Benralizumab Efficacy in Moderate to Very Severe Chronic Obstructive Pulmonary Disease (COPD) With Exacerbation History

NCT ID: NCT02138916

Last Updated: 2019-06-13

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1656 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-06-13

Study Completion Date

2018-04-10

Brief Summary

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The purpose of the study is to determine if benralizumab reduces COPD exacerbation rate in symptomatic patients with moderate to very severe COPD who are receiving standard of care therapies

Detailed Description

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Conditions

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Moderate to Very Severe Chronic Obstructive Pulmonary Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Benralizumab Arm A

Benralizumab administered subcutaneously

Group Type EXPERIMENTAL

Benralizumab Arm A

Intervention Type DRUG

Benralizumab subcutaneously on study week 0 until study week 48 inclusive

Benralizumab Arm B

Benralizumab administered subcutaneously

Group Type EXPERIMENTAL

Benralizumab Arm B

Intervention Type DRUG

Benralizumab subcutaneously on study week 0 until study week 48 inclusive

Placebo

Placebo administered subcutaneously

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo subcutaneously on study week 0 until study week 48 inclusive

Interventions

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Benralizumab Arm A

Benralizumab subcutaneously on study week 0 until study week 48 inclusive

Intervention Type DRUG

Benralizumab Arm B

Benralizumab subcutaneously on study week 0 until study week 48 inclusive

Intervention Type DRUG

Placebo

Placebo subcutaneously on study week 0 until study week 48 inclusive

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

2\. Any disorder or major physical impairment that is not stable by Investigator opinion and/or could affect: - subject safety-study findings or their interpretation or subject's ability to complete the entire study duration.

3\. Unstable ischemic heart disease, arrhythmia, cardiomyopathy, or other relevant cardiovascular disorder that in Investigator's judgment may put the patient at risk or negatively affect the study outcome.

4\. Treatment with systemic corticosteroids and/or antibiotics, and/or hospitalization for a COPD exacerbation within 2 weeks prior to Visit1 or during the enrolment and run-in period.

5\. Acute upper or lower respiratory infection requiring antibiotics or antiviral medication within 2 weeks prior to Visit1or during the enrolment and run-in period.

6\. Pneumonia within 8 weeks prior to Visit1 or during the enrolment and run-in period.

7\. Pregnant, breastfeeding, or lactating women. 8. Risk factors for pneumonia 9. History of anaphylaxis to any other biologic therapy. 10. Long term oxygen therapy with signs and/or symptoms of cor pulmonale, right ventricular failure.

11\. Use of immunosuppressive medication within 2 weeks prior to Visit1 and/or during the enrolment and run-in period.

12\. Receipt of any investigational non-biologic product within 30 days or 5 half-lives prior to Visit 1.

13\. Evidence of active tuberculosis (TB) without an appropriate course of treatment.

14\. Lung volume reduction surgery within the 6 months prior to Visit 1. History of partial or total lung resection (single lobe or segmentectomy is acceptable).

15\. Asthma as a primary or main diagnosis according to the Global Initiative for Asthma (GINA) guidelines or other accepted guidelines.

16\. Previous treatment with benralizumab. 17. Helminth parasitic infection diagnosed within 24 weeks prior to Visit 1.
Minimum Eligible Age

40 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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MedImmune LLC

INDUSTRY

Sponsor Role collaborator

AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gerard Criner, MD

Role: PRINCIPAL_INVESTIGATOR

Temple University School of Medicine, 3401 North Broad Street, Suite 745 PP, Philadelphia, PA 19140

Locations

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Andalusia, Alabama, United States

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Birmingham, Alabama, United States

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Birmingham, Alabama, United States

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Dothan, Alabama, United States

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Jasper, Alabama, United States

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Little Rock, Arkansas, United States

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Beverly Hills, California, United States

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Gold River, California, United States

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Huntington Beach, California, United States

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Huntington Park, California, United States

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Lakewood, California, United States

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Lomita, California, United States

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Newport Beach, California, United States

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Palm Desert, California, United States

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Palo Alto, California, United States

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Riverside, California, United States

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Sacramento, California, United States

