Mepolizumab as Add-on Treatment IN Participants With COPD Characterized by Frequent Exacerbations and Eosinophil Level

NCT ID: NCT04133909

Last Updated: 2025-08-15

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

806 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-10-30

Study Completion Date

2024-08-08

Brief Summary

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This is a multi-center, randomized, placebo-controlled, double-blind, parallel group study designed to confirm the benefits of mepolizumab treatment on moderate or severe exacerbations in chronic obstructive pulmonary disease (COPD) participants given as an add on to their optimized maintenance COPD therapy. The maximum duration of participant participation is approximately 109 weeks, consisting of 2 screening visits (up to 3 weeks), a run-in period (up to 2 weeks), and an intervention period of at least 52 weeks and up to 104 weeks. 800 participants will be randomized in a 1:1 ratio to receive mepolizumab 100 milligrams (mg) or placebo every 4 weeks for at least 13 doses (52 weeks treatment period) up to a maximum of 26 doses (104 weeks treatment period). The number of randomized participants may increase up to approximately 1400.

Detailed Description

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Conditions

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Pulmonary Disease, Chronic Obstructive

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Mepolizumab 100 mg

Participants with Chronic Obstructive Pulmonary Disease (COPD) received a 100 milligrams (mg) dose of mepolizumab as a subcutaneous injection every 4 weeks. Participants remained in the study for an assessment period of minimum of 52 weeks and a maximum of 104 weeks.

Group Type EXPERIMENTAL

Mepolizumab

Intervention Type BIOLOGICAL

Mepolizumab was a sterile liquid formulation. It was administered as a subcutaneous injection (100 milligrams per milliliter \[mg/mL\]) delivered once every 4 weeks using a pre-filled safety syringe.

Placebo

Participants with COPD received matching placebo as a subcutaneous injection every 4 weeks. Participants remained in the study for an assessment period of minimum of 52 weeks and a maximum of 104 weeks.

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

Placebo was a 0.9% sodium chloride solution. It was administered as a subcutaneous injection delivered once every 4 weeks using a pre-filled safety syringe.

Interventions

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Mepolizumab

Mepolizumab was a sterile liquid formulation. It was administered as a subcutaneous injection (100 milligrams per milliliter \[mg/mL\]) delivered once every 4 weeks using a pre-filled safety syringe.

Intervention Type BIOLOGICAL

Placebo

Placebo was a 0.9% sodium chloride solution. It was administered as a subcutaneous injection delivered once every 4 weeks using a pre-filled safety syringe.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Participant must be at least 40 years of age at Screening Visit 1.
* Participants with a peripheral blood eosinophil count of \>=300 cells per microliter (μL) from the hematology sample collected at Screening Visit 0 AND a documented historical blood eosinophil count of \>=150 cells per μL in the 12 months prior to Screening Visit 0 that meets the following: It must have been measured between 12 months and 1 month prior to Screening Visit 0, and it must not have been measured within 14 days of a COPD exacerbation. Participants with no documented historical blood eosinophil count of \>=150 cells per µL must meet this threshold at the Screening Visit 1 assessment.
* Participants with a clinically documented history of COPD for at least 1 year in accordance with the definition by the American Thoracic Society or European Respiratory Society.
* Participants must present with a measured pre- and post-salbutamol Forced expiratory volume in one second (FEV1)/Forced vital capacity (FVC) ratio of \<0.70 at Screening Visit 1 to confirm the diagnosis of COPD and with a measured post-salbutamol FEV1\>20% and \<=80% of predicted normal values calculated using NHANES III reference equations at Screening Visit 1.
* Participants must have a well-documented history (for example, medical record verification) in the 12 months prior to Screening Visit 1 of two or more moderate COPD exacerbations that were treated with systemic corticosteroids (intramuscular \[IM\], intravenous, or oral) with or without antibiotics or at least one severe COPD exacerbation requiring hospitalization.
* Participants must have a well-documented requirement for optimized standard of care background therapy that includes inhaled corticosteroids (ICS) plus 2 additional COPD medications (ICS-based triple therapy) for the 12 months prior to Screening Visit 1 and meets the following criteria: immediately prior to Screening Visit 1, minimum of 3 months of use of an 1) inhaled corticosteroid at a dose \>=500 microgram (mcg) per day fluticasone propionate dose equivalent plus 2) Long acting beta2-agonist (LABA) and 3) Long acting muscarinic antagonist (LAMA) unless documentation of safety or intolerance issues related to LABA or LAMA. For participants who are not continually maintained on ICS plus LABA plus LAMA for the entire 12 months prior to Visit 1 use of the following is allowed (but not in the 3 months immediately prior to Visit 1); inhaled corticosteroid at a dose \>=500 mcg per day fluticasone propionate dose equivalent plus inhaled LABA or inhaled LAMA and Phosphodiesterase-4-inhibitors, methylxanthines, or scheduled daily use of short acting beta2-agonist (SABA) and/or short acting muscarinic antagonist (SAMA).
* Current or former cigarette smokers with a history of cigarette smoking of \>=10 pack-years at Screening (Visit 1) calculated as (number of pack years = \[number of cigarettes per day/20\] multiplied by number of years smoked \[For example, 20 cigarettes per day for 10 years or 10 cigarettes per day for 20 years\]).
* Contraceptive use for female participant should be consistent with local regulations regarding the methods of contraception for those participating in clinical studies.
* A female participant is eligible to participate if she is not pregnant or breastfeeding, and at least one of the following conditions applies: She is not a woman of childbearing potential (WOCBP) or she is a WOCBP and using a contraceptive method that is highly effective, with a failure rate of \<1%, during the intervention period and for at least 16 weeks after the last dose of study intervention. The principal investigator (PI) should evaluate the effectiveness of the contraceptive method in relation to the first dose of study intervention.
* A WOCBP must have a negative highly sensitive pregnancy urine test within 24 hours before the first dose of study intervention. If a urine test cannot be confirmed as negative (For example, an ambiguous result), a serum pregnancy test is required. In such cases, the participant must be excluded from participation if the serum pregnancy result is positive.
* Participants capable of giving signed informed consent which includes compliance with the requirements and restrictions listed in the informed consent form (ICF) and in this protocol.

