Study of Ravulizumab in Proliferative Lupus Nephritis (LN) or Immunoglobulin A Nephropathy (IgAN)

NCT ID: NCT04564339

Last Updated: 2025-10-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

123 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-01-19

Study Completion Date

2025-08-18

Brief Summary

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The objectives of this study are to evaluate the safety and efficacy of ravulizumab administered by intravenous (IV) infusion compared to placebo and demonstrate proof-of-concept of the efficacy of terminal complement inhibition in participants with LN (LN Cohort) or IgAN (IgAN Cohort).

Detailed Description

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This study consists of a 6-week Screening Period, 26-week Initial Evaluation Period, a 24-week Extension Period, and a 36-week post-treatment Follow-up Period.

Conditions

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Lupus Nephritis Immunoglobulin A Nephropathy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors
Participants, all investigative site personnel, and any Alexion employee, or designee, directly associated with the conduct of the study will be blinded to participant treatment assignments during the 26-week Initial Evaluation Period. Both the participants and the investigative site personnel will remain blinded for the remaining 24-week Extension Period.

Study Groups

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Ravulizumab: LN Cohort

Eligible participants will receive ravulizumab IV infusion in combination with background therapy during both the Initial Evaluation Period (26 weeks) and Extension Period (24 weeks). During the Follow-up Period (36 weeks) participants will receive background therapy according to the standard of care.

Group Type EXPERIMENTAL

Ravulizumab

Intervention Type DRUG

Dosages (loading and maintenance) will be based on the participant's body weight.

Background Therapy

Intervention Type OTHER

Participants will receive background therapy consistent with the standard of care.

Placebo: LN Cohort

Eligible participants will receive placebo IV infusion in combination with background therapy during both the Initial Evaluation Period (26 weeks) and Extension Period (24 weeks). During the Follow-up Period (36 weeks) participants will receive background therapy according to the standard of care.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Dosages (loading and maintenance) will be based on the participant's body weight.

Background Therapy

Intervention Type OTHER

Participants will receive background therapy consistent with the standard of care.

Ravulizumab: IgAN Cohort

Eligible participants will receive ravulizumab IV infusion in combination with background therapy during both the Initial Evaluation Period (26 weeks) and Extension Period (24 weeks). During the Follow-up Period (36 weeks) participants will receive background therapy according to the standard of care.

Group Type EXPERIMENTAL

Ravulizumab

Intervention Type DRUG

Dosages (loading and maintenance) will be based on the participant's body weight.

Background Therapy

Intervention Type OTHER

Participants will receive background therapy consistent with the standard of care.

Placebo: IgAN Cohort

Eligible participants will receive placebo IV infusion in combination with background therapy during the Initial Evaluation Period (26 weeks) and will switch to ravulizumab for the Extension Period (24 weeks). During the Follow-up Period (36 weeks) participants will receive background therapy according to the standard of care.

Group Type PLACEBO_COMPARATOR

Ravulizumab

Intervention Type DRUG

Dosages (loading and maintenance) will be based on the participant's body weight.

Placebo

Intervention Type DRUG

Dosages (loading and maintenance) will be based on the participant's body weight.

Background Therapy

Intervention Type OTHER

Participants will receive background therapy consistent with the standard of care.

Interventions

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Ravulizumab

Dosages (loading and maintenance) will be based on the participant's body weight.

Intervention Type DRUG

Placebo

Dosages (loading and maintenance) will be based on the participant's body weight.

Intervention Type DRUG

Background Therapy

Participants will receive background therapy consistent with the standard of care.