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San Diego, California, United States

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Santa Ana, California, United States

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Thousand Oaks, California, United States

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Torrance, California, United States

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New Haven, Connecticut, United States

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Waterbury, Connecticut, United States

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Boynton Beach, Florida, United States

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Brandon, Florida, United States

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Clearwater, Florida, United States

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Clearwater, Florida, United States

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Fort Lauderdale, Florida, United States

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Gainesville, Florida, United States

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Hialeah, Florida, United States

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Kissimmee, Florida, United States

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Loxahatchee Groves, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami Springs, Florida, United States

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Orlando, Florida, United States

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Orlando, Florida, United States

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Orlando, Florida, United States

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Panama City, Florida, United States

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Port Orange, Florida, United States

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Sebring, Florida, United States

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St. Petersburg, Florida, United States

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St. Petersburg, Florida, United States

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Vero Beach, Florida, United States

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Winter Park, Florida, United States

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Atlanta, Georgia, United States

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Calhoun, Georgia, United States

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Decatur, Georgia, United States

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Duluth, Georgia, United States

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Marietta, Georgia, United States

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Eagle, Idaho, United States

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Aurora, Illinois, United States

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Chicago, Illinois, United States

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Evanston, Illinois, United States

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Michigan City, Indiana, United States

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Valparaiso, Indiana, United States

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Iowa City, Iowa, United States

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Fort Mitchell, Kentucky, United States

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Hazard, Kentucky, United States

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Baltimore, Maryland, United States

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Baltimore, Maryland, United States

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Columbia, Maryland, United States

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North Dartmouth, Massachusetts, United States

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Farmington Hills, Michigan, United States

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Rochester, Michigan, United States

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Minneapolis, Minnesota, United States

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Saint Charles, Missouri, United States

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St Louis, Missouri, United States

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Las Vegas, Nevada, United States

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Summit, New Jersey, United States

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Albuquerque, New Mexico, United States

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Bronxville, New York, United States

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Buffalo, New York, United States

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Fayetteville, New York, United States

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New York, New York, United States

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Asheville, North Carolina, United States

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Charlotte, North Carolina, United States

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Durham, North Carolina, United States

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Elizabeth City, North Carolina, United States

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Gastonia, North Carolina, United States

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Greensboro, North Carolina, United States

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Mount Airy, North Carolina, United States

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New Bern, North Carolina, United States

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Wilmington, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Canton, Ohio, United States

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Cincinnati, Ohio, United States

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Dayton, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Bend, Oregon, United States

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Medford, Oregon, United States

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Portland, Oregon, United States

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Altoona, Pennsylvania, United States

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Erie, Pennsylvania, United States

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Jefferson Hills, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Wyomissing, Pennsylvania, United States

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Charleston, South Carolina, United States

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Columbia, South Carolina, United States

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Gaffney, South Carolina, United States

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Greenville, South Carolina, United States

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Mt. Pleasant, South Carolina, United States

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Old Point Station, South Carolina, United States

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Rock Hill, South Carolina, United States

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Spartanburg, South Carolina, United States

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Rapid City, South Dakota, United States

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Chattanooga, Tennessee, United States

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Franklin, Tennessee, United States

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Hendersonville, Tennessee, United States

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Arlington, Texas, United States

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Boerne, Texas, United States

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Tyler, Texas, United States

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Richmond, Virginia, United States

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Richmond, Virginia, United States

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Richmond, Virginia, United States

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Richland, Washington, United States

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Feldkirch, , Austria

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Graz, , Austria

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Innsbruck, , Austria

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Linz, , Austria

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Salzburg, , Austria

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Vienna, , Austria

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Wels, , Austria

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Calgary, Alberta, Canada

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Calgary, Alberta, Canada

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Sherwood Park, Alberta, Canada

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Vancouver, British Columbia, Canada

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Vancouver, British Columbia, Canada

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Ajax, Ontario, Canada

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Burlington, Ontario, Canada

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Grimsby, Ontario, Canada

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Hamilton, Ontario, Canada

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Montreal, Quebec, Canada

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Pointe-Claire, Quebec, Canada

