A Study to Evaluate the Efficacy and Safety of BIIB093 in Participants With Brain Contusion

NCT ID: NCT03954041

Last Updated: 2024-11-27

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

92 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-10-06

Study Completion Date

2023-06-27

Brief Summary

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The primary objective is to determine if BIIB093 reduces brain contusion expansion by Hour 96 when compared to placebo.

The secondary objectives are to evaluate the effects of BIIB093 on acute neurologic status, functional outcomes, and treatment requirements, to further differentiate the mechanism of action of BIIB093 on contusion expansion by examining differential effects on hematoma and edema expansion, and to determine if BIIB093 improves survival at Day 90 when compared to placebo.

Detailed Description

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Conditions

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Brain Contusion

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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BIIB093 3 mg

Participants will be administered BIIB093 3 milligrams per day (mg/day) as a IV bolus followed by rapid and slow intravenous (IV) infusions for 96 hours.

Group Type EXPERIMENTAL

BIIB093

Intervention Type DRUG

Administered as specified in the treatment arm.

BIIB093 5 mg

Participants will be administered BIIB093 5 mg/day as a IV bolus followed by rapid and slow IV infusions for 96 hours.

Group Type EXPERIMENTAL

BIIB093

Intervention Type DRUG

Administered as specified in the treatment arm.

Placebo

Participants will be administered BIIB093 matching placebo as a IV bolus followed by rapid and slow IV infusions for 96 hours.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered as specified in the treatment arm.

Interventions

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BIIB093

Administered as specified in the treatment arm.

Intervention Type DRUG

Placebo

Administered as specified in the treatment arm.

Intervention Type DRUG

Other Intervention Names

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Glibenclamide CIRARA RP 1127

Eligibility Criteria

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Inclusion Criteria

* Clinical diagnosis of brain contusion with lesions within the supratentorial brain parenchyma totaling \>3 mL in volume per Investigator assessment of baseline non-contrast computed tomography scan (NCCT) at Screening.
* A score of 5 to 15 on the Glasgow Coma Scale (GCS).
* Functionally independent, in the opinion of the Investigator, prior to index head injury.

Exclusion Criteria

* In the judgment of the Investigator, participant is likely to have supportive care withdrawn within 24 hours.
* Indication for immediate evacuation of IPH or DC.
* Clinical signs of brainstem herniation, in the opinion of the Investigator.
* NCCT or magnetic resonance imaging (MRI) evidence of penetrating brain parenchyma. Cerebrospinal fluid leak in isolation is not exclusionary unless evidence of parenchymal penetration by an external force (e.g., blunt object, bullet, or depressed skull fracture).
* Any presence of midbrain or posterior fossa injury as assessed by imaging and clinical examination.
* Presence of concomitant spinal cord injury as assessed by imaging and clinical examination.
* Life-threatening or nonsurvivable polytrauma, per Investigator's judgment.
* Use of novel oral anticoagulants (NOACS; including direct thrombin inhibitors such as dabigatran, or Factor Xa inhibitors such as rivaroxaban or apixaban), in preceding 3 days prior to the injury, if known.
Minimum Eligible Age

18 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Remedy Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Remedy Pharmaceuticals

Locations

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Barrow Neurological Institute

Phoenix, Arizona, United States

Site Status

Scottsdale Healthcare Hospitals d/b/a HonorHealth

Scottsdale, Arizona, United States

Site Status

University of Arizona Medical Center

Tucson, Arizona, United States

Site Status

Yale New Haven Hospital

New Haven, Connecticut, United States

Site Status

Grady Memorial Hospital

Atlanta, Georgia, United States

Site Status

WellStar Medical Group Neurosurgery

Marietta, Georgia, United States

Site Status

Goodman Campbell Brain and Spine

Carmel, Indiana, United States

Site Status

University Medical Center New Orleans

New Orleans, Louisiana, United States

Site Status

University of Maryland Medical Center

Baltimore, Maryland, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Northwell Health

