A Study of Patritumab Deruxtecan in Pediatric Participants With Relapsed or Refractory Solid Tumors (MK-9999-01C/LIGHTBEAM-U01)

NCT ID: NCT06941272

Last Updated: 2025-11-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

50 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-05-26

Study Completion Date

2030-12-30

Brief Summary

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Researchers are looking for new ways to treat children with hepatoblastoma or rhabdomyosarcoma (RMS) that has relapsed or is refractory:

* Hepatoblastoma is a common liver cancer in babies and very young children
* RMS is a cancer that starts in muscle cells, often in a child's head and neck, bladder, arms, or legs
* Relapsed means the cancer came back after treatment
* Refractory means the cancer did not respond (get smaller or go away) to treatment

The study treatment HER3-DXd (also known as MK-1022 or patritumab deruxtecan) is an antibody-drug conjugate (ADC). An ADC attaches to a protein on cancer cells and delivers treatment to destroy those cells. The goals of this study are to learn:

* About the safety of HER3-DXd in children and if they tolerate it
* What happens to HER3-DXd in children's bodies over time
* If children who receive HER3-DXd have the cancer get smaller or go away

Detailed Description

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This study will have 2 parts: a safety lead-in to demonstrate a tolerable safety profile and confirm a preliminary recommended phase 2 dose (RP2D) (Part 1) followed by an efficacy evaluation (Part 2).

Conditions

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Malignant Neoplasm

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Patritumab Deruxtecan

Participants receive patritumab deruxtecan via IV infusion on Day 1 of each 3-week cycle until discontinuation or progression.

Group Type EXPERIMENTAL

Patritumab Deruxtecan

Intervention Type BIOLOGICAL

IV Infusion

Interventions

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Patritumab Deruxtecan

IV Infusion

Intervention Type BIOLOGICAL

Other Intervention Names

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MK-1022 HER3-DXd U3-1402

Eligibility Criteria

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Inclusion Criteria

* Has one of the following histologically confirmed advanced or metastatic solid tumors: Rhabdomyosarcoma (RMS), or Hepatoblastoma
* Has progressed after at least 1 prior systemic treatment for RMS or hepatoblastoma and who has no satisfactory alternative treatment option (ie, is ineligible for other standard treatment regimens)
* Participants who have adverse events (AEs) due to previous anticancer therapies must have recovered to Grade ≤1 or baseline. Participants with endocrine-related AEs who are adequately treated with hormone replacement or participants who have Grade ≤2 neuropathy are eligible
* Hepatitis B surface antigen (HBsAg) positive participants are eligible if they have received hepatitis B virus (HBV) antiviral therapy and have undetectable HBV viral load
* Participants with a history of hepatitis C virus (HCV) infection are eligible if HCV viral load is undetectable

Exclusion Criteria

* Has a history of (noninfectious) interstitial lung disease (ILD)/pneumonitis that required steroids or has current ILD/pneumonitis, and/or suspected ILD/pneumonitis that cannot be ruled out by standard diagnostic assessments
* Has clinically severe respiratory compromise resulting from intercurrent pulmonary illness
* Has a history of solid organ transplant
* Has a history of allogeneic stem cell transplant
* Has clinically significant corneal disease
* Has known active central nervous system (CNS) metastases and/or carcinomatous meningitis/leptomeningeal disease; participants with previously treated brain metastases may participate provided they are radiologically stable (ie, without evidence of progression) for at least 4 weeks
* Has uncontrolled or significant cardiovascular disorder
* Has a history of clinically significant congenital cardiac syndrome
* Has a history of human immunodeficiency virus (HIV) infection
* Has a known additional malignancy that is progressing or has required active treatment within the past 1 year
* Has an active infection requiring systemic therapy
* Has concurrent active hepatitis B (HBsAg positive and/or detectable HBV deoxyribonucleic acid \[DNA\]) and HCV defined as anti-HCV antibody (Ab) positive and detectable HCV ribonucleic acid \[RNA\]) infection
* Has not adequately recovered from major surgery or have ongoing surgical complications
Minimum Eligible Age

