Study to Assess PT010 in Adult and Adolescent Participants With Inadequately Controlled Asthma (KALOS)

NCT ID: NCT04609878

Last Updated: 2025-04-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

2274 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-12-15

Study Completion Date

2025-03-21

Brief Summary

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This is a variable length study to evaluate the efficacy and safety of budesonide/glycopyrronium/formoterol inhaler in adults and adolescents with severe asthma inadequately controlled with standard of care

Detailed Description

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This is a randomized, double-blind, double dummy, parallel group, multicenter 24 to 52 week variable length study to assess the efficacy and safety of budesonide, glycopyrronium, and formoterol fumarate metered dose inhaler (MDI) relative to budesonide and formoterol fumarate MDI and Symbicort® pressurized MDI in adult and adolescent participants with inadequately controlled asthma. Approximately 2200 participants will be randomized globally.

Conditions

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Asthma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Budesonide, glycopyrronium, and formoterol fumarate (BGF) MDI 320/28.8/9.6 μg

BGF MDI 320/28.8/9.6 μg Budesonide, glycopyrronium, and formoterol fumarate (PT010) Metered Dose Inhaler (MDI)

Group Type EXPERIMENTAL

BGF MDI 320/28.8/9.6 μg

Intervention Type DRUG

Budesonide, glycopyrronium, and formoterol fumarate metered dose inhaler

BGF MDI 320/14.4/9.6 μg

BGF MDI 320/14.4/9.6 μg Budesonide, glycopyrronium, and formoterol fumarate (PT010) Metered Dose Inhaler (MDI)

Group Type EXPERIMENTAL

BGF MDI 320/14.4/9.6 μg

Intervention Type DRUG

Budesonide, glycopyrronium, and formoterol fumarate metered dose inhaler

Budesonide and formoterol fumarate (BFF) MDI 320/9.6 μg

BFF MDI 320/9.6 μg (Experimental/Comparator) Budesonide and formoterol fumarate (PT009) Metered Dose Inhaler (MDI)

Group Type ACTIVE_COMPARATOR

BFF MDI 320/9.6 μg

Intervention Type DRUG

Budesonide and formoterol fumarate metered dose inhaler

Symbicort®

Budesonide/ formoterol fumarate pressurized metered dose inhaler (pMDI) 320/9 μg

Group Type ACTIVE_COMPARATOR

BFF pMDI 320/9 μg

Intervention Type DRUG

Budesonide/formoterol fumarate pressurized metered dose inhaler

Interventions

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BGF MDI 320/28.8/9.6 μg

Budesonide, glycopyrronium, and formoterol fumarate metered dose inhaler

Intervention Type DRUG

BGF MDI 320/14.4/9.6 μg

Budesonide, glycopyrronium, and formoterol fumarate metered dose inhaler

Intervention Type DRUG

BFF MDI 320/9.6 μg

Budesonide and formoterol fumarate metered dose inhaler

Intervention Type DRUG

BFF pMDI 320/9 μg

Budesonide/formoterol fumarate pressurized metered dose inhaler

Intervention Type DRUG

Other Intervention Names

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BGF BGF BFF Symbicort®

Eligibility Criteria

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Inclusion Criteria

1. 12 to 80 years of age, male and female, BMI \<40 kg/m2; females must be not of childbearing potential or using a form of highly effective birth control.
2. Documented history of physician-diagnosed asthma \> and/or = 1 year prior to V1.
3. Regularly using a stable daily ICS/LABA regimen (including a stable ICS dose) with medium-to-high ICS doses for at least 4 weeks prior to V1.
4. ACQ-7 total score ≥1.5 at Visits 1, 3, and 5 (pre-randomization).
5. FEV1 % (assessed as an average of the 60 and 30 minute pre-dose assessments) predicted normal at V1, 2, 3, 4, and 5 (pre-randomization)

* Participants ≥ 18 years of age: \< 80%
* Participants 12 to \<18 years of age: \< 90%
6. FEV1 post-albuterol at V2 or V3 (if repeat needed).

