Study of PF-07248144 in Advanced or Metastatic Solid Tumors

NCT ID: NCT04606446

Last Updated: 2025-08-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1

Total Enrollment

320 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-11-16

Study Completion Date

2029-09-22

Brief Summary

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This is an open-label, multi center study to evaluate safety, tolerability, pharmacokinetics (PK), and pharmacodynamics (PD) of PF-07248144 and early signs of clinical efficacy of PF-07248144 as a single agent and in combination with other agents

Detailed Description

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Study has two parts, Part 1 (dose escalation) and Part 2 (dose expansion). Part 1 is divided into Parts 1A, 1B, 1C, 1D and 1E and Part 2 is divided into Parts 2A, 2B, 2D and 2E. In Part 1A, single escalating doses of PF-07248144 alone will be administered to determine the maximum tolerable dose (MTD) and select the recommended dose for expansion (RDE). In Part 1B, 1C, 1D and 1E PF-07248144 will be administered in combination with either fulvestrant (Part 1B); palbociclib + letrozole (Part 1C) or PF-07220060+fulvestrant (Part 1D) or vepdegestrant (Part 1E). After the determination of the monotherapy RDE in Part 1A, PF-07248144 will be evaluated in a dose expansion cohort as a monotherapy in Part 2A.

After determination of the combination RDE from Part 1B, PF-07248144 in combination with fulvestrant, PF-07248144 will be evaluated in a combination dose expansion with fulvestrant in Part 2B. In Part 1C, PF-07248144 in combination with letrozole + palbociclib will be evaluated for dose finding to determine the MTD and RDE for this combination. After determination of the triple combination RDE from Part 1D, PF-07248144 in combination with PF-07220060 + fulvestrant will be evaluated in a combination dose-expansion cohort, Part 2D. After determination of the combination RDE from Part 1E, PF-07248144 in combination with vepdegestrant will be evaluated in a combination dose-expansion cohort, Part 2E.

Conditions

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Locally Advanced or Metastatic ER+ HER2- Breast Cancer Locally Advanced or Metastatic Castration-resistant Prostate Cancer Locally Advanced or Metastatic Non-small Cell Lung Cancer

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

The dose escalation parts and the dose finding parts of the study will be guided by a Bayesian analysis of Cycle 1 dose-limiting toxicity (DLT) data for PF-07248144 as monotherapy or in combination (Part 1B, Part 1C, Part 1D and Part 1E).

A traditional 2-parameter Bayesian Logistic Regression Model (BLRM) will be used to model the DLT relationship of PF-07248144 monotherapy and a more complex BLRM model specifically designed for combinations will be used to model the dose/DLT relationship of PF-07248144 given in combination with fulvestrant, with letrozole + palbociclib, with PF-07220060 + fulvestrant or with vepdegestrant.
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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1A Monotherapy Dose Escalation