Exclusion Criteria

* Participants with a past history or concurrent diagnosis of asthma are excluded regardless of whether they have active or inactive disease.
* The Investigator must judge that COPD is the primary diagnosis accounting for the clinical manifestations of the lung disease. Participants with alpha1-antitrypsin deficiency as the underlying cause of COPD are excluded. Also, excluded are participants with active tuberculosis, lung cancer, bronchiectasis, sarcoidosis, lung fibrosis, primary pulmonary hypertension, interstitial lung diseases or other active pulmonary diseases.
* Participants with pneumonia, COPD exacerbation, or lower respiratory tract infection within the 4 weeks prior to Screening Visit 1.
* Participants with lung volume reduction surgery within the 12 months prior to Screening Visit 1.
* Participation in the acute phase of a pulmonary rehabilitation program within 4 weeks prior to Screening Visit 1. Participants who are in the maintenance phase of a pulmonary rehabilitation program are not excluded.
* Participants receiving treatment with oxygen more than 2 liter (L) per minute at rest over 24 hours. For participants receiving oxygen treatment, participants should demonstrate an oxyhemoglobin saturation greater than or equal to 89% while breathing supplemental oxygen.
* Participants with a QT interval, from the electrocardiogram (ECG) conducted at Screening Visit 1, corrected with Fridericia's formula (QTcF) \>450 millisecond (msec) (or QTcF \>480 msec in participants with bundle branch block). Fridericia's formula must be used to determine eligibility and discontinuation for an individual participant. Participants are excluded if an abnormal ECG finding from the 12-lead ECG conducted at Screening Visit 1 is considered to be clinically significant and would impact the participant's participation during the study, based on the evaluation of the Investigator.
* Participants with any of the following would be excluded: myocardial infarction or unstable angina in the 6 months prior to Screening Visit 1; unstable or life threatening cardiac arrhythmia requiring intervention in the 3 months prior to Screening Visit 1; New York Heart Association (NYHA) Class IV Heart failure.
* Participants with (historical or) current evidence of clinically significant, neurological, psychiatric, renal, hepatic, immunological, endocrine (including uncontrolled diabetes or thyroid disease) or hematological abnormalities that are uncontrolled. Significant is defined as any disease that, in the opinion of the Investigator, would put the safety of the participant at risk through participation, or which could affect the efficacy or safety analysis if the disease/condition exacerbated during the study.
* Participants with other conditions that could lead to elevated eosinophils such as Hypereosinophilic syndromes including Eosinophilic Granulomatosis with Polyangiitis (EGPA), also known as Churg-Strauss Syndrome, or Eosinophilic Esophagitis.
* Participants with a known, pre-existing parasitic infestation within 6 months prior to Screening Visit 1.
* A current malignancy or previous history of cancer in remission for less than 12 months prior to Screening Visit 1 (participants that had localized carcinoma of the skin or cervix which was resected for cure will not be excluded).
* Participants with a known immunodeficiency (For example, human immunodeficiency virus \[HIV\]), other than that explained by the use of corticosteroids taken for COPD.
* Participants with cirrhosis or current unstable liver disease per investigator assessment defined by the presence of ascites, encephalopathy, coagulopathy, hypoalbuminemia, esophageal or gastric varices, or persistent jaundice. Stable non-cirrhotic chronic liver disease (including Gilbert's syndrome, asymptomatic gallstones, and chronic stable hepatitis B or C -e.g., presence of hepatitis B surface antigen \[HbsAg\] or positive hepatitis C antibody test result) is acceptable if the participant otherwise meets entry criteria.
* Participants who have received interventional product in previous mepolizumab studies are excluded.
* Participants who have received any monoclonal antibody within 5 half-lives of Screening Visit 1.
* Participants who have received an investigational drug within 30 days of Visit 1, or within 5 drug half-lives of the investigational drug, whichever is longer (this also includes investigational formulations of a marketed product).
* Participants who have received short term use of oral corticosteroids within 30 days of Visit 1.
* Participants with a known allergy or sensitivity to any of the study interventions, or components thereof, or drug or other allergy that, in the opinion of the Investigator or Medical Monitor, contraindicates participation in the study or intolerance to another monoclonal antibody or biologic including history of anaphylaxis to another biologic.
* Participants at risk of non-compliance, or unable to comply with the study procedures. Any infirmity, disability, or geographic location that would limit compliance for scheduled visits.
* Participants with conditions that will limit the validity of informed consent to participate in the study, for example, uncontrolled psychiatric disease or intellectual deficiency.
* Participants with a known or suspected history of alcohol or drug abuse within 2 years prior to Visit 1.
* Participant is an Investigator, sub-Investigator, study coordinator, employee of a participating Investigator or study site, or immediate family member of the aforementioned that is involved in this study.
* Participants with a current active COVID-19 infection, either laboratory confirmed or according to the investigator's medical judgement and who are known to be in contact with active COVID-19 positive individuals within the past 14 days.
Minimum Eligible Age

