Alzheimer's Autism and Cognitive Impairment Stem Cell Treatment Study

NCT ID: NCT03724136

Last Updated: 2024-04-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ENROLLING_BY_INVITATION

Clinical Phase

NA

Total Enrollment

100 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-10-24

Study Completion Date

2025-07-31

Brief Summary

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The purpose of the study is to evaluate the use of autologous Bone Marrow Derived Stem Cells (BMSC) as a means to improve cognitive impairment as occurs in Alzheimer's Disease and other dementias and to improve behavior and socialization issues which occur in adult Autism Spectrum Disorder. The use of Near Infrared Light, in conjunction with the use of BMSC, will also be assessed.

Detailed Description

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Cognition is the process of generating thoughts, recalling memories, processing information, and higher order associations including social interactivity that all take place in the brain. It requires sufficient health and interactivity of neurons in the brain including their ability to form and maintain synaptic connections.

Cognitive impairment results from the loss of these abilities. ACIST will test the hypothesis that the delivery of Bone Marrow Derived Stem Cells (BMSC) via the methods in the study with or without the addition of Near Infrared Light will improve cognition through the ability of BMSC to positively affect the health and function of neurons and the brain.

Patients enrolling with cognitive impairment will require assessment with the Mini-Mental Status Exam (MMSE). A score of 24 or less will be required. Progressive dementias such as Alzheimer's Disease (ALZ) show a decline of 2 to 4 points per year on MMSE. The goal for ACIST in progressive and stable dementia will be stability over the 1 year follow up and ideally an improvement of 3 points on MMSE.

Patients enrolling with Autism Spectrum Disorder (ASD) will be required to be adults (over 18 years of age) and to have a score on the Autism Spectrum Quotient of 20 or above. The goal will be a decrease of 5 or more on the scale over the 1 year follow up period.

Conditions

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Alzheimer Disease Alzheimer Dementia Vascular Dementia Lewy Body Disease Lewy Body Dementia With Behavioral Disturbance (Disorder) Dementia, Mixed Parkinson-Dementia Syndrome Chronic Traumatic Encephalopathy Huntington's Dementia Wernicke Korsakoff Syndrome Traumatic Brain Injury Dementia, Multi-Infarct Autism Autism Spectrum Disorder Autistic Behavior Autistic Disorder, Current or Active State Cadasil LATE Limbic-predominant Age-related TDP-43 Encephalopathy

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Patients will be assigned to one of 3 arms with monitoring and retesting at 1,3,6 and 12 months following treatment.
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm 1

Intravenous Bone Marrow Stem Cell (BMSC) Fraction

Group Type ACTIVE_COMPARATOR

Intravenous Bone Marrow Stem Cell (BMSC) Fraction

Intervention Type PROCEDURE

14 cc of BMSC fraction separated from bone marrow aspirate and filtered with 150 micron filter and administered intravenously.

Arm 2

Intravenous Bone Marrow Stem Cell (BMSC) Fraction combined with Near Infrared Light exposure .

Group Type ACTIVE_COMPARATOR

Intravenous Bone Marrow Stem Cell (BMSC) Fraction

Intervention Type PROCEDURE

14 cc of BMSC fraction separated from bone marrow aspirate and filtered with 150 micron filter and administered intravenously.

Near Infrared Light

Intervention Type PROCEDURE

Near Infrared Light will be administered using an FDA cleared medical device on the preoperative day and the first postoperative day as tolerated to the general area of the frontal bone.

Arm 3

Intravenous Bone Marrow Stem Cell (BMSC) Fraction combined with Intranasal topical Bone Marrow Stem Cell (BMSC) Fraction.

Group Type ACTIVE_COMPARATOR

Intravenous Bone Marrow Stem Cell (BMSC) Fraction

Intervention Type PROCEDURE

14 cc of BMSC fraction separated from bone marrow aspirate and filtered with 150 micron filter and administered intravenously.

Intranasal Topical Bone Marrow Stem Cell (BMSC) Fraction

Intervention Type PROCEDURE

Approximately 1 cc of BMSC fraction separated from bone marrow aspirate and administered to the nasal mucosa topically.

Interventions

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Intravenous Bone Marrow Stem Cell (BMSC) Fraction

14 cc of BMSC fraction separated from bone marrow aspirate and filtered with 150 micron filter and administered intravenously.

Intervention Type PROCEDURE

Intranasal Topical Bone Marrow Stem Cell (BMSC) Fraction

Approximately 1 cc of BMSC fraction separated from bone marrow aspirate and administered to the nasal mucosa topically.

Intervention Type PROCEDURE

Near Infrared Light

Near Infrared Light will be administered using an FDA cleared medical device on the preoperative day and the first postoperative day as tolerated to the general area of the frontal bone.

