KPL-301 for Subjects With Giant Cell Arteritis

NCT ID: NCT03827018

Last Updated: 2023-10-23

Study Results

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

70 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-09-20

Study Completion Date

2020-11-25

Brief Summary

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The primary objective of the study is to evaluate the efficacy of mavrilimumab (KPL-301) versus placebo, co-administered with a 26-week corticosteroid taper, for maintaining sustained remission for 26 weeks in subjects with new onset or relapsing/refractory giant cell arteritis (GCA).

Detailed Description

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This Phase 2 randomized, double-blind, placebo-controlled proof of concept study will evaluate the efficacy and safety of mavrilimumab co-administered with a 26-week corticosteroid taper in subjects with GCA. The study will consist of a screening period (up to 6 weeks), a 26-week double-blind placebo-controlled period during which subjects will receive blinded mavrilimumab or placebo co-administered with a 26-week corticosteroid taper, and a 12-week washout safety follow-up period during which subjects will discontinue and wash off blinded mavrilimumab or placebo.

Conditions

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Giant Cell Arteritis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Upon successful completion of the screening procedures, diagnosis criteria will be entered into an interactive web response system, and eligible subjects will be stratified for randomized study treatment into two cohorts according to whether subjects have new-onset or relapsing/refractory disease.
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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mavrilimumab

Subjects randomized to mavrilimumab will receive 150 mg every other week by subcutaneous injection co-administered with a 26-week corticosteroid taper.

Group Type ACTIVE_COMPARATOR

mavrilimumab

Intervention Type COMBINATION_PRODUCT

1 mL of 150 mg in a pre-filled syringe

prednisone

Intervention Type DRUG

Prednisone tablets for oral administration containing either 1 mg, 2.5 mg, 5 mg, 10 mg, 20 mg or 50 mg of prednisone United States Pharmacopeia (USP)

placebo

Subjects randomized to placebo will receive placebo every other week by subcutaneous injection co-administered with a 26-week corticosteroid taper.

Group Type PLACEBO_COMPARATOR

placebo

Intervention Type COMBINATION_PRODUCT

1 mL of placebo in a pre-filled syringe

prednisone

Intervention Type DRUG

Prednisone tablets for oral administration containing either 1 mg, 2.5 mg, 5 mg, 10 mg, 20 mg or 50 mg of prednisone United States Pharmacopeia (USP)

Interventions

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mavrilimumab

1 mL of 150 mg in a pre-filled syringe

Intervention Type COMBINATION_PRODUCT

placebo

1 mL of placebo in a pre-filled syringe

Intervention Type COMBINATION_PRODUCT

prednisone

Prednisone tablets for oral administration containing either 1 mg, 2.5 mg, 5 mg, 10 mg, 20 mg or 50 mg of prednisone United States Pharmacopeia (USP)

Intervention Type DRUG

Other Intervention Names

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KPL-301

Eligibility Criteria

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Inclusion Criteria

1. Subjects with new-onset or relapsing/refractory GCA.
2. Westergren erythrocyte sedimentation rate \> 30 mm/hour or c-reactive protein ≥ 1 mg/ dL.
3. Remission of GCA at or before Day 0.
4. Female subjects must be postmenopausal or permanently sterile following documented hysterectomy, bilateral salpingectomy, bilateral oophorectomy, or tubal ligation or having a male partner with vasectomy as affirmed by the subject, or nonpregnant, nonlactating, and if sexually active having agreed to use a highly effective method of contraception.
5. Male subjects must have documented vasectomy or if sexually active must agree to use a highly effective method of contraception with their partners of childbearing potential.