40 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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PPD Development, LP

INDUSTRY

Sponsor Role collaborator

GlaxoSmithKline

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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GSK Clinical Trials

Role: STUDY_DIRECTOR

GlaxoSmithKline

Locations

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Birmingham, Alabama, United States

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Dothan, Alabama, United States

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Huntsville, Alabama, United States

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Jasper, Alabama, United States

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Sheffield, Alabama, United States

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Chandler, Arizona, United States

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Chandler, Arizona, United States

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Gilbert, Arizona, United States

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Mesa, Arizona, United States

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Phoenix, Arizona, United States

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Phoenix, Arizona, United States

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Phoenix, Arizona, United States

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Phoenix, Arizona, United States

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Tucson, Arizona, United States

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Conway, Arkansas, United States

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Alpine, California, United States

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Cerritos, California, United States

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Newport Beach, California, United States

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Riverside, California, United States

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San Diego, California, United States

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Torrance, California, United States

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Vista, California, United States

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Colorado Springs, Colorado, United States

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Boynton Beach, Florida, United States

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Clearwater, Florida, United States

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Daytona Beach, Florida, United States

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Doral, Florida, United States

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Ft. Pierce, Florida, United States

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Gainesville, Florida, United States

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Hialeah, Florida, United States

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Homestead, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami Lakes, Florida, United States

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Miami Lakes, Florida, United States

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New Port Richey, Florida, United States

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Orlando, Florida, United States

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Pinellas Park, Florida, United States

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Plantation, Florida, United States

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Port Orange, Florida, United States

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St. Petersburg, Florida, United States

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Tampa, Florida, United States

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Adairsville, Georgia, United States

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Johns Creek, Georgia, United States

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Lawrenceville, Georgia, United States

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Woodstock, Georgia, United States

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Chicago, Illinois, United States

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Evansville, Indiana, United States

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Valparaiso, Indiana, United States

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Iowa City, Iowa, United States

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Lexington, Kentucky, United States

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Natchitoches, Louisiana, United States

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Baltimore, Maryland, United States

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Columbia, Maryland, United States

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Lathrup Village, Michigan, United States

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St Louis, Missouri, United States

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Las Vegas, Nevada, United States

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Toms River, New Jersey, United States

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Albuquerque, New Mexico, United States

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The Bronx, New York, United States

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Charlotte, North Carolina, United States

