Study of Deferasirox for Treatment of Transfusional Iron Overload in Myelodysplastic Patients

NCT ID: NCT00110266

Last Updated: 2021-08-16

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

176 participants

Study Classification

INTERVENTIONAL

Study Start Date

2005-07-25

Study Completion Date

2008-03-28

Brief Summary

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The purpose of this trial is to examine the safety and efficacy of deferasirox in patients with Myelodysplastic Syndrome (MDS) and chronic iron overload from blood transfusions.

Detailed Description

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Study entry requires a diagnosis of low or intermediate (INT-1) risk MDS per International Prognostic Scoring System (IPSS) criteria and serum ferritin ≥ 1000 ng/mL. Patients must have had at least 30 prior red blood cell transfusions. Deferasirox will be administered at an initial dose of 20 mg/kg orally once per day. Patient transfusion history and at least three complete blood count (CBC) values must be available for the 12 weeks prior to study registration for patients with MDS and chronic iron overload from blood transfusions.

Conditions

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Myelodysplastic Syndrome Iron Overload

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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ICL670

Evaluate the safety and tolerability of deferasirox 20 mg/kg/day over one year in patients with MDS

Group Type EXPERIMENTAL

Deferasirox

Intervention Type DRUG

20 mg/kg/day over one year in patients with MDS

Interventions

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Deferasirox

20 mg/kg/day over one year in patients with MDS

Intervention Type DRUG

Other Intervention Names

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ICL670A chelator desferal iron chelation

Eligibility Criteria

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Inclusion Criteria

* Male or female patients with low or intermediate (INT-1) risk MDS
* Patients can be EITHER naïve to iron chelation OR have had prior treatment with deferoxamine (DFO).
* Age greater than or equal to 18 years
* Availability of transfusion records for the 12 weeks prior to registration
* A lifetime minimum of 30 previous packed red blood cell transfusions
* Availability of at least three CBC values (pretransfusion) during the 12 weeks prior to registration
* Serum Ferritin:

For entry into the screening period, serum ferritin ≥ 1000 ng/mL on at least two occasions, at least two weeks apart, during the prior year.

Serum ferritin ≥ 1000 ng/mL at screening via the central lab.

* Life expectancy ≥ 6 months
* Sexually active women must use an effective method of contraception, or must have undergone clinically documented total hysterectomy and/or oophorectomy, or tubal ligation or be postmenopausal (defined as amenorrhea for at least 12 months)
* Able to provide written informed consent

Exclusion Criteria

* Serum creatinine above the upper limit of normal
* Alanine aminotransferase (ALT) \> 500 U/L during screening
* Clinical or laboratory evidence of active Hepatitis B or C
* Urinary protein/creatinine ratio \> 0.5 mg/mg
* History of HIV positive test result (ELISA or Western blot)
* Eastern Cooperative Oncology Group (ECOG) Performance Status \> 2
* Patients with uncontrolled systemic hypertension
* Unstable cardiac disease not controlled by standard medical therapy
* Patients with a diagnosis of or history of clinically relevant ocular toxicity related to iron chelation
* Systemic diseases (cardiovascular, renal, hepatic, etc.) which would prevent study treatment
* Pregnancy or breast feeding
* Treatment with systemic investigational drug within the past 4 weeks or topical investigational drug within the past 7 days
* Other surgical or medical condition which might significantly alter the absorption, distribution, metabolism or excretion of study drug
* History of non-compliance to medical regimens or patients who are considered potentially unreliable and/or not cooperative
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Univ of Alabama Birmingham

