Feasibility of Allogeneic Stem Cell Transplantation in Higher-risk-MDS (ACROBAT)

NCT ID: NCT04184505

Last Updated: 2025-04-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

274 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-11-27

Study Completion Date

2026-03-01

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

Open-label, randomized multicenter phase III non-inferiority study

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Open-label, randomized, prospective multicenter phase III study to compare the role of HMT followed by HSCT vs HSCT upfront in HR-MDS with \<10% of BM blasts and of CHT vs HMT followed by HSCT in HR-MDS with \>10% BM blasts in terms of feasibility of HSCT (non-inferiority trial).

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

High-risk MDS

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Standard clinical treatment

If BM-blasts \>= 10%: Conventional chemotherapy: induction one cycle (3+7 protocol) and one optional consolidation cycle, followed by HSCT if a suitable sibling or unrelated donor is available versus

If BM blasts are \<10%: HSCT upfront

Group Type ACTIVE_COMPARATOR

Standard Chemotherapy

Intervention Type DRUG

1. cycle (induction): i.v. 3+7 (Citarabine 200 mg/m2 iv continuous infusion (24 h) for 7 days, Daunorubicine 60 mg/mq iv day 1-3)
2. cycle (consolidation): i.v. 3+7 (Citarabine 200 mg/m2 iv continuous infusion (24 h) for 7 days, Daunorubicine 45 mg/mq iv day 1-3)

Allogeneic stem cell transplantation

Intervention Type PROCEDURE

Allogeneic stem cell transplantation

Experimental treatment

If BM-blasts \>= 10%: Azacitidine (AZA) 75mg/sqm/day subcutaneously for 7 days every 28 days (1 cycle of 28 days) for at least 4 cycles, followed by HSCT if a suitable sibling or unrelated donor is available

If BM blasts are \<10%: Azacitidine (AZA) 75mg/sqm/day subcutaneously for 7 days every 28 days (1 cycle of 28 days) for at least 4 cycles, followed by HSCT if a suitable sibling or unrelated donor is available

Group Type EXPERIMENTAL

Azacitidine

Intervention Type DRUG

75mg/mq/day subcutaneously for 7 days every 28 days

Allogeneic stem cell transplantation

Intervention Type PROCEDURE

Allogeneic stem cell transplantation

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Azacitidine

75mg/mq/day subcutaneously for 7 days every 28 days

Intervention Type DRUG

Standard Chemotherapy

1. cycle (induction): i.v. 3+7 (Citarabine 200 mg/m2 iv continuous infusion (24 h) for 7 days, Daunorubicine 60 mg/mq iv day 1-3)
2. cycle (consolidation): i.v. 3+7 (Citarabine 200 mg/m2 iv continuous infusion (24 h) for 7 days, Daunorubicine 45 mg/mq iv day 1-3)

Intervention Type DRUG

Allogeneic stem cell transplantation

Allogeneic stem cell transplantation

Intervention Type PROCEDURE

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

AZA STD CHT HSCT

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Patients with newly diagnosed higher-risk MDS, including IPSS Intermediate-2 and high, and IPSS-R intermediate to very-high
2. Age 18-70 years
3. Previously untreated for HR-MDS
4. HSCT - eligible
5. Life expectancy ≥3 months;
6. Signed written informed consent according to ICH/EU/GCP and national local laws
7. Eastern Cooperative Oncology Group Performance Status Grade of 0-2

Exclusion Criteria

1. Acute myeloid leukaemia with \>20% blasts in BM or peripheral blood (PB);
2. concurrent malignancy diagnosed in the past 12 months (with the exception of skin basalioma);
3. severe renal, cardiac, liver or lung impairment;
4. pregnant or lactating or potentially fertile (both males and females), who have not agreed to avoid pregnancy during the trial period; Women of childbearing potential and men must agree to use effective contraception during and up to 3 months after treatment with azacitidine.
5. HIV infection; active, uncontrolled HCV or HBV infections or liver cirrhosis;
6. clinically relevant neurological or psychiatric diseases;
7. hypersensitivity (known or suspected) to AZA;
8. prior Treatments:

1. prior investigational drugs (within 30 days);
2. radiotherapy, chemotherapy, or cytotoxic therapy for non-MDS conditions within the previous 6 months;
3. growth factors (EPO, G-CSF or GM-CSF) during the previous 21 days;
4. androgenic hormones during the previous 14 days;
5. prior transplantation or cytotoxic therapy, including azacitidine, AZA or chemotherapy, administered to treat MDS (a previous treatment with Lenalidomide is admitted, provided that lenalidomide had been stopped at least 60 days before enrolment).
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Gruppo Italiano Malattie EMatologiche dell'Adulto