PF-07248144 Monotherapy Escalation

Group Type EXPERIMENTAL

PF-07248144

Intervention Type DRUG

KAT6 Inhibitor

1B Combination Dose Escalation

PF-07248144 with Fulvestrant Combination Dose Escalation

Group Type EXPERIMENTAL

PF-07248144

Intervention Type DRUG

KAT6 Inhibitor

Fulvestrant

Intervention Type DRUG

Endocrine Therapy

1C Combination Dose Escalation

PF-07248144 with Letrozole + Palbociclib Combination Dose Escalation

Group Type EXPERIMENTAL

PF-07248144

Intervention Type DRUG

KAT6 Inhibitor

Letrozole

Intervention Type DRUG

Endocrine Therapy

Palbociclib

Intervention Type DRUG

CDK4/6 Inhibitor

2A Monotherapy Dose Expansion Arm

PF-07248144 Monotherapy Dose Expansion

Group Type EXPERIMENTAL

PF-07248144

Intervention Type DRUG

KAT6 Inhibitor

2B Combination Dose Expansion Arm

PF-07248144 with Fulvestrant Dose Expansion

Group Type EXPERIMENTAL

PF-07248144

Intervention Type DRUG

KAT6 Inhibitor

Fulvestrant

Intervention Type DRUG

Endocrine Therapy

1D Combination Dose Escalation

PF-07248144 with PF-07220060 +Fulvestrant

Group Type EXPERIMENTAL

PF-07248144

Intervention Type DRUG

KAT6 Inhibitor

Fulvestrant

Intervention Type DRUG

Endocrine Therapy

PF-07220060

Intervention Type DRUG

CDK4 inhibitor

2D Combination Dose Expansion Arm

PF-07248144 with PF-07220060 +Fulvestrant Dose Expansion

Group Type EXPERIMENTAL

PF-07248144

Intervention Type DRUG

KAT6 Inhibitor

Fulvestrant

Intervention Type DRUG

Endocrine Therapy

PF-07220060

Intervention Type DRUG

CDK4 inhibitor

China Monotherapy Dose Expansion

PF-07248144 Monotherapy Dose Expansion

Group Type EXPERIMENTAL

PF-07248144

Intervention Type DRUG

KAT6 Inhibitor

1E Combination Dose Escalation

PF-07248144 with Vepdegestrant Combination Dose Escalation

Group Type EXPERIMENTAL

PF-07248144

Intervention Type DRUG

KAT6 Inhibitor

PF-07850327, ARV-471, vepdegestrant

Intervention Type DRUG

PROTAC (PROteolysis Targeting Chimera) ER degrader

2E Combination Dose Expansion Arm

PF-07248144 with Vepdegestrant Combination Dose Expansion

Group Type EXPERIMENTAL

PF-07248144

Intervention Type DRUG

KAT6 Inhibitor

PF-07850327, ARV-471, vepdegestrant

Intervention Type DRUG

PROTAC (PROteolysis Targeting Chimera) ER degrader

Interventions

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PF-07248144

KAT6 Inhibitor

Intervention Type DRUG

Fulvestrant

Endocrine Therapy

Intervention Type DRUG

Letrozole

Endocrine Therapy

Intervention Type DRUG

Palbociclib

CDK4/6 Inhibitor

Intervention Type DRUG

PF-07220060

CDK4 inhibitor

Intervention Type DRUG

PF-07850327, ARV-471, vepdegestrant

PROTAC (PROteolysis Targeting Chimera) ER degrader

Intervention Type DRUG

Other Intervention Names

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Faslodex Femara Ibrance

Eligibility Criteria

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Inclusion Criteria

* Disease Characteristics - Breast, Prostate, and Lung Cancer
* Part 1A (Monotherapy Dose Escalation) Histological or cytological diagnosis of locally advanced or metastatic ER+HER2- breast cancer, CRPC, or NSCLC that is intolerant or resistant to standard therapy or for which no standard therapy is available.
* Part 1B, Part 1C, Part 1D and Part 1E (Combination Dose Escalation) Histological or cytological diagnosis of locally advanced or metastatic ER+HER2- breast cancer. Participants must have progressed after at least 1 prior line of treatment with an endocrine therapy and CDK4/6 inhibitor in the advanced or metastatic setting.
* Part 2A (ER+HER2- breast cancer 2L+, monotherapy) Histological or cytological diagnosis of locally advanced or metastatic ER+HER2- breast cancer. Participants must have progressed after at least 1 prior line of CDK4/6 inhibitor and 1 line of endocrine therapy.
* Part 2B (ER+HER2- breast cancer 2-4L, combination with fulvestrant) Histological or cytological diagnosis of advanced or metastatic ER+HER2- breast cancer. Participants must have progressive disease after at least 1 prior line of a CDK4/6 inhibitor and at least 1 prior line of endocrine therapy.. Participants must not have received more than 3 prior lines of systemic therapies including up to 1 line of cytotoxic chemotherapy for visceral disease in advanced or metastatic setting; Participants may have but are not required to have prior treatment with fulvestrant.
* Part 2D (ER+HER2- breast cancer 2-4L, combination with PF-07220060 (CDK4i) and fulvestrant):

Histological or cytological diagnosis of advanced or metastatic ER+HER2- breast cancer. Participants must have progressive disease after at least 1 prior line of a CDK4/6 inhibitor and at least 1 prior line of endocrine therapy.

