AML Patients Bearing FLT3 Mutations Based on Peripheral Blast Clearance

NCT ID: NCT04174612

Last Updated: 2022-03-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE3

Total Enrollment

172 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-04-24

Study Completion Date

2025-08-01

Brief Summary

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Prospective, multi-center, interventional, randomized, open clinical trial for the treatment of acute myeloid leukemia with FLT3 mutations customized upon the prognostic parameter PBC

Detailed Description

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Conditions

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Acute Myeloid Leukemia With FLT3/ITD Mutation

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Standard clinical treatment

Patients will complete "3+7" + Midostaurin induction course.

Group Type ACTIVE_COMPARATOR

Cytarabine

Intervention Type DRUG

100 mg/m2/bid day 1-3 100 mg/m2/die day 4-7

Daunorubicin

Intervention Type DRUG

60 mg/m2/die day 1-3

Midostaurin

Intervention Type DRUG

50 mg/bid day 8-21

Experimental treatment

The experimental arm will provide 2 main modifications compared to standard:

i) immediate switch to intensified induction with high-doses Cytarabine (on days 5, 6 and 7 of induction) ii) early allocation to high-risk disease category to be refined according to ELN stratification and post induction MRD status

Group Type EXPERIMENTAL

Daunorubicin

Intervention Type DRUG

60 mg/m2/die day 1-3

Midostaurin

Intervention Type DRUG

50 mg/bid day 8-21

Cytarabine HD

Intervention Type DRUG

100 mg/m2/bid day 1-3 100 mg/m2/die day 4 1.500 mg bid day 5-7

Interventions

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Cytarabine

100 mg/m2/bid day 1-3 100 mg/m2/die day 4-7

Intervention Type DRUG

Daunorubicin

60 mg/m2/die day 1-3

Intervention Type DRUG

Midostaurin

50 mg/bid day 8-21

Intervention Type DRUG

Cytarabine HD

100 mg/m2/bid day 1-3 100 mg/m2/die day 4 1.500 mg bid day 5-7

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Patients with de novo AML, untreated, newly diagnosed, according to WHO 2016 criteria
2. Presence of a mutation of FLT3 gene, either ITD and/or TKD
3. Adequate availability of diagnostic biologic material for full cytological, cytogenetic, genetic and immunophenotypic disease characterization according to ELN criteria.
4. Presence of morphologically identifiable blasts on peripheral blood at diagnosis
5. Presence of a Leukemia-associated aberrant immune-phenotype (LAIP) as assessed by MFC (multiparametric flow cytometry) at diagnosis
6. Age between 18 and 65 years, included
7. ECOG performance status 0-2 or disease-related reversible ECOG 3 score following adequate supportive care.
8. Signed written informed consent according to ICH/EU/GCP and national local laws

Exclusion Criteria

1. Diagnosis of acute promyelocytic leukemia
2. Diagnosis of AML with t(8;21)(q22:q22)/RUNX1-RUNX1T1 and t(16;16)(p13:q22) or inversion of chromosome 16 (16)(p13q22)/CBFB-MYH11; in case of suspicion of CBF-related AML due to morphological and/or immunophenotypic features, specific FISH or molecular testing is strongly recommended in accordance with WHO criteria3,157
3. Patients with LVEF less than 45% (by echocardiogram or MUGA)
4. Pre-existing, uncontrolled pathology such as heart failure (congestive/ischaemic, acute myocardial infarction within the post 3 months, untreatable arrhythmias, NYHA classes III and IV), sever liver disease with total bilirubin ≥2,5 x ULN and/or ALT\>3 ULN (unless attributable to AML), acute or chronic pancreatitis, kidney function impairment with serum creatinine ≥2,5 (unless attributable to AML) and severe neuropsychiatric disorder that impairs the patient's ability to understand and sign the informed consent or to cope with the intended treatment plan. For altered liver, pancreas and kidney function tests, eligibility criteria can be reassessed at 24-96 hours, following the institution of adequate supportive measures.
5. Uncontrolled bacterial or fungal infections
6. QTc \>470 msec on screening ECG (Fridericia's formula)
7. A history of cancer that is not in remission phase following surgery and/or chemotherapy and/or radiotherapy with life expectancy \< 1 year.
8. Pregnancy declared by the patient herself. A pregnancy test is performed at diagnosis and, if applicable, before allogeneic HSCT . Female and male patients who are fertile must agree to use an effective form of contraception with their sexual partners from enrollment through 4 months after the end of treatment.
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gruppo Italiano Malattie EMatologiche dell'Adulto