OTHER

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Voso

Role: PRINCIPAL_INVESTIGATOR

AOU POLICLINICO TOR VERGATA - ROMA - UOC TRAPIANTO CELLULE STAMINALI

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

058 - Aon Ss. Antonio E Biagio E C. Arrigo - Soc Ematologia

Alessandria, , Italy

Site Status RECRUITING

Aou Ospedali Riuniti "Umberto I - G.M. Lancisi - G. Salesi - Sod Clinica Ematologica

Ancona, , Italy

Site Status RECRUITING

Presidio Ospedaliero Av5 Osp. Gen. Prov.Le "C.G.Mazzoni" - Uoc Ematologia

Ascoli Piceno, , Italy

Site Status RECRUITING

Aou Consorziale Policlinico - Bari - Uo Ematologia Con Trapianto

Bari, , Italy

Site Status RECRUITING

Aou Di Bologna - Policlinico S. Orsola-Malpighi - Uoc Ematologia

Bologna, , Italy

Site Status RECRUITING

Asst Degli Spedali Civili Di Brescia - Uo Ematologia

Brescia, , Italy

Site Status RECRUITING

Asl Brindisi, Ospedale 'Perrino'- Uo Ematologia

Brindisi, , Italy

Site Status RECRUITING

U.O.C. Oncoematologia - Istituto Oncologico Veneto Irccs - Presidio Ospedaliero S. Giacomo Apostolo

Castelfranco Veneto, , Italy

Site Status RECRUITING

Aou Policlinico Vittorio Emanuele, Po Ospedaliero "G. Rodolico" - Uo Ematologia Con Trapianto Di Midollo Osseo

Catania, , Italy

Site Status RECRUITING

Aou Arcispedale Sant'Anna - Cona (Fe) - Uoc Ematologia E Fisiopatologia Della Coagulazione

Cona, , Italy

Site Status RECRUITING

Aso S. Croce E Carle - Sc Ematologia

Cuneo, , Italy

Site Status RECRUITING

Aou Ospedali Riuniti- Uoc Ematologia

Foggia, , Italy

Site Status RECRUITING

Asl Latina, Presidio Ospedaliero Nord - Ospedale Santa Maria Goretti - Uoc Ematologia

Latina, , Italy

Site Status RECRUITING

Asl Lecce, Ospedale 'V. Fazzi' - Uo Ematologia

Lecce, , Italy

Site Status RECRUITING

Aulss 3 Serenissima, Ospedale Dell'Angelo Uo Ematologia

Mestre, , Italy

Site Status RECRUITING

Asst Grande Ospedale Metropolitano Niguarda - Milano - Sc Ematologia

Milan, , Italy

Site Status RECRUITING

Irccs Ospedale S. Raffaele - Milano - Uo Oncoematologia

Milan, , Italy

Site Status RECRUITING

Aou Di Modena - Sc Ematologia

Modena, , Italy

Site Status RECRUITING

Ao Di Rilievo Nazionale Antonio Cardarelli - Napoli - Uoc Ematologia Con Trapianto Di Midollo

Napoli, , Italy

Site Status RECRUITING

Aou San Luigi Gonzaga - Orbassano - Scdu Ematologia Generale E Oncoematologia

Orbassano, , Italy

Site Status RECRUITING

Asl Salerno, Presidio Ospedaliero Tortora Pagani - Ematologia

Pagani, , Italy

Site Status RECRUITING

Aou Policlinico P. Giaccone - Uo Ematologia

Palermo, , Italy

Site Status RECRUITING

Asl Pescara, Presidio Ospedaliero 'Spirito Santo' - Uoc Ematologia Clinica

Pescara, , Italy

Site Status RECRUITING

Asl Di Piacenza, Ospedale "Guglielmo Da Saliceto" - Ematologia E Centro Trapianti

Piacenza, , Italy

Site Status RECRUITING

Aou Pisana - Uo Ematologia Universitaria

Pisa, , Italy

Site Status RECRUITING

Grande Ospedale Metropolitano "Bianchi-Melacrino-Morelli" Po E. Morelli - Reggio Calabria - Uoc Ematologia

Reggio Calabria, , Italy

Site Status RECRUITING

Arcispedale Santa Maria Nuova, Irccs - Sc Ematologia

Reggio Emilia, , Italy

Site Status RECRUITING

Ausl Della Romagna, Ospedale "Infermi" - Uo Ematologia

Rimini, , Italy

Site Status RECRUITING

Ao Complesso Ospedaliero San Giovanni / Addolorata - Roma - Uoc Ematologia

Roma, , Italy

Site Status RECRUITING

Ao San Camillo Forlanini Uoc Ematologia E Trapianto Cellule Staminali

Roma, , Italy

Site Status RECRUITING

Aou Policlinico Tor Vergata - Roma - Uoc Trapianto Cellule Staminali

Roma, , Italy

Site Status RECRUITING

Aou Sant'Andrea - Roma - Uoc Ematologia

Roma, , Italy

Site Status RECRUITING

Asl Roma 2, Ospedale S. Eugenio- Uoc Ematologia

Roma, , Italy

Site Status RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli Irccs - Roma - Area Ematologica

