BR101801 in Adult Patients With Advanced Hematologic Malignancies(Phase I)

NCT ID: NCT04018248

Last Updated: 2025-09-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

26 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-04-21

Study Completion Date

2023-09-21

Brief Summary

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This is a Phase I, multi-center, open-label, FIH study comprising of 2 study parts (Phase Ia, Phase Ib).

The Phase Ia (dose escalation) part of the study is designed to determine the safety, tolerability, and maximum tolerated dose (MTD)/recommended dose for expansion (RP2D) of BR101801 in subjects with relapsed/refractory B cell lymphoma, chronic lymphocytic leukemia (CLL)/small lymphocytic leukemia (SLL), and peripheral T cell lymphoma (PTCL).

The Phase Ib (dose expansion) part of the study is designed to assess tumor response and safety in specific advanced relapsed/refractory Peripheral T-cell lymphoma(PTCL) at a dose of BR101801 identified in Phase Ia. Once the RP2D has been determined in Phase Ia (dose escalation), Phase Ib (dose expansion) will commence.

Detailed Description

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1. Phase Ia (Dose Escalation)

Primary Objectives
* To assess the safety and tolerability of BR101801 in patients with relapsed/refractory B-cell lymphoma, CLL/SLL, and PTCL.
* To assess DLT and to determine the MTD and/or the RDE dose for BR101801 when administered orally on a daily schedule in 4-week cycles until disease progression.

SecondaryObjectives
* To characterize the plasma and urine PK of BR101801.
* To assess the preliminary antitumor activity of BR101801.
2. Phase Ib (Dose Expansion)

Primary Objectives

• To assess the safety and tolerability of BR101801 at the RP2D dose in subjects with relapsed/refractory Peripheral T-cell lymphoma (PTCL).

SecondaryObjectives

* To assess clinical activity of BR101801 when administered orally on a daily schedule in 4-week cycles until disease progression.
* To assess the plasma PK of BR101801.

OUTLINE: This is a Phase I, multi-center, open-label, FIH study. The safety monitoring committee(SMC) will be responsible for safety oversight.

Conditions

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Diffuse Large B Cell Lymphoma Follicular Lymphoma Chronic Lymphocytic Leukemia Small Lymphocytic Leukemia B Cell Lymphoma Marginal Zone Lymphoma Waldenstrom Macroglobulinemia Peripheral T Cell Lymphoma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Treatment (BR101801): Phase Ia (dose escalation)

Patients will receive BR101801 capsules orally, QD in 28-day cycles. The regimen may be changed to BID dosing based on emerging data.

Group Type EXPERIMENTAL

BR101801 (Phase Ia)

Intervention Type DRUG

Phase Ia (dose escalation):25 mg capsules and 100 mg capsules Planned doses are 50, 100, 200, 325, and 450 mg.

Treatment (BR101801):Phase Ib (dose expansion)

• Subjects with PTCL NOS, PTCL AITL, Nodal PTCL with TFH and PTCL FTCL

Group Type EXPERIMENTAL

BR101801 (Phase Ib)

Intervention Type DRUG

Phase Ib (dose expansion):25 and 100 mg capsules Doses administered will be determined from Phase Ia data.

Interventions

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BR101801 (Phase Ia)

Phase Ia (dose escalation):25 mg capsules and 100 mg capsules Planned doses are 50, 100, 200, 325, and 450 mg.

Intervention Type DRUG

BR101801 (Phase Ib)

Phase Ib (dose expansion):25 and 100 mg capsules Doses administered will be determined from Phase Ia data.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Patients must sign an informed consent document
2. Female or male patients aged ≥ 18 years.
3. ECOG performance status ≤ 2.
4. Life expectancy more than 3 months.
5. Phase Ia:Patients with relapsed and/or refractory relapsed/refractory B-cell lymphoma, CLL/SLL, and PTCL diagnosed with World Health Organization (WHO) classification
6. Phase Ib: Subjects with PTCL NOS, PTCL AITL, Nodal PTCL with TFH and PTCL FTCL.
7. Patients have measurable disease based on the appropriate tumor type criteria( Phase Ib only)
8. Have a current need for systemic therapy, the assessment of the investigator.
9. An archival or fresh tumor tissue (ie, tissue block or series of at least 5 slides, up to 15 slides) is required and should be provided during the Screening Visit for Lymphoma subjects. Local review of pathology is required for study entry in Phase Ib only.
10. Phase Ia subjects should be prepared to undergo a fresh tumor biopsy during the study (tumor biopsies will be obtained from 1 to 2 subjects per cohort in Phase Ia).
11. Subject having laboratory values defined as:

* Creatinine clearance (measured or calculated per institutional standard practice) ≥ 60 mL/min. GFR can also be used in place of creatinine clearance.
* Total bilirubin \< 1.5 × ULN, except for subjects with Gilbert's syndrome who are excluded if total bilirubin \> 3.0 × ULN or direct bilirubin \< 1.5 × ULN.
* ALT \< 2.5 × ULN, except for subjects who have tumor involvement of the liver, who are included if ALT \< 5 × ULN.
* AST \< 2.5 × ULN, except for subjects that have tumor involvement of the liver, who are included if AST \< 5 × ULN.
* Absolute neutrophil count \> 1.0 × 109/L.
* Platelet count \> 75 × 109/L.
* Hemoglobin \> 8 g/dL.

