Placebo-controlled Study Comparing Niraparib Plus Pembrolizumab Versus Placebo Plus Pembrolizumab as Maintenance Therapy in Participants With Advanced/Metastatic Non-Small Cell Lung Cancer

NCT ID: NCT04475939

Last Updated: 2026-01-08

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

666 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-10-26

Study Completion Date

2026-03-06

Brief Summary

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This is a multicenter, randomized, double-blind, placebo-controlled study of niraparib plus pembrolizumab versus placebo plus pembrolizumab as maintenance therapy in participants with advanced or metastatic non-small cell lung cancer (NSCLC) who have achieved stable disease (SD), partial response (PR), or complete response (CR) following completion of standard of care first-line (SoC 1L) platinum-based induction chemotherapy with pembrolizumab. The primary hypotheses are: participants with confirmed diagnosis of NSCLC could benefit from niraparib plus pembrolizumab versus placebo plus pembrolizumab with respect to Progression-free survival (PFS) and Overall survival (OS).

Detailed Description

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Conditions

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Lung Cancer, Non-Small Cell

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators
The participant Investigator study staff and the Sponsor study team will be blinded.

Study Groups

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Participants receiving niraparib plus pembrolizumab

Eligible participants will receive niraparib along with pembrolizumab.

Group Type EXPERIMENTAL

Niraparib

Intervention Type DRUG

Niraparib will be administered.

Pembrolizumab

Intervention Type BIOLOGICAL

Pembrolizumab will be administered

Participants receiving placebo plus pembrolizumab

Eligible participants will receive matching placebo along with pembrolizumab.

Group Type PLACEBO_COMPARATOR

Pembrolizumab

Intervention Type BIOLOGICAL

Pembrolizumab will be administered

Placebo

Intervention Type DRUG

Matching placebo will be administered

Interventions

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Niraparib

Niraparib will be administered.

Intervention Type DRUG

Pembrolizumab

Pembrolizumab will be administered

Intervention Type BIOLOGICAL

Placebo

Matching placebo will be administered

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Participant must be \>=18 years of age.
* Has a histologically or cytologically confirmed diagnosis of NSCLC without known targetable driver alteration (either non-squamous or squamous histology; mixed histology is allowed for which an approved targeted therapy is available in the 1L induction/maintenance therapy setting).
* Has advanced (Stage IIIB or Stage IIIC, not amenable to definitive chemoradiotherapy) or metastatic (Stage IV) or metastatic (Stage IV) NSCLC.
* Has completed at least 4 but no more than 6 cycles of SoC 1L platinum-based induction chemotherapy with pembrolizumab.
* Has SD, PR, or CR of the NSCLC per Investigator's assessment after completion of 4 to 6 cycles of SoC 1L platinum-based induction chemotherapy with pembrolizumab.
* Has an Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.
* Has a life expectancy of at least 12 weeks.
* Has adequate organ and bone marrow function.
* Must submit tumor specimens.
* Must be able to swallow and retain orally administered study treatment.
* A female is eligible to participate if she is not pregnant or breastfeeding and must follow contraceptive guidance during the treatment period and 180 days afterwards.
* A male is eligible to participate if he agrees to contraceptive guidance and refrains from sperm donation during the intervention period and for at least 90 days after the last dose of study treatment.
* Is able to understand the study procedures and agrees to participate in the study by providing written informed consent. Participants must be informed that their participation is voluntary. Participants will be required to sign a statement of informed consent to participate in the study.

