Durvalumab+ Gemcitabine/Cisplatin (Neoadjuvant Treatment) and Durvalumab (Adjuvant Treatment) in Patients With MIBC

NCT ID: NCT03732677

Last Updated: 2025-11-21

Study Results

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Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

1063 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-11-16

Study Completion Date

2026-06-30

Brief Summary

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A Global Study to Determine the Efficacy and Safety of Durvalumab in Combination with Gemcitabine+Cisplatin for Neoadjuvant Treatment and Durvalumab Alone for Adjuvant Treatment in Patients with Muscle-Invasive Bladder Cancer

Detailed Description

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Conditions

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Muscle Invasive Bladder Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm 1

Chemotherapy + Durvalumab

Group Type EXPERIMENTAL

Durvalumab

Intervention Type DRUG

Anti- PD-L1 Antibody

Cisplatin

Intervention Type DRUG

Chemotherapy Agent

Gemcitabine

Intervention Type DRUG

Chemotherapy agent

Arm 2

Chemotherapy alone

Group Type ACTIVE_COMPARATOR

Cisplatin

Intervention Type DRUG

Chemotherapy Agent

Gemcitabine

Intervention Type DRUG

Chemotherapy agent

Interventions

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Durvalumab

Anti- PD-L1 Antibody

Intervention Type DRUG

Cisplatin

Chemotherapy Agent

Intervention Type DRUG

Gemcitabine

Chemotherapy agent

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patient resectable muscle-invasive bladder cancer with clinical stage T2-T4aN0/1M0 with transitional and mixed transitional cell histology
* Patients must be planning to undergo a radical cystectomy
* Patients who have not received prior systemic chemotherapy or immunotherapy for treatment of MIBC
* ECOG performance status of 0 or 1
* Must have a life expectancy of at least 12 weeks at randomization

Exclusion:

* Evidence of lymph node (N2-N3) or metastatic (M1) disease at time of screening.
* Prior pelvic radiotherapy treatment within 2 years of randomization to study
* Prior exposure to immune-mediated therapy (with exclusion of Bacillus-Calmette Guerin \[BCG\]), including but not limited to other anti-CTLA-4, anti-PD-1, anti PD-L1, or anti-PD-L2 antibodies.
* Current or prior use of immunosuppressive medication within 14 days before the first dose of investigational product (IP). The following are exceptions to this criterion: Intranasal, inhaled, topical steroids, or local steroid injections (eg, intra articular injection); Systemic corticosteroids at physiologic doses not to exceed 10 mg/day of prednisone or its equivalent; Steroids as premedication for hypersensitivity reactions (eg, CT scan premedication)
* Receipt of live attenuated vaccine within 30 days prior to the first dose of IP.
* Uncontrolled intercurrent illness
* Active infection including Tuberculosis, Hepatitis B, Hepatitis C, and Human Immunodeficiency
Minimum Eligible Age

18 Years

Maximum Eligible Age

130 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Research Site

Birmingham, Alabama, United States

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Los Angeles, California, United States

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Palo Alto, California, United States

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New Haven, Connecticut, United States

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Chicago, Illinois, United States

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Geneva, Illinois, United States

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Iowa City, Iowa, United States

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Westwood, Kansas, United States

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Louisville, Kentucky, United States

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New Orleans, Louisiana, United States

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Towson, Maryland, United States

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Ann Arbor, Michigan, United States

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Detroit, Michigan, United States

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New York, New York, United States

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Rochester, New York, United States

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Bethlehem, Pennsylvania, United States

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Burlington, Vermont, United States

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Milwaukee, Wisconsin, United States

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Brisbane, , Australia

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Elizabeth Vale, , Australia

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Macquarie University, , Australia

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Melbourne, , Australia

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Murdoch, , Australia

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South Brisbane, , Australia

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Bruges, , Belgium

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Charleroi, , Belgium

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Kortrijk, , Belgium

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Leuven, , Belgium

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Liège, , Belgium

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Roeselare, , Belgium

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Barretos, , Brazil

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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Rio de Janeiro, , Brazil

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Santa Maria, , Brazil

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São José do Rio Preto, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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Edmonton, Alberta, Canada

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Vancouver, British Columbia, Canada

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London, Ontario, Canada

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Ottawa, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Sherbrooke, Quebec, Canada

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Antofagasta, , Chile

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Port Montt, , Chile

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Santiago, , Chile

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Temuco, , Chile

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Temuco, , Chile

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Viña del Mar, , Chile

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Brno, , Czechia

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Brno, , Czechia

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Hradec Králové, , Czechia

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Olomouc, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Angers, , France

