Extension Study of Iron Chelation Therapy With Deferasirox in β-thalassemia and Rare Chronic Anemia Patients

NCT ID: NCT00303329

Last Updated: 2011-05-09

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

184 participants

Study Classification

INTERVENTIONAL

Study Start Date

2004-03-31

Study Completion Date

2008-10-31

Brief Summary

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A 1-year randomized Phase II core trial was conducted to investigate the efficacy of deferasirox in regularly transfused patients with β-thalassemia and other rare chronic anemia 2 years of age and older. Patients who successfully completed the main trial may continue in the extension trial to receive chelation therapy with deferasirox for up to 3 years. Extension was prolonged to 4 years.

The objective of this study is to assess the long-term safety and efficacy of deferasirox in these patient groups.

Detailed Description

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Conditions

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Anemia Hemosiderosis

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Deferasirox

Deferasirox daily oral dose between 5-40 mg/kg/day

Group Type EXPERIMENTAL

Deferasirox

Intervention Type DRUG

Deferasirox available as 125 mg, 250 mg or 500 mg tablets

Interventions

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Deferasirox

Deferasirox available as 125 mg, 250 mg or 500 mg tablets

Intervention Type DRUG

Other Intervention Names

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ICL670

Eligibility Criteria

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Inclusion Criteria

* Patients completed the planned 12-month core study
* Female patients who have reached menarche and who are sexually active must use double-barrier contraception, oral contraceptive plus barrier contraceptive, or must have undergone clinically documented total hysterectomy and/or ovariectomy, or tubal ligation
* Written informed consent obtained from the patient and/or legal guardian on the patient's behalf in accordance with the national legislation

Exclusion Criteria

* Pregnant or breast feeding patients
Minimum Eligible Age

2 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Novartis Pharmaceuticals

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Children's Hospital and Research center at Oakland

Oakland, California, United States

Site Status

Stanford Hospital

Stanford, California, United States

Site Status

Childres's Hospital Boston

Boston, Massachusetts, United States

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New York Presbyterian Hospital

New York, New York, United States

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Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

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Novartis Investigative Site

Bruges, , Belgium

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Novartis Investigative Site

Brussels, , Belgium

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Novartis Investigative Site

Ghent, , Belgium

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Novartis Investigative Site

La Louvière, , Belgium

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Novartis Investigative Site

Leuven, , Belgium

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Novartis Investigative Site

Montreal, , Canada

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Novartis Investigative Site

Toronto, , Canada

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Novartis Investigative Site

Créteil, , France

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Novartis Investigative Site

Le Kremlin-Bicêtre, , France

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Novartis Investigative Site

Lille, , France

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Novartis Investigative Site

Troyes, , France

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Novartis Investigative Site

Düsseldorf, , Germany

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Novartis Investigative Site

Hanover, , Germany

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Novartis Investigative Site

Ulm, , Germany

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Novartis Investigative Site

Bologna, , Italy

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Novartis Investigative Site

Brindisi, , Italy

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Novartis Investigative Site

Cagliari, , Italy

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Novartis Investigative Site

Genova, , Italy

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Novartis Investigative Site

Milan, , Italy

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Novartis Investigative Site

Pavia, , Italy

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Novartis Investigative Site

Rome, , Italy

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Novartis Investigative Site

Torino, , Italy

Site Status

Novartis Investigative Site

London, , United Kingdom

Site Status

Countries

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United States Belgium Canada France Germany Italy United Kingdom

Other Identifiers

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CICL670A0108E1

Identifier Type: -

Identifier Source: org_study_id

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