A Study of Tepotinib Plus Osimertinib in Osimertinib Relapsed MET Amplified NSCLC (INSIGHT 2)

NCT ID: NCT03940703

Last Updated: 2025-12-12

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

140 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-09-19

Study Completion Date

2026-05-01

Brief Summary

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This study was to assess the antitumor activity, safety, tolerability, and pharmacokinetics (PK) of the Mesenchymal-epithelial Transition Factor (MET) inhibitor tepotinib combined with the 3rd generation EGFR inhibitor osimertinib in participants with advanced or metastatic non-small cell lung cancer (NSCLC).

Detailed Description

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Conditions

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Non-small Cell Lung Cancer

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Tepotinib and Osimertinib

Participants received a single oral dose of Tepotinib 500 milligrams (mg) followed by Omisertinib 80 mg once daily until disease progression, death, adverse event leading to discontinuation, study withdrawal or consent withdrawal.

Group Type EXPERIMENTAL

Tepotinib

Intervention Type DRUG

Participants were administered with Tepotinib orally once daily at a dose of 500 mg.

Osimertinib

Intervention Type DRUG

Participants received Osimertinib at a dose of 80 mg orally once daily.

Tepotinib Mono-therapy

Participants received a single oral dose of Tepotinib 500 mg until disease progression, death, adverse event leading to discontinuation, study withdrawal or consent withdrawal.

Group Type EXPERIMENTAL

Tepotinib

Intervention Type DRUG

Participants were administered with Tepotinib orally once daily at a dose of 500 mg.

Interventions

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Tepotinib

Participants were administered with Tepotinib orally once daily at a dose of 500 mg.

Intervention Type DRUG

Osimertinib

Participants received Osimertinib at a dose of 80 mg orally once daily.

Intervention Type DRUG

Other Intervention Names

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Tagrisso®

Eligibility Criteria

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Inclusion Criteria

* Locally advanced or metastatic Non-small Cell Lung Cancer (NSCLC) histology (confirmed by either histology or cytology) with documented activating Epidermal Growth Factor Receptor (EGFR) mutation
* Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1 and a minimum life expectancy of 12 weeks
* Acquired resistance on previous first-line osimertinib. Participants must meet both of the following 2 criteria:
* Radiological documentation of disease progression on first-line osimertinib
* Objective clinical benefit documented during previous osimertinib therapy, defined by either partial or complete radiological response, or durable stable disease (SD) (SD should last greater than (\>) 6 months after initiation of osimertinib
* Have received only first-line osimertinib as a prior line of therapy in the non curative advanced or metastatic NSCLC setting
* MET amplification as determined by either FISH testing (central or local) on tumor tissue (TBx) or central blood-based next generation sequencing (LBx). Tumor and blood samples must be collected following progression on prior first-line osimertinib at Prescreening
* Submission of tumor tissue and blood sample obtained after progression on first-line osimertinib, is mandatory for all patients for MET amplification testing
* Submission of tumor tissue during Prescreening or Screening is mandatory for patients with tumor tissue tested by local FISH, to confirm MET amplification status. Central confirmation is not mandated prior to the start of study treatment

Exclusion Criteria

* Spinal cord compression or brain metastasis unless asymptomatic, stable or not requiring steroids for at least 2 weeks prior to start of study intervention
* Any unresolved toxicity Grade 2 or more according to National cancer institute common terminology criteria for adverse events( NCI-CTCAE) version 5, from previous anticancer therapy with the exception of alopecia
* Inadequate hematological, liver and renal function
* Impaired cardiac function
* History of interstitial lung disease(ILD) or interstitial pneumonitis including radiation pneumonitis that required steroid treatment
* Hypertension uncontrolled by standard therapies (not stabilized to \< 150/90 millimeter of mercury (mmHg)
* Contraindication to the administration of osimertinib
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck KGaA, Darmstadt, Germany

INDUSTRY

Sponsor Role collaborator

EMD Serono Research & Development Institute, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Responsible

Role: STUDY_DIRECTOR

Merck Healthcare KGaA, Darmstadt, Germany, an affiliate of Merck KGaA, Darmstadt, Germany

Locations

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Yuma Regional Medical Center

Yuma, Arizona, United States

Site Status

Compassionate Care Research Group Inc - Edinger Medical Group, Inc.

