A Phase 3 Open Label Extension Study of Fostamatinib Disodium in the Treatment of Warm Antibody Autoimmune Hemolytic Anemia

NCT ID: NCT04138927

Last Updated: 2022-03-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ENROLLING_BY_INVITATION

Clinical Phase

PHASE3

Total Enrollment

90 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-10-30

Study Completion Date

2024-04-30

Brief Summary

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The primary objective of this study is:

• To evaluate the long-term safety of fostamatinib in subjects with warm antibody autoimmune hemolytic anemia (wAIHA).

Detailed Description

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Conditions

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Warm Antibody Autoimmune Hemolytic Anemia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Fostamatinib

Subjects who at any time during the C-935788-057 study achieved a hemoglobin response will continue at their dose and regimen from the Week 22 visit in the C-935788-057 study.

All other subjects who enter the extension study will initially receive fostamatinib 100 mg PO bid. Starting at Week 4, the initial fostamatinib dose of 100 mg PO bid will be increased to fostamatinib 150 mg PO bid if subjects have adequately tolerated the study drug, based on the Investigator's judgment.

Group Type EXPERIMENTAL

Fostamatinib disodium

Intervention Type DRUG

Fostamatinib is supplied in two (2) dosage strengths: 100 mg and 150 mg.

Interventions

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Fostamatinib disodium

Fostamatinib is supplied in two (2) dosage strengths: 100 mg and 150 mg.

Intervention Type DRUG

Other Intervention Names

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R935788 Fostamatinib

Eligibility Criteria

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Inclusion Criteria

1. Subject must be willing and able to give written informed consent by signing an IRB approved Informed Consent Form prior to undergoing any study-specific procedures.
2. Subject must have completed all 24 weeks of participation in the study C-935788-057.

Exclusion Criteria

1\. Any subject who discontinued participation in Study C-935788-057 prior to Week 24.
Minimum Eligible Age

18 Years

Maximum Eligible Age

100 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Rigel Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Southern California - Janice and Robert Hall Clinical Trials Biospecimen Laboratory

Los Angeles, California, United States

Site Status

Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center

Torrance, California, United States

Site Status

Lombardi Comprehensive Cancer Center

Washington D.C., District of Columbia, United States

Site Status

John Hopkins Bayview Medical Center

Baltimore, Maryland, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, United States

Site Status

American Oncology Network Vista Oncology Division

Olympia, Washington, United States

Site Status

University of Washington

Seattle, Washington, United States

Site Status

Princess Alexandra Hospital - Cancer Trials Unit

Brisbane, Queensland, Australia

Site Status

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status

Hanusch-Krankenhaus

Vienna, , Austria

Site Status

Universitätsklinik f. Innere Medizin I - Klin. Abt. f. Hämatologie u. Hämostaseologie

Vienna, , Austria

Site Status

Vitebsk Regional Clinical Hospital

Vitebsk, , Belarus

Site Status

Vitebsk Regional Clinical Oncology Dispensary

Vitebsk, , Belarus

Site Status

AZ Nikolaas

Sint-Niklaas, , Belgium

Site Status

University Multiprofile Hospital for Active Treatment "Sveti Georgi" EAD, Plovdiv, Clinic of Medical oncology

Pleven, , Bulgaria

Site Status

University Multiprofile Hospital for Active Treatment Sv. Ivan Rilski EAD, Varna, Clinic of Clinical Haematology

Sofia, , Bulgaria

Site Status

Specialized Hospital for Active Treatment of Hematological Disease EAD,

Sofia, , Bulgaria

Site Status

Fakultni nemocnice Brno Interni hematologicka a onkologicka klinika

Brno, , Czechia

Site Status

Fakultni nemocnice Ostrava Klinika hematoonkologie

Ostrava, , Czechia

Site Status

CHU de Bordeaux - GH Sud- Hôpital Haut Lévêque Service Médecine Interne et Maladies Infectieuses

Pessac, , France

Site Status

LTD Multiprofile Clinic Consilium Medulla

Tbilisi, , Georgia

Site Status

M. Zodelava Hematology Centre, Tbilisi

Tbilisi, , Georgia

Site Status

Universitätsklinikum Essen

Essen, , Germany

Site Status

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico, UO Ematologia

Milan, , Italy

Site Status

Fondazione IRCCS Ca'Granda - Ospedale Maggiore Policlinico di Milano - UO Ematologia

Milan, , Italy

Site Status

SCDU Ematologia AOU "Maggiore della Carità"

Novara, , Italy

Site Status

Academisch Medisch Centrum

Amsterdam, , Netherlands

Site Status

Haukeland University Hospital

Bergen, , Norway

Site Status

National Research Center for Hematology

Moscow, , Russia

Site Status

State Budgetary Healthcare Institution Oncology Dispensary No. 2 of the Ministry of Health of the Krasnodar Territory

Sochi, , Russia

Site Status

Clinical Centre of Vojvodina, Clinic for Hematology

Novi Sad, , Serbia

Site Status

Hospital Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

City Clinical Hospital № 4, Hematology Center

Dnipro, , Ukraine

Site Status

Kyiv City Clinical Hospital №9, hematology department №1

Kyiv, , Ukraine

Site Status

Roald Dahl Haemostasis and Thrombosis Centre, Royal Liverpool University Hospital, Liverpool University Hospitals NHS Foundation Trust

Liverpool, , United Kingdom

Site Status

Countries

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United States Australia Austria Belarus Belgium Bulgaria Czechia France Georgia Germany Italy Netherlands Norway Russia Serbia Spain Ukraine United Kingdom

Other Identifiers

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C-935788-058

Identifier Type: -

Identifier Source: org_study_id

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