A Study of the Safety of Oral Elsubrutinib Capsules and Oral Upadacitinib Tablets Given Alone or in Combination (ABBV-599) for Adult Participants With Moderately to Severely Active Systemic Lupus Erythematosus to Assess Change in Disease State

NCT ID: NCT04451772

Last Updated: 2025-01-14

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

185 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-07-27

Study Completion Date

2024-01-03

Brief Summary

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Systemic Lupus Erythematosus (SLE) is an immune-mediated disease associated with inflammation of multiple organ systems. This study will evaluate how well elsubrutinib and upadacitinib given alone or as the ABBV-599 combination (elsubrutinib/upadacitinib) works within the body, in participants who completed study M19-130. This study will assess the change in disease symptoms.

ABBV-599 is an investigational drug being developed for the treatment of Systemic Lupus Erythematosus (SLE). This study is "double-blinded", which means that neither the trial participants nor the study doctors will know who will be given which study drug. Study doctors put the participants into 1 of 4 groups called treatment arms. Each group receives a different treatment. Adult participants with a diagnosis of SLE will be enrolled. Around 260 participants will be enrolled in the study in approximately 100 sites worldwide.

Participants will receive the following for up to 56 weeks:

Participants will receive oral elsubrutinib capsules and/or oral upadacitinib tablets once daily for up to 56 weeks. Participants who were receiving elsubrutinib and/or upadacitnib in M19-130 will continue to receive the same treatment in this study. Participants who were receiving placebo in M19-130 will be re-randomized to one of the 2 combination treatment arms in this study.

Arm 1: Elsubrutinib Dose A and Upadacitinib Dose A Arm 2: Elsubrutinib Dose A and Upadacitinib Dose B

There may be higher burden for participants in this trial compared to their standard of care. Participants will attend monthly visits during the course of the study at a hospital or clinic. The effect of the treatment will be checked by medical assessments, blood tests, checking for side effects and completing questionnaires.

Detailed Description

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Conditions

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Systemic Lupus Erythematosus (SLE)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ABBV-599 High Dose (Elsubrutinib 60 mg/upadacitinib 30 mg) -> ABBV-599 High Dose

Participants received elsubrutinib 60 mg capsules once a day by mouth and upadacitinib 30 mg film-coated tablets once a day by mouth for 48 weeks in Study M19-130. Participants continued on this regimen in the current study (M20-186) for up to 56 weeks.

Group Type EXPERIMENTAL

Elsubrutinib

Intervention Type DRUG

Capsule; Oral

Upadacitinib

Intervention Type DRUG

Film-coated tablet; Oral

Elsubrutinib placebo/upadacitinib 30 mg -> Elsubrutinib placebo/upadacitinib 30 mg

Participants received placebo capsules for elsubrutinib once a day by mouth and upadacitinib 30 mg film-coated tablets once a day by mouth for 48 weeks in Study M19-130. Participants continued on this regimen in the current study (M20-186) for up to 56 weeks.

Group Type EXPERIMENTAL

Placebo for Elsubrutinib

Intervention Type DRUG

Capsule; Oral

Upadacitinib

Intervention Type DRUG

Film-coated tablet; Oral

Elsubrutinib placebo/upadacitinib placebo -> ABBV-599 High Dose

Participants received placebo capsules for elsubrutinib once a day by mouth and placebo film-coated tablets for upadacitinib once a day by mouth for 48 weeks in Study M19-130. Participants received elsubrutinib 60 mg capsules once a day by mouth and upadacitinib 30 mg film-coated tablets once a day in the current study (M20-186) for up to 56 weeks.

Group Type EXPERIMENTAL

Elsubrutinib

Intervention Type DRUG

Capsule; Oral

Upadacitinib

Intervention Type DRUG

Film-coated tablet; Oral

ABBV-599 Low Dose (Elsubrutinib 60 mg/upadacitinib 15 mg) -> ABBV-599 Low Dose

Participants received elsubrutinib 60 mg capsules once a day by mouth and upadacitinib 15 mg film-coated tablets once a day by mouth for 48 weeks in Study M19-130. Participants continued on this regimen in the current study (M20-186) for up to 56 weeks.

