Extension Study to Assess Effects of Non-interrupted Versus Interrupted and Long Term Treatment of Two Dose Regimes of Secukinumab in Subjects With Hidradenitis Suppurativa

NCT ID: NCT04179175

Last Updated: 2025-11-03

Study Results

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Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

703 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-03-18

Study Completion Date

2026-07-15

Brief Summary

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The purpose of this extension study is to evaluate maintenance of Hidradenitis Suppurativa Clinical Response (HiSCR response) in either continuous or interrupted therapy (using a randomized withdrawal period) of two dose regimens and to assess long-term efficacy, safety and tolerability of Secukinumab in subjects with moderate to severe hidradenitis suppurativa completing either of the 2 Phase III studies. This is an expanded access trial for the core trials CAIN457M2301 (NCT03713619) and CAIN457M2302 (NCT03713619).

Detailed Description

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This is a multicenter extension study to both core Phase III studies CAIN457M2301 and CAIN457M2302 (Core studies). This study contains a randomized withdrawal design, double blinded and placebo controlled up to Week 104 or loss of response. The subjects with HiSCR response after 52 weeks of treatment in the "Core studies" will be randomized at 2:1 ratio to either continue on one of the two Secukinumab dosing regimens assigned in "Core studies" for another 52 weeks or will be placed on placebo. The primary endpoint is loss of response (LOR) assessed during the 52-week treatment duration (up to Week 104). Subjects who attained LOR will be transferred to open-label treatment to continue until the end of the study. Subjects on placebo who did not reach LOR up to Week 104 will be offered to continue in the open-label treatment or discontinue the study. Thus for subjects who were HiSCR responders at Week 52 of "Core studies", the open label treatment duration will vary and start either from the time of LOR or from Week 104 dose and last until Week 260 followed by 8 weeks of a post treatment follow-up period to week 268.

Subjects who were HiSCR non-responders at the end of "Core studies" will be offered to continue in open-label treatment until Week 260.

Subjects who prematurely discontinue the study, or who complete the study will enter a post-treatment follow up period (8 weeks) The primary objective is to evaluate maintenance of HiSCR response at Week 104 in either continuous or interrupted therapy compared to placebo. Secondary objectives are to assess the long-term safety and tolerability evaluated by adverse events, abnormal laboratory values and vital signs.

Conditions

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Hidradenitis Suppurativa

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Multicenter, double-blind, randomized withdrawal extension, parallel group study followed by an open-label, active-treatment period with two Secukinumab dose regimens in approximately 856 patients with moderate to severe hidradenitis suppurativa (HS)
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators
Patients considered HiSCR responders will be randomized 2:1 to continue their current regimen or undergo withdrawal to placebo. HiScr non-responders will enter open label therapy with Secukinumab if desired

Study Groups

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secukinumab 1 HiSCR Responder

HiSCR responder at Week 52 in core trial, secukinumab 300mg every 2 weeks

Group Type ACTIVE_COMPARATOR

secukinumab

Intervention Type DRUG

secukinumab 300mg every 2 weeks

secukinumab 2 HiSCR Responder

HiSCR responder at Week 52 in core trial, secukinumab 300mg every 4 weeks

Group Type ACTIVE_COMPARATOR

secukinumab

Intervention Type DRUG

secukinumab 300mg every 4 weeks

placebo 1 HiSCR Responder

HiSCR responder at Week 52 in core trial, placebo to secukinumab 300mg every 2 weeks

Group Type PLACEBO_COMPARATOR

secukinumab

Intervention Type DRUG

secukinumab 300mg every 2 weeks

placebo 2 HiSCR Responder

HiSCR responder at Week 52 in core trial, placebo to secukinumab 300 mg every 4 weeks

Group Type PLACEBO_COMPARATOR

secukinumab

Intervention Type DRUG

secukinumab 300mg every 4 weeks

HiSCR non-responders

non-responder at Week 52 in core trial treatment; secukinumab 300mg every 2 weeks

Group Type OTHER

secukinumab

Intervention Type DRUG

secukinumab 300mg every 2 weeks

Interventions

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secukinumab

secukinumab 300mg every 2 weeks

Intervention Type DRUG

secukinumab

secukinumab 300mg every 4 weeks

Intervention Type DRUG

Other Intervention Names

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AIN457 AIN457

Eligibility Criteria

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Inclusion Criteria

* written informed consent must be obtained before any assessment is performed
* subject must have completed the study treatment period (52 weeks) in the core studies (AIN457M2301 or AIN457M2302) and had received secukinumab treatment during Treatment Period 2