Roma, , Italy

Site Status RECRUITING

Istituti Fisioterapici Ospitalieri - Ifo - Istituto Regina Elena - Roma - Uosd Ematologia

Roma, , Italy

Site Status RECRUITING

Policlinico Universitario Campus Bio Medico - Roma - Uoc Ematologia E Trapianto Di Cellule Staminali

Roma, , Italy

Site Status RECRUITING

Università Degli Studi Di Roma "Sapienza" - Dipartimento Di Medicina Traslazionale E Di Precisione - U.O.C. Ematologia

Roma, , Italy

Site Status RECRUITING

Aou "San Giovanni Di Sio E Ruggi D'Aragona" - Uoc Ematologia E Trapianti Di Cellule Staminali Emopoietiche

Salerno, , Italy

Site Status RECRUITING

Aou Di Sassari - Cliniche Universitarie - Stabilimento Cliniche Di San Pietro - Uoc Ematologia

Sassari, , Italy

Site Status RECRUITING

Aou Senese - Uoc Ematologia E Trapianti

Siena, , Italy

Site Status RECRUITING

Aou Citta' Della Salute E Della Scienza - Osp. S. Giovanni Battista Molinette - Sc Ematologia 2

Torino, , Italy

Site Status RECRUITING

Aou Città Della Salute E Della Scienza, Ospedale S. Giovanni Battista Molinette - Torino - Sc Ematologia - Università Degli Studi Di Torino

Torino, , Italy

Site Status RECRUITING

ENTE ECCLESIASTICO CARDINALE G. PANICo - UO EMATOLOGIA

Tricase, , Italy

Site Status RECRUITING

Asui Di Udine - Presidio Ospedaliero "Santa Maria Della Misericordia" - Clinica Ematologica

Udine, , Italy

Site Status RECRUITING

Aou Integrata Di Verona, Policlinico G.B. Rossi - Uoc Ematologia

Verona, , Italy

Site Status RECRUITING

Asl Di Viterbo, Complesso Ospedaliero Di Belcolle - Uoc Ematologia

Viterbo, , Italy

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

Italy

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Paola Fazi

Role: CONTACT

0670390528

Enrico Crea

Role: CONTACT

0670390514

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Zallio

Role: primary

Poloni

Role: primary

0715964736

Galieni

Role: primary

0736358128

Paola Carluccio

Role: primary

3383401921

Carlo Finelli

Role: primary

3355444425

Erika Borlenghi

Role: primary

3402526539

Pastore

Role: primary

3393061521

Gottardi

Role: primary

3476260749

Milone

Role: primary

Cuneo

Role: primary

0532236977

Mordini

Role: primary

Melillo

Role: primary

0881736444

Giuseppe Cimino

Role: primary

3495378159

Di Renzo

Role: primary

0832661922

Sancetta

Role: primary

Roberto S Cairoli

Role: primary

3478939057

Fabio Ciceri

Role: primary

0226437503

Mario Luppi

Role: primary

0594224641

Alessandra Picardi

Role: primary

081 7472260

Daniela Cilloni

Role: primary

3332818086

Califano

Role: primary

0819213366

Siragusa

Role: primary

Santarone

Role: primary

Vallisa

Role: primary

0523303701

Petrini

Role: primary

050 993488

Ester Olivia

Role: primary

3297978204

Capodanno

Role: primary

Tomassetti

Role: primary

Laura Cudillo

Role: primary

3398320774

Santopietro

Role: primary

0658703485

Maria Teresa Voso

Role: primary

3494743547

Agostino Tafuri

Role: primary

3392145880

De Fabritiis

Role: primary

0651005740

Luana Fianchi

Role: primary

3479378107

Gumenyuk Svitlana

Role: primary

Giuseppe Avvisati

Role: primary

3281595114

Breccia

Role: primary

06 49974440

Selleri

Role: primary

089 673152

Claudio Fozza

Role: primary

3397560639

Bocchia

Role: primary

0577586740

Frairia

Role: primary

Benedetto Bruno

Role: primary

Pavone

Role: primary

0833773450

Tiribelli

Role: primary

0432559701

Tanasi

Role: primary

Di Veroli

Role: primary

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

MDS0519

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

A Trial of AK117 (Anti-CD47) in Patients With Myelodysplastic Syndrome
NCT04900350 ACTIVE_NOT_RECRUITING PHASE1/PHASE2
Omacetaxine + Azacitidine in Untreated Patients With High Grade MDS
NCT03564873 ACTIVE_NOT_RECRUITING PHASE1/PHASE2