Group Type EXPERIMENTAL

Elsubrutinib

Intervention Type DRUG

Capsule; Oral

Upadacitinib

Intervention Type DRUG

Film-coated tablet; Oral

Elsubrutinib 60 mg/upadacitinib placebo -> Elsubrutinib 60 mg/upadacitinib placebo

Participants received elsubrutinib 60 mg capsules once a day by mouth and placebo film-coated tablets for upadacitinib once a day by mouth for 48 weeks in Study M19-130. Participants continued on this regimen in the current study (M20-186) for up to 56 weeks.

Group Type EXPERIMENTAL

Elsubrutinib

Intervention Type DRUG

Capsule; Oral

Placebo for Upadacitinib

Intervention Type DRUG

Film-coated tablet; Oral

Elsubrutinib placebo/upadacitinib placebo -> ABBV-599 Low Dose

Participants received placebo capsules for elsubrutinib once a day by mouth and placebo film-coated tablets for upadacitinib once a day by mouth for 48 weeks in Study M19-130. Participants received elsubrutinib 60 mg capsules once a day by mouth and upadacitinib 15 mg film-coated tablets once a day by mouth for 48 weeks in the current study (M20-186) for up to 56 weeks.

Group Type EXPERIMENTAL

Elsubrutinib

Intervention Type DRUG

Capsule; Oral

Upadacitinib

Intervention Type DRUG

Film-coated tablet; Oral

Interventions

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Elsubrutinib

Capsule; Oral

Intervention Type DRUG

Placebo for Elsubrutinib

Capsule; Oral

Intervention Type DRUG

Upadacitinib

Film-coated tablet; Oral

Intervention Type DRUG

Placebo for Upadacitinib

Film-coated tablet; Oral

Intervention Type DRUG

Other Intervention Names

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ABBV-105 ABT-494 RINVOQ

Eligibility Criteria

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Inclusion Criteria

* Completed Study M19-130 (i.e., the randomized controlled trial of elsubrutinib, upadacitinib, and ABBV-599 \[elsubrutinib/upadacitinib\] combination or matching placebo) and will not have developed any laboratory or clinical discontinuation criteria as defined in that study.
* On stable background treatment for SLE throughout the study.

Exclusion Criteria

* Active, chronic, or recurrent viral, or bacterial infection.
* Active tuberculosis (TB)
* History of gastrointestinal (GI) perforation, diverticulitis, or a significantly increased risk for GI perforation per investigator assessment.
* Participant require vaccination with live vaccine during study participation.
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AbbVie

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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ABBVIE INC.

Role: STUDY_DIRECTOR

AbbVie

Locations

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Duplicate_AZ Arthritis and Rheumotology Research, PLLC /ID# 227833

