

460 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-09-30

Study Completion Date

2023-08-31

Brief Summary

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This Phase 3 study will evaluate the efficacy, durability, and safety of KSI-301 compared to aflibercept in participants with treatment-naïve DME.

Detailed Description

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This is a Phase 3, prospective, randomized, double-masked, two-arm, multi-center non-inferiority study evaluating the efficacy and safety of repeated intravitreal dosing of KSI-301 5 mg in participants with treatment-naïve DME.

The primary endpoint will be assessed at Year 1; additional secondary endpoints for efficacy will be assessed at Years 1 and 2.

Conditions

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Diabetic Macular Edema

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Participants will be randomized 1:1 into one of two treatment arms: KSI-301 or aflibercept.
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Outcome Assessors
For masking purposes, sham injections will be administered at every monthly visit if an active treatment is not administered. To preserve masking, two investigators are required for this study. The masked Investigator will be responsible for the examinations and safety assessments. The unmasked Investigator will perform the injections and post-treatment assessments.

Study Groups

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KSI-301 (Arm A)

Intravitreal injection of KSI-301 (5 mg) once every 4 weeks for 3 monthly doses followed by an individualized dosing regimen (every 8 to 24 weeks) via intravitreal injection from Week 16 to Week 100.

Group Type EXPERIMENTAL

KSI-301

Intervention Type DRUG

Intravitreal Injection

Sham Procedure

Intervention Type OTHER

The sham is a procedure that mimics an intravitreal injection. It involves pressing the blunt end of an empty syringe (without a needle) against the anesthetized eye. It will be administered to participants in both treatments arms at applicable visits to maintain masking.

Aflibercept (Arm B)

Intravitreal injection of aflibercept (2 mg) once every 4 weeks for 5 monthly doses followed by aflibercept (2 mg) once every 8 weeks via intravitreal injection from Week 24 to 100.

Group Type ACTIVE_COMPARATOR

Aflibercept

Intervention Type DRUG

Intravitreal Injection

Sham Procedure

Intervention Type OTHER

The sham is a procedure that mimics an intravitreal injection. It involves pressing the blunt end of an empty syringe (without a needle) against the anesthetized eye. It will be administered to participants in both treatments arms at applicable visits to maintain masking.

Interventions

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KSI-301

Intravitreal Injection

Intervention Type DRUG

Aflibercept

Intravitreal Injection

Intervention Type DRUG

Sham Procedure

The sham is a procedure that mimics an intravitreal injection. It involves pressing the blunt end of an empty syringe (without a needle) against the anesthetized eye. It will be administered to participants in both treatments arms at applicable visits to maintain masking.

Intervention Type OTHER

Other Intervention Names

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Eylea

Eligibility Criteria

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Inclusion Criteria

1. Signed informed consent prior to participation in the study.
2. Treatment-naïve diabetic macular edema, with vision loss and center involvement (if present) diagnosed within 9 months of screening.
3. BCVA ETDRS letter score between 78 and 25 (-20/25 to 20/320 Snellen equivalent), inclusive, in the Study Eye.
4. CST of ≥ 320 microns on SD-OCT (Heidelberg Spectralis or equivalent on other OCT instruments) as determined by the Reading Center.
5. Decrease in vision determined by the Investigator to be primarily the result of DME.
6. Type 1 or Type 2 diabetes mellitus and a HbA1c of ≤12%.

Exclusion Criteria

1. Macular edema in the Study Eye considered to be secondary to a cause other than DME.
2. Active iris or angle neovascularization or neovascular glaucoma in the Study Eye.
3. High-risk proliferative diabetic retinopathy characteristics in the Study Eye.
4. History of Pan-retinal Photocoagulation (PRP) laser in the Study Eye within 3 months of screening.
5. Tractional retinal detachment in the Study Eye.
6. Active retinal disease other than the condition under investigation in the Study Eye.
7. Any history or evidence of a concurrent ocular condition present, that in the opinion of the Investigator could require either medical or surgical intervention or affect macular edema or alter visual acuity during the study (e.g., vitreomacular traction, epiretinal membrane).
8. Active or suspected ocular or periocular infection or inflammation in either eye at Day 1.
9. Any prior use of an approved or investigational treatment for DME in the Study Eye (e.g., anti-VEGF, intraocular or periocular steroids, macular laser photocoagulation).
10. Women who are pregnant or lactating or intending to become pregnant during the study.
11. Uncontrolled blood pressure defined as a systolic value ≥ 180 mmHg or diastolic value ≥100 mmHg while at rest.
12. Recent history (within the 6 months prior to screening) of myocardial infarction, stroke, transient ischemic attack, acute congestive heart failure or any acute coronary event.
13. History of a medical condition that, in the judgment of the Investigator, would preclude scheduled study visits, completion of the study, or a safe administration of investigational product.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Kodiak Sciences Inc