* Participants must have not received more than 3 lines of systemic therapies including up to 1 line of cytotoxic chemotherapy for visceral disease in advanced or metastatic setting; Participants may have but are not required to have prior treatment with fulvestrant.
* Part 2E (ER+HER2- breast cancer 2-4L, combination with vepdegestrant): Histological or cytological diagnosis of advanced or metastatic ER+HER2- breast cancer. Participants must have progressive disease after at least 1 prior line of a CDK4/6 inhibitor and at least 1 prior line of endocrine therapy; Participants must have not received more than 3 lines of systemic therapies including up to 1 line of cytotoxic chemotherapy for visceral disease in advanced or metastatic setting; Participants may have received fulvestrant
* Participants with ER+HER2- advanced or metastatic breast cancer must have documentation of ER-positive tumor (≥1% positive stained cells) based on most recent tumor biopsy utilizing an assay consistent with local standards.
* Participants with ER+HER2- advanced or metastatic breast cancer must have documentation of HER2-negative tumor: HER2-negative tumor is determined as immunohistochemistry score 0/1+ or negative by in situ hybridization (FISH/CISH/SISH/DISH) defined as a HER2/CEP17 ratio \<2 or for single probe assessment a HER2 copy number \<4.
* Female participants with ER+HER2- advanced or metastatic breast cancer considered to be of childbearing potential (or have tubal ligations only) must be willing to undergo medically induced menopause by treatment with the approved LHRH agonist such as goserelin, leuprolide or equivalent agents to induce chemical menopause.
* Female participants with ER+HER2- advanced or metastatic breast cancer of nonchildbearing potential must meet at least 1 criteria of achieving postmenopausal status.
* Participants must have at least 1 measurable lesion as defined by RECIST version 1.1 that has not been previously irradiated.
* Eastern Cooperative Oncology Group (ECOG) Performance Status PS 0 or 1
* Female or male patients aged ≥ 18 years (Japan ≥ 20 years) (South Korea ≥ 19 years).
* Adequate renal, liver, and bone marrow function.
* Resolved acute effects of any prior therapy to baseline severity or CTCAE Grade 1 except for adverse events (AEs) not constituting a safety risk by investigator judgment.

Exclusion Criteria

* Unmanageable ascites (limited medical treatment to control ascites is permitted, but all participants with ascites require review by sponsor's medical monitor).
* Participants with any other active malignancy within 3 years prior to enrollment, except for adequately treated basal cell or squamous cell skin cancer, or carcinoma in situ.
* Major surgery, radiation therapy, or systemic anti-cancer therapy within 3 weeks prior to study entry.
* Prior irradiation to \>25% of the bone marrow.
* ECG clinically relevant abnormalities (eg, QTc \>470 msec, complete LBBB, second/third degree AV block, ST elevation or EKG changes suggesting myocardial infarction or active myocardia ischemia).
* Therapeutic anticoagulation. However, low molecular weight heparin is allowed. Vitamin K antagonists or factor Xa inhibitors may be allowed following discussion with the Sponsor.
* Known or suspected hypersensitivity or severe allergy to active ingredient/excipients of PF-07248144.
* Active inflammatory GI disease, refractory and unresolved chronic diarrhea or previous gastric resection, lap band surgery or other GI conditions and surgeries that may significantly alter the absorption of PF-07248144 tablets. Gastroesophageal reflux disease under treatment is allowed.
* Pregnant or breastfeeding female participants.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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HonorHealth

Scottsdale, Arizona, United States

Site Status TERMINATED

Cedars Sinai Medical Center, Samuel Oschin Comprehensive Cancer Institute

Los Angeles, California, United States

Site Status RECRUITING

Cedars-Sinai Medical Center; SOCCI Pharmacy

Los Angeles, California, United States

Site Status RECRUITING

UCSF Medical Center at Mission Bay

San Francisco, California, United States

Site Status RECRUITING

Smilow Cancer Hospital at Yale - New Haven

New Haven, Connecticut, United States

Site Status RECRUITING

Yale-New Haven Hospital- Yale Cancer Center

New Haven, Connecticut, United States

Site Status RECRUITING

Smilow Cancer Hospital Phase 1 Unit

New Haven, Connecticut, United States

Site Status RECRUITING

Holy Cross Hospital

Fort Lauderdale, Florida, United States

Site Status TERMINATED

St. Elizabeth Healthcare

Edgewood, Kentucky, United States

Site Status RECRUITING

James Graham Brown Cancer Center

Louisville, Kentucky, United States

Site Status RECRUITING

University Medical Center, lnc.:DBA University of Louisville Hospital

Louisville, Kentucky, United States

Site Status RECRUITING

Tennessee Oncology PLLC

Franklin, Tennessee, United States

Site Status RECRUITING

Sarah Cannon Research Institute

Nashville, Tennessee, United States

Site Status RECRUITING

Tennessee Oncology PLLC

Nashville, Tennessee, United States

Site Status RECRUITING

The Sarah Cannon Research Institute / Tennessee Oncology, PLLC

Nashville, Tennessee, United States

Site Status RECRUITING

The University of Texas M. D. Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

