Study of Sacituzumab Govitecan-hziy Versus Treatment of Physician's Choice in Participants With HR+/HER2- Metastatic Breast Cancer

NCT ID: NCT03901339

Last Updated: 2024-10-21

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

543 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-05-08

Study Completion Date

2023-10-20

Brief Summary

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The primary objective of this study is to assess and compare the efficacy and safety of sacituzumab govitecan-hzi versus treatment of physician's choice (TPC) in participants with hormonal receptor-positive (HR+) human epidermal growth factor receptor 2 (HER2-) negative metastatic breast cancer (MBC).

Detailed Description

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Conditions

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Metastatic Breast Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Sacituzumab Govitecan-hziy

Participants will receive sacituzumab govitecan-hziy 10 mg/kg via intravenous (IV) injection administered on Day 1 and Day 8 of a 21-day cycle.

Group Type EXPERIMENTAL

Sacituzumab Govitecan-hziy

Intervention Type DRUG

Administered intravenously

Treatment of Physician's Choice (TPC)

Participants will receive TPC determined prior to randomization from one of the following single-agent treatment:

Dosing per National Comprehensive Cancer Network (NCCN) guidelines (with dose modifications for if toxic)

* Eribulin: 1.4 mg/m\^2 for North American sites, 1.23 mg/m\^2 for European sites) via IV on Days 1 and 8 of a 21-day cycle
* Capecitabine: 1000-1250 mg/m\^2 orally twice daily for 2 weeks followed by a 1-week rest period given as a 21-day cycle
* Gemcitabine: 800-1200 mg/m\^2 via IV on Days 1, 8, and 15 of each 28-day cycle or per institution
* Vinorelbine: 25 mg/m\^2 via IV on Day 1 weekly cycle per institution

Group Type ACTIVE_COMPARATOR

Eribulin

Intervention Type DRUG

Administered intravenously per NCCN guidelines

Capecitabine

Intervention Type DRUG

Administered orally per NCCN guidelines

Gemcitabine

Intervention Type DRUG

Administered intravenously per NCCN guidelines

Vinorelbine

Intervention Type DRUG

Administered intravenously per NCCN guidelines

Interventions

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Sacituzumab Govitecan-hziy

Administered intravenously

Intervention Type DRUG

Eribulin

Administered intravenously per NCCN guidelines

Intervention Type DRUG

Capecitabine

Administered orally per NCCN guidelines

Intervention Type DRUG

Gemcitabine

Administered intravenously per NCCN guidelines

Intervention Type DRUG

Vinorelbine

Administered intravenously per NCCN guidelines

Intervention Type DRUG

Other Intervention Names

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IMMU-132 GS-0132

Eligibility Criteria

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Inclusion Criteria

* Documented evidence of hormone receptor-positive human epidermal growth factor receptor 2 negative (HER2-negative) (hormonal receptor-positive (HR+)/HER2-) metastatic breast cancer (MBC) confirmed.
* Refractory to or relapsed after at least 2, and no more than 4, prior systemic chemotherapy regimens for metastatic disease:

* At least 1 taxane in any setting.
* At least 1 prior anticancer hormonal treatment in any setting.
* At least 1 cyclin-dependent kinase inhibitor 4/6 in any setting.
* Eligible for one of the chemotherapy options listed in the TPC arm.
* Documented disease progression after the most recent therapy.
* Adequate bone marrow function (hemoglobin ≥ 9 g/dL, absolute neutrophil count (ANC) ≥ 1,500 per mm\^3, platelets ≥ 100,000 per mm\^3).
* Adequate renal function: calculated creatinine clearance ≥ 30 mL/minute according to the Cockcroft and Gault formula .
* Adequate liver function (bilirubin ≤ 1.5 institutional upper limit of normal (IULN), or ≤ 3 IULN for individuals with documented Gilbert's syndrome, aspartate aminotransferase (AST) and Alanine aminotransferase (ALT) ≤ 2.5 x IULN (in the case of liver metastases ≤ 5.0 x IULN)).
* Females must not be lactating or pregnant at Screening or Baseline (as documented by a negative beta human chorionic gonadotropin (ß-hCG)).