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pablo Velazquez-Martin, MD

Role: STUDY_DIRECTOR

Kodiak Sciences Inc

Locations

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UCSD Jacobs Retina Center

La Jolla, California, United States

Site Status

Retina Consultants of Southern California

Redlands, California, United States

Site Status

California Retina Consultants

Santa Maria, California, United States

Site Status

Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center

Torrance, California, United States

Site Status

Colorado Retina Associates PC

Lakewood, Colorado, United States

Site Status

Conneticut Eye Consultants

Danbury, Connecticut, United States

Site Status

Retina Group of Florida

Boca Raton, Florida, United States

Site Status

Blue Ocean Clinical Research

Clearwater, Florida, United States

Site Status

Vitreo Retinal Associates

Gainesville, Florida, United States

Site Status

Florida Retina Consultants

Lakeland, Florida, United States

Site Status

Florida Eye Associates

Melbourne, Florida, United States

Site Status

Florida Retina Institute

Orlando, Florida, United States

Site Status

Retina Specialty Institute

Pensacola, Florida, United States

Site Status

Retina Associates of Florida

Tampa, Florida, United States

Site Status

Retina Vitreous Associates of Florida

Tampa, Florida, United States

Site Status

Center for Retina & Macular Disease

Winter Haven, Florida, United States

Site Status

Springfield Clinic LLP

Springfield, Illinois, United States

Site Status

Wolfe Eye Clinic

West Des Moines, Iowa, United States

Site Status

Retina Associates PA

Lenexa, Kansas, United States

Site Status

Vitreo Retinal Consultants and Surgeons

Wichita, Kansas, United States

Site Status

Retina Associates of Kentucky

Lexington, Kentucky, United States

Site Status

Cumberland Valley Retina Consultants PC

Hagerstown, Maryland, United States

Site Status

Ophthalmic Consultants of Boston

Boston, Massachusetts, United States

Site Status

Foundation for Vision Research

Grand Rapids, Michigan, United States

Site Status

The Retina Center of New Jersey

Bloomfield, New Jersey, United States

Site Status

NJ Retina

Teaneck, New Jersey, United States

Site Status

Charlotte Eye Ear Nose & Throat Associates, P.A.

Charlotte, North Carolina, United States

Site Status

Retina Northwest

Portland, Oregon, United States

Site Status

Cascade Medical Research Institute

Springfield, Oregon, United States

Site Status

MidAtlantic Retina

Philadelphia, Pennsylvania, United States

Site Status

Retina Research of Beaufort

Beaufort, South Carolina, United States

Site Status

Charleston Neuroscience Institute - West Ashley

Charleston, South Carolina, United States

Site Status

Pametto Retina Center

Florence, South Carolina, United States

Site Status

Charleston Neuroscience Institute

Ladson, South Carolina, United States

Site Status

Palmetto Retina Center

West Columbia, South Carolina, United States

Site Status

Black Hills Regional Eye Institute

Rapid City, South Dakota, United States

Site Status

Charles Retina Institute

Germantown, Tennessee, United States

Site Status

Tennessee Retina PC

Nashville, Tennessee, United States

Site Status

Southwest Retina Specialists

Amarillo, Texas, United States

Site Status

Texas Retina Associates

Arlington, Texas, United States

Site Status

Austin Retina Associates

Austin, Texas, United States

Site Status

Star Retina

Burleson, Texas, United States

Site Status

Retina Consultants of Texas

Houston, Texas, United States

Site Status

Retina Consultants of San Antonio

San Antonio, Texas, United States

Site Status

Strategic Clinical Research Group, LLC

Willow Park, Texas, United States

Site Status

Piedmont Eye Center

Lynchburg, Virginia, United States

Site Status

Retina Center Northwest

Silverdale, Washington, United States

Site Status

Spokane Eye

Spokane, Washington, United States

Site Status

Universitätsklinikum Freiburg

Freiburg im Breisgau, Baden-Wurttemberg, Germany

Site Status

Universitätsklinikum Regensburg

Regensburg, Bavaria, Germany

Site Status

Dietrich Bonhoeffer Klinikum Neubrandenburg

Neubrandenburg, Mecklenburg-Vorpommern, Germany

Site Status

St. Elisabeth Krankenhaus

Cologne, North Rhine-Westphalia, Germany

Site Status

St Franziskus Hospital

Münster, North Rhine-Westphalia, Germany

Site Status

Jahn Ferenc Dél-Pesti Kórház és Rendelointézet

Budapest, , Hungary

Site Status

Ganglion Medical Center

Pécs, , Hungary

Site Status

Fondazione PTV Policlinico Tor Vergata

Roma, , Italy

Site Status

Signes Ozolinas Doctor Praxis In Ophthalmology

Jelgava, , Latvia

Site Status

Pauls Stradins Clinical University Hospital

Riga, , Latvia

Site Status

Riga Eastern Clinical University Hospital Clinic Bikernieki

Riga, , Latvia

Site Status

Latvian American Eye Center

Riga, , Latvia

Site Status

Emanuelli Research & Development Center LLC

Arecibo, , Puerto Rico

Site Status

Fakultna nemocnica s poliklinikou F. D. Roosevelta

Banská Bystrica, , Slovakia

Site Status

Univerzitna nemocnica Bratislava

Bratislava, , Slovakia

Site Status

Uvea Klinika, S.R.O.

Martin, , Slovakia

Site Status

Nemocnica s poliklinikou Trebisov a.s. Ocne oddelenie - jednonova zdravotna starostlivost

Trebišov, , Slovakia

Site Status

Fakultna nemocnica Trencin

Trencín, , Slovakia

Site Status

Fakultna nemocnica s poliklinikou Zilina

Žilina, , Slovakia

Site Status

Hospital dos de Maig

Barcelona, , Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Hospital Universitari General de Catalunya - Grupo Quironsalud

Barcelona, , Spain

Site Status

Hospital Universitario Puerta de Hierro - Majadahonda

Madrid, , Spain

Site Status

Hospital Universitari i Politecnic La Fe de Valencia

Valencia, , Spain

Site Status

Hospital Universitario Rio Hortega

Valladolid, , Spain

Site Status

Hospital Clinico Universitario Lozano Blesa

Zaragoza, , Spain

Site Status

Hospital Universitario Miguel Servet

Zaragoza, , Spain

Site Status

Countries

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United States Germany Hungary Italy Latvia Puerto Rico Slovakia Spain

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2020-001062-11

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

KS301P104

Identifier Type: -

Identifier Source: org_study_id

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