U.T. MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

NEXT Oncology

San Antonio, Texas, United States

Site Status RECRUITING

Swedish Cancer Institute

Seattle, Washington, United States

Site Status RECRUITING

Swedish Medical Center

Seattle, Washington, United States

Site Status RECRUITING

Chris O'Brien Lifehouse

Camperdown, New South Wales, Australia

Site Status TERMINATED

Cancer Research South Australia

Adelaide, South Australia, Australia

Site Status RECRUITING

Peter MacCallum Cancer Centre

Melbourne, Victoria, Australia

Site Status RECRUITING

Royal Melbourne Hospital

Parkville, Victoria, Australia

Site Status RECRUITING

Western Health-Sunshine & Footscray Hospitals

St Albans, Victoria, Australia

Site Status RECRUITING

St. John of God Subiaco Hospital

Subiaco, Western Australia, Australia

Site Status RECRUITING

Beijing Cancer hospital

Beijing, Beijing Municipality, China

Site Status RECRUITING

SUN Yat-Sen University Cancer Center

Guangzhou, Guangdong, China

Site Status RECRUITING

Hubei Cancer Hospital

Wuhan, Hubei, China

Site Status NOT_YET_RECRUITING

Jilin Province Tumor Hospital

Changchun, Jilin, China

Site Status RECRUITING

The First Affiliated Hospital of Xi'an Jiaotong University

Xi'an, Shaanxi, China

Site Status RECRUITING

Aichi Cancer Center Hospital

Nagoya, Aichi-ken, Japan

Site Status RECRUITING

National Cancer Center Hospital East

Kashiwa, Chiba, Japan

Site Status RECRUITING

Kanagawa cancer center

Yokohama, Kanagawa, Japan

Site Status RECRUITING

National Cancer Center Hospital

Chuo-ku, Tokyo, Japan

Site Status RECRUITING

Seoul National University Bundang Hospital

Seongnam, Ky?nggi-do, South Korea

Site Status RECRUITING

Seoul National University Hospital

Seoul, Seoul-teukbyeolsi [seoul], South Korea

Site Status RECRUITING

Severance Hospital, Yonsei University Health System

Seoul, Seoul-teukbyeolsi [seoul], South Korea

Site Status RECRUITING

Samsung Medical Center

Seoul, Seoul-teukbyeolsi [seoul], South Korea

Site Status RECRUITING

Kyungpook National University Chilgok Hospital

Daegu, Taegu-kwangyǒkshi, South Korea

Site Status RECRUITING

Asan Medical Center

Seoul, , South Korea

Site Status RECRUITING

Countries

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United States Australia China Japan South Korea

Central Contacts

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Pfizer CT.gov Call Center

Role: CONTACT

1-800-718-1021

References

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Mukohara T, Park YH, Sommerhalder D, Yonemori K, Hamilton E, Kim SB, Kim JH, Iwata H, Yamashita T, Layman RM, Mita M, Clay T, Chae YS, Oakman C, Yan F, Kim GM, Im SA, Lindeman GJ, Rugo HS, Liyanage M, Saul M, Le Corre C, Skoura A, Liu L, Li M, LoRusso PM. Inhibition of lysine acetyltransferase KAT6 in ER+HER2- metastatic breast cancer: a phase 1 trial. Nat Med. 2024 Aug;30(8):2242-2250. doi: 10.1038/s41591-024-03060-0. Epub 2024 Jun 1.

Reference Type DERIVED
PMID: 38824244 (View on PubMed)

Bishop TR, Subramanian C, Bilotta EM, Garnar-Wortzel L, Ramos AR, Zhang Y, Asiaban JN, Ott CJ, Rock CO, Erb MA. Acetyl-CoA biosynthesis drives resistance to histone acetyltransferase inhibition. Nat Chem Biol. 2023 Oct;19(10):1215-1222. doi: 10.1038/s41589-023-01320-7. Epub 2023 May 1.

Reference Type DERIVED
PMID: 37127754 (View on PubMed)

Related Links

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https://pmiform.com/clinical-trial-info-request?StudyID=C4551001

To obtain contact information for a study center near you, click here.

Other Identifiers

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NCT04606446

Identifier Type: REGISTRY

Identifier Source: secondary_id

C4551001

Identifier Type: -

Identifier Source: org_study_id

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