Exclusion Criteria

* Previous treatment with topoisomerase 1 Inhibitors as a free form or as other formulations.
* History of significant cardiovascular disease or clinically significant electrocardiogram (ECG) abnormality.
* Active serious infection requiring antibiotics.
* Any medical or other condition which, in the opinion of the Investigator, causes the individual to be medically unfit to receive sacituzumab govitecan or unsuitable for any reason.
* Locally advanced MBC (stage IIIc) in individuals who are candidates for curative intent therapy at the time of study enrollment.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gilead Study Director

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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HonorHealth Research Institute

Avondale, Arizona, United States

Site Status

Arizona Oncology Associates, PC

Tucson, Arizona, United States

Site Status

Highlands Oncology Group

Fayetteville, Arkansas, United States

Site Status

University of California, San Diego Moores Cancer Center

La Jolla, California, United States

Site Status

Los Angeles Hematology Oncology Medical Group

Los Angeles, California, United States

Site Status

UCLA Department of Medicine - Hematology/Oncology

Los Angeles, California, United States

Site Status

University of California, Irvine Medical Center-Chao Family Comprehensive Cancer Center

Orange, California, United States

Site Status

Southern California Permanente Medical Group

San Diego, California, United States

Site Status

UCSF Helen Diller Family Comprehensive Cancer Center

San Francisco, California, United States

Site Status

Rocky Mountain Cancer Centers

Aurora, Colorado, United States

Site Status

University of Colorado

Aurora, Colorado, United States

Site Status

Yale University Cancer Center

New Haven, Connecticut, United States

Site Status

Georgetown University Medical Center

Washington D.C., District of Columbia, United States

Site Status

University of Miami - Sylvester Comprehensive Cancer Center

Miami, Florida, United States

Site Status

Miami Cancer Institute

Miami, Florida, United States

Site Status

Orlando Health, Inc.

Orlando, Florida, United States

Site Status

Moffitt Cancer Center

Tampa, Florida, United States

Site Status

Emory University - Winship Cancer Institute

Atlanta, Georgia, United States

Site Status

Northside Hospital, Inc.

Atlanta, Georgia, United States

Site Status

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

The University of Kansas Cancer Center

Westwood, Kansas, United States

Site Status

James Graham Brown Cancer Center

Louisville, Kentucky, United States

Site Status

Mercy Medical Center, Medical Oncology & Hematology

Baltimore, Maryland, United States

Site Status

Maryland Oncology Hematology, P.A.

Rockville, Maryland, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status

Dana Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Allina Health, Virginia Piper Cancer Institute

Minneapolis, Minnesota, United States

Site Status

Masonic Cancer Center, University of Minnesota

Minneapolis, Minnesota, United States

Site Status

Saint Luke's Cancer Institute

Kansas City, Missouri, United States

Site Status

Washington University School of Medicine - Siteman Cancer Center

St Louis, Missouri, United States

Site Status

St. Vincent Frontier Cancer Center

Billings, Montana, United States

Site Status

Summit Medical Group

Florham Park, New Jersey, United States

Site Status

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, United States

Site Status

New York Oncology Hematology, P.C.

Albany, New York, United States

Site Status

Laura and Isaac Perlmutter Cancer Center/NYU Langone Health

New York, New York, United States

Site Status

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Site Status

Columbia University Medical Center

New York, New York, United States

Site Status

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status

The Ohio State University

Columbus, Ohio, United States

Site Status

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Site Status

Magee-Womens Hospital of UPMC

Pittsburgh, Pennsylvania, United States

Site Status

The West Clinic, PC dba West Cancer Center

Germantown, Tennessee, United States

Site Status

Tennessee Oncology, PLLC

Nashville, Tennessee, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Texas Oncology-Baylor Charles A. Sammons Cancer Center

Dallas, Texas, United States

Site Status

University of Texas Southwestern Harold C. Simmons Comprehensive Cancer Center

Dallas, Texas, United States

Site Status

Texas Oncology-Denton South

Denton, Texas, United States

Site Status

Houston Methodist Hospital/Houston Methodist Cancer Center

Houston, Texas, United States

Site Status

Texas Oncology-Longview Cancer Center

Longview, Texas, United States

Site Status

UT Health San Antonio - Mays Cancer Center

San Antonio, Texas, United States

Site Status

Virginia Cancer Specialists

Arlington, Virginia, United States

Site Status

Virginia Oncology Associates

Norfolk, Virginia, United States

Site Status

Oncology & Hematology Associates of Southwest Virginia, Inc. DBA Blue Ridge Cancer Care

