Randomized Trial in Adult Participants With Acute Migraines

NCT ID: NCT04571060

Last Updated: 2023-04-24

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1978 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-10-27

Study Completion Date

2021-10-22

Brief Summary

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The purpose of this study is to test the safety and efficacy of BHV-3500 (zavegepant) versus placebo in the acute treatment of moderate or severe migraine.

Detailed Description

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Conditions

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Migraine

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators
Double-blind to Sponsor, Investigator and Participant.

Study Groups

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Zavegepant

Participants administered a single intranasal dose of zavegepant 10 mg on occurrence of migraine with moderate or severe intensity within 45 days after randomization. The dose was administered using an Aptar Unidose System (UDS) liquid spray device.

Group Type EXPERIMENTAL

Zavegepant

Intervention Type DRUG

One dose of zavegepant

Placebo

Participants administered a single intranasal dose of zavegepant matching placebo on occurrence of migraine with moderate or severe intensity within 45 days after randomization. The dose was administered using an Aptar UDS liquid spray device.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

One dose of matching placebo

Interventions

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Zavegepant

One dose of zavegepant

Intervention Type DRUG

Placebo

One dose of matching placebo

Intervention Type DRUG

Other Intervention Names

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BHV3500

Eligibility Criteria

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Inclusion Criteria

1. Participant has at least 1-year history of migraines (with or without aura), consistent with a diagnosis according to the International Classification of Headache Disorder, 3rd Edition, including the following:

1. Migraine attacks present for more than 1 year with the age of onset prior to 50 years of age
2. Migraine attacks, on average, lasting about 4-72 hours if untreated
3. Not more than 8 attacks of moderate to severe intensity per month within the last 3 months
4. At least 2 consistent migraine headache attacks of moderate or severe intensity in each of the 3 months prior to the Screening Visit and maintains this requirement during the Screening period
5. Less than 15 days with headache (migraine or non-migraine) per month in each of the 3 months prior to the Screening Visit and maintains this requirement during the Screening Period.
6. Participants on prophylactic migraine medication are permitted to remain on therapy provided they have been on a stable dose for at least 3 months prior to screening visit and the dose is not expected to change during the course of the study.
7. Participants with contraindications for use of triptans may be included provided they meet all other study entry criteria.
2. Male and Female participants ≥18 years of age.

Exclusion Criteria

1. Participant with a history of HIV disease
2. Participant history with current evidence of uncontrolled, unstable or recently diagnosed cardiovascular disease, such as ischemic heart disease, coronary artery vasospasm, and cerebral ischemia. Participants with Myocardial Infarction (MI), Acute Coronary Syndrome (ACS), Percutaneous Coronary Intervention (PCI), cardiac surgery, stroke or transient ischemic attack (TIA) during the 6 months prior to screening.
3. Uncontrolled hypertension (high blood pressure), or uncontrolled diabetes (however participants can be included who have stable hypertension and/or diabetes for at least 3 months prior to being enrolled).
4. Participants with major depressive episode within the last 12 months, major depressive disorder or any anxiety disorder requiring more than 1 medication for each disorder.
5. History of, treatment for, or evidence of, alcohol or drug abuse within the past 12 months or participants who have met DSM-V criteria for any significant substance use disorder within the past 12 months.
6. History of nasal surgery in the 6 months.
7. Evidence at screening of significant nasal conditions that may affect the administration or absorption of the nasal product (e.g. severe septum deviation, nasal deformity or blockage, inflammation, perforation, mucosal erosion or ulceration, polyposis, nasal trauma)
8. Participation in any other investigational clinical trial while participating in this clinical trial. Participation in a COVID-19 mRNA vaccine study (vaccine must be authorized under FDA emergency use authorization or approval) who are at least 30 days post last dose of the vaccine are permitted to be screened for this study.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Medical Affiliated Research Center

Huntsville, Alabama, United States

Site Status

Coastal Clinical Research, LLC, An AMR Co.