Exclusion Criteria

1. Presence of overt leptomeningeal or active CNS metastases, or CNS metastases that require local CNS-directed therapy or increasing doses of corticosteroids within the prior 2 weeks. Patients with treated brain metastases should be neurologically stable and off steroids for at least 2 weeks before administration of any study treatment.
2. Impaired cardiac function or clinically significant cardiac disease
3. Patients with interstitial pneumonia or history of drug-induced interstitial pneumonia/pneumonitis.
4. Human immunodeficiency virus (HIV) infection.
5. Patients who are positive for hepatitis B surface antigen (HBsAg), hepatitis B core antibody (HBcAb), or hepatitis C virus antibody (HCVAb).
6. Chronic liver disease or chronic hepatitis
7. Any gastrointestinal disorders interfering with study drug absorption or are unable to swallow tablets or capsules.
8. Malignant disease, other than that being treated in this study.
9. Prior PI3K inhibitor will be accepted in the dose escalation part of the study (Phase Ia) only.
10. For patients with lymphoma:

* Systemic antineoplastic therapy (including cytotoxic chemotherapy, alfa-interferon \[INF\], and toxin immunoconjugates) or any experimental therapy within 3 weeks or 5 half lives, whichever is shorter, before the first dose of study treatment.
* Therapy with tyrosine kinase inhibitor within 5 half-lives before the first dose of study treatment.
* Unconjugated monoclonal antibody therapies \< 6 weeks before the first dose of study treatment.
11. Patients receiving systemic chronic steroid therapy or any immunosuppressive therapy (≥ 10 mg/day prednisone or equivalent).
12. Use of any live vaccines against infectious diseases within 4 weeks of initiation of study treatment.
13. Use of hematopoietic colony-stimulating growth factors, thrombopoietin mimetics, or erythroid-stimulating agents ≤ 2 weeks prior to start of study drug.
14. Patients with a history of stroke or having active neurological symptoms, with the exception of chronic conditions which, in the opinion of the neurologist, Investigator, and the Sponsor, would not impact ongoing neurologic assessments while on study treatment.
15. Active infection requiring systemic or antiviral antibiotic therapy.
16. Subjects with active CMV infection.
17. Subjects receiving moderate or potent CYP3A4 inhibitors or inducers and are unable to withdraw until 2 weeks or 5 times longer than the half-life, whichever is shorter, before the first dose of study treatment.
18. Major surgery within 2 weeks of the first dose of study treatment (mediastinoscopy, insertion of a central venous access device, and insertion of a feeding tube are not considered major surgery).
19. Radiotherapy within 2 weeks of the first dose of study treatment, except for palliative radiotherapy to a limited-field, such as for the treatment of bone pain or a focally painful tumor mass.
20. Presence of CTCAE ≥ Grade 2 toxicity (except alopecia, peripheral neuropathy, and ototoxicity, which are excluded if ≥ CTCAE Grade 3) due to prior cancer therapy.
21. Participation in an interventional, investigational study within 2 weeks or 5 half-lives, whichever is shorter, of the first dose of study treatment.
22. Any medical condition that would, in the Investigator's judgment, prevent the subject's participation in the clinical study due to safety concerns, compliance with clinical study procedures, or interpretation of study results.
23. Pregnant or lactating women, where pregnancy is defined as the state of a female after conception and until the termination of gestation, confirmed by a positive human chorionic gonadotropin laboratory test.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Boryung Pharmaceutical Co., Ltd

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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TM Kim, M.D, Ph.D

Role: PRINCIPAL_INVESTIGATOR

Seoul National University Hospital

SJ Kim, M.D, Ph.D

Role: PRINCIPAL_INVESTIGATOR

Samsung Medical Center

DH Yoon, M.D, Ph.D

Role: PRINCIPAL_INVESTIGATOR

Asan Medical Center

Jorge Chaves, M.D, Ph.D

Role: PRINCIPAL_INVESTIGATOR

Northwest Medical Specialities, PLLC

Emily Curran, M.D, Ph.D

Role: PRINCIPAL_INVESTIGATOR

University of Cincinnati

JS Kim, M.D, Ph.D

Role: PRINCIPAL_INVESTIGATOR

Severance Hospital, Yonsei University Health System

EY Lee, M.D, M.S

Role: PRINCIPAL_INVESTIGATOR

National Cancer Center

JO Lee, M.D, Ph.D

Role: PRINCIPAL_INVESTIGATOR

Seoul National University Bundang Hospital

DH Yang, M.D, Ph.D

Role: PRINCIPAL_INVESTIGATOR

Chonnam National University Hospital

WS Lee, M.D, Ph.D

Role: PRINCIPAL_INVESTIGATOR

Inje University

Locations

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Henry Ford Hospital

Detroit, Michigan, United States

Site Status

National Cancer Center

Goyang-si, Gyeonggi-do, South Korea

Site Status

Seoul National University Bundang Hospital

Seongnam-si, Gyeonggi-do, South Korea

Site Status

Chonnam National University Hwasun Hospital

Hwasun, Jeollanam-do, South Korea

Site Status

Inje University Busan Paik Hospital

Busan, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Seoul national university hospital

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Countries

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United States South Korea

Other Identifiers

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BR-101801-CT-101

Identifier Type: -

Identifier Source: org_study_id

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