Salem, Virginia, United States

Site Status

Northwest Medical Specialties, PLLC

Tacoma, Washington, United States

Site Status

Chirec Cancer Institute

Brussels, , Belgium

Site Status

Institut Jules Bordet

Brussels, , Belgium

Site Status

Universitair Ziekenhuis Leuven

Leuven, , Belgium

Site Status

CHU UCL Namur/Site Sainte Elisabeth

Namur, , Belgium

Site Status

Nova Scotia Cancer Centre

Halifax, Nova Scotia, Canada

Site Status

Centre Hospitalier de L'Universite de Montreal - Hôpital Notre-Dame

Montreal, , Canada

Site Status

Centre Hospitalier Universitaire de Sherbrooke - Fleurimont

Sherbrooke, , Canada

Site Status

Hopital de Mercy

Ars-Laquenexy, , France

Site Status

Institut Sainte Catherine

Avignon, , France

Site Status

Hôpital Jean-Minjoz

Besançon, , France

Site Status

Centre Georges-Francois Leclerc

Dijon, , France

Site Status

Centre Leon Berard

Lyon, , France

Site Status

Institut Régional du Cancer de Montpellier

Montpellier, , France

Site Status

Institut Curie

Paris, , France

Site Status

Hospices Civils de Lyon

Pierre-Bénite, , France

Site Status

Institut de Cancérologie Lucien Neuwirth

Saint-Priest-en-Jarez, , France

Site Status

Institut Claudius Regaud

Toulouse, , France

Site Status

HELIOS Klinikum Berlin-Buch

Berlin, , Germany

Site Status

Gynakologisches Zentrum Bonn

Bonn, , Germany

Site Status

Marienhospital Bottrop

Bottrop, , Germany

Site Status

Städtisches Klinikum Dessau

Dessau, , Germany

Site Status

Universitätsklinikum Erlangen

Erlangen, , Germany

Site Status

Kliniken Essen-Mitte

Essen, , Germany

Site Status

Centrum für Hämatologie und Onkologie Bethanien

Frankfurt, , Germany

Site Status

Onkologische Schwerpunktpraxis Eppendorf

Hamburg, , Germany

Site Status

Gynakologisch-Onkologische Praxis Hannover

Hanover, , Germany

Site Status

DIAKOVERE Krankenhaus gGmbH Henriettenstift - Standort Kirchrode

Hanover, , Germany

Site Status

Nationales Centrum für Tumorerkrankungen - Heidelberg

Heidelberg, , Germany

Site Status

Praxisklinik für Hämatologie und Onkologie Koblenz

Koblenz, , Germany

Site Status

Universitätsmedizin Mannheim

Mannheim, , Germany

Site Status

Klinikum Mutterhaus der Borromäerinnen

Trier, , Germany

Site Status

Azienda Ospedaliera Spedali Civili di Brescia

Brescia, , Italy

Site Status

Ospedale di Desio

Desio, , Italy

Site Status

Ospedale Vito Fazzi di Lecce

Lecce, , Italy

Site Status

Ospedale San Raffaele

Milan, , Italy

Site Status

Azienda Ospedaliera San Gerardo di Monza

Monza, , Italy

Site Status

Azienda Unità Sanitaria Locale di Piacenza-Ospedale Guglielmo da Saliceto

Piacenza, , Italy

Site Status

IFO Istituto Nazionale dei Tumori Regina Elena

Rome, , Italy

Site Status

Antoni van Leeuwenhoekziekenhuis

Amsterdam, , Netherlands

Site Status

Medisch Centrum Haaglanden Antoniushove

Leidschendam, , Netherlands

Site Status

Maastricht UMC+

Maastricht, , Netherlands

Site Status

Complejo Hospitalario Universitario A Coruna

A Coruña, , Spain

Site Status

Hospital Quirónsalud Barcelona Instituto Oncologico Baselga

Barcelona, , Spain

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital de la Santa Creu I Sant Pau

Barcelona, , Spain

Site Status

Hospital Provincial de Castellón

Castillón, , Spain

Site Status

Hospital Universitari Arnau de Vilanova

Lleida, , Spain

Site Status

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status

Instituto Oncologico Bureau (IOB)

Madrid, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Hospital Clinico Universitario de Santiago de Compostela

Santiago de Compostela, , Spain

Site Status

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status

Royal Cornwall Hospital NHS Trust

Cornwell, , United Kingdom

Site Status

Royal Surrey County Hospital

Guildford, , United Kingdom

Site Status

Leicester Royal Infirmary

Leicester, , United Kingdom

Site Status

Barts Health NHS Trust

London, , United Kingdom

Site Status

The Royal Marsden NHS Foundation Trust

London, , United Kingdom

Site Status

The Christie NHS Foundation Trust

Manchester, , United Kingdom

Site Status

Countries

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United States Belgium Canada France Germany Italy Netherlands Spain United Kingdom