Exclusion Criteria

* Has mixed small cell lung cancer or sarcomatoid variant NSCLC.
* Has received prior Poly (adenosine diphosphate-ribose) polymerase (PARP) inhibitor(s) in prior lines of treatment.
* Has systolic blood pressure (BP) \>140 millimeters of mercury (mmHg) or diastolic BP \>90 mmHg.
* Has any clinically significant gastrointestinal abnormalities that may alter absorption such as malabsorption syndrome or major resection of the stomach and/or bowels.
* Has leptomeningeal disease, carcinomatous meningitis, symptomatic brain metastases, or radiographic signs of CNS hemorrhage.
* Has received colony-stimulating factors (granulocyte macrophage colony-stimulating factor or recombinant erythropoietin) within 4 weeks prior to the first dose of study treatment.
* Has an active or previously documented autoimmune or inflammatory disorder.
* Is receiving chronic systemic steroids (prednisone \>20 mg per day) other than intermittent use of bronchodilators, inhaled steroids, or local steroid.
* Has other active concomitant malignancy that warrants systemic, biologic, or hormonal therapy.
* Is pregnant, breastfeeding, or expecting to conceive children while receiving study treatment and/or for up to 180 days after the last dose of study treatment.
* Has a known history of Myelodysplastic syndrome (MDS) or Acute myeloid leukemia (AML).
* Has a known history of active tuberculosis.
* Has current active pneumonitis within 90 days of planned start of the study or a known history of interstitial lung disease, drug-related pneumonitis, or radiation pneumonitis requiring steroid treatment.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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GlaxoSmithKline

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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GSK Clinical Trials

Role: STUDY_DIRECTOR

GlaxoSmithKline

Locations

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Fullerton, California, United States

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Los Angeles, California, United States

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Lone Tree, Colorado, United States

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Norwich, Connecticut, United States

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Tallahassee, Florida, United States

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Atlanta, Georgia, United States

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Newnan, Georgia, United States

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Niles, Illinois, United States

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Iowa City, Iowa, United States

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Worcester, Massachusetts, United States

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Mineola, New York, United States

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New York, New York, United States

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Charlotte, North Carolina, United States

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Pittsburgh, Pennsylvania, United States

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Chattanooga, Tennessee, United States

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Nashville, Tennessee, United States

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Dallas, Texas, United States

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San Antonio, Texas, United States

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Sherman, Texas, United States

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Sugar Land, Texas, United States

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Waco, Texas, United States

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Fairfax, Virginia, United States

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Cipoletti Rio Negro, , Argentina

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Ciudad Autonoma de Buenos Aire, , Argentina

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Ciudad Autonoma de Buenos Aire, , Argentina

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Córdoba, , Argentina

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Florida, , Argentina

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La Plata, , Argentina

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Rosario, , Argentina

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Blacktown, New South Wales, Australia

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Hobart, Tasmania, Australia

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Ballarat, Victoria, Australia

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Heidelberg, Victoria, Australia

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Brussels, , Belgium

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Edegem, , Belgium

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Leuven, , Belgium

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Roeselare, , Belgium

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Belo Horizonte, , Brazil

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Cachoeiro de Itapemirim, , Brazil

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Curitiba, , Brazil

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Porto Alegre, , Brazil

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Rio de Janeiro, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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Uberlândia, , Brazil

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Panagyurishte, , Bulgaria

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Pleven, , Bulgaria

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Plovdiv, , Bulgaria

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Rousse, , Bulgaria

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Sofia, , Bulgaria

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Santiago, , Chile

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Temuco, , Chile

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Bogotá, , Colombia

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Montería, , Colombia

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Brest, , France

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Créteil, , France

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Grenoble, , France

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Lille, , France

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Paris, , France

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Paris, , France

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Rennes, , France

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Saint-Herblain, , France

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Strasbourg, , France

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Toulon, , France

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Toulouse, , France

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Berlin, , Germany

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Bonn, , Germany

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Essen, , Germany

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Frankfurt, , Germany

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Gauting, , Germany

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Großhansdorf, , Germany

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Halle, , Germany

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Hamburg, , Germany

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Hanover, , Germany

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Heidelberg, , Germany

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Hemer, , Germany

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Jena, , Germany

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München, , Germany

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München, , Germany

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Stuttgart, , Germany

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Velbert, , Germany

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Athens, , Greece

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Athens, , Greece

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Athens, , Greece

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Athens, , Greece

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Athens, , Greece

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Athens, , Greece

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Athens, , Greece

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Heraklion Crete, , Greece

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Larissa, , Greece

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Neo Faliro, , Greece

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Pátrai, , Greece

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Pylaia Thessaloniki, , Greece