Exclusion Criteria

* protocol deviation in the core study which will prevent the meaningful analysis of the extension study
* ongoing or planned use of prohibited HS or non-HS treatment
* participation in the extension could expose the subject to an undue safety risk
* current sever progressive or uncontrolled disease which renders the subject unsuitable for the study
Minimum Eligible Age

18 Years

Maximum Eligible Age

100 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Novartis Investigative Site

Peterborough, Ontario, Canada

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Waterloo, Ontario, Canada

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Barranquilla, Atlántico, Colombia

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Zagreb, HRV, Croatia

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Prague, Prague 1, Czechia

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Jihlava, , Czechia

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Plzen Bory, , Czechia

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Ústí nad Labem, , Czechia

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Limoges, Haute Vienne, France

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Toulon, Val De Marne, France

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Antony, , France

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Bordeaux, , France

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Brest, , France

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Créteil, , France

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Lyon, , France

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Martigues, , France

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Montpellier, , France

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Nantes, , France

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Langenau, Baden-Wurttemberg, Germany

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Munich, Bavaria, Germany

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Würzburg, Bavaria, Germany

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Halle, Saxony-Anhalt, Germany

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Berlin, , Germany

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Berlin, , Germany

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Bielefeld, , Germany

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Bochum, , Germany

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Erlangen, , Germany

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Frankfurt, , Germany

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Hamburg, , Germany

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Heidelberg, , Germany

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Memmingen, , Germany

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München, , Germany

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Münster, , Germany

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Potsdam, , Germany

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Jerusalem, , Israel

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Petah Tikva, , Israel

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Ramat Gan, , Israel

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Tel Aviv, , Israel

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Ancona, AN, Italy

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Cona, FE, Italy

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Florence, FI, Italy

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Milan, MI, Italy

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Pisa, PI, Italy

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Roma, RM, Italy

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Lausanne, , Switzerland

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Taipei, , Taiwan

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Taoyuan District, , Taiwan

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Aydin, Efeler, Turkey (Türkiye)

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Istanbul, Fatih, Turkey (Türkiye)

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Antalya, Konyaalti, Turkey (Türkiye)

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Kayseri, Melikgazi, Turkey (Türkiye)

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Istanbul, Pendik, Turkey (Türkiye)

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Gaziantep, Sehitkamil, Turkey (Türkiye)

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Exeter, Devon, United Kingdom

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Dudley, West Midlands, United Kingdom

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Bradford, West Yorkshire, United Kingdom

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Leeds, West Yorkshire, United Kingdom

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Barnsley, , United Kingdom

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Bristol, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Salford, , United Kingdom

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Northwest Arkansas Center

Rogers, Arkansas, United States

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MedDerm Associates

San Diego, California, United States

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University Clinical Trials

San Diego, California, United States

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Southern California Skin and Laser

Whittier, California, United States

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Florida Academic Centers Research and Education LLC

Coral Gables, Florida, United States

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University of MiamiHealth System

Miami, Florida, United States

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Olympian Clinical Research

Tampa, Florida, United States

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University Of South Florida

Tampa, Florida, United States

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Advanced Medical Research

Sandy Springs, Georgia, United States

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Endeavor Health

Glenview, Illinois, United States

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Dundee Dermatology

West Dundee, Illinois, United States

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Dawes Fretzin Clinical Rea Group

Indianapolis, Indiana, United States

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Tufts Medical Center

Boston, Massachusetts, United States

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Beth Israel Deaconess Med Center

Boston, Massachusetts, United States

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Minnesota Clinical Study Center

New Brighton, Minnesota, United States

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MediSearch Clinical Trials

Saint Joseph, Missouri, United States

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St Louis U Clinical Trials

St Louis, Missouri, United States

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WA Uni School Of Med

St Louis, Missouri, United States

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Skin Specialists PC

Omaha, Nebraska, United States

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Icahn School Of Med At Mount Sinai

New York, New York, United States

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University of North Carolina

Chapel Hill, North Carolina, United States

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Wright State University

Fairborn, Ohio, United States

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UP Medical Center H System

Pittsburgh, Pennsylvania, United States

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Clinical Research Ctr of Carolinas

Charleston, South Carolina, United States

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Bellaire Dermatology Associates

Bellaire, Texas, United States

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MDRI Baylor University

Dallas, Texas, United States

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Austin Inst for Clinical Research