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Aou Consorziale Policlinico - Bari - Uo Ematologia Con Trapianto

Bari, , Italy

Site Status RECRUITING

Irccs Oncologico Istituto Tumori Giovanni Paolo Ii - Bari - Uo Ematologia

Bari, , Italy

Site Status RECRUITING

Aou Di Bologna - Policlinico S. Orsola-Malpighi - Uoc Ematologia

Bologna, , Italy

Site Status RECRUITING

Asst Degli Spedali Civili Di Brescia - Uo Ematologia

Brescia, , Italy

Site Status RECRUITING

Aou Careggi- Sod Ematologia

Florence, , Italy

Site Status RECRUITING

Asl Latina, Presidio Ospedaliero Nord - Ospedale Santa Maria Goretti - Uoc Ematologia

Latina, , Italy

Site Status RECRUITING

Asl Lecce, Ospedale 'V. Fazzi' - Uo Ematologia

Lecce, , Italy

Site Status RECRUITING

Aulss 3 Serenissima, Ospedale Dell'Angelo - Mestre - Uo Ematologia

Mestre, , Italy

Site Status RECRUITING

Aou San Luigi Gonzaga - Orbassano - Scdu Ematologia Generale E Oncoematologia

Orbassano, , Italy

Site Status RECRUITING

Ao Ospedali Riuniti Villa Sofia Cervello - Palermo - Uo Ematologia Con Utmo

Palermo, , Italy

Site Status RECRUITING

Aou Policlinico P. Giaccone - Palermo - Uo Ematologia

Palermo, , Italy

Site Status RECRUITING

Fondazione Ircss Policlinico San Matteo - Pavia - Uo Ematologia

Pavia, , Italy

Site Status RECRUITING

Ausl Della Romagna, Ospedale "Santa Maria Delle Croci" - Ravenna - Ematologia

Ravenna, , Italy

Site Status RECRUITING

Grande Ospedale Metropolitano "Bianchi-Melacrino-Morelli" Po E. Morelli - Reggio Calabria - Uoc Ematologia

Reggio Calabria, , Italy

Site Status RECRUITING

Ausl Di Reggio Emilia - Arcispedale Santa Maria Nuova, Irccs - Sc Ematologia

Reggio Emilia, , Italy

Site Status RECRUITING

C.R.O.B. - I.R.C.C.S. - Rionero in Volture - Uoc Ematologia

Rionero in Vulture, , Italy

Site Status RECRUITING

Aou Policlinico Tor Vergata - Roma - Uoc Trapianto Cellule Staminali

Roma, , Italy

Site Status RECRUITING

Aou Senese - Uoc Ematologia E Trapianti

Siena, , Italy

Site Status RECRUITING

Aou Città Della Salute E Della Scienza, Ospedale S. Giovanni Battista Molinette - Torino - Sc Ematologia 2

Torino, , Italy

Site Status RECRUITING

Ospedale Mauriziano Umberto I - Torino - Scdu Ematologia

Torino, , Italy

Site Status RECRUITING

Countries

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Italy

Central Contacts

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Paola Fazi

Role: CONTACT

0670390528

Enrico Crea

Role: CONTACT

0670390514

Facility Contacts

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Francesco Albano

Role: primary

Crescenza Pasciolla

Role: primary

Antonio Curti

Role: primary

Chiara Cattaneo

Role: primary

Vannucchi

Role: primary

Giuseppe U Cimino

Role: primary

3495378159

Nicola Di Renzo

Role: primary

3388178577

Renato Bassan

Role: primary

3398508691

Daniela E Cilloni

Role: primary

3332818086

Antonino C Mulè

Role: primary

Maria Enza U Mitra

Role: primary

Patrizia U Zappasodi

Role: primary

Michela Rondoni

Role: primary

Bruno Marino Martino

Role: primary

3489335096

Alessia S Tieghi

Role: primary

Giuseppe U Pietrantuono

Role: primary

Adriano Venditti

Role: primary

Monica Bocchia

Role: primary

Ernesta E Audisio

Role: primary

Alessandro Cignetti

Role: primary

Other Identifiers

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AML1919

Identifier Type: -

Identifier Source: org_study_id

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