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Dijon, , France

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Grenoble, , France

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Montpellier, , France

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Nîmes, , France

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Pierre-Bénite, , France

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Poitiers, , France

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Rouen, , France

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Bergisch Gladbach, , Germany

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Bonn, , Germany

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Cologne, , Germany

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Erlangen, , Germany

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Göttingen, , Germany

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Herne, , Germany

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Jena, , Germany

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Magdeburg, , Germany

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Mannheim, , Germany

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Münster, , Germany

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Nuremberg, , Germany

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Oldenburg, , Germany

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Regensburg, , Germany

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Ulm, , Germany

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Würzburg, , Germany

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Haifa, , Israel

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Jerusalem, , Israel

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Kfar Saba, , Israel

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Petah Tikva, , Israel

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Ramat Gan, , Israel

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Bari, , Italy

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Bologna, , Italy

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Florence, , Italy

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Milan, , Italy

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Milan, , Italy

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Napoli, , Italy

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Orbassano, , Italy

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Pozzuoli, , Italy

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Verona, , Italy

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Bunkyō City, , Japan

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Fukuoka, , Japan

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Fukuoka, , Japan

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Hirosaki-shi, , Japan

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Hiroshima, , Japan

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Kanazawa, , Japan

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Kōtoku, , Japan

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Kumamoto, , Japan

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Miyazaki, , Japan

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Nagasaki, , Japan

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Nagoya, , Japan

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Niigata, , Japan

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Osaka, , Japan

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Osaka, , Japan

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Osakasayama-shi, , Japan

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Sendai, , Japan

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Toyama, , Japan

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Tsukuba, , Japan

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Yokohama, , Japan

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Yokohama, , Japan

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Amsterdam, , Netherlands

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Amsterdam, , Netherlands

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Breda, , Netherlands

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Rotterdam, , Netherlands

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Baguio City, , Philippines

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Cebu, , Philippines

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Davao City, , Philippines

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Makati, , Philippines

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Manila, , Philippines

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Quezon City, , Philippines

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Quezon City, , Philippines

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Bialystok, , Poland

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Gdansk, , Poland

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Grudziądz, , Poland

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Koszalin, , Poland

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Krakow, , Poland

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Olsztyn, , Poland

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Ostrołęka, , Poland

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Poznan, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Krasnoyarsk, , Russia

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Moscow, , Russia

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Nizhny Novgorod, , Russia

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Novosibirsk, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Samara, , Russia

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Ufa, , Russia

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Vologda, , Russia

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Daegu, , South Korea

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Goyang-si, , South Korea

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Gyeonggi-do, , South Korea

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Incheon, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Badalona, , Spain

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Barcelona, , Spain

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Córdoba, , Spain

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Las Palmas de Gran Canaria, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Santander, , Spain

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Seville, , Spain

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Kaohsiung City, , Taiwan

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Taichung, , Taiwan

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Taichung, , Taiwan

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Tainan, , Taiwan

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Tainan, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taoyuan, , Taiwan

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Ankara, , Turkey (Türkiye)

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Edirne, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Karşıyaka, , Turkey (Türkiye)

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Edinburgh, , United Kingdom

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London, , United Kingdom

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Metropolitan Borough of Wirral, , United Kingdom

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Nottingham, , United Kingdom

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Sheffield, , United Kingdom

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Hanoi, , Vietnam

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Ho Chi Minh City, , Vietnam

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Hochiminh, , Vietnam

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Countries

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United States Australia Belgium Brazil Canada Chile Czechia France Germany Israel Italy Japan Netherlands Philippines Poland Russia South Korea Spain Taiwan Turkey (Türkiye) United Kingdom Vietnam

References

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Powles T, Catto JWF, Galsky MD, Al-Ahmadie H, Meeks JJ, Nishiyama H, Vu TQ, Antonuzzo L, Wiechno P, Atduev V, Kann AG, Kim TH, Suarez C, Chang CH, Roghmann F, Ozguroglu M, Eigl BJ, Oliveira N, Buchler T, Gadot M, Zakharia Y, Armstrong J, Gupta A, Hois S, van der Heijden MS; NIAGARA Investigators. Perioperative Durvalumab with Neoadjuvant Chemotherapy in Operable Bladder Cancer. N Engl J Med. 2024 Nov 14;391(19):1773-1786. doi: 10.1056/NEJMoa2408154. Epub 2024 Sep 15.

Reference Type DERIVED
PMID: 39282910 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2023-510015-19-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

2018-001811-59

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

D933RC00001

Identifier Type: -

Identifier Source: org_study_id

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