Phase 3 Study of OTO-104 in Subjects With Unilateral Meniere's Disease

NCT ID: NCT03664674

Last Updated: 2022-12-07

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

148 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-08-27

Study Completion Date

2020-12-22

Brief Summary

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The purpose of this study is to evaluate the effectiveness of OTO-104 for the treatment of Meniere's disease.

Detailed Description

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Conditions

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Meniere Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Randomized, Double-blind, Placebo-controlled, Multicenter
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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OTO-104

Group Type EXPERIMENTAL

OTO-104

Intervention Type DRUG

Single intratympanic injection of 12 mg dexamethasone

placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Single intratympanic injection of placebo

Interventions

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OTO-104

Single intratympanic injection of 12 mg dexamethasone

Intervention Type DRUG

Placebo

Single intratympanic injection of placebo

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Subject has a diagnosis of unilateral Meniere's disease by 1995 American Academy of Otolaryngology - Head and Neck Surgery (AAOHNS) criteria and reports active vertigo for the 2 months prior to the study lead-in period.
* Subject has experienced active vertigo during the lead-in period.
* Subject has documented asymmetric sensorineural hearing loss.
* Subject agrees to maintain their current treatments for Meniere's disease while on-study.

Exclusion Criteria

* Subject is pregnant or lactating.
* Subject has a history of immunodeficiency disease.
* Subject has a history of significant middle ear or inner ear surgery, or endolymphatic sac surgery in the affected ear.
* Subject has a history of tympanostomy tubes with evidence of perforation or lack of closure.
* Subject has a history of vestibular migraine.
* Subject has used an investigational drug or device in the 3 months prior to screening.
* Subject has previously been randomized to a clinical study of OTO-104.
Minimum Eligible Age

18 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Otonomy, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Central California Clinical Research

Fresno, California, United States

Site Status

University of Colorado School of Medicine

Aurora, Colorado, United States

Site Status

Colorado ENT & Allergy

Colorado Springs, Colorado, United States

Site Status

Yale University School of Medicine

New Haven, Connecticut, United States

Site Status

Ear, Nose and Throat Associates of South Florida

Boynton Beach, Florida, United States

Site Status

Ear Research Foundation

Sarasota, Florida, United States

Site Status

Tandem Clinical Research

Marrero, Louisiana, United States

Site Status

Michigan Ear Institute

Farmington Hills, Michigan, United States

Site Status

Saint Louis University

St Louis, Missouri, United States

Site Status

Dent Neurologic Institute

Amherst, New York, United States

Site Status

New York Eye and Ear Infirmary of Mount Sinai

New York, New York, United States

Site Status

Charlotte Eye Ear Nose & Throat Associates, P.A.

Matthews, North Carolina, United States

Site Status

Piedmont Ear, Nose, and Throat Associates, PA

Winston-Salem, North Carolina, United States

Site Status

Medical University of South Carolina, Department of Otolaryngology

Charleston, South Carolina, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Intermountain Ear, Nose & Throat Specialists

Draper, Utah, United States

Site Status

West Virginia University School of Medicine

Morgantown, West Virginia, United States

Site Status

Universitair Ziekenhuis Antwerpen - Ear-Nose-Throat Department

Edegem, , Belgium

Site Status

UZ Gent - Ear-Nose-Throat Department

Ghent, , Belgium

Site Status

UZ Leuven - Ear-Nose-Throat Department

Leuven, , Belgium

Site Status

CHU de Liège - Ear-Nose-Throat Department

Liège, , Belgium

Site Status

Uniklinik RWTH Aachen, Klinik für Hals-, Nasen-, Ohrenheilkunde und Plastische Kopf- und Halschirurgie

Aachen, , Germany

Site Status

Praxis Bad Essen

Bad Essen, , Germany

Site Status

Charité Universitätsmedizin Berlin

Berlin, , Germany

Site Status

HNO Zentrum am Kudamm

Berlin, , Germany

Site Status

HNO-Praxis Göttingen

Göttingen, , Germany

Site Status

HNO Praxis am Neckar

Heidelberg, , Germany

Site Status

HNO Praxis Dres. med. Florian Heimlich und Angelika Witzel-Heimlich

Heidelberg, , Germany

Site Status

Universitätsklinikum Mannheim

Mannheim, , Germany

Site Status

HNO Praxis Dr. med. Roger Fisher

Markkleeberg, , Germany

Site Status

Klinikum der Universität München

München, , Germany

Site Status

Universitätsklinikum Ulm, HNO-Klinik. Kopf-Hals-Chirurgie

Ulm, , Germany

Site Status

U.O. di Otorinolaringoiatria Universitaria

Bari, NAP, Italy

Site Status

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico - U.O.S.D. Audiologia

Milan, , Italy

Site Status

Unità Operativa di Otorinolaringoiatria

Piacenza, , Italy

Site Status

Azienda Ospedaliera-Universitaria Sant' Andrea; Dipartimento Organi di Senso-U.O.C. Otorinolaringoiatria

