A Study of RVT-1201 in Patients With Pulmonary Arterial Hypertension (ELEVATE 1)

NCT ID: NCT03924154

Last Updated: 2020-03-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

3 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-08-01

Study Completion Date

2020-02-24

Brief Summary

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This is an exploratory Phase 2a, randomized, double-blind, placebo-controlled, parallel-group, multicenter study to evaluate the safety, tolerability, pharmacokinetics, and pharmacodynamic effects of RVT-1201 in patients with pulmonary arterial hypertension (PAH).

Detailed Description

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This is an exploratory Phase 2a, randomized, double-blind, placebo-controlled, parallel-group, multicenter study to evaluate the safety, tolerability, pharmacokinetics, and pharmacodynamic effects of RVT-1201 in patients with pulmonary arterial hypertension (PAH).

Study participation for each patient will last approximately 3 months and will consist of a screening period (up to 28 days in duration), a baseline period (day 1, pre-dose), a 6-week treatment period, and a 2-week follow-up period.

The study will enroll approximately 36 patients at approximately 20 centers across the United States and Canada.

Conditions

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Pulmonary Arterial Hypertension

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Following screening assessments, PAH patients who meet all entrance criteria will be randomly assigned to receive one of the following treatments in a ratio of 2:1:

* Arm 1 (n=24) - RVT-1201 Treatment: RVT-1201 immediate-release tablets will be administered orally, at a dose of 600 mg twice daily (BID), for a total of 6 weeks in addition to the patient's current standard of care (SOC) medication(s) for PAH.
* Arm 2 (n=12) - Placebo Treatment: Matching placebo tablets will be administered orally, at a dose of 600 mg twice daily (BID), for a total of 6 weeks in addition to the patient's current SOC medication(s) for PAH.

Participants will be followed in face-to-face visits with trial personnel every 2 weeks for 8 weeks (6 weeks of treatment plus a 2-week follow-up), with an additional phone call at Week 1, to assess drug effects and monitor safety during their treatments.
Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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RVT-1201

RVT-1201 600 mg immediate-release tablet, administered orally twice daily with food for 6 weeks, in addition to the patient's current standard of care medication(s) for PAH (n=24 \[Anticipated\])

Group Type EXPERIMENTAL

RVT-1201

Intervention Type DRUG

RVT-1201 600 mg immediate-release tablet

Placebo

Matching placebo tablet, administered orally twice daily with food for 6 weeks, in addition to the patient's current standard of care medication(s) for PAH (n=12 \[Anticipated\])

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Inactive pill manufactured to mimic RVT-1201 600 mg immediate-release tablet

Interventions

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RVT-1201

RVT-1201 600 mg immediate-release tablet

Intervention Type DRUG

Placebo

Inactive pill manufactured to mimic RVT-1201 600 mg immediate-release tablet

Intervention Type DRUG

Other Intervention Names

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rodatristat ethyl Placebo (for RVT-1201)

Eligibility Criteria

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Inclusion Criteria

* Symptomatic PAH belonging to one of the following types:

* Idiopathic
* Heritable
* Drug- or toxin- induced
* Associated with one of the following: connective tissue disease or congenital heart disease
* World Health Organization (WHO) Functional Class (FC) II or III
* PAH diagnosed by right heart cardiac catheterization prior to Screening
* Receiving standard of care treatment for PAH with oral monotherapy or dual therapy for at least 12 weeks prior to Screening at a dose which has been stable for at least 8 weeks prior to Screening
* If on a diuretic, dose must be stable for at least 4 weeks prior to Screening, with no changes anticipated during study participation
* 6-Minute Walk Distance (6MWD) between 150 and 500 meters at Screening and Baseline visits
* Plasma N-terminal pro B-type natriuretic peptide (NT-proBNP) level ≥ 300 pg/mL at Screening
* Ability and willingness to give written informed consent and to comply with the requirements of the study

Exclusion Criteria

* PAH associated with human immunodeficiency virus (HIV) infection, portal hypertension or schistosomiasis
* Other types of pulmonary hypertension (PH):

* Pulmonary hypertension due to left heart disease (WHO PH Group 2)
* Pulmonary hypertension due to lung diseases and/or hypoxia (WHO PH Group 3)
* Chronic thromboembolic pulmonary hypertension (WHO PH Group 4)
* Pulmonary hypertension with unclear multifactorial mechanisms (WHO PH Group 5)
* Hospitalization for pulmonary hypertension within 12 weeks of screening
* Cardiopulmonary rehabilitation program based on exercise (planned, or started ≤ 12 weeks prior to Screening)
* Prostanoid or prostacyclin receptor agonist therapy within 12 weeks of screening
* Evidence of left-sided heart disease
* If Pulmonary function tests were done prior to screening, Pulmonary function tests demonstrate obstructive or restrictive lung disease
* Use of telotristat (Xermelo®) within the last 6 months
* Use of any investigational drug within 30 days or five half-lives (whichever is longer) prior to Screening, or 90 days if an investigational drug for PAH
* Have uncontrolled atrial fibrillation (AFib) or other uncontrolled arrhythmias
* Body mass index (BMI) \>45 kg/m2
* Women of childbearing potential who are pregnant, planning to become pregnant, or lactating or female/male patients unwilling to use effective contraception
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Altavant Sciences, Inc.

UNKNOWN

Sponsor Role collaborator

PPD Development, LP

INDUSTRY

Sponsor Role collaborator

Altavant Sciences GmbH

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Ed Parsley, DO

Role: STUDY_DIRECTOR

Altavant Sciences

Locations

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Pulmonary Associates, PA

Phoenix, Arizona, United States

Site Status

University of California Davis Medical Center

Sacramento, California, United States

Site Status

SBPA Research LLC

Santa Barbara, California, United States

Site Status

University of Colorado

Aurora, Colorado, United States

Site Status

George Washington Medical Faculty Associates - Pulmonary Hypertension Program

Washington D.C., District of Columbia, United States

Site Status

University of Florida

Gainesville, Florida, United States

Site Status

San Marcus Research Clinic, Inc.

Miami Lakes, Florida, United States

Site Status

Central Florida Pulmonary Group, P.A.

Orlando, Florida, United States

Site Status

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

Kentuckiana Pulmonary Research Center

Louisville, Kentucky, United States

Site Status

Louisiana State University Health Sciences Center

New Orleans, Louisiana, United States

Site Status

Boston Children's Hospital

Boston, Massachusetts, United States

Site Status

Baystate Medical Center

Springfield, Massachusetts, United States

Site Status

Pulmonary Research Institute of Southeast Michigan

Farmington Hills, Michigan, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

University of Texas Health Science Center at Houston, McGovern Medical School

Houston, Texas, United States

Site Status

University of Calgary

Calgary, Alberta, Canada

Site Status

University of Alberta

Edmonton, Alberta, Canada

Site Status

London Health Sciences Centre

London, Ontario, Canada

Site Status

Countries

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United States Canada

Other Identifiers

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RVT-1201-2001

Identifier Type: -

Identifier Source: org_study_id

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