Phoenix, Arizona, United States

Site Status

Wallace Rheumatic Studies Center, LLC /ID# 224374

Beverly Hills, California, United States

Site Status

Valerius Medical Group & Research Center /ID# 223922

Los Alamitos, California, United States

Site Status

East Bay Rheumatology Medical /ID# 225493

San Leandro, California, United States

Site Status

University of Colorado Hospital /ID# 245087

Aurora, Colorado, United States

Site Status

Duplicate_Arthritis & Rheumatic Disease Specialties /ID# 227828

Aventura, Florida, United States

Site Status

Millennium Research /ID# 233192

Ormond Beach, Florida, United States

Site Status

IRIS Research and Development, LLC /ID# 227814

Plantation, Florida, United States

Site Status

Deerbrook Medical Associates /ID# 227330

Libertyville, Illinois, United States

Site Status

Qualmedica Research, LLC /ID# 227817

Evansville, Indiana, United States

Site Status

The Center for Rheumatology and Bone Research /ID# 225479

Wheaton, Maryland, United States

Site Status

Beth Israel Deaconess Medical Center /ID# 222505

Boston, Massachusetts, United States

Site Status

June DO, PC /ID# 221841

Lansing, Michigan, United States

Site Status

Duplicate_NYU Langone Health/NYU School of Medicine /ID# 245088

New York, New York, United States

Site Status

STAT Research, Inc. /ID# 221840

Vandalia, Ohio, United States

Site Status

Allegheny Health Network Research Institute /ID# 245086

Pittsburgh, Pennsylvania, United States

Site Status

Dr. Ramesh Gupta /ID# 225524

Memphis, Tennessee, United States

Site Status

Tekton Research, Inc. /ID# 224411

Austin, Texas, United States

Site Status

Accurate Clinical Management /ID# 225509

Houston, Texas, United States

Site Status

SW Rheumatology Res. LLC /ID# 225485

Mesquite, Texas, United States

Site Status

Carilion Clinic /ID# 227832

Roanoke, Virginia, United States

Site Status

Hospital Militar Central Cirujano Mayor Dr. Cosme Argerich /ID# 222569

Ciudad Autonoma Buenos Aires, Buenos Aires, Argentina

Site Status

Hospital Interzonal General de Agudos General Jose de San Martin /ID# 221893

La Plata, Buenos Aires, Argentina

Site Status

CER Instituto Medico /ID# 223175

Quilmes, Buenos Aires, Argentina

Site Status

Aprillus Asistencia e Investigacion /ID# 221890

Ciudad Autonoma de Buenos Aire, Buenos Aires F.D., Argentina

Site Status

Instituto CAICI S.R.L /ID# 221892

Rosario, Santa Fe Province, Argentina

Site Status

Centro de Investigaciones Medicas Tucuman /ID# 221888

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status

Investigaciones Clinicas Tucuman /ID# 221889

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status

Rheumatology Research Unit Sunshine Coast /ID# 221816

Maroochydore, Queensland, Australia

Site Status

Emeritus Research /ID# 223027

Camberwell, Victoria, Australia

Site Status

Monash Medical Centre /ID# 221814

Clayton, Victoria, Australia

Site Status

UMHAT Sveti Ivan Rilski /ID# 223358

Sofia, , Bulgaria

Site Status

UMHAT Sveti Ivan Rilski /ID# 223359

Sofia, , Bulgaria

Site Status

Duplicate_Peking Union Medical College Hospital /ID# 222950

Beijing, Beijing Municipality, China

Site Status

Guangdong Provincial People's Hospital /ID# 222851

Guangzhou, Guangdong, China

Site Status

People's Hospital of Xinjiang /ID# 222928

Urumqi, Guizhou, China

Site Status

Huashan Hospital, Fudan University /ID# 222929

Shanghai, Shanghai Municipality, China

Site Status

Duplicate_Centro Integral de Reumatologia del Caribe Circaribe SAS /ID# 221879

Barranquilla, Atlántico, Colombia

Site Status

Duplicate_Centro de Investigacion en Reumatologia y Especialidades Medicas- CIRE /ID# 221884

Bogota, Cundinamarca, Colombia

Site Status

Preventive Care Sas /Id# 221881

Chía, Cundinamarca, Colombia

Site Status

Healthy Medical Center S.A.S /ID# 221882

Zipaquirá, Cundinamarca, Colombia

Site Status

Clinica Universitaria Bolivari /ID# 221880

Medellin, Valle del Cauca Department, Colombia

Site Status

Duplicate_Charite Universitaetsmedizin Berlin - Campus Mitte /ID# 222963

Berlin, , Germany

Site Status

Universitaetsklinikum Carl Gustav Carus an der TU Dresden /ID# 222964

Dresden, , Germany

Site Status

Duplicate_Debreceni Egyetem Klinikai Kozpont /ID# 222480

Debrecen, Hajdú-Bihar, Hungary

Site Status

Vital Medicina Kft /ID# 222479

Veszprém, Veszprém megye, Hungary

Site Status

Duplicate_Azienda Ospedaliero-Universitaria di Ferrara-Arcispedale Sant Anna /ID# 221919

Cona, Ferrara, Italy

Site Status

Chukyo Hospital /ID# 223398

Nagoya, Aichi-ken, Japan

Site Status

NHO Nagoya Medical Center /ID# 222397

Nagoya, Aichi-ken, Japan

Site Status

Hospital of the University of Occupational and Environmental Health, Japan /ID# 222499