Mobile, Alabama, United States

Site Status

MD First Research

Chandler, Arizona, United States

Site Status

Tucson Neuroscience Research

Tucson, Arizona, United States

Site Status

Baptist Health Center for Clinical Research

Little Rock, Arkansas, United States

Site Status

Axiom Research, LLC

Colton, California, United States

Site Status

Pharmacology Research Institute

Encino, California, United States

Site Status

eStudySite

La Mesa, California, United States

Site Status

Synergy San Diego

Lemon Grove, California, United States

Site Status

Collaborative Neuroscience Network, LLC

Long Beach, California, United States

Site Status

Pharmacology Research Institute

Los Alamitos, California, United States

Site Status

Clinical Research Institute

Los Angeles, California, United States

Site Status

Wr-Pri, Llc

Newport Beach, California, United States

Site Status

Artemis Institute for Clinical Research

Riverside, California, United States

Site Status

Artemis Institute for Clinical Research

San Diego, California, United States

Site Status

California Neuroscience Research Medical Group, Inc.

Sherman Oaks, California, United States

Site Status

CT Clinical Research

Cromwell, Connecticut, United States

Site Status

Ki Health Partners, LLC dba New England Institute for Clinical Research

Stamford, Connecticut, United States

Site Status

Neurology Offices of South Florida

Boca Raton, Florida, United States

Site Status

Clinical Neuroscience Solutions, Inc.

Jacksonville, Florida, United States

Site Status

Multi-Specialty Research Associates, Inc.

Lake City, Florida, United States

Site Status

Meridien Research

Lake Mary, Florida, United States

Site Status

AppleMed Research Group, LLC

Miami, Florida, United States

Site Status

The Neurology Research Group

Miami, Florida, United States

Site Status

Clinical Neuroscience Solutions, Inc.

Orlando, Florida, United States

Site Status

Clinical Neuroscience Solutions, Inc.

Orlando, Florida, United States

Site Status

Complete Health Research

Ormond Beach, Florida, United States

Site Status

Ideal Clinical Research

Pembroke Pines, Florida, United States

Site Status

Clinical Research Center of Florida

Pompano Beach, Florida, United States

Site Status

Clin-Med Research & Development, LLC

South Miami, Florida, United States

Site Status

ForCare Clinical Research

Tampa, Florida, United States

Site Status

JSV Clinical Research Study, Inc.

Tampa, Florida, United States

Site Status

iResearch Atlanta, LLC

Decatur, Georgia, United States

Site Status

Meridian Clinical Research, LLC

Savannah, Georgia, United States

Site Status

Northwest Clinical Trials Inc.

Boise, Idaho, United States

Site Status

Cedar Crosse Research Center

Chicago, Illinois, United States

Site Status

Healthcare Research Network II, LLC

Flossmoor, Illinois, United States

Site Status

Fort Wayne Neurological Center

Fort Wayne, Indiana, United States

Site Status

Collective Medical Research

Prairie Village, Kansas, United States

Site Status

Alliance for Multispecialty Research, LLC

Wichita, Kansas, United States

Site Status

L-MARC Research Center

Louisville, Kentucky, United States

Site Status

Crescent City Headache and Neurology Center

Chalmette, Louisiana, United States

Site Status

DelRicht Research

New Orleans, Louisiana, United States

Site Status

Boston Clinical Trials

Boston, Massachusetts, United States

Site Status

Community Clinical Research Network

Marlborough, Massachusetts, United States

Site Status

Boston Neuro Research Center

South Dartmouth, Massachusetts, United States

Site Status

Medvadis Research Corporation

Waltham, Massachusetts, United States

Site Status

Michigan Headache and Neurological Institute

Ann Arbor, Michigan, United States

Site Status

Clinical Research Institute, Inc.

Minneapolis, Minnesota, United States

Site Status

StudyMetrix Research

City of Saint Peters, Missouri, United States

Site Status

Healthcare Research Network

Hazelwood, Missouri, United States

Site Status

Clinvest Research LLC

Springfield, Missouri, United States

Site Status

Sundance Clinical Research, LLC

St Louis, Missouri, United States

Site Status

Excel Clinical Research

Las Vegas, Nevada, United States

Site Status

Center for Emotional Fitness

Cherry Hill, New Jersey, United States

Site Status

Albuquerque Clinical Trials, Inc.