Fountain Valley, California, United States

Site Status

Memorial Care

Long Beach, California, United States

Site Status

Ventura County Hematology Oncology Specialists

Oxnard, California, United States

Site Status

Innovative Clinical Research Institute

Whittier, California, United States

Site Status

Eastern Connecticut Hematology & Oncology Associates

Norwich, Connecticut, United States

Site Status

Holy Cross

Fort Lauderdale, Florida, United States

Site Status

Memorial Healthcare System

Hollywood, Florida, United States

Site Status

Cancer Specialists of North Florida

Jacksonville, Florida, United States

Site Status

Ocala Oncology

Ocala, Florida, United States

Site Status

University Cancer and Blood Center

Athens, Georgia, United States

Site Status

Hawaii Cancer Care

Honolulu, Hawaii, United States

Site Status

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

Fort Wayne Medical Oncology and Hematology

Fort Wayne, Indiana, United States

Site Status

Community Health Network

Indianapolis, Indiana, United States

Site Status

Beacon Health

South Bend, Indiana, United States

Site Status

Norton Cancer Institute

Louisville, Kentucky, United States

Site Status

Pontchartrain

Hammond, Louisiana, United States

Site Status

Medstar Franklin Square Clinical Research Center

Baltimore, Maryland, United States

Site Status

The Center for Cancer & Blood Disorders - Maryland

Bethesda, Maryland, United States

Site Status

Frederick Health- James M Stockman Cancer Institute

Frederick, Maryland, United States

Site Status

Boston Medical Center - Dept. Hematology/Oncology

Boston, Massachusetts, United States

Site Status

Southcoast Center for Cancer Care

Fairhaven, Massachusetts, United States

Site Status

Sparrow Hospital Herbert - Herman Cancer Center

Lansing, Michigan, United States

Site Status

Central Care Cancer Center (CCCC)

Bolivar, Missouri, United States

Site Status

St. Louis Cancer Care, LLP

Bridgeton, Missouri, United States

Site Status

Mosaic Life Care

Saint Joseph, Missouri, United States

Site Status

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, United States

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New Jersey Cancer Care and Blood Disorders

Belleville, New Jersey, United States

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Summit Medical Group

Florham Park, New Jersey, United States

Site Status

NYU Langone Clinical Cancer Center - NYU Langone Medical Center

New York, New York, United States

Site Status

NYU Langone Clinical Cancer Center - NYU Langone Medical Cente

New York, New York, United States

Site Status

Weill Cornell Medical College - Gastroenterology

New York, New York, United States

Site Status

Southeastern Medical Oncology Center

Goldsboro, North Carolina, United States

Site Status

University Hospitals Seidman

Cleveland, Ohio, United States

Site Status

OhioHealth

Columbus, Ohio, United States

Site Status

Oklahoma Cancer Specialists and Research Institute

Tulsa, Oklahoma, United States

Site Status

Oregon Oncology Specialists

Salem, Oregon, United States

Site Status

Gettysburg Cancer Center

Gettysburg, Pennsylvania, United States

Site Status

Sanford Health

Sioux Falls, South Dakota, United States

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Avera Cancer Institute

Sioux Falls, South Dakota, United States

Site Status

Baptist Cancer Center

Memphis, Tennessee, United States

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Tennessee Oncology

Nashville, Tennessee, United States

Site Status

Mary Crowley Cancer Research

Dallas, Texas, United States

Site Status

University of Texas MD Anderson Cancer Center - Unit 432 Thoracic Head and Neck Medical Oncology

Houston, Texas, United States

Site Status

Community Cancer Trials of Utah

Ogden, Utah, United States

Site Status

Utah Cancer Specialists

Salt Lake City, Utah, United States

Site Status

Hematology Oncology Associates of Fredericksburg

Fredericksburg, Virginia, United States

Site Status

Northwest Medical Specialties

Tacoma, Washington, United States

Site Status

UZ Antwerpen - Department of Oncology

Edegem, , Belgium

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UZ Leuven

Gasthuisberg, , Belgium

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AZ Delta

Roeselare, , Belgium

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Beijing Hospital

Beijing, , China

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Peking Union Medical College Hospital

Beijing, , China

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Peking University Cancer Hospital

Beijing, , China

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Jilin Cancer Hospital - Oncology

Changchun, , China

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The First Hospital of Jilin University

Changchun, , China

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Hunan Cancer Hospital

Changsha, , China

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West China Hospital, Sichuan University

Chengdu, , China

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Fujian Cancer Hospital

Fuzhou, , China

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Guangdong General Hospital

Guangzhou, , China

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The First Affiliated Hospital, Zhejiang University