Kitakyushu-shi, Fukuoka, Japan

Site Status

Hiroshima Red Cross Hospital & Atomic-bomb Survivors Hospital /ID# 222393

Hiroshima, Hiroshima, Japan

Site Status

National Hospital Organization Asahikawa Medical Center /ID# 222394

Asahikawa-shi, Hokkaido, Japan

Site Status

EIRAKU Internal Medicine Clinic /ID# 222385

Kagoshima, Kagoshima-ken, Japan

Site Status

Tohoku University Hospital /ID# 222392

Sendai, Miyagi, Japan

Site Status

Shinshu University Hospital /ID# 222395

Matsumoto-shi, Nagano, Japan

Site Status

Saitama Medical Center /ID# 222389

Kawagoe-shi, Saitama, Japan

Site Status

Keio University Hospital /ID# 222498

Shinjuku-ku, Tokyo, Japan

Site Status

Morales Vargas Centro de Investigacion S.C. /ID# 221912

León, Guanajuato, Mexico

Site Status

Centro Integral en Reumatologia S.A de C.V /ID# 221914

Guadalajara, Jalisco, Mexico

Site Status

Centro de Estudios de Investigación Básica y Clínica, S.C. /ID# 221910

Guadalajara, Jalisco, Mexico

Site Status

RM Pharma Specialists S.A de C.V. /ID# 221915

Mexico City, Mexico City, Mexico

Site Status

CINTRE, Centro de Investigación y Tratamiento Reumatológico SC /ID# 221913

Mexico City, Mexico City, Mexico

Site Status

Medical Care & Research SA de CV /ID# 221911

Mérida, Yucatán, Mexico

Site Status

North Shore Hospital /ID# 221850

Takapuna, Auckland, New Zealand

Site Status

Ortopedyczno-Rehabilitacyjny Szpital Kliniczny im. Wiktora Degi /ID# 221859

Poznan, Greater Poland Voivodeship, Poland

Site Status

Centrum Nowoczesnych Terapii Dobry Lekarz Sp. z o.o. /ID# 224430

Krakow, Lesser Poland Voivodeship, Poland

Site Status

WroMedica I. Bielicka, A. Strzalkowska s.c. /ID# 221860

Wroclaw, Lower Silesian Voivodeship, Poland

Site Status

MTZ Clinical Research Powered by Pratia /ID# 224431

Warsaw, Masovian Voivodeship, Poland

Site Status

GCM Medical Group PSC /ID# 224394

San Juan, , Puerto Rico

Site Status

Mindful Medical Research /ID# 222513

San Juan, , Puerto Rico

Site Status

Seoul National University Hospital /ID# 221897

Seoul, Seoul Teugbyeolsi, South Korea

Site Status

HUA - Txagorritxu /ID# 221992

Vitoria-Gasteiz, Alava, Spain

Site Status

Consorci Corporacio Sanitaria Parc Tauli Sabadell /ID# 221995

Sabadell, Barcelona, Spain

Site Status

Hospital Universitario Basurto /ID# 221999

Bilbao, Vizcaya, Spain

Site Status

Hospital Universitario de Galdakao /ID# 221996

Galdakao, Vizcaya, Spain

Site Status

Duplicate_Hospital Universitario A Coruna - CHUAC /ID# 221993

A Coruña, , Spain

Site Status

Hospital Universitario 12 de Octubre /ID# 221994

Madrid, , Spain

Site Status

Hospital Universitario Virgen de Valme /ID# 221997

Seville, , Spain

Site Status

Hospital Universitario y Politecnico La Fe /ID# 221998

Valencia, , Spain

Site Status

Taichung Veterans General Hospital /ID# 221748

Taichung, Keelung, Taiwan

Site Status

Taipei Veterans General Hosp /ID# 221746

Taipei, Keelung, Taiwan

Site Status

National Taiwan University Hospital /ID# 221745

Taipei City, Taipei, Taiwan

Site Status

China Medical University Hospital /ID# 221747

Taichung, , Taiwan

Site Status

Taipei Medical University Hospital /ID# 227653

Taipei, , Taiwan

Site Status

Linkou Chang Gung Memorial Hospital /ID# 222469

Taoyuan, , Taiwan

Site Status

Guys and St Thomas NHS Foundation Trust /ID# 221863

London, London, City of, United Kingdom

Site Status

Duplicate_Manchester University NHS Foundation Trust /ID# 221861

Manchester, , United Kingdom

Site Status

Countries

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United States Argentina Australia Bulgaria China Colombia Germany Hungary Italy Japan Mexico New Zealand Poland Puerto Rico South Korea Spain Taiwan United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2020-001690-72

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

M20-186

Identifier Type: -

Identifier Source: org_study_id

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