Study Comparing Continuous Subcutaneous Infusion Of ABBV-951 With Oral Carbidopa/Levodopa Tablets For Treatment Of Motor Fluctuations In Adult Participants With Advanced Parkinson's Disease

NCT ID: NCT04380142

Last Updated: 2022-11-18

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

174 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-10-19

Study Completion Date

2021-09-29

Brief Summary

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Parkinson's disease (PD) is a neurological condition, which affects the brain. PD gets worse over time, but how quickly it progresses varies a lot from person to person. Some symptoms of PD are tremors, stiffness, and slowness of movement. This study measures the efficacy, safety, and tolerability of ABBV-951 versus oral Levodopa (LD)/Carbidopa (CD) \[LD/CD\] in advanced PD participants to achieve reduction in motor fluctuations.

ABBV-951 is an investigational (unapproved) drug containing Levodopa Phosphate/Carbidopa Phosphate (LDP/CDP) given subcutaneously (under the skin) for the treatment of Parkinson's Disease. Adult participants with advanced PD will be enrolled. Approximately 130 participants will be enrolled in the study in approximately 80 sites across the world.

In one arm, participants will receive ABBV-951 solution as a continuous infusion under the skin plus oral placebo capsules for LD/CD. In the second arm, participants will receive placebo solution for ABBV-951 as a continuous infusion under the skin plus oral capsules containing LD/CD tablets. The treatment duration is 12 weeks.

There may be higher treatment burden for participants in this trial compared to their standard of care. Participants will attend regular visits during the course of the study at a hospital or clinic. The effect of the treatment will be checked by medical assessments, blood tests, checking for side effects, and completing questionnaires.

Detailed Description

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Conditions

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Parkinson's Disease (PD)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ABBV-951 + Placebo for Levodopa/Carbidopa (LD/CD)

After an open-label LD/CD Stabilization Period, participants will receive double-blind ABBV-951 by continuous subcutaneous infusion (CSCI) and oral placebo for LD/CD for 12 weeks

Group Type EXPERIMENTAL

ABBV-951

Intervention Type DRUG

Solution for continuous subcutaneous infusion (CSCI)

Placebo for Levodopa/Carbidopa (LD/CD)

Intervention Type DRUG

Oral capsule

Levodopa/Carbidopa (LD/CD) + Placebo for ABBV-951

After an open-label LD/CD Stabilization Period, participants will receive double-blind oral LD/CD and CSCI of placebo for ABBV-951 for 12 weeks

Group Type ACTIVE_COMPARATOR

Levodopa/Carbidopa (LD/CD)

Intervention Type DRUG

Oral encapsulated tablet

Placebo for ABBV-951

Intervention Type DRUG

Solution for continuous subcutaneous infusion (CSCI)

Interventions

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ABBV-951

Solution for continuous subcutaneous infusion (CSCI)

Intervention Type DRUG

Placebo for Levodopa/Carbidopa (LD/CD)

Oral capsule

Intervention Type DRUG

Levodopa/Carbidopa (LD/CD)

Oral encapsulated tablet

Intervention Type DRUG

Placebo for ABBV-951

Solution for continuous subcutaneous infusion (CSCI)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of idiopathic Parkinson's Disease (PD) that is levodopa-responsive.
* Participant must be taking a minimum of 400 milligrams/day (mg/day) of Levodopa (LD) equivalents and be judged by the investigator to have motor symptoms inadequately controlled by current therapy, have a recognizable/identifiable "Off" and "On" states (motor fluctuations), and have an average "Off" time of at least 2.5 hours/day over 3 consecutive PD Diary days with a minimum of 2 hours each day.
* Participant or caregiver, if applicable, demonstrates the understanding and correct use of the delivery system, including the insertion of the cannula into the participant's abdomen, as assessed by the investigator or designee during the Screening period.

Exclusion Criteria

* Clinically significant, unstable medical conditions or any other reason that the investigator determines would interfere with the participant's participation in this study or would make the participant an unsuitable candidate to receive study drug.
* History of allergic reaction or significant sensitivity to LD or constituents of the study drug (and its excipients) and/or other products in the same class.
* Participant has not received deep brain stimulation, CD/LD enteral suspension, or any other PD medication as continuous daily infusion, whether commercially available or investigational. Previous exposure to ABBV-951 is not allowed.
Minimum Eligible Age

30 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AbbVie

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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ABBVIE INC.