Hangzhou, , China

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Zhejiang Cancer Hospital

Hangzhou, , China

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Affiliated Tumor Hospital of Harbin Medical University

Harbin, , China

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Anhui Chest Hospital

Hefei, , China

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Linyi Tumor Hospital

Linyi, , China

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Jiangsu Province Hospital

Nanjing, , China

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Shanghai Cancer Hospital, Fudan University

Shanghai, , China

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Shanghai Chest Hospital

Shanghai, , China

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Liaoning Cancer Hospital & Institute

Shenyang, , China

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The Affiliated Cancer Hospital of Xinjiang Medical university

Ürümqi, , China

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Hubei Cancer Hospital

Wuhan, , China

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Union Hospital Tongji Medical College Huazhong University of Science and Technology

Wuhan, , China

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Centre Francois Baclesse - Service d'Oncologie Medicale

Caen, , France

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Centre Hospitalier Intercommunal de Créteil - Service de Pneumologie

Créteil, , France

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CHU Limoges - Hôpital Dupuytren - Unite d'Oncologie Thoracique et Cutanée

Limoges, , France

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Centre Léon Bérard

Lyon, , France

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Hopital Albert Calmette - CHU Lille - service de pneumologie et immuno allergologie

Nord, , France

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Hopital Tenon - service pneumologie

Paris, , France

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Hospital Cochin Service, Service de Pneumologie et Mucoviscidose

Paris, , France

Site Status

Groupe Hospitalier Sud - Hôpital Haut-Lévêque - Maison du Ha

Pessac, , France

Site Status

CHU de Toulouse - Hôpital Larrey - Service de Pneumologie et Oncologie Pneumologique

Toulouse, , France

Site Status

Universitaetsklinikum Koeln - Innere Medizin I, Onkologie, Haematologie

Cologne, , Germany

Site Status

Universitaetsklinikum Carl Gustav Carus TU Dresden

Dresden, , Germany

Site Status

Asklepios Fachkliniken Muenchen-Gauting - Abteilung internistische Onkologie

Gauting, , Germany

Site Status

Universitaetsklinikum Giessen und Marburg GmbH Standort Giessen

Giessen, , Germany

Site Status

Universitaetsmedizin Goettingen

Göttingen, , Germany

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Evangelisches Krankenhaus Hamm gGmbH

Hamm, , Germany

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Evangelisches Krankenhaus Hamm GmbH

Hamm, , Germany

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Thoraxklinik-Heidelberg gGmbH

Heidelberg, , Germany

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Staedtisches Krankenhaus Kiel

Kiel, , Germany

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POIS Leipzig GbR

Leipzig, , Germany

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Universitaetsklinikum Schleswig-Holstein - Campus Luebeck

Lübeck, , Germany

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Pius-Hospital Oldenburg - Klinik f. Haematologie und Onkologie

Oldenburg, , Germany

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Missionsärztliche Klinik

Würzburg, , Germany

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Queen Elizabeth Hospital - Department of Medicine

Hong Kong, , Hong Kong

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The University of Hong Kong

Hong Kong, , Hong Kong

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The Chinese University of Hong Kong - Emergency Medicine

Shatin, , Hong Kong

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Fondazione Policlinico Universitario Agostino Gemelli IRCCS - UOC Oncologia Medica

Lazio, , Italy

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IEO Istituto Europeo di Oncologia

Milan, , Italy

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Azienda Socio Sanitaria Territoriale di Monza (Presidio San Gerardo) - U.O Oncologia Medica

Monza, , Italy

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Ospedale Monaldi

Napoli, , Italy

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IOV - Istituto Oncologico Veneto IRCCS - Oncologia Medica 2

Padua, , Italy

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AO Ospedali Riuniti Cervello - Presidio Villa Sofia - U.O.S. di Neuroimmunologia

Palermo, , Italy

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Azienda Ospedaliero Universitaria Pisana - U.O. Pneumologia II

Pisa, , Italy

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Istituto Nazionale Tumori Regina Elena IRCCS - S.C. Oncologia Medica B

Roma, , Italy

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Istituto Clinico Humanitas

Rozzano, , Italy

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Azienda Socio Sanitaria Territoriale Sette Laghi (Presidio Ospedale di Circolo e Fondazione Macchi) - Oncologia Medica

Varese, , Italy

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Azienda Ospedaliera Universitaria Integrata Verona (Ospedale Borgo Roma) - U.O.C. Oncologia

