Efficacy and Safety of Gefapixant (MK-7264) in Women With Chronic Cough and Stress Urinary Incontinence (MK-7264-042)

NCT ID: NCT04193176

Last Updated: 2024-11-05

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

376 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-05-10

Study Completion Date

2022-09-02

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of gefapixant, in improving symptoms of cough-induced stress urinary incontinence (SUI) in adult female participants with refractory or unexplained chronic cough. The primary hypothesis is that gefapixant is superior to placebo in reducing the frequency of cough-induced SUI episodes over 12 weeks.

Detailed Description

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Conditions

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Chronic Cough

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Gefapixant

Participants will receive gefapixant at a dose of 45 mg administered as an oral tablet twice daily for 12 weeks.

Group Type EXPERIMENTAL

Gefapixant

Intervention Type DRUG

Administered twice daily as an oral tablet of 45 mg

Placebo

Participants will receive placebo matching gefapixant, administered as an oral tablet twice daily for 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered twice daily as a placebo oral tablet matching gefapixant

Interventions

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Gefapixant

Administered twice daily as an oral tablet of 45 mg

Intervention Type DRUG

Placebo

Administered twice daily as a placebo oral tablet matching gefapixant

Intervention Type DRUG

Other Intervention Names

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MK-7264

Eligibility Criteria

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Inclusion Criteria

* Has a chest radiograph or computed tomography scan of the thorax (within 5 years of Screening and after the onset of chronic cough) not demonstrating any abnormality considered to be significantly contributing to the chronic cough or any other lung disease
* Has chronic cough (defined as duration of \>8 weeks after onset of cough symptoms) for ≥12 months
* Has a diagnosis of refractory chronic cough or unexplained chronic cough
* Has symptoms of SUI, defined as involuntary loss of urine on effort, physical exertion, or on sneezing or coughing, for ≥3 months
* Is a female who is not pregnant, not breastfeeding, not of childbearing potential, or agrees to follow contraceptive guidance

Exclusion Criteria

* Is a current smoker
* Has given up smoking within 12 months of screening
* Is a former smoker with a smoking history greater than 20 pack-years (1 pack of 20 cigarettes per day for 20 years)
* Has a history of respiratory tract infection or recent change in pulmonary status within 4 weeks of screening
* Has a history of chronic bronchitis
* Has a history of surgery to treat SUI within 1 year of screening
* Has a history of other specialized treatments for SUI, including intravesical balloon or urethral bulking agent therapy
* Has other external incontinence device currently or within 1 month of screening
* Has a history of Grade 3 or higher pelvic organ prolapse previously documented or diagnosed on screening
* Has a neurogenic bladder
* Has a history of adult nocturnal incontinence
* Has a history of continuous urine leakage within 1 month of screening
* Has a history of interstitial cystitis
* Has a history of neurological disease or injury
* Has active or recurrent urinary tract infection
* Has a history of having a permanent urinary catheter or any urinary catheterization within 3 months of screening
* Has a history of malignancy ≤5 years prior to signing informed consent
* Is a user of recreational or illicit drugs or a recent history (within the last year) of drug or alcohol abuse
* Has a known allergy to gefapixant or its excipients
* Has donated or lost ≥1 unit (\~300 mL) of blood within 8 weeks prior to first dose of gefapixant
* Requires certain medications and/or other therapies that may impact their cough or bladder function
* Has previously received gefapixant
* Is currently participating or has participated in an interventional clinical study within 30 days of participating in this current study
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Merck Sharp & Dohme LLC

Locations

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City Polyclinic N20 ( Site 2806)

Odesa, Odesa Oblast, Ukraine

Site Status

SE O.S.Kolomiychenko Institute of Otolaryngology of NAMS of Ukraine ( Site 2817)

Kyiv, Kyivska Oblast, Ukraine

Site Status

Odesa regional clinical hospital ( Site 2804)

Odesa, Odesa Oblast, Ukraine

Site Status

Center for Clinical Trials, LLC ( Site 0021)

Paramount, California, United States

Site Status

Health Awareness, Inc. ( Site 0038)

Jupiter, Florida, United States

Site Status

Well Pharma Medical Research, Corp. ( Site 0040)

Miami, Florida, United States

Site Status

Lenus Research & Medical Group Llc ( Site 0007)

Sweetwater, Florida, United States

Site Status

Florida Pulmonary Research Institute, LLC ( Site 0008)

Winter Park, Florida, United States

Site Status

Paul A. Shapero, MD ( Site 0037)

Bangor, Maine, United States

Site Status

Chesapeake Clinical Research, Inc ( Site 0022)

White Marsh, Maryland, United States

Site Status

University of Missouri ENT & Allergy Center ( Site 0010)

Columbia, Missouri, United States

Site Status

Alliance for Multispecialty Research, LLC ( Site 0035)

Las Vegas, Nevada, United States

Site Status

Albuquerque Clinical Trials ( Site 0019)

Albuquerque, New Mexico, United States

Site Status

American Health Research ( Site 0027)

Charlotte, North Carolina, United States

Site Status

Clinical Research of Gastonia ( Site 0016)

