Basket Trial in Solid Tumors Harboring a Fusion of FGFR1, FGFR2 or FGFR3- (FUZE Clinical Trial)

NCT ID: NCT03834220

Last Updated: 2024-02-07

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

63 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-03-22

Study Completion Date

2022-01-04

Brief Summary

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The primary objective of this study is to assess the efficacy of Debio 1347 in terms of objective response rate (ORR) in participants with solid tumors harboring fibroblast growth factor receptor (FGFR)1-3 gene fusion/rearrangement.

Detailed Description

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Conditions

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Solid Tumor

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Cohort 1: Debio 1347 (Biliary Tract Cancer)

Participants with biliary tract cancer were included in this cohort to receive Debio 1347 80 milligrams (mg) tablets, orally, once daily (QD), from Day 1 to Day 28 in 28-day cycles until the occurrence of disease progression or unacceptable toxicity (up to a median duration of 20 weeks).

Group Type EXPERIMENTAL

Debio 1347

Intervention Type DRUG

Debio 1347 oral tablets.

Cohort 2: Debio 1347 (Urothelial Cancer)

Participants with urothelial cancer were included in this cohort to receive Debio 1347 80 mg tablets, orally, QD, from Day 1 to Day 28 in 28-day cycles until the occurrence of disease progression or unacceptable toxicity (up to a median duration of 5.86 weeks).

Group Type EXPERIMENTAL

Debio 1347

Intervention Type DRUG

Debio 1347 oral tablets.

Cohort 3: Debio 1347 (All Other Solid Tumor Histologies)

Participants with all other solid tumor histologies were included in this cohort to receive Debio 1347 80 mg tablets, orally, QD, from Day 1 to Day 28 in 28-day cycles until the occurrence of disease progression or unacceptable toxicity (up to a median duration of 8.14 weeks).

Group Type EXPERIMENTAL

Debio 1347

Intervention Type DRUG

Debio 1347 oral tablets.

Interventions

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Debio 1347

Debio 1347 oral tablets.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Cytologically or histologically confirmed advanced solid tumor
* Radiographic progression on prior systemic therapy; prior localized therapy (i.e., radiation, ablation, embolization) is allowed provided radiographic progression out-of-field or in the treatment, field is shown
* Locally-advanced (unresectable) or metastatic disease harboring an FGFR1-3 gene fusion/rearrangement potentially leading to a functional FGFR aberrant protein, identified through local and/or central molecular assay

Exclusion Criteria

* History of hypersensitivity to any of the excipients in the Debio 1347 formulation
* History and/or current evidence of ectopic mineralization/calcification, including but not limited to soft tissue, kidneys, intestine, myocardia, or lung, excepting calcified lymph nodes, lung nodules and asymptomatic vascular or cartilage/tendon calcifications
* Administration of any investigational agent within 2 weeks prior to initial dosing with Debio 1347 (3 weeks for immune checkpoint inhibitors)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Caris Life Sciences

INDUSTRY

Sponsor Role collaborator

Optimal Research (Just In Time sites)

UNKNOWN

Sponsor Role collaborator

Debiopharm International SA

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Ironwood Cancer & Research Centers - Scottsdale

Scottsdale, Arizona, United States

Site Status

University of Arizona Cancer Center

Tucson, Arizona, United States

Site Status

Moores UCSD Cancer Center

La Jolla, California, United States

Site Status

University of California San Francisco

San Francisco, California, United States

Site Status

Sarcoma Oncology Center

Santa Monica, California, United States

Site Status

H. Lee Moffitt Cancer Center and Research Institute, Inc

Tampa, Florida, United States

Site Status

James Graham Brown Cancer Center

Louisville, Kentucky, United States

Site Status

Tulane University Cancer Center

New Orleans, Louisiana, United States

Site Status

The John Hopkins Hospital

Baltimore, Maryland, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

Memorial Sloan Kettering Cancer Center

Middletown, New Jersey, United States

Site Status

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, United States

Site Status

Memorial Sloan Kettering Cancer Center

Harrison, New York, United States

Site Status

Memorial Sloan-Kettering Hospital

New York, New York, United States

Site Status

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

UC Health, LLC.