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Gastonia, North Carolina, United States

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Greenville, North Carolina, United States

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Hickory, North Carolina, United States

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Shelby, North Carolina, United States

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Wilmington, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Cincinnati, Ohio, United States

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Columbus, Ohio, United States

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Columbus, Ohio, United States

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Hilliard, Ohio, United States

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Kettering, Ohio, United States

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Norman, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Portland, Oregon, United States

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Altoona, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Anderson, South Carolina, United States

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Charleston, South Carolina, United States

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Clinton, South Carolina, United States

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Fort Mill, South Carolina, United States

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Greenville, South Carolina, United States

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Rock Hill, South Carolina, United States

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Spartanburg, South Carolina, United States

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Knoxville, Tennessee, United States

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Corsicana, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Lampasas, Texas, United States

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McAllen, Texas, United States

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McKinney, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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Sherman, Texas, United States

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Webster, Texas, United States

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Rutland, Vermont, United States

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Berazategui Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Ciudad AutOnoma de Buenos Aire, , Argentina

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Ciudad Autonoma de Bueno, , Argentina

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Ciudad Autonoma de Bueno, , Argentina

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Córdoba, , Argentina

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La Plata, , Argentina

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Lobos, , Argentina

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Mar del Plata, , Argentina

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Mar del Plata, , Argentina

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Mendoza, , Argentina

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Mendoza, , Argentina

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Quilmes, , Argentina

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Rosario, , Argentina

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Rosario, , Argentina

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Rosario Provincia de Santa FE, , Argentina

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San Miguel de Tucumán, , Argentina

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San Rafael, , Argentina

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Coffs Harbour, New South Wales, Australia

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New Lambton, New South Wales, Australia

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Sydney, New South Wales, Australia

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Westmead, New South Wales, Australia

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Kent Town, South Australia, Australia

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Frankston, Victoria, Australia

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Jambes, , Belgium

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Liège, , Belgium

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Yvoir, , Belgium

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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São Paulo, , Brazil

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Vancouver, British Columbia, Canada

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Truro, Nova Scotia, Canada

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Ajax, Ontario, Canada

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Newmarket, Ontario, Canada

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Sarnia, Ontario, Canada

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Windsor, Ontario, Canada

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Saint-Charles-Borromée, Quebec, Canada