Pflugerville, Texas, United States

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Dr. Stephen Miller, MDPA

San Antonio, Texas, United States

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Virginia Clinical Research

Norfolk, Virginia, United States

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Novartis Investigative Site

CABA, Buenos Aires, Argentina

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La Plata, Buenos Aires, Argentina

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Rosario, Santa Fe Province, Argentina

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Buenos Aires, , Argentina

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Caba, , Argentina

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Capital Federal, , Argentina

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Phillip, Australian Capital Territory, Australia

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Benowa, Queensland, Australia

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East Melbourne, Victoria, Australia

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Linz, , Austria

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Vienna, , Austria

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Brussels, , Belgium

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Ghent, , Belgium

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Liège, , Belgium

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Pleven, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Stara Zagora, , Bulgaria

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Barrie, Ontario, Canada

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London, Ontario, Canada

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Nice, , France

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Paris, , France

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Reims, , France

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Rouen, , France

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Saint-Mandé, , France

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Saint-Priest-en-Jarez, , France

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Toulouse, , France

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Schwerin, , Germany

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Athens, , Greece

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Chaïdári, , Greece

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Thessaloniki, , Greece

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Thessaloniki, , Greece

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Guatemala City, , Guatemala

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Guatemala City, , Guatemala

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Debrecen, , Hungary

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Kaposvár, , Hungary

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Pécs, , Hungary

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Mysore, Karnataka, India

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Nagpur, Maharashtra, India

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Nashik, Maharashtra, India

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New Delhi, National Capital Territory of Delhi, India

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Napoli, , Italy

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Nagoya, Aichi-ken, Japan

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Kisarazu, Chiba, Japan

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Ginowan, Okinawa, Japan

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Koshigaya, Saitama, Japan

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Itabashi-ku, Tokyo, Japan

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Osaka, , Japan

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Saida, , Lebanon

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Kaunas, LTU, Lithuania

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Vilnius, , Lithuania

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Kuala Lumpur, Kuala Lumpur, Malaysia

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George Town, Pulau Pinang, Malaysia

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Johor Bahru, , Malaysia

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Guadalajara, Jalisco, Mexico

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Monterrey, Nuevo León, Mexico

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Amersfroort, Utrecht, Netherlands

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Las Piñas, , Philippines

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Makati City, , Philippines

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Warsaw, Mazowian, Poland

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Ossy, , Poland

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Rzeszów, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Lisbon, , Portugal

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Lisbon, , Portugal

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Porto, , Portugal

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Chelyabinsk, , Russia

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Kazan', , Russia

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Krasnodar, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Smolensk, , Russia

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Yaroslavl, , Russia

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Singapore, , Singapore

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Singapore, , Singapore

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Banská Bystrica, , Slovakia

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Košice, , Slovakia

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Prešov, , Slovakia

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Raslouw Centurion, Gauteng, South Africa

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Soweto, Gauteng, South Africa

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Seoul, Korea, South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Cadiz, Andalusia, Spain

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Granada, Andalusia, Spain

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Barcelona, Catalonia, Spain

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Fuenlabrada, Madrid, Spain

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Manises, Valencia, Spain

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Alicante, , Spain

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Barcelona, , Spain

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Las Palmas GC, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Pontevedra, , Spain

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Bern, , Switzerland

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Geneva, , Switzerland

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Hanoi, , Vietnam

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Ho Chi Minh City, , Vietnam

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Countries

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United States Argentina Australia Austria Belgium Bulgaria Canada Colombia Croatia Czechia France Germany Greece Guatemala Hungary India Israel Italy Japan Lebanon Lithuania Malaysia Mexico Netherlands Philippines Poland Portugal Russia Singapore Slovakia South Africa South Korea Spain Switzerland Taiwan Turkey (Türkiye) United Kingdom Vietnam

References

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Kimball AB, Bechara FG, Badat A, Giamarellos-Bourboulis EJ, Gottlieb AB, Jemec GBE, Reguiai Z, Villani AP, Alarcon I, Bansal A, Gasperoni F, Martin R, Paguet B, Uhlmann L, Zouater H, Ravichandran S, Alavi A. Long-term efficacy and safety of secukinumab in patients with moderate-to-severe hidradenitis suppurativa: week 104 results from the SUNSHINE and SUNRISE extension trial. Br J Dermatol. 2025 Mar 18;192(4):629-640. doi: 10.1093/bjd/ljae469.

Reference Type DERIVED
PMID: 39611771 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2023-508956-20

Identifier Type: REGISTRY

Identifier Source: secondary_id

CAIN457M2301E1

Identifier Type: -

Identifier Source: org_study_id

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