Intervention Type OTHER

Other Intervention Names

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Ultomiris

Eligibility Criteria

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Inclusion Criteria

Common to both disease cohorts:

* Proteinuria ≥1 (gram \[g\]/day or g/g)
* Vaccinated against meningococcal infection
* Vaccinated for Haemophilus influenzae type b (Hib) and Streptococcus pneumoniae according to national/local regulatory requirements

For LN cohort:

* Diagnosis of active focal or diffuse proliferative LN Class III or IV
* Clinically active LN, requiring/receiving immunosuppression induction treatment

For IgAN cohort:

* Diagnosis of primary IgAN
* Compliance with stable and optimal dose of renin-angiotensin system inhibitor treatment for ≥ 3 months

Exclusion Criteria

Common to both disease cohorts:

* eGFR \< 30 milliliters/minute/1.73 meters squared
* Previously received a complement inhibitor (for example, eculizumab)
* Concomitant significant renal disease other than LN or IgAN
* History of other solid organ or bone marrow transplant
* Uncontrolled hypertension

For IgAN cohort:

* Diagnosis of rapid progressive glomerulonephritis
* Prednisone or prednisone equivalent \> 20 milligram (mg) per day for \> 14 consecutive days or any other immunosuppression within 6 months
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Alexion Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Research Site

San Dimas, California, United States

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Santa Monica, California, United States

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South Gate, California, United States

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Stanford, California, United States

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Orlando, Florida, United States

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Plantation, Florida, United States

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Lawrenceville, Georgia, United States

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Lexington, Kentucky, United States

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Louisville, Kentucky, United States

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Boston, Massachusetts, United States

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Boston, Massachusetts, United States

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Kansas City, Missouri, United States

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New York, New York, United States

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Chapel Hill, North Carolina, United States

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Columbus, Ohio, United States

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El Paso, Texas, United States

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Houston, Texas, United States

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Herston, , Australia

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Parkville, , Australia

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Westmead, , Australia

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London, Ontario, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Clermont-Ferrand, , France

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Le Kremlin-Bicêtre, , France

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Paris, , France

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Saint-Priest-en-Jarez, , France

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Strasbourg, , France

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Toulouse, , France

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Berlin, , Germany

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Essen, , Germany

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Hanover, , Germany

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Lübeck, , Germany

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Bologna, , Italy

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Brescia, , Italy

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Florence, , Italy

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Torino, , Italy

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Maastricht, , Netherlands

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Lodz, , Poland

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Anyang-si, , South Korea

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Seongnam-si, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Barcelona, , Spain

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Barcelona, , Spain

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Lleida, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Málaga, , Spain

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Palma de Mallorca, , Spain

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Seville, , Spain

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Valencia, , Spain

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Zaragoza, , Spain

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Kaohsiung City, , Taiwan

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Kaohsiung City, , Taiwan

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New Taipei City, , Taiwan

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Taichung, , Taiwan

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Edgbaston, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Salford, , United Kingdom

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Countries

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United States Australia Canada France Germany Italy Netherlands Poland South Korea Spain Taiwan United Kingdom

References

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Lafayette R, Tumlin J, Fenoglio R, Kaufeld J, Perez Valdivia MA, Wu MS, Susan Huang SH, Alamartine E, Kim SG, Yee M, Kateifides A, Rice K, Garlo K, Barratt J; SANCTUARY Study Investigators. Efficacy and Safety of Ravulizumab in IgA Nephropathy: A Phase 2 Randomized Double-Blind Placebo-Controlled Trial. J Am Soc Nephrol. 2025 Apr 1;36(4):645-656. doi: 10.1681/ASN.0000000534. Epub 2024 Oct 25.

Reference Type DERIVED
PMID: 39455063 (View on PubMed)

Avasare R, Drexler Y, Caster DJ, Mitrofanova A, Jefferson JA. Management of Lupus Nephritis: New Treatments and Updated Guidelines. Kidney360. 2023 Oct 1;4(10):1503-1511. doi: 10.34067/KID.0000000000000230.

Reference Type DERIVED
PMID: 37528520 (View on PubMed)

Other Identifiers

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ALXN1210-NEPH-202

Identifier Type: -

Identifier Source: org_study_id

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