Verona, , Italy

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Hamamatsu University School of Medicine, University Hospital - Dept of Respiratory Medicine

Hamamatsu, , Japan

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Saitama Cancer Center

Kitaadachi-gun, , Japan

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Kurume University Hospital

Kurume-shi, , Japan

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Nagoya University Hospital - Dept of Respiratory Medicine

Nagoya, , Japan

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Niigata Cancer Center Hospital - Dept of Internal Medicine

Niigata, , Japan

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Hyogo College of Medicine Hospital - Dept of Respiratory Medicine

Nishinomiya-shi, , Japan

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Okayama University Hospital - Dept of Respiratory Medicine/Allergy

Okayama, , Japan

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Osaka City General Hospital

Osaka, , Japan

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Kindai University Hospital

Osakasayama-shi, , Japan

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NHO Yamaguchi - Ube Medical Center

Ube-shi, , Japan

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Kanagawa Cancer Center - Dept of Respiratory Medicine

Yokohama, , Japan

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Pantai Hospital Kuala Lumpur

Kuala Lumpur, , Malaysia

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University Malaya Medical Centre

Kuala Lumpur, , Malaysia

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Beacon International Specialist Centre Sdn Bhd

Kuala Selangor, , Malaysia

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Hospital Tengku Ampuan Afzan

Kuantan, , Malaysia

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Hospital Umum Sarawak

Kuching, , Malaysia

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Sunway Medical Centre

Petaling Jaya, Selangor, , Malaysia

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Hospital Pulau Pinang - Clinic Respiratory

Pulau Pinang, , Malaysia

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The Netherlands Cancer Institute

Amsterdam, , Netherlands

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Universitair Medisch Centrum Groningen - Department of Internal Medicine

Groningen, , Netherlands

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Maastricht University Medical Center - Dept of Medical Oncology

Maastricht, , Netherlands

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SBHI "Krasnoyarsk Regional Oncology Dispensary n.a. A.I. Kryzhanovsky"

Krasnoyarsk, , Russia

Site Status

"VitaMed" LLC

Moscow, , Russia

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LLC "Tonus"

Nizniy Novgorod, , Russia

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BHI of Omsk region "Clinical Oncology Dispensary"

Omsk, , Russia

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LLC "ClinicaUZI4D"

Pyatigorsk, , Russia

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FBI "Scientific Research Institute of Oncology n. a. N. N. Petrov"

Saint Petersburg, , Russia

Site Status

Pavlov First Saint Petersburg State Medical University - Research Institute of Pulmunology

Saint Petersburg, , Russia

Site Status

Icon Cancer Centre

Connexion, , Singapore

Site Status

National Cancer Centre - Medical Oncology Pharmacy

Singapore, , Singapore

Site Status

Tan Tock Seng Hospital - CTRU/OCS, Research

Singapore, , Singapore

Site Status

National Cancer Center

Goyang-si, , South Korea

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Chonnam National University Hwasun Hospital

Hwasun-gun, , South Korea

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Seoul National University Bundang Hospital

Seongnam-si, , South Korea

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Asan Medical Center

Seoul, , South Korea

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Korea University Anam Hospital

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

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Seoul National University Hospital

Seoul, , South Korea

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The Catholic University of Korea, Seoul St. Mary's Hospital

Seoul, , South Korea

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Ulsan University Hospital

Ulsan, , South Korea

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ICO Badalona - Hospital Germans Trias i Pujol - Servicio de Oncologia Medica

Badalona, , Spain

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Hospital del Mar - Servicio de Oncologia

Barcelona, , Spain

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Hospital Universitari Dexeus - Servicio de Oncologia Medica

Barcelona, , Spain

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Hospital Universitari Quiron Dexeus - Servicio de Oncologia Medica