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Québec, Quebec, Canada

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Québec, Quebec, Canada

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Québec, Quebec, Canada

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Saint-Charles-Borromée, Quebec, Canada

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Trois-Rivières, Quebec, Canada

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Saskatoon, Saskatchewan, Canada

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Jindřichův Hradec, , Czechia

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Karlovy Vary, , Czechia

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Kralupy nad Vltavou, , Czechia

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Mladá Boleslav, , Czechia

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Olomouc, , Czechia

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Prague, , Czechia

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Rokycany, , Czechia

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Strakonice, , Czechia

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Teplice, , Czechia

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Bamberg, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Bonn, , Germany

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Frankfurt am Main, , Germany

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Frankfurt am Main, , Germany

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Geesthacht, , Germany

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Hamburg, , Germany

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Leipzig, , Germany

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Marburg, , Germany

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Neu-Isenburg, , Germany

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Rodgau-Dudenhofen, , Germany

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Teuchern, , Germany

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Witten, , Germany

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Balassagyarmat, , Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Edelény, , Hungary

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Farkasgyepü, , Hungary

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Gödöllő, , Hungary

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Hajdúnánás, , Hungary

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Hatvan, , Hungary

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Mátraháza, , Hungary

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Miskolc, , Hungary

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Százhalombatta, , Hungary

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Szeged, , Hungary

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Székesfehérvár, , Hungary

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Bolzano, , Italy

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Catania, , Italy

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Ferrara, , Italy

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Genova, , Italy

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Orbassano, , Italy

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Palermo, , Italy

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Parma, , Italy

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Pavia, , Italy

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Pisa, , Italy

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Tradate, , Italy

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Chūōku, , Japan

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Fukuoka, , Japan

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Fukuoka, , Japan

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Fukuyama-shi, , Japan

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Higashiibaraki-gun, , Japan

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Himeji-shi, , Japan

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Hirosaki-shi, , Japan

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Iwata-shi, , Japan

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Izumo-shi, , Japan

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Joyo-shi, , Japan

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Kagoshima, , Japan

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Kasugai-shi, , Japan

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Kawaguchi-shi, , Japan

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Kawasaki-shi, , Japan

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Kiryu-shi, , Japan

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Kishiwada-shi, , Japan

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Kitakami-shi, , Japan

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Kobe, , Japan

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Kochi, , Japan

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Kodaira-shi, , Japan

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Kokubunji-shi, , Japan

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Koshi-shi, , Japan

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Kuki-shi, , Japan

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Kumamoto, , Japan

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Kurashiki-shi, , Japan

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Kurume-shi, , Japan

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Kyoto, , Japan

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Matsue, , Japan

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Matsue, , Japan

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Matsumoto-shi, , Japan

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Matsusaka-shi, , Japan

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Meguro-ku, , Japan

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Morioka, , Japan

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Nagaoka-shi, , Japan

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Nagoya, , Japan

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Nagoya, , Japan

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Niigata, , Japan

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Obihiro-shi, , Japan

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Ohota-ku, , Japan

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Saiki-shi, , Japan

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Sakaishi, , Japan

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Sapporo, , Japan

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Sapporo, , Japan

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Sapporo, , Japan

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Sapporo, , Japan

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Sendai, , Japan

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Seto-shi, , Japan

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Shinagawa-ku, , Japan

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Shinjuku-ku, , Japan

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Takamatsu, , Japan

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Takatsuki-shi, , Japan

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Yokohama, , Japan

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Yokohama, , Japan

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Yokohama, , Japan

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Yokohama, , Japan

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Breda, , Netherlands

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Eindhoven, , Netherlands

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Heerlen, , Netherlands

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Horn, , Netherlands

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Nijmegen, , Netherlands

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Zwolle, , Netherlands

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Bydgoszcz, , Poland

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Dobre Miasto, , Poland

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Gdansk, , Poland

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Gdansk, , Poland

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Katowice, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Mrągowo, , Poland