Gastonia, North Carolina, United States

Site Status

PMG Research of Wilmington ( Site 0004)

Wilmington, North Carolina, United States

Site Status

Temple University ( Site 0003)

Philadelphia, Pennsylvania, United States

Site Status

AAPRI Clinical Research Institute ( Site 0031)

Warwick, Rhode Island, United States

Site Status

Diagnostics Research Group ( Site 0013)

San Antonio, Texas, United States

Site Status

TPMG Clinical Research ( Site 0025)

Newport News, Virginia, United States

Site Status

Tidewater Physician Multispecialty Group, PC ( Site 0028)

Williamsburg, Virginia, United States

Site Status

Bellingham Asthma & Allergy ( Site 0006)

Bellingham, Washington, United States

Site Status

Centro Medico Dra De Salvo ( Site 0300)

Buenos Aires, , Argentina

Site Status

Investigaciones en Patologias Respiratorias ( Site 0302)

San Miguel de Tucumán, , Argentina

Site Status

Fundacion Centro de Investigacion Clinica CIC ( Site 0401)

Medellín, Antioquia, Colombia

Site Status

Universidad Pontificia Bolivariana - Clinica Universitaria Bolivariana ( Site 0408)

Medellín, Antioquia, Colombia

Site Status

Medplus Medicina Prepagada ( Site 0402)

Bogotá, Bogota D.C., Colombia

Site Status

Healthy Medical Center S.A.S ( Site 0404)

Zipaquirá, Cundinamarca, Colombia

Site Status

Praxis Dr. Wehgartner-Winkler ( Site 0906)

Augsburg, Bavaria, Germany

Site Status

Zentrum fuer ambulante pneumologische Forschung Marburg GbR ( Site 0900)

Marburg, Hesse, Germany

Site Status

Ballenberger Freytag Wenisch Institut fuer klinische Forschung GmbH ( Site 0905)

Neu-Isenburg, Hesse, Germany

Site Status

Pneumologicum im Suedstadtforum ( Site 0908)

Hanover, Lower Saxony, Germany

Site Status

Praxis an der Oper ( Site 0912)

Berlin, , Germany

Site Status

Bethel Soluciones Medicas S.A. ( Site 0506)

Guatemala City, , Guatemala

Site Status

Centro de Investigaciones Clinicas de Latinoamerica S.A. - CELAN ( Site 0500)

Guatemala City, , Guatemala

Site Status

Clinica Medica Especializada en Neumologia y Tisiologia ( Site 0504)

Guatemala City, , Guatemala

Site Status

Clinica Medica Especializada en Neumologia ( Site 0502)

Guatemala City, , Guatemala

Site Status

Private Clinic ( Site 0505)

Guatemala City, , Guatemala

Site Status

Clinica Privada Dr. Jose Francisco Flores Lopez ( Site 0503)

Guatemala City, , Guatemala

Site Status

Carmel Medical Center ( Site 1104)

Haifa, , Israel

Site Status

Shaare Zedek Medical Center ( Site 1107)

Jerusalem, , Israel

Site Status

Hadassah Ein Karem Jerusalem ( Site 1108)

Jerusalem, , Israel

Site Status

Rabin Medical Center ( Site 1102)

Petah Tikva, , Israel

Site Status

Chaim Sheba Medical Center ( Site 1101)

Ramat Gan, , Israel

Site Status

Kaplan Medical Center ( Site 1103)

Rehovot, , Israel

Site Status

Sourasky Medical Center ( Site 1100)

Tel Aviv, , Israel

Site Status

Clinica Ricardo Palma ( Site 0601)

San Isidro, Lima region, Peru

Site Status

Asociacion Civil por la Salud ( Site 0602)

Lima, , Peru

Site Status

Hospital Nacional Arzobispo Loayza ( Site 0607)

Lima, , Peru

Site Status

Clinica Belen ( Site 0604)

Piura, , Peru

Site Status

RSBHI Belgorod regional clinical hospital of Prelate Ioasafa ( Site 1416)

Belgorod, Belgorod Oblast, Russia

Site Status

GBUZ Regional Clinical Hospital 3 ( Site 1420)

Chelyabinsk, Chelyabinsk Oblast, Russia

Site Status

City Clinical Hospital No. 3 them. M. A. Podgorbunskogo ( Site 1400)

Kemerovo, Kemerovo Oblast, Russia

Site Status

Open Joint Stock Company Clinical and Diagnostic Center Euromedservice ( Site 1466)

Moscow, Moscow, Russia

Site Status

Krasnogorsk City Hospital Number 1 ( Site 1470)

Krasnogorsk, Moscow Oblast, Russia

Site Status

City Clinical Hospital of Emergency Care #2 ( Site 1448)

Novosibirsk, Novosibirsk Oblast, Russia

Site Status

Clinic of FSBEI HE OmSMU of Minzdrav ( Site 1438)

Omsk, Omsk Oblast, Russia

Site Status

Perm Clinical Center of the Federal Medical and Biological Agency ( Site 1450)