Role: STUDY_DIRECTOR

AbbVie

Locations

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University of Alabama at Birmingham - Main /ID# 216595

Birmingham, Alabama, United States

Site Status

University of South Alabama /ID# 216757

Mobile, Alabama, United States

Site Status

Xenoscience, Inc /ID# 217110

Phoenix, Arizona, United States

Site Status

Barrow Neurological Institute /ID# 216566

Phoenix, Arizona, United States

Site Status

HonorHealth /ID# 216642

Phoenix, Arizona, United States

Site Status

Movement Disorders Center of Arizona /ID# 216503

Scottsdale, Arizona, United States

Site Status

Banner Sun Health Res Inst /ID# 216507

Sun City, Arizona, United States

Site Status

University of Arkansas for Medical Sciences /ID# 216501

Little Rock, Arkansas, United States

Site Status

The Parkinson's & Movement Disorder Institute - Fountain Valley /ID# 216705

Fountain Valley, California, United States

Site Status

Neuro Pain Medical Center /ID# 216551

Fresno, California, United States

Site Status

University of California, San /ID# 216598

La Jolla, California, United States

Site Status

Loma Linda University Medical /ID# 216500

Loma Linda, California, United States

Site Status

Collaborative Neuroscience Research - Long Beach /ID# 216970

Long Beach, California, United States

Site Status

University of California, Los Angeles /ID# 216674

Los Angeles, California, United States

Site Status

SC3 Research Group - Pasadena /ID# 216821

Pasadena, California, United States

Site Status

Cedars-Sinai Medical Center-West Hollywood /ID# 216561

West Hollywood, California, United States

Site Status

University of Colorado Hospital /ID# 216527

Aurora, Colorado, United States

Site Status

Alpine Clinical Research Center /ID# 216637

Boulder, Colorado, United States

Site Status

Denver Neurological Research, LLC /ID# 216784

Denver, Colorado, United States

Site Status

Rocky Mountain Movement Disorders Center /ID# 216737

Englewood, Colorado, United States

Site Status

Christiana Care Health Service /ID# 216515

Newark, Delaware, United States

Site Status

Georgetown University Hospital /ID# 216632

Washington D.C., District of Columbia, United States

Site Status

Parkinson's Disease and Movement Disorders Center of Boca Raton /ID# 216517

Boca Raton, Florida, United States

Site Status

Brain Matters Research /ID# 217089

Delray Beach, Florida, United States

Site Status

Fixel Institute for Neurological Diseases /ID# 216514

Gainesville, Florida, United States

Site Status

Visionary Investigators Network - Miami /ID# 216679

Miami, Florida, United States

Site Status

Renstar Medical Research /ID# 216765

Ocala, Florida, United States

Site Status

Neurology Associates Ormond Beach /ID# 216521

Ormond Beach, Florida, United States

Site Status

Parkinson's Disease Treatment Center of Southwest Florida /ID# 222656

Port Charlotte, Florida, United States

Site Status

University of South Florida /ID# 216638

Tampa, Florida, United States

Site Status

Premiere Research Institute - Palm Beach /ID# 217207

West Palm Beach, Florida, United States

Site Status

Duplicate_Atlanta Center for Medical Res /ID# 217091

Atlanta, Georgia, United States

Site Status

The Neurological Center of North Georgia /ID# 216499

Gainesville, Georgia, United States

Site Status

Rush University Medical Center /ID# 216567

Chicago, Illinois, United States

Site Status

University of Chicago Medical /ID# 217187

Chicago, Illinois, United States

Site Status

Indiana Clinical Research Cent /ID# 216615

Indianapolis, Indiana, United States

Site Status

Univ Kansas Med Ctr /ID# 216528

Kansas City, Kansas, United States

Site Status

St Elizabeth's Medical Center - Brighton /ID# 216716

Brighton, Massachusetts, United States

Site Status

Michigan State University /ID# 217158

East Lansing, Michigan, United States

Site Status

Clinical Research Professionals - Chesterfield /ID# 216669

Chesterfield, Missouri, United States

Site Status

St. Luke's Hosp. of Kansas City /ID# 216633

Kansas City, Missouri, United States

Site Status

Washington University-School of Medicine /ID# 216548

St Louis, Missouri, United States

Site Status

Global Neurosciences Institute /ID# 217875

Lawrenceville, New Jersey, United States

Site Status

Northwell Health /ID# 216833