* Participants \> and/or = 18 years of age: Increase \> and/or = 12% and \> and/or = 200 mL.
* Participants 12 to \<18 years of age: Increase =12% either in the 12 months prior to Visit 1 or at Visit 2, or at Visit 3.
* Note: Even if there is documented history of reversibility, all participants must be assessed for reversibility at Visit 2 (and Visit 3, if reversibility is not demonstrated at Visit 2) to provide reversibility baseline data for characterization.
7. Willing and, in the opinion of the Investigator, able to adjust current asthma therapy, as required by the protocol.
8. Demonstrate acceptable MDI/pMDI administration technique.
9. Received no asthma medication other than run-in BFF MDI BID and albuterol as needed during screening (except for allowed medications as defined in Table 9 and systemic corticosteroid or ICS for the treatment of an asthma exacerbation).
10. eDiary 14-day compliance ≥70% during screening (defined as completing the daily eDiary for any 10 mornings and any 10 evenings and answering "Yes" to taking 2 puffs of run-in BFF MDI for any 10 mornings and 10 evenings in the last 14 days prior to randomization).
11. No respiratory infection in the 4 weeks prior to randomization, or asthma exacerbation treated with systemic corticosteroid and/or additional ICS treatment in the 4 weeks prior to randomization.

Exclusion Criteria

1\. Completed treatment for respiratory infection or asthma exacerbation with systemic corticosteroids within 4 weeks of V1.

2a. Participants where, in the opinion of the Investigator, treatment with biological therapy for asthma would be appropriate.

2b. Any marketed or investigational biologics within 3 months or 5 half-lives of V1, whichever is longer and must not be used during study duration.

3\. Current smokers, former smokers with \>10 pack-years history, or former smokers who stopped smoking \<6 months prior to V1 (including all forms of tobacco, e-cigarettes or other vaping devices, and marijuana).

4\. Current evidence of Chronic Obstructive Pulmonary Disease (COPD).

5a. Oral and IV corticosteroid use (any dose) within 4 weeks of V1.

5b. Use of systemic corticosteroids for any other reason except for the acute treatment of severe asthma exacerbation is prohibited for the duration of the study.

5c. Depot corticosteroid use for any reason within 3 months of V1.

6\. Use of Long-Acting Muscarinic Antagonist (LAMA), either alone or as part of an inhaled combination therapy, in the 12 weeks prior to V1.

7\. Use of oral beta2-agonist within 3 months of V1.

8\. Use of any immunomodulators or immunosuppressive medication within 3 months or 5 half-lives, whichever is longer, and must not be used during the study duration.

9\. Narrow angle glaucoma not adequately treated and/or change in vision that may be relevant, in the opinion of the Investigator, within 3 months of Visit 1.

10\. Life-threatening asthma defined as a history of significant asthma episode(s) requiring intubation associated with hypercapnia, respiratory arrest, hypoxic seizures, or asthma-related syncopal episode(s).

11\. Hospitalization for asthma within 2 months of Visit 1.

12\. Known history of drug or alcohol abuse within 12 months of Visit 1.

13\. Regular use of a nebulizer or a home nebulizer for receiving asthma medications.

14\. Using any herbal products by inhalation or nebulizer within 4 weeks of Visit 1 and does not agree to stop during the study duration.

15\. Participation in another clinical study with a study intervention administered in the last 30 days or 5 half-lives, whichever is longer. Any other study intervention that is not identified in the protocol is prohibited for use during study duration.

16\. Participants with a known hypersensitivity to beta2-agonists, corticosteroids, anticholinergics, or any component of the MDI or pMDI.

17\. Study Investigators, sub-Investigators, coordinators, and their employees or immediate family members.