Albuquerque, New Mexico, United States

Site Status

Dent Neurosciences Research Center

Amherst, New York, United States

Site Status

Regional Clinical Research

Endwell, New York, United States

Site Status

Central New York Clinical Research

Manlius, New York, United States

Site Status

Fieve Clinical Research, Inc

New York, New York, United States

Site Status

Rochester Clinical Research, Inc.

Rochester, New York, United States

Site Status

Montefiore Medical Center: Headache Center

The Bronx, New York, United States

Site Status

Headache Wellness Center

Greensboro, North Carolina, United States

Site Status

PharmQuest LLC

Greensboro, North Carolina, United States

Site Status

PMG of Raleigh, LLC

Raleigh, North Carolina, United States

Site Status

Wilmington Health, PLLC

Wilmington, North Carolina, United States

Site Status

Hometown Urgent Care & Research/ Wellnow

Cincinnati, Ohio, United States

Site Status

Hometown Urgent Care and Research

Columbus, Ohio, United States

Site Status

Hometown Urgent Care and Research

Dayton, Ohio, United States

Site Status

The Orthopedic Foundation

New Albany, Ohio, United States

Site Status

OK Clinical Research LLC

Edmond, Oklahoma, United States

Site Status

Tekton Research, Inc.

Yukon, Oklahoma, United States

Site Status

Summit Research Network

Portland, Oregon, United States

Site Status

Clinical Research of Philadelphia, LLC

Philadelphia, Pennsylvania, United States

Site Status

Preferred Primary Care Physicians, Inc.

Pittsburgh, Pennsylvania, United States

Site Status

Preferred Primary Care Physicians, Inc.

Union, Pennsylvania, United States

Site Status

MD First Research

Lancaster, South Carolina, United States

Site Status

Coastal Carolina Research Center

Mt. Pleasant, South Carolina, United States

Site Status

Volunteer Research Group

Knoxville, Tennessee, United States

Site Status

Clinical Neuroscience Solutions, Inc.

Memphis, Tennessee, United States

Site Status

FutureSearch Trials of Neurology

Austin, Texas, United States

Site Status

Donald J. Garcia, Jr, MD, PA

Austin, Texas, United States

Site Status

FutureSearch Trials of Dallas, LP

Dallas, Texas, United States

Site Status

Red Star Research LLC

Lake Jackson, Texas, United States

Site Status

Clinical Trials of Texas, Inc. (CTT)

San Antonio, Texas, United States

Site Status

DM Clinical Research

Tomball, Texas, United States

Site Status

Alpine Medical Group

Salt Lake City, Utah, United States

Site Status

J. Lewis Research, Inc. / Jordan River Family Medicine

South Jordan, Utah, United States

Site Status

Charlottesville Medical Research Center, LLC

Charlottesville, Virginia, United States

Site Status

Health Research of Hampton Roads, Inc.

Newport News, Virginia, United States

Site Status

Tidewater Integrated Medical Research

Virginia Beach, Virginia, United States

Site Status

Northwest Clinical Research Center

Bellevue, Washington, United States

Site Status

Seattle Women's: Health, Research, Gynecology

Seattle, Washington, United States

Site Status

Clinical Investigation Specialist, Inc.

Kenosha, Wisconsin, United States

Site Status

Countries

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United States

References

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Lipton RB, Croop R, Stock DA, Madonia J, Forshaw M, Lovegren M, Mosher L, Coric V, Goadsby PJ. Safety, tolerability, and efficacy of zavegepant 10 mg nasal spray for the acute treatment of migraine in the USA: a phase 3, double-blind, randomised, placebo-controlled multicentre trial. Lancet Neurol. 2023 Mar;22(3):209-217. doi: 10.1016/S1474-4422(22)00517-8.

Reference Type DERIVED
PMID: 36804093 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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C5301001

Identifier Type: OTHER

Identifier Source: secondary_id

BHV3500-301

Identifier Type: -

Identifier Source: org_study_id

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