Lake Success, New York, United States

Site Status

Mount Sinai Beth Israel /ID# 216712

New York, New York, United States

Site Status

University of Rochester /ID# 218737

Rochester, New York, United States

Site Status

Wake Forest Univ HS /ID# 216522

Winston-Salem, North Carolina, United States

Site Status

Ohio State University - Wexner Medical Center /ID# 216900

Columbus, Ohio, United States

Site Status

The Orthopedic Foundation /ID# 217157

New Albany, Ohio, United States

Site Status

The Movement Disorder Clinic of Oklahoma /ID# 216860

Tulsa, Oklahoma, United States

Site Status

Legacy Research Institute /ID# 216558

Portland, Oregon, United States

Site Status

University of Pennsylvania /ID# 216560

Philadelphia, Pennsylvania, United States

Site Status

Thomas Jefferson University Hospital /ID# 216553

Philadelphia, Pennsylvania, United States

Site Status

Prisma Health-Upstate /ID# 216594

Greenville, South Carolina, United States

Site Status

Premier Neurology, P.C. /ID# 217308

Greer, South Carolina, United States

Site Status

Coastal Neurology /ID# 217190

Port Royal, South Carolina, United States

Site Status

KCA Neurology - Franklin /ID# 217419

Franklin, Tennessee, United States

Site Status

Vanderbilt University Medical Center /ID# 216675

Nashville, Tennessee, United States

Site Status

Houston Pulmonary Sleep and Allergy Associates /ID# 216942

Cypress, Texas, United States

Site Status

Kerwin Research Center /ID# 216587

Dallas, Texas, United States

Site Status

Neurology Consultants of Dallas - LBJ Fwy /ID# 216564

Dallas, Texas, United States

Site Status

Texas Movement Disorder Specialists /ID# 216523

Georgetown, Texas, United States

Site Status

Houston Methodist Hospital /ID# 216707

Houston, Texas, United States

Site Status

Central Texas Neurology Consul /ID# 216629

Round Rock, Texas, United States

Site Status

University of Utah Health Care /ID# 216710

Salt Lake City, Utah, United States

Site Status

Meridian Clinical Research /ID# 216731

Norfolk, Virginia, United States

Site Status

Neurological Associates - Forest Ave /ID# 216636

Richmond, Virginia, United States

Site Status

Swedish Neuroscience /ID# 216526

Seattle, Washington, United States

Site Status

Inland Northwest Research /ID# 221036

Spokane, Washington, United States

Site Status

Medical College of Wisconsin /ID# 216498

Milwaukee, Wisconsin, United States

Site Status

Liverpool Hospital /ID# 218681

Liverpool, New South Wales, Australia

Site Status

Westmead Hospital /ID# 216535

Westmead, New South Wales, Australia

Site Status

Gold coast University Hospital /ID# 218373

Southport, Queensland, Australia

Site Status

Royal Adelaide Hospital /ID# 216533

Adelaide, South Australia, Australia

Site Status

Kingston Centre /ID# 216537

Cheltenham, Victoria, Australia

Site Status

The Royal Melbourne Hospital /ID# 216536

Parkville, Victoria, Australia

Site Status

Countries

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United States Australia

References

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Pahwa R, Aldred J, Soileau MJ, Standaert DG, Fung VSC, Kimber T, Malaty IA, Santos-Garcia D, Carroll C, Henriksen T, Parab A, Yan CH, Facheris MF, Spiegel A, Harmer L, Zamudio J, Chaudhuri KR. Improvement in Motor Consistency and Stability with Foslevodopa/Foscarbidopa in Advanced Parkinson's Disease: Post Hoc Analysis of Two Phase 3 Clinical Trials. Neurol Ther. 2025 Oct 4. doi: 10.1007/s40120-025-00827-6. Online ahead of print.

Reference Type DERIVED
PMID: 41045349 (View on PubMed)

Soileau MJ, Aldred J, Budur K, Fisseha N, Fung VS, Jeong A, Kimber TE, Klos K, Litvan I, O'Neill D, Robieson WZ, Spindler MA, Standaert DG, Talapala S, Vaou EO, Zheng H, Facheris MF, Hauser RA. Safety and efficacy of continuous subcutaneous foslevodopa-foscarbidopa in patients with advanced Parkinson's disease: a randomised, double-blind, active-controlled, phase 3 trial. Lancet Neurol. 2022 Dec;21(12):1099-1109. doi: 10.1016/S1474-4422(22)00400-8.

Reference Type DERIVED
PMID: 36402160 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2019-003930-18

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

M15-736

Identifier Type: -

Identifier Source: org_study_id

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