Roma, , Italy

Site Status

10 Wojskowy Szpital Kliniczny z Polikliniką SP ZOZ Oddział

Bydgoszcz, , Poland

Site Status

Centrum Medyczne ZDROWA

Krakow, , Poland

Site Status

Centrum Medyczne PROMED

Krakow, , Poland

Site Status

MT Medic Specjalistyczna Praktyka Lekarska Tomasz Stapiński

Krosno, , Poland

Site Status

ETG Łódź

Lodz, , Poland

Site Status

Centrum Słuchu i Mowy Sp. z o.o.

Nadarzyn, , Poland

Site Status

Kliniczny Szpital Wojewódzki Nr 1 im. Fryderyka Chopina

Rzeszów, , Poland

Site Status

Agencia Pública Empresarial Sanitaria Hospital de Poniente

El Ejido, Almería, Spain

Site Status

Hospital Universitario de Getafe

Getafe, Madrid, Spain

Site Status

Hospital Universitario Virgen de las Nieves

Granada, , Spain

Site Status

Hospital Universitario Virgen Macarena

Seville, , Spain

Site Status

Hacettepe Universitesi Tip Fakultesi Kulak Burun Bogaz Hastaliklari Anabilim Dali

Ankara, , Turkey (Türkiye)

Site Status

Baskent Universitesi Ankara Hastanesi, Kulak Burun Bogaz Hastaliklari Ana Bilim Dali

Ankara, , Turkey (Türkiye)

Site Status

Bayindir Hastanesi Sogutozu, Kulak Burun Bogaz Bas ve Boyun Cerrahisi Bolumu

Ankara, , Turkey (Türkiye)

Site Status

Uludag Universitesi Saglik Uygulama ve Arastirma Merkezi, Kulak Burum Bogaz Hastaliklari Ana Bilim Dali

Bursa, , Turkey (Türkiye)

Site Status

Istanbul Universitesi Istanbul Tip Fakultesi Kulak Burun Bogaz Hastaliklari Anabilim Dali

Istanbul, , Turkey (Türkiye)

Site Status

Acibadem Maslak Hastanesi Kulak Burun Bogaz Bolumu

Istanbul, , Turkey (Türkiye)

Site Status

Ege Universitesi Tip Fakultesi Kulak Burun Bogaz Hastaliklari Anabilim Dali

Izmir, , Turkey (Türkiye)

Site Status

Dokuz Eylul Universitesi Tip Fakultesi Tip Bilimleri Bolumu Kulak Burun Bogaz Anabilim Dali

Izmir, , Turkey (Türkiye)

Site Status

Ninewells Hospital and Medical School

Dundee, Angus, United Kingdom

Site Status

Royal Victoria Hospital

Belfast, , United Kingdom

Site Status

Cambridge University Hospitals NHS Foundation Trust

Cambridge, , United Kingdom

Site Status

University Hospital of Wales

Cardiff, , United Kingdom

Site Status

Gloucestershire Royal Hospital

Gloucester, , United Kingdom

Site Status

University Hospitals of Leicester NHS Trust, Leicester Royal Infirmary

Leicester, , United Kingdom

Site Status

Guy's and St Thomas' NHS Foundation Trust

London, , United Kingdom

Site Status

Manchester Head and Neck Centre, Peter Mount Building

Manchester, , United Kingdom

Site Status

Norfolk & Norwich University Hospital

Norwich, , United Kingdom

Site Status

The Royal Hallamshire Hospital

Sheffield, , United Kingdom

Site Status

Countries

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United States Belgium Germany Italy Poland Spain Turkey (Türkiye) United Kingdom

References

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Phillips J, Mikulec AA, Robinson JM, Skarinsky D, Anderson JJ. Efficacy of Intratympanic OTO-104 for the Treatment of Meniere's Disease: The Outcome of Three Randomized, Double-Blind, Placebo-Controlled Studies. Otol Neurotol. 2023 Jul 1;44(6):584-592. doi: 10.1097/MAO.0000000000003886. Epub 2023 Apr 22.

Reference Type DERIVED
PMID: 37185596 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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104-201811

Identifier Type: -

Identifier Source: org_study_id

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