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Rio Patras, , Greece

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Thessaloniki, , Greece

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Thessaloniki, , Greece

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Thessaloniki, , Greece

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Thessaloniki, , Greece

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Budapest, , Hungary

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Budapest, , Hungary

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Gyöngyös, , Hungary

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Tatabánya, , Hungary

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Törökbálint, , Hungary

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Cork, , Ireland

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Dublin, , Ireland

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Avellino, , Italy

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Aviano PN, , Italy

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Bari, , Italy

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Catania, , Italy

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Florence, , Italy

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Milan, , Italy

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Milan, , Italy

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Milan, , Italy

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Monza, , Italy

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Napoli, , Italy

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Orbassano to, , Italy

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Pisa, , Italy

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Roma, , Italy

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Verona, , Italy

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Mexico City, , Mexico

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Mexico City, , Mexico

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Mexico City, , Mexico

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Monterrey, , Mexico

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Puebla Puebla, , Mexico

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's-Hertogenbosch, , Netherlands

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Amersfoort, , Netherlands

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Amsterdam, , Netherlands

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Enschede, , Netherlands

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Maastricht, , Netherlands

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Utrecht, , Netherlands

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Zwolle, , Netherlands

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Drammen, , Norway

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Lrenskog, , Norway

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Oslo, , Norway

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Lima, , Peru

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Bialystok, , Poland

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Lodz, , Poland

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Olsztyn, , Poland

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Bucharest, , Romania

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Bucharest, , Romania

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Cluj-Napoca, , Romania

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Craiova, , Romania

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Iași, , Romania

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Satu Mare, , Romania

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Timișoara, , Romania

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Moscow, , Russia

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Moscow, , Russia

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Nizhny Novgorod, , Russia

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Omsk, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Seongnam-si, , South Korea

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Seongnam-si Gyeonggi-do, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Suwon Kyunggi-do, , South Korea

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A Coruña, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Córdoba, , Spain

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Girona, , Spain

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Las Palmas de Gran Canar, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Málaga, , Spain

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PamplonaNavarra, , Spain

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Santander, , Spain

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Zaragoza, , Spain

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Gävle, , Sweden

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Stockholm, , Sweden

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Uppsala, , Sweden

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Lausanne, , Switzerland

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Ankara, , Turkey (Türkiye)

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Ankara, , Turkey (Türkiye)

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Ankara, , Turkey (Türkiye)

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Edirne, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Bournemouth, , United Kingdom

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Dundee, , United Kingdom

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Middlesex, , United Kingdom

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Oxford, , United Kingdom

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Wrexham, , United Kingdom

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Countries

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United States Argentina Australia Belgium Brazil Bulgaria Chile Colombia France Germany Greece Hungary Ireland Italy Mexico Netherlands Norway Peru Poland Romania Russia South Korea Spain Sweden Switzerland Turkey (Türkiye) United Kingdom

References

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Ramalingam SS, Thara E, Awad MM, Dowlati A, Haque B, Stinchcombe TE, Dy GK, Spigel DR, Lu S, Iyer Singh N, Tang Y, Teslenko I, Iannotti N. JASPER: Phase 2 trial of first-line niraparib plus pembrolizumab in patients with advanced non-small cell lung cancer. Cancer. 2022 Jan 1;128(1):65-74. doi: 10.1002/cncr.33885. Epub 2021 Sep 3.

Reference Type DERIVED
PMID: 34478166 (View on PubMed)

Other Identifiers

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2023-508443-40

Identifier Type: REGISTRY

Identifier Source: secondary_id

2020-002202-20

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

213400

Identifier Type: -

Identifier Source: org_study_id

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