Perm, Permskiy Kray, Russia

Site Status

Medi Kom ( Site 1456)

Saint Petersburg, Sankt-Peterburg, Russia

Site Status

Limited Liability Company Kurator ( Site 1424)

Saint Petersburg, Sankt-Peterburg, Russia

Site Status

SEIHPE Saint Petersburg SMU ( Site 1434)

Saint Petersburg, Sankt-Peterburg, Russia

Site Status

Saratov City Clinical Hospital 2 n.a. V.I. Razumovsky ( Site 1452)

Saratov, Saratov Oblast, Russia

Site Status

Family Clinic ( Site 1464)

Yekaterinburg, Sverdlovsk Oblast, Russia

Site Status

State health Agency Ulyanovsk regional clinical hospital ( Site 1414)

Ulyanovsk, Ulyanovsk Oblast, Russia

Site Status

Voronezh Regional Clinical Hospital #1 ( Site 1440)

Voronezh, Voronezskaja Oblast, Russia

Site Status

SBCIH of the Yaroslavl region Central city hospital ( Site 1428)

Yaroslavl, Yaroslavl Oblast, Russia

Site Status

Jeonbuk National University Hospital ( Site 1507)

Jeonju, Jeonrabugdo, South Korea

Site Status

Wonju Severance Christian Hospital ( Site 1502)

Wŏnju, Kang-won-do, South Korea

Site Status

The Catholic University of Korea Eunpyeong St Mary s Hospital ( Site 1506)

Seoul, , South Korea

Site Status

Konkuk University Medical Center ( Site 1504)

Seoul, , South Korea

Site Status

Asan Medical Center ( Site 1505)

Seoul, , South Korea

Site Status

Hospital Parc Tauli ( Site 1806)

Sabadell, Barcelona, Spain

Site Status

Hospital Clinic i Provincial de Barcelona ( Site 1804)

Barcelona, Catalonia, Spain

Site Status

Hospital Clinico Universitario de Santiago ( Site 1805)

Santiago de Compostela, La Coruna, Spain

Site Status

Hospital General Universitario Gregorio Maranon ( Site 1808)

Madrid, Madrid, Comunidad de, Spain

Site Status

F.G.Yanovskyy Institute of Phthisiology and Pulmonology ( Site 2808)

Kyiv, Kyivska Oblast, Ukraine

Site Status

F.G.Yanovskyy Institute of Phthisiology and Pulmonology ( Site 2819)

Kyiv, Kyivska Oblast, Ukraine

Site Status

SE Road Clinical Hospital 2 of Kyiv station ( Site 2812)

Kyiv, Kyivska Oblast, Ukraine

Site Status

Municipal enterprise "1st City clinical hospital of Poltava -Internal medicine department ( Site 281

Poltava, Poltava Oblast, Ukraine

Site Status

Private Small-Scale Enterprise Medical Centre "Pulse" ( Site 2809)

Vinnytsia, Vinnytsia Oblast, Ukraine

Site Status

Volyn Regional Clinical Hospital ( Site 2816)

Lutsk, Volyn Oblast, Ukraine

Site Status

Medical Center of LLC Medical Clinic Blahomed ( Site 2815)

Kyiv, , Ukraine

Site Status

GP Direct ( Site 2714)

Harrow, England, United Kingdom

Site Status

West Walk Surgery ( Site 2700)

Yate, Gloucestershire, United Kingdom

Site Status

Medinova Lakeside Dedicated Research Centre ( Site 2712)

Corby, Northamptonshire, United Kingdom

Site Status

Kings College Hospital NHS Foundation Trust ( Site 2702)

London, Southwark, United Kingdom

Site Status

Accellacare South London Quality Research Centre ( Site 2706)

Orpington, Surrey, United Kingdom

Site Status

Wokingham Medical Centre ( Site 2708)

Wokingham, West Berkshire, United Kingdom

Site Status

Medinova North London Dedicated Research Centre ( Site 2705)

Northwood, Worcestershire, United Kingdom

Site Status

Medinova Warwickshire Dedicated Research Centre ( Site 2715)

Coventry, , United Kingdom

Site Status

Countries

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United States Argentina Colombia Germany Guatemala Israel Peru Russia South Korea Spain Ukraine United Kingdom

References

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Birring SS, Cardozo L, Dmochowski R, Dicpinigaitis P, Afzal A, La Rosa C, Lu S, Nguyen AM, Yao R, Reyfman PA. Efficacy and safety of gefapixant in women with chronic cough and cough-induced stress urinary incontinence: a phase 3b, randomised, multicentre, double-blind, placebo-controlled trial. Lancet Respir Med. 2024 Nov;12(11):855-864. doi: 10.1016/S2213-2600(24)00222-4. Epub 2024 Aug 30.

Reference Type RESULT
PMID: 39222649 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Related Links

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https://www.merckclinicaltrials.com

Merck Clinical Trials Information

Other Identifiers

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MK-7264-042

Identifier Type: OTHER

Identifier Source: secondary_id

2019-002321-29

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

7264-042

Identifier Type: -

Identifier Source: org_study_id

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