Cincinnati, Ohio, United States

Site Status

The Ohio State University Wexner Medical Center - James Cancer Hospital

Columbus, Ohio, United States

Site Status

CTCA Cancer Treatment Centers

Tulsa, Oklahoma, United States

Site Status

West Penn - Allegheny Oncology Network

Pittsburgh, Pennsylvania, United States

Site Status

MD Anderson Cancer Center

Houston, Texas, United States

Site Status

University of Utah Hospitals & Clinics

Salt Lake City, Utah, United States

Site Status

Fred Hutchinson/Seattle Care Alliance

Seattle, Washington, United States

Site Status

University of Wisconsin

Madison, Wisconsin, United States

Site Status

Southern Highlands Private Hospital

Bowral, , Australia

Site Status

Peninsula and Southeast Oncology (PASO)

Frankston, , Australia

Site Status

Linear Clinical Research, B Block Sir Charles Gairdner Hospital

Nedlands, , Australia

Site Status

John Flynn Private Hospital

Tugun, , Australia

Site Status

LKH - Universitätsklinikum der PMU Salzburg

Salzburg, , Austria

Site Status

Landesklinikum Wiener Neustadt

Wiener Neustadt, , Austria

Site Status

Hospital de Caridade de Ijuí, Avenida David J Martins

Ijuí, , Brazil

Site Status

Hospital de Clínicas de Porto Alegre

Rio Grande, , Brazil

Site Status

CEPHO - Centro de Estudos e Pesquisas de Hematologia e Oncologia

Santo André, , Brazil

Site Status

ICESP - Instituto do Câncer do Estado de São Paulo Octavio Frias de Oliveira, Avenida Doutor Arnaldo

São Paulo, , Brazil

Site Status

MHAT - Dobrich

Dobrich, , Bulgaria

Site Status

Complex Oncological Center - Plovdiv, EOOD

Plovdiv, , Bulgaria

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MHAT "Serdika", EOOD

Sofia, , Bulgaria

Site Status

General Hospital Varazdin

Varaždin, , Croatia

Site Status

University Hospital Centre, Sestre Milosrdnice

Zagreb, , Croatia

Site Status

Fakultni nemocnice u sv. Anny v Brne

Brno, , Czechia

Site Status

Fakultni nemocnice Hradec Kralove

Hradec Králové, , Czechia

Site Status

Fakultni nemocnice Olomouc

Olomouc, , Czechia

Site Status

Fakultni nemocnice Kralovske Vinohrady

Prague, , Czechia

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Thomayerova nemocnice

Prague, , Czechia

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Ålborg Universitets Hospital

Aalborg, , Denmark

Site Status

Herlev Hospital

Herlev, , Denmark

Site Status

Odense Universitetshospital

Odense, , Denmark

Site Status

Docrates Syöpäsairaala

Helsinki, , Finland

Site Status

Helsinki University Hospital

Helsinki, , Finland

Site Status

ICO - Site Paul Papin

Angers, , France

Site Status

CHU Bordeaux - Hôpital Saint André, Groupe Hospitalier Sud - Hôpital Haut-Lévêque

Bordeaux, , France

Site Status

Centre Oscar Lambret

Lille, , France

Site Status

Groupe Hospitalier Sud - Hôpital Haut Lévêque

Pessac, , France

Site Status

ICO - Site René Gauducheau

Saint-Herblain, , France

Site Status

Institut Gustave Roussy

Villejuif, , France

Site Status

General Hospital of Athens Laiko

Athens, , Greece

Site Status

General Hospital of Athens of Chest Diseases "SOTIRIA"

Athens, , Greece

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General Hospital of Athens "Alexandra"

Athens, , Greece

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University General Hospital of Ioannina

Ioannina, , Greece

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VU Medisch Centrum

Amsterdam, , Netherlands

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Haga Ziekenhuis

The Hague, , Netherlands

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Akershus University Hospital

Lørenskog, , Norway

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Radiumhospitalet, Montebello

Oslo, , Norway

Site Status

Cebu Doctors' University Hospital (CDUH), Research Office

Cebu City, , Philippines

Site Status

Philippine General Hospital, Clinical Trial Unit Room 5, Medical Research Laboratory