18\. For women only - currently pregnant (confirmed with positive highly sensitive pregnancy test), breast-feeding, or planned pregnancy during the study or not using acceptable contraception measures, as judged by the Investigator.
Minimum Eligible Age

12 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Saraland, Alabama, United States

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Phoenix, Arizona, United States

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Phoenix, Arizona, United States

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Sun City West, Arizona, United States

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Tucson, Arizona, United States

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Tucson, Arizona, United States

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Little Rock, Arkansas, United States

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Covina, California, United States

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Encinitas, California, United States

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Fresno, California, United States

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Laguna Hills, California, United States

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Long Beach, California, United States

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Los Angeles, California, United States

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Los Angeles, California, United States

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Mission Hills, California, United States

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Newport Beach, California, United States

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Northridge, California, United States

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San Diego, California, United States

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Stockton, California, United States

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Thousand Oaks, California, United States

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Upland, California, United States

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Westminster, California, United States

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Colorado Springs, Colorado, United States

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Lakewood, Colorado, United States

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Brandon, Florida, United States

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Miami, Florida, United States

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Tampa, Florida, United States

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Adairsville, Georgia, United States

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Atlanta, Georgia, United States

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Columbus, Georgia, United States

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Lawrenceville, Georgia, United States

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Rincon, Georgia, United States

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Savannah, Georgia, United States

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Tyrone, Georgia, United States

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Chicago, Illinois, United States

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River Forest, Illinois, United States

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Brownsburg, Indiana, United States

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Indianapolis, Indiana, United States

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Louisville, Kentucky, United States

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Crowley, Louisiana, United States

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Lafayette, Louisiana, United States

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Lake Charles, Louisiana, United States

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Bangor, Maine, United States

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Potomac, Maryland, United States

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Waldorf, Maryland, United States

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Boston, Massachusetts, United States

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Hannibal, Missouri, United States

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St Louis, Missouri, United States

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Missoula, Montana, United States

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Bellevue, Nebraska, United States

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Lincoln, Nebraska, United States

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Las Vegas, Nevada, United States

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Toms River, New Jersey, United States

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Albuquerque, New Mexico, United States

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New Hyde Park, New York, United States

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New Windsor, New York, United States

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New York, New York, United States

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The Bronx, New York, United States

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Charlotte, North Carolina, United States

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Denver, North Carolina, United States

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Gastonia, North Carolina, United States

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Raleigh, North Carolina, United States

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Fargo, North Dakota, United States

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Cincinnati, Ohio, United States

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Cincinnati, Ohio, United States

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Maumee, Ohio, United States

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Toledo, Ohio, United States

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Edmond, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Tulsa, Oklahoma, United States

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Grants Pass, Oregon, United States

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DuBois, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Scottdale, Pennsylvania, United States

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Smithfield, Pennsylvania, United States

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East Providence, Rhode Island, United States

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Anderson, South Carolina, United States

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Greenville, South Carolina, United States

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North Charleston, South Carolina, United States

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Franklin, Tennessee, United States

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Amarillo, Texas, United States

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Austin, Texas, United States

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Boerne, Texas, United States

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Cypress, Texas, United States

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Dallas, Texas, United States

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El Paso, Texas, United States

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Harlingen, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Kerrville, Texas, United States

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Lampasas, Texas, United States

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Nederland, Texas, United States

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Pearland, Texas, United States

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Red Oak, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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Spring, Texas, United States

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Tomball, Texas, United States

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Ogden, Utah, United States

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West Valley City, Utah, United States

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Colchester, Vermont, United States

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Manassas, Virginia, United States

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Kingwood, West Virginia, United States

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Morgantown, West Virginia, United States

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Cudahy, Wisconsin, United States

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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CABA, , Argentina

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CABA, , Argentina

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CABA, , Argentina

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Ciudad de Buenos Aires, , Argentina