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Olsztyn, , Poland

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Radom, , Poland

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Zakopane, , Poland

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Bragadiru, , Romania

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Brasov, , Romania

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Constanța, , Romania

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Deva, , Romania

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Timișoara, , Romania

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Chelyabinsk, , Russia

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Ivanovo, , Russia

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Izhevsk, , Russia

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Kazan', , Russia

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Kemerovo, , Russia

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Kemerovo, , Russia

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Kemerovo, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Nizhny Novgorod, , Russia

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Novosibirsk, , Russia

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Novosibirsk, , Russia

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Novosibirsk, , Russia

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Penza, , Russia

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Perm, , Russia

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Pskov, , Russia

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Pyatigorsk, , Russia

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Ryazan, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saratov, , Russia

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Smolensk, , Russia

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Tomsk, , Russia

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Tomsk, , Russia

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Ufa, , Russia

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Ulyanovsk, , Russia

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Vladikavkaz, , Russia

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Vladimir, , Russia

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Volgograd, , Russia

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Volgograd, , Russia

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Yekaterinburg, , Russia

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Yekaterinburg, , Russia

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Yekaterinburg, , Russia

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Yekaterinburg, , Russia

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Bloemfontein, , South Africa

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Cape Town, , South Africa

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Durban, , South Africa

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eManzimtoti, , South Africa

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Gauteng, , South Africa

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Middelburg, , South Africa

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Bucheon-si, , South Korea

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Daegu, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Wŏnju, , South Korea

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Alicante, , Spain

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Badalona(Barcelona), , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Madrid, , Spain

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Málaga, , Spain

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Palma de Mallorca, , Spain

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Sabadell (Barcelona), , Spain

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Santander, , Spain

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Valencia, , Spain

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Basel, , Switzerland

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Biel, , Switzerland

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Gossau, , Switzerland

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Liestal, , Switzerland

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Sankt Gallen, , Switzerland

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Aberdeen, , United Kingdom

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Birmingham, , United Kingdom

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Bradford, , United Kingdom

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Cambridge, , United Kingdom

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Chertsey, , United Kingdom

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Edinburgh, , United Kingdom

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Glasgow, , United Kingdom

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LE3 9QP, , United Kingdom

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London, , United Kingdom

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Manchester, , United Kingdom

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Manchester, , United Kingdom

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Newcastle upon Tyne, , United Kingdom

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Newcastle-under-Lyme, , United Kingdom

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Oxford, , United Kingdom

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Plymouth, , United Kingdom

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Southampton, , United Kingdom

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Wishaw, , United Kingdom

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Wolverhampton, , United Kingdom

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Countries

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United States Austria Canada Czechia Germany Hungary Italy Japan Netherlands Poland Romania Russia South Africa South Korea Spain Switzerland United Kingdom

References

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Criner GJ, Celli BR, Singh D, Agusti A, Papi A, Jison M, Makulova N, Shih VH, Brooks L, Barker P, Martin UJ, Newbold P. Predicting response to benralizumab in chronic obstructive pulmonary disease: analyses of GALATHEA and TERRANOVA studies. Lancet Respir Med. 2020 Feb;8(2):158-170. doi: 10.1016/S2213-2600(19)30338-8. Epub 2019 Sep 28.

Reference Type DERIVED
PMID: 31575508 (View on PubMed)

Criner GJ, Celli BR, Brightling CE, Agusti A, Papi A, Singh D, Sin DD, Vogelmeier CF, Sciurba FC, Bafadhel M, Backer V, Kato M, Ramirez-Venegas A, Wei YF, Bjermer L, Shih VH, Jison M, O'Quinn S, Makulova N, Newbold P, Goldman M, Martin UJ; GALATHEA Study Investigators; TERRANOVA Study Investigators. Benralizumab for the Prevention of COPD Exacerbations. N Engl J Med. 2019 Sep 12;381(11):1023-1034. doi: 10.1056/NEJMoa1905248. Epub 2019 May 20.

Reference Type DERIVED
PMID: 31112385 (View on PubMed)

Provided Documents

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Document Type: Statistical Analysis Plan

View Document

Document Type: Study Protocol

View Document

Other Identifiers

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D3251C00003

Identifier Type: -

Identifier Source: org_study_id

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