1 Month

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Daiichi Sankyo

INDUSTRY

Sponsor Role collaborator

Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Merck Sharp & Dohme LLC

Locations

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Children's Hospital Colorado-Center for Cancer and Blood Disorders ( Site 3016)

Aurora, Colorado, United States

Site Status RECRUITING

University of Iowa Health Care Holden Comprehensive Cancer Center ( Site 3017)

Iowa City, Iowa, United States

Site Status RECRUITING

Corewell Health ( Site 3001)

Grand Rapids, Michigan, United States

Site Status RECRUITING

Children's Mercy Hospital ( Site 3024)

Kansas City, Missouri, United States

Site Status RECRUITING

Rutgers Cancer Institute of New Jersey ( Site 3008)

New Brunswick, New Jersey, United States

Site Status RECRUITING

New York Medical College ( Site 3023)

Valhalla, New York, United States

Site Status RECRUITING

Sanford Fargo Medical Center-Roger Maris Cancer Center ( Site 3003)

Fargo, North Dakota, United States

Site Status RECRUITING

Children's Hospital of Philadelphia (CHOP) ( Site 3021)

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Sanford Children's Hospital ( Site 3015)

Sioux Falls, South Dakota, United States

Site Status RECRUITING

University of Texas-MD Anderson Cancer Center ( Site 3007)

Houston, Texas, United States

Site Status RECRUITING

Intermountain - Primary Children's Hospital ( Site 3014)

Salt Lake City, Utah, United States

Site Status RECRUITING

UZ Gent ( Site 3428)

Ghent, Oost-Vlaanderen, Belgium

Site Status RECRUITING

Bordeaux University Hospital - Pellegrin ( Site 3105)

Bordeaux, Aquitaine, France

Site Status RECRUITING

Centre Hospitalier Universitaire de Nantes - Hôpital Femme-Enfant-Adolescent Chu De Nantes ( Site 3104)

Nantes, Loire-Atlantique, France

Site Status RECRUITING

Centre Leon-Berard ( Site 3100)

Lyon, Rhone, France

Site Status RECRUITING

Rambam Health Care Campus ( Site 3674)

Haifa, , Israel

Site Status RECRUITING

Sheba Medical Center ( Site 3675)

Ramat Gan, , Israel

Site Status RECRUITING

Prinses Maxima Centrum voor Kinderoncologie ( Site 3510)

Utrecht, , Netherlands

Site Status RECRUITING

Seoul National University Hospital-Pediatrics ( Site 3972)

Seoul, , South Korea

Site Status RECRUITING

Asan Medical Center-Pediatrics - Pedicatric Oncology ( Site 3973)

Seoul, , South Korea

Site Status RECRUITING

Hospital Sant Joan de Déu ( Site 3717)

Esplugues de Llobregat, Barcelona, Spain

Site Status RECRUITING

Hospital Universitari Vall d''Hebron ( Site 3716)

Barcelona, , Spain

Site Status RECRUITING

Hospital Infantil Universitario Nino Jesus ( Site 3715)

Madrid, , Spain

Site Status RECRUITING

Sahlgrenska Universitetssjukhuset. ( Site 3634)

Gothenburg, Västra Götaland County, Sweden

Site Status RECRUITING

National Taiwan University Hospital ( Site 3983)

Taiwan, Taipei, Taiwan

Site Status RECRUITING

Royal Victoria Infirmary ( Site 3348)

Newcastle upon Tyne, England, United Kingdom

Site Status RECRUITING

Countries

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United States Belgium France Israel Netherlands South Korea Spain Sweden Taiwan United Kingdom

Central Contacts

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Toll Free Number

Role: CONTACT

Phone: 1-888-577-8839

Email: [email protected]

Facility Contacts

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Related Links

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http://www.merckclinicaltrials.com

Merck Clinical Trials Information

Other Identifiers

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MK-9999-01C

Identifier Type: OTHER

Identifier Source: secondary_id

LIGHTBEAM-U01

Identifier Type: OTHER

Identifier Source: secondary_id

U1111-1314-1866

Identifier Type: REGISTRY

Identifier Source: secondary_id

2024-518771-66-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

9999-01C

Identifier Type: -

Identifier Source: org_study_id