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Córdoba, , Argentina

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Florida, , Argentina

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Mar del Plata, , Argentina

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Mendoza, , Argentina

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Ranelagh, , Argentina

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Rosario, , Argentina

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Rosario, , Argentina

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San Fernando, , Argentina

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Liège, , Belgium

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Namur, , Belgium

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Dupnitsa, , Bulgaria

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Dupnitsa, , Bulgaria

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Haskovo, , Bulgaria

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Kozloduy, , Bulgaria

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Lovech, , Bulgaria

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Pazardzhik, , Bulgaria

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Petrich, , Bulgaria

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Pleven, , Bulgaria

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Rousse, , Bulgaria

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Rousse, , Bulgaria

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Sevlievo, , Bulgaria

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Sliven, , Bulgaria

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Smolyan, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Stara Zagora, , Bulgaria

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Stara Zagora, , Bulgaria

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Varna, , Bulgaria

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Veliko Tarnovo, , Bulgaria

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Vidin, , Bulgaria

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Vratsa, , Bulgaria

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Edmonton, Alberta, Canada

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Sherwood Park, Alberta, Canada

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Kelowna, British Columbia, Canada

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Vancouver, British Columbia, Canada

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Vancouver, British Columbia, Canada

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Winnipeg, Manitoba, Canada

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Winnipeg, Manitoba, Canada

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Ajax, Ontario, Canada

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Burlington, Ontario, Canada

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Hamilton, Ontario, Canada

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London, Ontario, Canada

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Newmarket, Ontario, Canada

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Niagara Falls, Ontario, Canada

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Toronto, Ontario, Canada

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Toronto, Ontario, Canada

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Québec, Quebec, Canada

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Québec, Quebec, Canada

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Québec, Quebec, Canada

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Curicó, , Chile

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Quillota, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Talca, , Chile

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Balassagyarmat, , Hungary

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Budapest, , Hungary

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Edelény, , Hungary

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Encs, , Hungary

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Gödöllő, , Hungary

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Hajdúnánás, , Hungary

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Komárom, , Hungary

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Pécs, , Hungary

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Szeged, , Hungary

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Szeged, , Hungary

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Szigetvár, , Hungary

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Ahmedabad, , India

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Aligarh, , India

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Belagavi, , India

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Coimbatore, , India

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Dehradun, , India

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Gurgaon, , India

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Jaipur, , India

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Mohali, , India

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Nagpur, , India

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New Delhi, , India

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New Delhi, , India

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New Delhi, , India

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Thāne, , India

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Visakhapatnam, , India

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Bari, , Italy

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Casatenovo, , Italy

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Cona, , Italy

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Monserrato, , Italy

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Napoli, , Italy

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Pisa, , Italy

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Roma, , Italy

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Roma, , Italy

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Chino-shi, , Japan

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Chūōku, , Japan

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Chūōku, , Japan

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Chūōku, , Japan

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Fukui-shi, , Japan

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Fukuoka, , Japan

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Fukuoka, , Japan

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Habikino-shi, , Japan

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Hamamatsu, , Japan

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Higashiibaraki-gun, , Japan

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Himeji-shi, , Japan

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Hiroshima-shi, Naka-ku, , Japan