Barcelona, , Spain

Site Status

Hospital Universitari Vall d'Hebron - Dept of Oncology

Barcelona, , Spain

Site Status

ICO l´Hospitalet - Hospital Duran i Reynals - Servicio de Oncologia

L'Hospitalet de Llobregat, , Spain

Site Status

Hospital Universitario Materno-Infantil de Canarias - Servicio de Oncologia

Las Palmas de Gran Canaria, , Spain

Site Status

Hospital Universitario HM Madrid Sanchinarro - Servicio de Oncologia

Madrid, , Spain

Site Status

Hospital Regional Universitario de Malaga

Málaga, , Spain

Site Status

Hospital Universitari Son Espases - Servicio de Oncologia Medica

Palma, , Spain

Site Status

Hospital Universitario Quiron Madrid - Unidad Integral de Oncologia

Pozuelo de Alarcón, , Spain

Site Status

Hospital Universitario Virgen Macarena - Servicio de Oncologia

Seville, , Spain

Site Status

Hospital Universitari i Politecnic La Fe - Servicio de Oncologia Medica

Valencia, , Spain

Site Status

Kaohsiung Chang Gung Memorial Hospital

Kaohsiung City, , Taiwan

Site Status

China Medical University Hospital

Taichung, , Taiwan

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Taichung Veterans General Hospital

Taichung, , Taiwan

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Chi Mei Medical Center, Liou Ying

Tainan, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Tri-Service General Hospital

Taipei, , Taiwan

Site Status

Siriraj Hospital

Bangkoknoi, , Thailand

Site Status

Songklanagarind Hospital

Hat Yai, , Thailand

Site Status

Maharaj Nakorn Chiang Mai Hospital

Muang, , Thailand

Site Status

King Chulalongkorn Memorial Hospital

Pathumwan, , Thailand

Site Status

Bach Mai Hospital

Hanoi, , Vietnam

Site Status

K Hospital

Hanoi, , Vietnam

Site Status

National Lungs Hospital

Hanoi, , Vietnam

Site Status

Cho Ray Hospital

Ho Chi Minh City, , Vietnam

Site Status

HCMC Oncology Hospital

Ho Chi Minh City, , Vietnam

Site Status

Pham Ngoc Thach Hospital

Ho Chi Minh City, , Vietnam

Site Status

Countries

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United States Belgium China France Germany Hong Kong Italy Japan Malaysia Netherlands Russia Singapore South Korea Spain Taiwan Thailand Vietnam

References

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F Smit E, Dooms C, Raskin J, Nadal E, Tho LM, Le X, Mazieres J, S Hin H, Morise M, W Zhu V, Tan D, H Holmberg K, Ellers-Lenz B, Adrian S, Brutlach S, Schumacher KM, Karachaliou N, Wu YL. INSIGHT 2: a phase II study of tepotinib plus osimertinib in MET-amplified NSCLC and first-line osimertinib resistance. Future Oncol. 2022 Mar;18(9):1039-1054. doi: 10.2217/fon-2021-1406. Epub 2021 Dec 17.

Reference Type BACKGROUND
PMID: 34918545 (View on PubMed)

Wu YL, Guarneri V, Voon PJ, Lim BK, Yang JJ, Wislez M, Huang C, Liam CK, Mazieres J, Tho LM, Hayashi H, Nhung NV, Chia PL, de Marinis F, Raskin J, Zhou Q, Finocchiaro G, Le AT, Wang J, Dooms C, Kato T, Nadal E, Hin HS, Smit EF, Wermke M, Tan D, Morise M, O'Brate A, Adrian S, Pfeiffer BM, Stroh C, Juraeva D, Strotmann R, Goteti K, Berghoff K, Ellers-Lenz B, Karachaliou N, Le X, Kim TM; INSIGHT 2 investigators. Tepotinib plus osimertinib in patients with EGFR-mutated non-small-cell lung cancer with MET amplification following progression on first-line osimertinib (INSIGHT 2): a multicentre, open-label, phase 2 trial. Lancet Oncol. 2024 Aug;25(8):989-1002. doi: 10.1016/S1470-2045(24)00270-5.

Reference Type DERIVED
PMID: 39089305 (View on PubMed)

Hallick J, Baird AM, Falchook G, Le X, Hong D, Viteri S, Raskin J, Reinmuth N, Vlassak S, Militaru M, Paik PK. Plain language summary of the development of tepotinib: a treatment for a subtype of non-small cell lung cancer called MET exon 14 skipping. Future Oncol. 2023 Mar;19(10):683-696. doi: 10.2217/fon-2022-1035. Epub 2023 Mar 31.

Reference Type DERIVED
PMID: 36999526 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://medical.emdserono.com/en_US/home.html

US Medical Information website, Medical Resources

https://www.clinicaltrials.targeting-met.com/en

Targeting MET Clinical Trial Program

Other Identifiers

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2019-001538-33

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2024-512005-87-00

Identifier Type: CTIS

Identifier Source: secondary_id

MS200095_0031

Identifier Type: -

Identifier Source: org_study_id

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