References

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Rugo HS, Bardia A, Marme F, Cortes J, Schmid P, Loirat D, Tredan O, Ciruelos E, Dalenc F, Gomez Pardo P, Jhaveri KL, Delaney R, Valdez T, Wang H, Motwani M, Yoon OK, Verret W, Tolaney SM. Overall survival with sacituzumab govitecan in hormone receptor-positive and human epidermal growth factor receptor 2-negative metastatic breast cancer (TROPiCS-02): a randomised, open-label, multicentre, phase 3 trial. Lancet. 2023 Oct 21;402(10411):1423-1433. doi: 10.1016/S0140-6736(23)01245-X. Epub 2023 Aug 23.

Reference Type BACKGROUND
PMID: 37633306 (View on PubMed)

Rugo HS, Bardia A, Marme F, Cortes J, Schmid P, Loirat D, Tredan O, Ciruelos E, Dalenc F, Pardo PG, Jhaveri KL, Delaney R, Fu O, Lin L, Verret W, Tolaney SM. Sacituzumab Govitecan in Hormone Receptor-Positive/Human Epidermal Growth Factor Receptor 2-Negative Metastatic Breast Cancer. J Clin Oncol. 2022 Oct 10;40(29):3365-3376. doi: 10.1200/JCO.22.01002. Epub 2022 Aug 26.

Reference Type BACKGROUND
PMID: 36027558 (View on PubMed)

Rugo HS, Bardia A, Tolaney SM, Arteaga C, Cortes J, Sohn J, Marme F, Hong Q, Delaney RJ, Hafeez A, Andre F, Schmid P. TROPiCS-02: A Phase III study investigating sacituzumab govitecan in the treatment of HR+/HER2- metastatic breast cancer. Future Oncol. 2020 Apr;16(12):705-715. doi: 10.2217/fon-2020-0163. Epub 2020 Mar 30.

Reference Type BACKGROUND
PMID: 32223649 (View on PubMed)

Rugo HS, Schmid P, Tolaney SM, Dalenc F, Marme F, Shi L, Verret W, Shah A, Gharaibeh M, Bardia A, Cortes J. Health-related quality of life with sacituzumab govitecan in HR+/HER2- metastatic breast cancer in the phase III TROPiCS-02 trial. Oncologist. 2024 Sep 6;29(9):768-779. doi: 10.1093/oncolo/oyae088.

Reference Type BACKGROUND
PMID: 38748596 (View on PubMed)

Rugo HS, Bardia A, Marme F, Cortes J, Schmid P, Spears PA, Tolaney SM. A plain language summary of the TROPiCS-02 study in patients with breast cancer (HR-positive/HER2-negative). Future Oncol. 2024 Apr;20(11):635-651. doi: 10.2217/fon-2023-0845. Epub 2024 Jan 25.

Reference Type BACKGROUND
PMID: 38270051 (View on PubMed)

Rugo HS, Bardia A, Tolaney S. Sacituzumab govitecan for metastatic breast cancer: the TROPiCS-02 trial - Authors' reply. Lancet. 2024 Jul 27;404(10450):339-340. doi: 10.1016/S0140-6736(24)01049-3. No abstract available.

Reference Type BACKGROUND
PMID: 39067902 (View on PubMed)

McCann KE, Hurvitz SA. Innovations in targeted therapies for triple negative breast cancer. Curr Opin Obstet Gynecol. 2021 Feb 1;33(1):34-47. doi: 10.1097/GCO.0000000000000671.

Reference Type DERIVED
PMID: 33093337 (View on PubMed)

Kalinsky K, Diamond JR, Vahdat LT, Tolaney SM, Juric D, O'Shaughnessy J, Moroose RL, Mayer IA, Abramson VG, Goldenberg DM, Sharkey RM, Maliakal P, Hong Q, Goswami T, Wegener WA, Bardia A. Sacituzumab govitecan in previously treated hormone receptor-positive/HER2-negative metastatic breast cancer: final results from a phase I/II, single-arm, basket trial. Ann Oncol. 2020 Dec;31(12):1709-1718. doi: 10.1016/j.annonc.2020.09.004. Epub 2020 Sep 15.

Reference Type DERIVED
PMID: 32946924 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2018-004201-33

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

IMMU-132-09

Identifier Type: -

Identifier Source: org_study_id

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