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Baotou, , China

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Beijing, , China

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Beijing, , China

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Beijing, , China

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Beijing, , China

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Changchun, , China

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Changchun, , China

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Changsha, , China

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Changsha, , China

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Changsha, , China

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Changsha, , China

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Guangzhou, , China

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Guangzhou, , China

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Guangzhou, , China

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Hangzhou, , China

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Hangzhou, , China

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Hohehot, , China

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Jiaxing, , China

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Jinan, , China

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Nanchang, , China

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Nanchang, , China

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Nanchang, , China

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Nanjing, , China

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Nanjing, , China

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Nanning, , China

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Qingdao, , China

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Sanya, , China

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Shanghai, , China

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Shanghai, , China

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Shanghai, , China

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Shanghai, , China

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Taiyuan, , China

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Taizhou, , China

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Ürümqi, , China

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Wuhan, , China

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Wuxi, , China

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Xiamen, , China

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Xining, , China

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Xinxiang, , China

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Zhuhai, , China

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Zigong, , China

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Aalborg, , Denmark

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Hvidovre, , Denmark

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Kbenhavn N, , Denmark

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Koebenhavn NV, , Denmark

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Odense C, , Denmark

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Roskilde, , Denmark

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Vejle, , Denmark

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Tallinn, , Estonia

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Brest, , France

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Cholet, , France

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Clermont-Ferrand, , France

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Epagny Metz-Tessy, , France

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Le Mans, , France

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Lyon, , France

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Montpellier, , France

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Mulhouse, , France

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Cottbus, , Germany

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Frankfurt, , Germany

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Frankfurt, , Germany

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Frankfurt, , Germany

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Fürstenwalde, , Germany

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Geesthacht, , Germany

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Gelsenkirchen, , Germany

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Halle, , Germany

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Immenhausen, , Germany

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Koblenz, , Germany

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Leipzig, , Germany

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Leipzig, , Germany

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Leipzig, , Germany

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Leipzig, , Germany

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Lübeck, , Germany

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Mainz, , Germany

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Neu-Isenburg, , Germany

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Peine, , Germany

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Rheine, , Germany

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Rodgau, , Germany

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Schleswig, , Germany

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Stuttgart, , Germany

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Alexandroupoli, , Greece

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Athens, , Greece

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Athens, , Greece

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Ioannina, , Greece

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Rio Patras, , Greece

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Thessaloniki, , Greece

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Budapest, , Hungary

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Budapest, , Hungary

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Debrecen, , Hungary

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Debrecen, , Hungary

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Gyula, , Hungary

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Hajdúnánás, , Hungary

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Hatvan, , Hungary

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Pécs, , Hungary

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Siófok, , Hungary

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Törökbálint, , Hungary

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Zalaegerszeg, , Hungary

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Ahmedabad, , India

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Hyderabad, , India

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Hyderabad, , India

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Jaipur, , India

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Kanpur, , India

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Lucknow, , India

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Nagpur, , India

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Nagpur, , India

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New Delhi, , India

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New Delhi, , India

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Puducherry, , India

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Drogheda, , Ireland

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Dublin, , Ireland

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Dublin, , Ireland

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Dublin, , Ireland

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Galway, , Ireland

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Limerick, , Ireland

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Ashkelon, , Israel

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Beer-Yaakov, , Israel

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Haifa, , Israel

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Holon, , Israel

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Jerusalem, , Israel

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Jerusalem, , Israel

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Kfar Saba, , Israel

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Petah Tikva, , Israel

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Ramat Gan, , Israel

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Rehovot, , Israel

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Bari, , Italy

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Ferrara, , Italy

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Roma, , Italy

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Telese Terme BN, , Italy

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Verona, , Italy

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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Jalisco, , Mexico

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Monterrey, , Mexico

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Monterrey, , Mexico

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Breda, , Netherlands

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Groningen, , Netherlands

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Heerlen, , Netherlands

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Rotterdam, , Netherlands

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The Hague, , Netherlands

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Zutphen, , Netherlands

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Auckland, , New Zealand

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Hamilton, , New Zealand

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Havelock North, , New Zealand

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Rotorua, , New Zealand

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Wellington, , New Zealand

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Bialystok, , Poland

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Bydgoszcz, , Poland

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Częstochowa, , Poland

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Elblag, , Poland

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Gdansk, , Poland

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Gdynia, , Poland

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Katowice, , Poland

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Katowice, , Poland

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Kielce, , Poland

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Krakow, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Lodz, , Poland

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Ostrowiec Świętokrzyski, , Poland

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Poznan, , Poland

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Poznan, , Poland

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Rzeszów, , Poland

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Rzeszów, , Poland

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Sopot, , Poland

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Sosnowiec, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Zamość, , Poland

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Daegu, , South Korea

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Incheon, , South Korea

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Incheon, , South Korea

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Jeonju, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Alzira, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Benalmádena, , Spain

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Cadiz, , Spain

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Cáceres, , Spain

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Galdakano, , Spain

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Granada, , Spain

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Granada, , Spain

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HebrOn, , Spain

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Madrid, , Spain

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Marbella, , Spain

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Pozuelo de AlarcOn Madr, , Spain

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Santiago de Compostela, , Spain

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Valencia, , Spain

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Zaragoza, , Spain

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Härnösand, , Sweden

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Malmo, , Sweden

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Uppsala, , Sweden

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Taichung, , Taiwan

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Taipei, , Taiwan

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Birmingham, , United Kingdom

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Cardiff, , United Kingdom

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Glasgow, , United Kingdom

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Hardwick, , United Kingdom

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Hexham, , United Kingdom

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Lancashire, , United Kingdom

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Liverpool, , United Kingdom

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London, , United Kingdom

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Manchester, , United Kingdom

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Norwich, , United Kingdom

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Reading, , United Kingdom

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Wishaw, , United Kingdom

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Countries

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United States Argentina Australia Belgium Brazil Canada China Denmark Estonia France Germany Greece Hungary India Ireland Israel Italy Mexico Netherlands New Zealand Poland South Korea Spain Sweden Taiwan United Kingdom

References

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Sciurba FC, Criner GJ, Christenson SA, Martinez FJ, Papi A, Roche N, Bourbeau J, Korn S, Bafadhel M, Han MK, Kolterer S, Miller K, Mouneimne D, Fletcher J, Mayer B, Min J, Pavord ID; MATINEE Study Investigators. Mepolizumab to Prevent Exacerbations of COPD with an Eosinophilic Phenotype. N Engl J Med. 2025 May 1;392(17):1710-1720. doi: 10.1056/NEJMoa2413181.

Reference Type BACKGROUND
PMID: 40305712 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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208657

Identifier Type: -

Identifier Source: org_study_id

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