Manhattan, New York, United States

Site Status

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

Vidant Medical Center

Greenville, North Carolina, United States

Site Status

Wake Forest Baptist Health Sciences

Winston-Salem, North Carolina, United States

Site Status

University of Cincinnati College of Medicine

Cincinnati, Ohio, United States

Site Status

Miami Valley Hospital

Dayton, Ohio, United States

Site Status

ProMedica Toledo Hospital

Toledo, Ohio, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Site Status

Rhode Island Hospital

East Providence, Rhode Island, United States

Site Status

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status

The University of Texas Health Science Center at Houston

Houston, Texas, United States

Site Status

University of Utah Health

Salt Lake City, Utah, United States

Site Status

Virginia Commonwealth University Medical Center

Richmond, Virginia, United States

Site Status

CHU de Brest - Hôpital de la Cavale Blanche

Brest, Finistere, France

Site Status

Hopital Caremeau

Nîmes, Gard, France

Site Status

Groupe Hospitalier Pellegrin - Hôpital Pellegrin

Bordeaux, Gironde, France

Site Status

CHU Rennes - Hôpital Pontchaillou

Rennes, Ille Et Vilaine, France

Site Status

CHU Clermont Ferrand - Hopital Gabriel Montpied

Clermont-Ferrand, Puy De Dome, France

Site Status

CHU Amiens - Hopital Sud

Amiens, Somme, France

Site Status

Universitaetsklinikum Heidelberg

Heidelberg, Baden-Wurttemberg, Germany

Site Status

Neurologische Klinik Bad Neustadt/Saale

Bad Neustadt/Saale, Bavaria, Germany

Site Status

Universitaetsmedizin Goettingen

Göttingen, Lower Saxony, Germany

Site Status

Universitaetsklinikum Schleswig-Holstein - Campus Kiel

Kiel, Schleswig, Germany

Site Status

Rabin MC

Petah Tikva, Central District, Israel

Site Status

Health Corporation of Galilee Medical Center

Naharya, Northern District, Israel

Site Status

Chaim Sheba Medical Center

Ramat Gan, Tel Aviv, Israel

Site Status

Rambam Health Care Center

Haifa, , Israel

Site Status

Shaare Zedek Medical Center

Jerusalem, , Israel

Site Status

Hadassah

Jerusalem, , Israel

Site Status

Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status

Azienda Ospedaliero Universitaria Ospedali Riuniti di Ancona

Torrette, Ancona, Italy

Site Status

ASST Monza - Ospedale San Gerardo di Monza

Monza Brianza, Milano, Italy

Site Status

Azienda Ospedaliero Universitaria di Parma

Pama, Parma, Italy

Site Status

Azienda Socio Sanitaria Territoriale Niguarda (Grande Ospedale Metropolitano Niguarda)

Milan, , Italy

Site Status

Ospedale Maggiore di Novara

Novara, , Italy

Site Status

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Roma, , Italy

Site Status

Azienda Ospedaliero-Universitaria Città della Salute e della Scienza di Torino

Torino, , Italy

Site Status

Kimitsu Chuo Hospital

Kisarazu-Shi, Chiba, Japan

Site Status

Kobe City Hospital Organization Kobe City Medical Center General Hospital

Kobe, Hyōgo, Japan

Site Status

Nara Medical University Hospital

Kashihara-shi, Nara, Japan

Site Status

Rinku General Medical Center

Izumisano, Osaka, Japan

Site Status

Nippon Medical School Hospital

Bunkyō City, Tokyo-to, Japan

Site Status

Yamaguchi University Hospital

Ube-Shi, Yamaguchi, Japan

Site Status

Hospital Universitari Son Espases

Palma de Mallorca, Balearic Islands, Spain

Site Status

Complejo Hospitalario Universitario de Santiago

Santiago de Compostela, La Coruna, Spain

Site Status

Hospital Alvaro Cunqueiro

Vigo, Pontevedra, Spain

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitari de Bellvitge

Barcelona, , Spain

Site Status

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Countries

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United States France Germany Israel Italy Japan Spain

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2018-003858-24

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

252BN201

Identifier Type: -

Identifier Source: org_study_id

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