Ermita, , Philippines

Site Status

St. Luke's Medical Center, Human Cancer Biobank Research Center

Quezon City, , Philippines

Site Status

Szpital Kliniczny im.Heliodora Swiecickiego Uniwersytetu Medycznego im.K. Marcinkowskiego w Poznaniu

Poznan, , Poland

Site Status

MTZ Clinical Research

Warsaw, , Poland

Site Status

Centrum Onkologii-Instytut im.M.Sklodowskiej Curie

Warsaw, , Poland

Site Status

S.C Delta Health Care S.R.L

Bucharest, , Romania

Site Status

S.C Medisprof S.R.L.

Cluj-Napoca, , Romania

Site Status

S.C Centrul de Oncologie Sf. Nectarie S.R.L.

Craiova, , Romania

Site Status

S.C Oncocenter Oncologie Clinica S.R.L.

Timișoara, , Romania

Site Status

SBIH of Arkhangelsk region "Arkhangelsk Clinical Oncological Dispensary"

Arkhangelsk, , Russia

Site Status

TSBHI "Altai Territorial oncological dispensary"

Barnaul, , Russia

Site Status

LLC Evimed

Chelyabinsk, , Russia

Site Status

FSBSI "Russian Oncological Scientific Center n.a. N.N. Blokhin"

Moscow, , Russia

Site Status

BHI of Omsk region "Clinical Oncology Dispensary"

Omsk, , Russia

Site Status

Tomsk Research Instutite of Oncology

Tomsk, , Russia

Site Status

Singapore National Cancer Center (SNCC)

Singapore, , Singapore

Site Status

Tan Tock Seng Hospital, Communicable Disease Centre

Singapore, , Singapore

Site Status

Seoul National University Bundang Hospital, Department of Oncology Medical office

Gyeonggi-do, , South Korea

Site Status

The Catholic University of Korea, St. Vincent's Hospital, CRC Room, 3F

Gyeonggi-do, , South Korea

Site Status

Gachon University Gil Medical Center, CRC Room, 18F, Artificial intelligence hospital

Incheon, , South Korea

Site Status

Korea University Anam Hospital

Seoul, , South Korea

Site Status

Seoul National University Hospital (SNUH)

Seoul, , South Korea

Site Status

Ajou University Hospital, CRC room, Clinical Trial Center

Suwon, , South Korea

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Centro Integral Oncologico Clara Campal

Madrid, , Spain

Site Status

Hospital Clinico Universitario de Valencia

Valencia, , Spain

Site Status

Shuang Ho Hospital

New Taipei City, , Taiwan

Site Status

Taichung Veterans General Hospital, The Radiation Oncology Department

Taichung, , Taiwan

Site Status

National Cheng Kung University Hospital

Tainan City, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Taipei Medical University Hospital (TMUH)

Taipei, , Taiwan

Site Status

Taipei Veterans General Hospital, Medical Science & Technology Building

Taipei, , Taiwan

Site Status

Linkou Chang-Gung Memorial Hospital

Taoyuan District, , Taiwan

Site Status

CI Dnipropetrovsk CMCH #4 of Dnipropetrovsk RC Dept of Chemotherapy SI Dnipropetrovsk MA of MOHU

Dnipro, , Ukraine

Site Status

SI V.T. Zaycev Institute of general & urgent surgery of National academy medical sciences of Ukraine, Department of purulent surgery

Kharkiv, , Ukraine

Site Status

Communal Non-profit Enterprise Regional Center of Oncology

Kharkiv, , Ukraine

Site Status

Ninewells Hospital

Dundee, , United Kingdom

Site Status

Guy's Hospital

London, , United Kingdom

Site Status

Hammersmith Hospital

London, , United Kingdom

Site Status

The Christie

Manchester, , United Kingdom

Site Status

Countries

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United States Australia Austria Brazil Bulgaria Croatia Czechia Denmark Finland France Greece Netherlands Norway Philippines Poland Romania Russia Singapore South Korea Spain Taiwan Ukraine United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2018-003584-53

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

Debio 1347-201

Identifier Type: -

Identifier Source: org_study_id

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