Intervention Type PROCEDURE

Eligibility Criteria

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Inclusion Criteria

1. Have documented cognitive impairment or diagnosis of disease associated with cognitive impairment such as Alzheimer's Disease, Autism Spectrum Disorder.
2. If under current medical therapy (pharmacologic or surgical treatment) for the condition be considered stable on that treatment and unlikely to have reversal of the associated cognitive impairment as a result of the ongoing pharmacologic or surgical treatment.
3. In the estimation of the investigator have the potential for improvement with BMSC treatment and be at minimal risk of any potential harm from the procedure.
4. Be over the age of 18
5. Be medically stable and able to be medically cleared by their primary care physician or a licensed primary care practitioner for the procedure. Medical clearance means that in the estimation of the primary care practitioner, the patient can reasonably be expected to undergo the procedure without significant medical risk to health.

Exclusion Criteria

1. All patients must be capable of an adequate neurologic examination and evaluation to document the pathology.
2. Patients must be capable and willing to undergo follow up neurologic exams with the the investigators or their own neurologists as outlined in the protocol.
3. Patients or their designated responsible party for medical decisions must be capable of providing informed consent. Cognitive or memory impairment does not necessarily mean the patient is incapable of giving informed consent. They may simply need more time to process or repetition of the content of the consent to reach understanding and provide informed consent.
4. In the estimation of the investigator the BMSC collection and treatment will not present a significant risk of harm to the patient's general health or to their neurologic function.
5. Patients who are not medically stable or who may be at significant risk to their health undergoing the procedure will not be eligible.
6. Women of childbearing age must not be pregnant at the time of treatment and should refrain from becoming pregnant for 3 months post treatment.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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MD Stem Cells

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Steven Levy, MD

Role: STUDY_CHAIR

MD Stem Cells

Jeffrey Weiss, MD

Role: PRINCIPAL_INVESTIGATOR

Coral Springs

Locations

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MD Stem Cells

Westport, Connecticut, United States

Site Status

MD Stem Cells

Coral Springs, Florida, United States

Site Status

Medcare Orthopaedics & Spine Hospital

Dubai, , United Arab Emirates

Site Status

Countries

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United States United Arab Emirates

References

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Danielyan L, Schafer R, von Ameln-Mayerhofer A, Buadze M, Geisler J, Klopfer T, Burkhardt U, Proksch B, Verleysdonk S, Ayturan M, Buniatian GH, Gleiter CH, Frey WH 2nd. Intranasal delivery of cells to the brain. Eur J Cell Biol. 2009 Jun;88(6):315-24. doi: 10.1016/j.ejcb.2009.02.001. Epub 2009 Mar 25.

Reference Type BACKGROUND
PMID: 19324456 (View on PubMed)

Duncan T, Valenzuela M. Alzheimer's disease, dementia, and stem cell therapy. Stem Cell Res Ther. 2017 May 12;8(1):111. doi: 10.1186/s13287-017-0567-5.

Reference Type BACKGROUND
PMID: 28494803 (View on PubMed)

Johnstone DM, Moro C, Stone J, Benabid AL, Mitrofanis J. Turning On Lights to Stop Neurodegeneration: The Potential of Near Infrared Light Therapy in Alzheimer's and Parkinson's Disease. Front Neurosci. 2016 Jan 11;9:500. doi: 10.3389/fnins.2015.00500. eCollection 2015.

Reference Type BACKGROUND
PMID: 26793049 (View on PubMed)

Robbins JP, Price J. Human induced pluripotent stem cells as a research tool in Alzheimer's disease. Psychol Med. 2017 Nov;47(15):2587-2592. doi: 10.1017/S0033291717002124. Epub 2017 Aug 14.

Reference Type BACKGROUND
PMID: 28805182 (View on PubMed)

Park SE, Lee NK, Na DL, Chang JW. Optimal mesenchymal stem cell delivery routes to enhance neurogenesis for the treatment of Alzheimer's disease: optimal MSCs delivery routes for the treatment of AD. Histol Histopathol. 2018 Jun;33(6):533-541. doi: 10.14670/HH-11-950. Epub 2017 Nov 29.

Reference Type BACKGROUND
PMID: 29185257 (View on PubMed)

Shroff G. Human Embryonic Stem Cells in the Treatment of Autism: A Case Series. Innov Clin Neurosci. 2017 Apr 1;14(3-4):12-16. eCollection 2017 Mar-Apr.

Reference Type BACKGROUND
PMID: 28584692 (View on PubMed)

Chez M, Lepage C, Parise C, Dang-Chu A, Hankins A, Carroll M. Safety and Observations from a Placebo-Controlled, Crossover Study to Assess Use of Autologous Umbilical Cord Blood Stem Cells to Improve Symptoms in Children with Autism. Stem Cells Transl Med. 2018 Apr;7(4):333-341. doi: 10.1002/sctm.17-0042. Epub 2018 Feb 6.

Reference Type BACKGROUND
PMID: 29405603 (View on PubMed)

Weiss JN, Levy S. Neurologic Stem Cell Treatment Study (NEST) using bone marrow derived stem cells for the treatment of neurological disorders and injuries: study protocol for a nonrandomized efficacy trial. Clin Trials Degener Dis. 2016 [cited 2019 Jun 18];1:176-80.

Reference Type BACKGROUND

Related Links

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Other Identifiers

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MDSC-ACIST

Identifier Type: -

Identifier Source: org_study_id

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