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Hitachi-Naka, , Japan

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Ikoma-shi, , Japan

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Kishiwada-shi, , Japan

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Kitakyushu, , Japan

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Kiyose-shi, , Japan

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Kokubunji-shi, , Japan

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Kyoto, , Japan

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Kyoto, , Japan

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Meguro-ku, , Japan

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Nagoya, , Japan

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Nankoku-shi, , Japan

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Obihiro, , Japan

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Omuta-shi, , Japan

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Osaka, , Japan

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Osaka, , Japan

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Osaka, , Japan

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Ōita, , Japan

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Saga, , Japan

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Sakaide-shi, , Japan

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Sapporo, , Japan

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Setagaya-ku, , Japan

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Setagaya-ku, , Japan

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Shibuya-ku, , Japan

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Shimotsuga-gun, , Japan

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Shinagawa-ku, , Japan

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Shinagawa-ku, , Japan

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Shinjuku-ku, , Japan

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Shinjuku-ku, , Japan

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Takarazuka-shi, , Japan

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Tanabe-shi, , Japan

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Toon-shi, , Japan

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Toshima-ku, , Japan

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Toshima-ku, , Japan

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Toshima-ku, , Japan

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Tsuchiura-shi, , Japan

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Utsunomiya, , Japan

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Yanagawa-shi, , Japan

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Yokohama, , Japan

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Yokohama, , Japan

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Yokohama, , Japan

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Yokohama, , Japan

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Auckland, , New Zealand

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Grafton, , New Zealand

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Nawton, , New Zealand

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Nelson, , New Zealand

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Rotorua, , New Zealand

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Wellington, , New Zealand

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Piura, , Peru

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Baguio City, , Philippines

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Davao City, , Philippines

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Iloilo City, , Philippines

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Las Piñas, , Philippines

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Lipa City, , Philippines

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Los Baños, , Philippines

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Manila, , Philippines

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Manila, , Philippines

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Marilao, , Philippines

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Quezon City, , Philippines

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Quezon City, , Philippines

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Bialystok, , Poland

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Bialystok, , Poland

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Bydgoszcz, , Poland

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Częstochowa, , Poland

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Karczew, , Poland

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Katowice, , Poland

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Kielce, , Poland

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Krakow, , Poland

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Krakow, , Poland

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Krakow, , Poland

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Piaseczno, , Poland

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Poznan, , Poland

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Poznan, , Poland

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Poznan, , Poland

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Rzeszów, , Poland

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Rzeszów, , Poland

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Rzeszów, , Poland

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Sosnowiec, , Poland

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Sosnowiec, , Poland

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Strzelce Opolskie, , Poland

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Szczecin, , Poland

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Tarnów, , Poland

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Wroclaw, , Poland

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Wroclaw, , Poland

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Caguas, , Puerto Rico

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Guaynabo, , Puerto Rico

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San Juan, , Puerto Rico

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Brasov, , Romania

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Brasov, , Romania

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Brasov, , Romania

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Bucharest, , Romania

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Timișoara, , Romania

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Cheongju-si, , South Korea

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Gangwon-do, , South Korea

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Jeonju, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Suwon, , South Korea

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Uijeongbu-si, , South Korea

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Ulsan, , South Korea

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Barcelona, , Spain

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Benalmádena, , Spain

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Coslada, , Spain

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L'Hospitalet de Llobregat, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Marbella (Málaga), , Spain

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Málaga, , Spain

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Pozuelo de Alarcón, , Spain

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Santander, , Spain

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Valencia, , Spain

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Zaragoza, , Spain

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Zaragoza, , Spain

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Changhua, , Taiwan

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Kaohsiung City, , Taiwan

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Kaohsiung City, , Taiwan

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New Taipei City, , Taiwan

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Taichung, , Taiwan

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Taichung, , Taiwan

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Tainan City, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taoyuan District, , Taiwan

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Bang Kra So, , Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Chanthaburi, , Thailand

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Hat Yai, , Thailand

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Khon Kaen, , Thailand

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Muang, , Thailand

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Mueang, , Thailand

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Hanoi, , Vietnam

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Hà Nội, , Vietnam

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Ho Chi Minh City, , Vietnam

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Ho Chi Minh City, , Vietnam

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Hochiminh, , Vietnam

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Countries

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United States Argentina Belgium Bulgaria Canada Chile Hungary India Italy Japan New Zealand Peru Philippines Poland Puerto Rico Romania South Korea Spain Taiwan Thailand Vietnam

References

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Oba Y, Anwer S, Maduke T, Patel T, Dias S. Effectiveness and tolerability of dual and triple combination inhaler therapies compared with each other and varying doses of inhaled corticosteroids in adolescents and adults with asthma: a systematic review and network meta-analysis. Cochrane Database Syst Rev. 2022 Dec 6;12(12):CD013799. doi: 10.1002/14651858.CD013799.pub2.

Reference Type DERIVED
PMID: 36472162 (View on PubMed)

Other Identifiers

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2023-505787-11

Identifier Type: REGISTRY

Identifier Source: secondary_id

2020-001520-34

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

D5982C00007

Identifier Type: -

Identifier Source: org_study_id

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