Birmingham, Alabama, United States

Site Status

Mayo Clinic

Phoenix, Arizona, United States

Site Status

Bay Area Cancer Research Group

Concord, California, United States

Site Status

City of Hope National Medical Center

Duarte, California, United States

Site Status

Cedars-Sinai Medical Center, UCLA School of Medicine

Los Angeles, California, United States

Site Status

UCLA Medical Center

Los Angeles, California, United States

Site Status

UCSF

San Francisco, California, United States

Site Status

UCSF

San Francisco, California, United States

Site Status

Rocky Mountain Cancer Centers

Aurora, Colorado, United States

Site Status

Mayo Clinic

Jacksonville, Florida, United States

Site Status

Emory University School of Medicine/Winship Cancer Institute

Atlanta, Georgia, United States

Site Status

Straub Clinic and Hospital

Honolulu, Hawaii, United States

Site Status

Novartis Investigative Site

Chicago, Illinois, United States

Site Status

University of Chicago Hospital

Chicago, Illinois, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

University of Kentucky College of Medicine, Markey Cancer Center

Lexington, Kentucky, United States

Site Status

Cabrini Center for Cancer Care/Christus St. Frances Cabrini Hospital

Alexandria, Louisiana, United States

Site Status

St. Agnes HealthCare

Baltimore, Maryland, United States

Site Status

Rush Cancer Institute Univ. of Massachussets Medical Center

Worcester, Massachusetts, United States

Site Status

Novartis Investigative Site

Southfield, Michigan, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

The Center for Cancer Care & Research (TCCCR)

St Louis, Missouri, United States

Site Status

Oncology Hematology West, PC

Omaha, Nebraska, United States

Site Status

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status

The Cancer Center at Hackensack University

Hackensack, New Jersey, United States

Site Status

NMOHC

Albuquerque, New Mexico, United States

Site Status

Roswell Park Cancer Center

Buffalo, New York, United States

Site Status

Rochester General Hospital/Lipson Cancer and Blood Center

Rochester, New York, United States

Site Status

Cancer Care of WNC

Asheville, North Carolina, United States

Site Status

Wake Forest UniversitComprehensive Cancer Center

Winston-Salem, North Carolina, United States

Site Status

The Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

The Ohio State University

Columbus, Ohio, United States

Site Status

Novartis Investigative Site

Portland, Oregon, United States

Site Status

Thomas Jefferson University; Jefferson Medical College, Kimmel Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

Western Pennsylvania Hospital Cancer Institute

Pittsburgh, Pennsylvania, United States

Site Status

The West Cancer Clinic

Memphis, Tennessee, United States

Site Status

Novartis Investigative site

Nashville, Tennessee, United States

Site Status

Baylor/The Methodist Hospital

Houston, Texas, United States

Site Status

Utah Cancer Specialists

Salt Lake City, Utah, United States

Site Status

Arlington Fairfax Hematology Oncology PC

Arlington, Virginia, United States

Site Status

Novartis Investigative Site

Spokane, Washington, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Novartis Investigative Site

Vancouver, British Columbia, Canada

Site Status

Novartis Investigative Site

Hamilton, Ontario, Canada

Site Status

Novartis Investigative Site

Toronto, Ontario, Canada

Site Status

Novartis Investigative Site

Toronto, Ontario, Canada

Site Status

Novartis Investigative Site

Montreal, Quebec, Canada

Site Status

Novartis Investigative Site

Montreal, Quebec, Canada

Site Status

Countries

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United States Canada

References

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List AF, Baer MR, Steensma DP, Raza A, Esposito J, Martinez-Lopez N, Paley C, Feigert J, Besa E. Deferasirox reduces serum ferritin and labile plasma iron in RBC transfusion-dependent patients with myelodysplastic syndrome. J Clin Oncol. 2012 Jun 10;30(17):2134-9. doi: 10.1200/JCO.2010.34.1222. Epub 2012 Apr 30.

Reference Type RESULT
PMID: 22547607 (View on PubMed)

Related Links

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https://www.novctrd.com/ctrdweb/trialresult/trialresults/pdf?trialResultId=2782

Results for CICL670AUS03 from the Novartis Clinical Trials website

https://www.ncbi.nlm.nih.gov/pubmed/?term=22547607

Publication (Embasse # 2012421150)

Other Identifiers

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CICL670AUS03

Identifier Type: -

Identifier Source: org_study_id

NCT00343837

Identifier Type: -

Identifier Source: nct_alias

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