Single Patient Expanded Access Treatment Plan For The Investigational Product Narsoplimab

NCT ID: NCT04247906

Last Updated: 2025-12-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

AVAILABLE

Study Classification

EXPANDED_ACCESS

Brief Summary

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The purpose of the EAP is to provide access to hematopoietic stem cell transplant-associated thrombotic microangiopathy (HSCT-TMA) patients who may benefit from treatment with narsoplimab based on the medical judgement of their respective physicians.

Detailed Description

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Conditions

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Hematopoietic Stem Cell Transplant Associated Thrombotic Microangiopathy (HSCT-TMA)

Interventions

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Narsoplimab

Intervention Type DRUG

Other Intervention Names

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OMS721

Eligibility Criteria

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Inclusion Criteria

* Patient (adult or pediatric) must have undergone allogeneic or autologous hematopoietic stem cell transplant (HSCT)
* Patient must be capable of understanding an informed consent form (ICF) or the parent or legal guardian of the patient is able to understand and sign a written ICF prior to the initiation of any treatment procedures.
* Patient must have HSCT- TMA defined as having thrombocytopenia and evidence of microangiopathic hemolytic anemia.
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Impatients N.V. trading as myTomorrows

INDUSTRY

Sponsor Role collaborator

Omeros Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Central Contacts

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My Tomorrows

Role: CONTACT

+31 885253888

Other Identifiers

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721-TMA-EA

Identifier Type: -

Identifier Source: org_study_id

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