Safety and Efficacy Study of NBI-98854 in Children and Adolescents With Tourette Syndrome

NCT ID: NCT02679079

Last Updated: 2021-01-15

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

98 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-03-23

Study Completion Date

2017-04-14

Brief Summary

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Phase 2, double-blind, placebo-controlled study to assess the safety and efficacy of NBI-98854 administered once daily (qd) for a total of 6 weeks of treatment. This study will enroll approximately 90 male and female pediatric subjects clinically diagnosed with Tourette Syndrome.

Detailed Description

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Conditions

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Tourette Syndrome

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Administered once daily for 6 weeks

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Dose Group 1

Administered once daily for 6 weeks

Group Type EXPERIMENTAL

NBI-98854

Intervention Type DRUG

Dose Group 2

Administered once daily for 6 weeks

Group Type EXPERIMENTAL

NBI-98854

Intervention Type DRUG

Interventions

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NBI-98854

Intervention Type DRUG

Placebo

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Have a clinical diagnosis of Tourette Syndrome (TS)
2. Have at least moderate tic severity
3. Have TS symptoms that impair school, occupational, and/or social function
4. If using maintenance medication(s) for TS or TS spectrum diagnoses (e.g. obsessive-compulsive disorder \[OCD\], Attention-Deficit Hyperactivity Disorder \[ADHD\]), be on stable doses
5. Be in good general health
6. Adolescent subjects (12 to 17 years of age) must have a negative urine drug screen for amphetamines, barbiturates, benzodiazepine, phencyclidine, cocaine, opiates, or cannabinoids and a negative alcohol screen
7. Subjects of childbearing potential who do not practice total abstinence must agree to use hormonal or two forms of nonhormonal contraception (dual contraception) consistently during the screening, treatment and follow-up periods of the study

Exclusion Criteria

1. Have an active, clinically significant unstable medical condition within 1 month prior to screening
2. Have a known history of long QT syndrome or cardiac arrhythmia
3. Have a known history of neuroleptic malignant syndrome
4. Have a cancer diagnosis within 3 years prior to screening (some exceptions allowed)
5. Have an allergy, hypersensitivity, or intolerance to VMAT2 inhibitors
6. Have a blood loss ≥250 mL or donated blood within 30 days prior to screening
7. Have a known history of substance dependence, substance (drug) or alcohol abuse
8. Have a significant risk of suicidal or violent behavior
9. Have initiated Comprehensive Behavioral Intervention for Tics (CBIT) during the screening period or at baseline or plan to initiate CBIT during the study
10. Have received an investigational drug within 30 days before screening or plan to use an investigational drug (other than NBI-98854) during the study
Minimum Eligible Age

6 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Neurocrine Biosciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Sun City, Arizona, United States

Site Status

Springdale, Arkansas, United States

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Long Beach, California, United States

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San Bernardino, California, United States

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San Diego, California, United States

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Upland, California, United States

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Bradenton, Florida, United States

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Gainesville, Florida, United States

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Hialeah, Florida, United States

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Loxahatchee Groves, Florida, United States

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Melbourne, Florida, United States

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Orlando, Florida, United States

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St. Petersburg, Florida, United States

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Tampa, Florida, United States

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Atlanta, Georgia, United States

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Chicago, Illinois, United States

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Naperville, Illinois, United States

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Wichita, Kansas, United States

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Boston, Massachusetts, United States

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Natick, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Bloomfield Hills, Michigan, United States

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Lincoln, Nebraska, United States

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Nashua, New Hampshire, United States

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Marlton, New Jersey, United States

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Summit, New Jersey, United States

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Manhasset, New York, United States

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New York, New York, United States

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Rochester, New York, United States

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Cincinnati, Ohio, United States

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Middleburg Heights, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Franklin, Tennessee, United States

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Nashville, Tennessee, United States

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Dallas, Texas, United States

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DeSoto, Texas, United States

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Fort Worth, Texas, United States

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Houston, Texas, United States

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Irving, Texas, United States

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Orem, Utah, United States

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Salt Lake City, Utah, United States

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Kirkland, Washington, United States

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Seattle, Washington, United States

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Spokane, Washington, United States

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Countries

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United States

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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NBI-98854-1501

Identifier Type: -

Identifier Source: org_study_id

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