Exclusion Criteria

1. Transplanted organs (except corneal transplant performed more than 3 months prior to randomization).
2. Concurrent enrollment in another interventional clinical study.
3. Treatment with non-biologic investigational drug therapy within 4 weeks or 5 half-lives of the study agent, whichever was longer, prior to screening.
4. Cell-depleting biological therapies within 12 months prior to Day 0, or noncell-depleting biological therapies within 8 weeks (or 5 half-lives, whichever is longer) prior to screening.
5. Treatment with alkylating agents within 12 weeks prior to screening.
6. Intramuscular, Intra-articular or IV corticosteroids within 4 weeks prior to screening.
7. Receipt of live (attenuated) vaccine within the 4 weeks before Day 0.
8. Treatment with hydroxychloroquine, cyclosporine A, azathioprine, cyclophosphamide, or mycophenolate mofetil (MMF) within 4 weeks of screening.
9. Female subjects who are pregnant, intending to become pregnant, or are breastfeeding.
10. Known history of allergy or reaction to any component of the mavrilimumab or placebo formulation or to any other biologic therapy or prednisone or any of its excipients.
11. Positive (or 2 indeterminate) QuantiFERON test results.
12. Clinically significant active infection or infection requiring hospitalization or IV antibiotics within 12 weeks before screening or opportunistic infection within 6 months before screening.
13. Chronic active hepatitis B infection.
14. Subjects at a high risk of infection, a history of an infected joint prosthesis still in situ, leg ulcers, indwelling urinary catheter, or persistent or recurrent chest infections.
15. History of cancer within the last 10 years, except for basal and squamous cell carcinoma of the skin or in situ carcinoma of the cervix treated and considered cured.
16. Evidence of clinically-uncontrolled respiratory disease.
17. History of chronic respiratory tract infections.
Minimum Eligible Age

50 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Kiniksa Pharmaceuticals, Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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John Paolini, M.D.

Role: STUDY_DIRECTOR

Kiniksa Pharmaceuticals, Ltd.

Locations

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Site 1703

Sarasota, Florida, United States

Site Status

Site 1708

Tampa, Florida, United States

Site Status

Site 1706

Atlanta, Georgia, United States

Site Status

Site 1701

Boston, Massachusetts, United States

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Site 1707

Lansing, Michigan, United States

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Site 1704

Saint Clair Shores, Michigan, United States

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Site 1702

Rochester, Minnesota, United States

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Site 1705

New York, New York, United States

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Site 2102

Kogarah, , Australia

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Site 2105

Nedlands, , Australia

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Site 2106

Parkville, , Australia

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Site 2101

Victoria Park, , Australia

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Site 2104

Woodville South, , Australia

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Site 2204

Brussels, , Belgium

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Site 2202

Leuven, , Belgium

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Site 2201

Liège, , Belgium

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Site 2203

Yvoir, , Belgium

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Site 2303

Zagreb, , Croatia

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Site 2401

Tallinn, , Estonia

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Site 2402

Tartu, , Estonia

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Site 2502

Tübingen, Baden-Wurttemberg, Germany

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Site 2504

Erlangen, Bavaria, Germany

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Site 2507

Freiburg im Breisgau, , Germany

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Site 2506

Hamburg, , Germany

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Site 2503

Hanover, , Germany

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Site 2508

Jena, , Germany

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Site 2501

Kirchheim unter Teck, , Germany

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Site 2601

Dublin, , Ireland

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Site 2703

Milan, , Italy

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Site 2701

Pieve Emanuele, , Italy

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Site 2702

Reggio Emilia, , Italy

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Site 2704

Udine, , Italy

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Site 2802

Groningen, , Netherlands

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Site 2801

Rotterdam, , Netherlands

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Site 2902

Christchurch, , New Zealand

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Site 2901

Wellington, , New Zealand

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Site 1002

Krakow, , Poland

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Site 1101

Belgrade, , Serbia

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Site 1102

Belgrade, , Serbia

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Site 1103

Belgrade, , Serbia

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Site 1201

Ljubljana, , Slovenia

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Site 1303

A Coruña, , Spain

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Site 1301

Barcelona, , Spain

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Site 1304

Bilbao, , Spain

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Site 1302

Santa Cruz de Tenerife, , Spain

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Site 1604

Edinburgh, , United Kingdom

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Site 1603

Essex, , United Kingdom

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Site 1602

London, , United Kingdom

Site Status

Site 1601

Newcastle upon Tyne, , United Kingdom

Site Status

Countries

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United States Australia Belgium Croatia Estonia Germany Ireland Italy Netherlands New Zealand Poland Serbia Slovenia Spain United Kingdom

References

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Cid MC, Unizony SH, Blockmans D, Brouwer E, Dagna L, Dasgupta B, Hellmich B, Molloy E, Salvarani C, Trapnell BC, Warrington KJ, Wicks I, Samant M, Zhou T, Pupim L, Paolini JF; KPL-301-C001 Investigators. Efficacy and safety of mavrilimumab in giant cell arteritis: a phase 2, randomised, double-blind, placebo-controlled trial. Ann Rheum Dis. 2022 May;81(5):653-661. doi: 10.1136/annrheumdis-2021-221865. Epub 2022 Mar 9.

Reference Type DERIVED
PMID: 35264321 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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KPL-301-C001

Identifier Type: -

Identifier Source: org_study_id

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