Expanded Access to Ulixertinib (BVD-523) in Patients With Advanced MAPK Pathway-Altered Malignancies

NCT ID: NCT04566393

Last Updated: 2026-01-28

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

AVAILABLE

Study Classification

EXPANDED_ACCESS

Brief Summary

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The objective of this expanded access program is to provide ulixertinib (BVD-523) for compassionate use in advanced cancer patients with MAPK pathway-altered solid tumor(s), including but not limited to KRAS, NRAS, HRAS, BRAF, MEK, and ERK mutations who have incomplete response to or have exhausted available therapies.

Ulixertinib is available for treatment as monotherapy or in combination with other clinically tolerable agent(s), conditionally approved by the drug manufacturer.

Detailed Description

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Conditions

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Pancreatic Cancer Small Bowel Cancer Colorectal Cancer Melanoma Non Small Cell Lung Cancer Thyroid Cancer Bladder Cancer Head and Neck Cancer Gastric Cancer Esophageal Cancer Cholangiocarcinoma Ovarian Cancer Hepatocellular Carcinoma Glioblastoma MAPK Gene Mutation KRAS Activating Mutation BRAF Gene Mutation NRAS Gene Mutation HRAS Gene Mutation MEK Mutation ERK Mutation

Interventions

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Ulixertinib (BVD-523)

Ulixertinib (BVD-523) is an oral, first-in-class ERK1/2 inhibitor

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Main Inclusion Criterion:

1\. Patient has a MAPK pathway-altered solid tumor(s), including but not limited to KRAS, NRAS, HRAS, BRAF, MEK, and ERK mutations.

1. In the opinion of the treating physician, the patient has exhausted or has inadequate response to available anti-cancer treatments.
2. In the opinion of the treating physician, the patient has adequate organ function to tolerate ulixertinib as defined in section 6.1
3. Male or female patients aged ≥ 12 years.
4. Patient must be able to swallow and retain orally administered medication.

Note: Ulixertinib is primarily absorbed in the duodenum and therefore patients with any prior stomach or duodenal resection should be evaluated with that understanding.
5. For females, evidence of post-menopausal status or negative urinary or serum pregnancy test for pre-menopausal patients.
6. Highly effective contraception for both male and female patients throughout the treatment and for at least 4 months after last treatment administration. In patients under the age of 18, who are not sexually active, abstinence is an acceptable form.
7. Toxicities related to any prior treatments are either stable, stable on supportive therapy, resolved, or in the opinion of the treating physician, clinically non-significant
8. Ability to understand a written informed consent document, and the willingness to sign it. Assent will be obtained when appropriate based on the patient's age.

Exclusion Criteria

1. Patient is already participating in or qualifies for and is able to enroll in a clinical trial of ulixertinib (BVD-523).
2. Patient has received systemic therapy with an investigational agent within 5 half-lives or 14 days prior to starting ulixertinib treatment, whichever is shorter.
3. Patient has received radiotherapy within 14 days prior to the first dose of ulixertinib treatment other than for the allowable treatment of symptomatic bone metastasis.
4. A history of current evidence/risk of retinal vein occlusion (RVO) or central serous retinopathy (CSR)
5. Current evidence of uncontrolled, significant intercurrent illness that would, in the treating physician's judgment, contraindicate the patient's treatment with ulixertinib due to safety concerns.
6. Patients who, in the opinion of the treating physician, have not fully recovered from recent major surgery to a sufficient extent to tolerate treatment with ulixertinib.
7. Known hypersensitivity to ulixertinib or any component in its formulation.
8. Patients taking prohibited medications as described in current Investigator's Brochure.

Note: Patients who require treatment with Drugs that are strong inhibitors or inducers of CYP1A2, CYP2D6, and CYP3A4 (see Appendix 3) were excluded from the FIH study of ulixertinib and should be discussed with xCures to review if any potential benefits outweigh the potential risks.
9. Patient is actively breastfeeding.
10. Prior stomach or duodenal resection that in the opinion of the treating physician would affect the breakdown and absorption of ulixertinib.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Cancer Commons

OTHER

Sponsor Role collaborator

xCures

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Clearview Cancer Institute

Huntsville, Alabama, United States

Site Status AVAILABLE

Infirmary Cancer Care

Mobile, Alabama, United States

Site Status AVAILABLE

PCR Oncology

Arroyo Grande, California, United States

Site Status AVAILABLE

Hoag Memorial Hospital Presbyterian

Newport Beach, California, United States

Site Status AVAILABLE

xCures Inc.

San Francisco, California, United States

Site Status AVAILABLE

Providence Saint John's Health Center

Santa Monica, California, United States

Site Status AVAILABLE

MedStar Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status AVAILABLE

Orlando Health

Orlando, Florida, United States

Site Status AVAILABLE

Mercy Medical Center

Cedar Rapids, Iowa, United States

Site Status AVAILABLE

Unity Point Health - St. Lukes Hospital

Cedar Rapids, Iowa, United States

Site Status AVAILABLE

Our Lady of the Lake Hospital

Baton Rouge, Louisiana, United States

Site Status AVAILABLE

Mary Bird Perkins Cancer Center

Baton Rouge, Louisiana, United States

Site Status AVAILABLE

Oakland Macomb Cancer Specialists

Sterling Heights, Michigan, United States

Site Status AVAILABLE

Lake Region Healthcare

Fergus Falls, Minnesota, United States

Site Status AVAILABLE

Nebraska Hematology Oncology

Lincoln, Nebraska, United States

Site Status AVAILABLE

Cancer Partners of Nebraska

Lincoln, Nebraska, United States

Site Status AVAILABLE

Hunterdon Hematology Oncology

Flemington, New Jersey, United States

Site Status AVAILABLE

Monmouth Medical Center

Long Branch, New Jersey, United States

Site Status AVAILABLE

The Minniti Center for Medical Oncology and Hematology

Mickleton, New Jersey, United States

Site Status AVAILABLE

Atlantic Health System/Overlook Medical Center

Summit, New Jersey, United States

Site Status AVAILABLE

Hirschfeld Oncology

Brooklyn, New York, United States

Site Status AVAILABLE

Stony Brook Cancer Center

Stony Brook, New York, United States

Site Status AVAILABLE

The Christ Hospital

Cincinnati, Ohio, United States

Site Status AVAILABLE

Lehigh Valley Health Network

Allentown, Pennsylvania, United States

Site Status AVAILABLE

MD Anderson

Houston, Texas, United States

Site Status AVAILABLE

UTHealth Houston

Houston, Texas, United States

Site Status AVAILABLE

UTHealth - Tyler

Tyler, Texas, United States

Site Status AVAILABLE

Countries

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United States

Central Contacts

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xCures Clinical Operations

Role: CONTACT

(707) 641-4475

Other Identifiers

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ULI-EAP-100

Identifier Type: -

Identifier Source: org_study_id

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