A Study of Soticlestat in Adults and Children With Rare Epilepsies

NCT ID: NCT03635073

Last Updated: 2025-09-05

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

156 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-07-19

Study Completion Date

2025-07-30

Brief Summary

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The main aim is to assess the long-term safety and tolerability of soticlestat when used along with other anti-seizure treatment.

Participants will receive soticlestat twice a day. Participants will visit the study clinic every 2-6 months throughout the study.

Study treatments may continue as long as the participant is receiving benefit from it.

Detailed Description

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The drug being tested in this study is called soticlestat (TAK-935). This global, open-label extension (OLE) study will assess the long-term safety and tolerability of soticlestat in participants with developmental and epileptic encephalopathy (DEE) who participated in previous short-term efficacy/safety studies of soticlestat. All participants will receive Soticlestat treatment.

Participants who rollover from previous blinded study will undergo up to 2 weeks of Dose Optimization Period (depending on the previous study) followed by Maintenance Period. Participants who rollover from an open-label study will continue on their current dose until development is stopped by the sponsor, or the product is approved for marketing, or at any time at the discretion of the sponsor. There will be a 4-week Safety Follow-up Period after the last dose in Maintenance Period, including a 2-week dose Tapering Period.

Conditions

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Epilepsy Dravet Syndrome (DS) Lennox-Gastaut Syndrome (LGS)

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Soticlestat

Treatment: Soticlestat, tablets orally twice daily at optimized dose, titrated in up to 2 weeks of Dose Optimization Period, followed by Maintenance Period, which lasts until development is stopped by the sponsor, or the product is approved for marketing, or at any time at the discretion of the sponsor.

Group Type EXPERIMENTAL

Soticlestat

Intervention Type DRUG

Soticlestat tablets or mini-tablets.

Interventions

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Soticlestat

Soticlestat tablets or mini-tablets.

Intervention Type DRUG

Other Intervention Names

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TAK-935

Eligibility Criteria

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Inclusion Criteria

1. Participants must have participated in a previous soticlestat study and meet one of the following conditions:

* Successfully completed a soticlestat clinical study.
* Received at least 10 weeks of treatment with the study drug in an antecedent placebo-controlled blinded soticlestat clinical study and the participant did not have a serious or severe AE that, in the investigator's or sponsor's opinion, was related to the study drug and would make it unsafe for the participant to continue receiving the study drug.
2. In the opinion of the investigator, the participant has the potential to benefit from the administration of soticlestat

Exclusion Criteria

1. Clinically significant disease, that, in the investigator's opinion, precludes study participation.
2. Enrollment in any other clinical trial involving an investigational drug, device, or treatment in the past 90 days (with the exception of an antecedent study involving Soticlestat).
3. Participant is currently pregnant or breastfeeding or is planning to become pregnant during the study or within 30 days of the last study drug administration.
4. Suicide attempt within the last year, at significant risk of suicide (either in the opinion of the investigator or defined as 'yes' to suicidal ideation question 4 or 5 on the C-SSRS at Screening) or appearing suicidal per investigator judgment.
Minimum Eligible Age

2 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Takeda

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Xenosciences Inc

Phoenix, Arizona, United States

Site Status

David Geffen School of Medicine at UCLA

Los Angeles, California, United States

Site Status

David Geffen School of Medicine at UCLA

Los Angeles, California, United States

Site Status

Colorado Children's Hospital

Aurora, Colorado, United States

Site Status

Colorado Children's Hospital

Aurora, Colorado, United States

Site Status

Nicklaus Children's Hospital

Miami, Florida, United States

Site Status

Nicklaus Children's Hospital

Miami, Florida, United States

Site Status

Medsol Clinical Research Center Inc

Port Charlotte, Florida, United States

Site Status

Medsol Clinical Research Center Inc

Port Charlotte, Florida, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Pediatric Neurology PA

Winter Park, Florida, United States

Site Status

Rare Disease Research, LLC

Atlanta, Georgia, United States

Site Status

Rare Disease Research, LLC

Atlanta, Georgia, United States

Site Status

Center for Rare Neurological Diseases

Norcross, Georgia, United States

Site Status

Ann and Robert H Lurie Childrens Hospital of Chicago

Chicago, Illinois, United States

Site Status

Bluegrass Epilepsy Research LLC

Lexington, Kentucky, United States

Site Status

Boston Children's Hospital

Boston, Massachusetts, United States

Site Status

Mayo Clinic - PIN

Rochester, Minnesota, United States

Site Status

Minnesota Epilepsy Group PA

Saint Paul, Minnesota, United States

Site Status

Max Benzaquen, M.D., PC

Chesterfield, Missouri, United States

Site Status

Northeast Regional Epilepsy Group

Hackensack, New Jersey, United States

Site Status

Children's Hospital at Saint Peter's University Hospital

New Brunswick, New Jersey, United States

Site Status

NYU - Ambulatory Care Center (ACC)

New York, New York, United States

Site Status

Columbia University Medical Center - PIN

New York, New York, United States

Site Status

Wake Forest Baptist Medical Center - PPDS

Winston-Salem, North Carolina, United States

Site Status

Medical University of South Carolina Childrens Hospital - PIN

Charleston, South Carolina, United States

Site Status

Cook Children's Medical Center - Jane and John Justin Neurosciences Center

Fort Worth, Texas, United States

Site Status

Monash Children's Hospital

Clayton, Victoria, Australia

Site Status

Austin Hospital

Heidelberg, Victoria, Australia

Site Status

Austin Hospital

Heidelberg West, Victoria, Australia

Site Status

Hospital For Sick Children

Toronto, Ontario, Canada

Site Status

Shenzhen Children's Hospital

Shenzhen, Guangdong, China

Site Status

Children's Hospital of Fudan University

Shanghai, Shanghai Municipality, China

Site Status

Peking University First Hospital

Beijing, , China

Site Status

Beijing Children's Hospital,Capital Medical University

Beijing, , China

Site Status

Beijing Children's Hospital,Capital Medical University

Beijing, , China

Site Status

Xiangya Hospital Central South University

Changsha, , China

Site Status

Xiangya Hospital of Central South University

Changsha, , China

Site Status

Tel Aviv Sourasky Medical Center PPDS

Tel Aviv, Tel Aviv, Israel

Site Status

Soroka University Medical Centre

Beersheba, , Israel

Site Status

Bnai Zion Medical Center

Haifa, , Israel

Site Status

Edith Wolfson Medical Center

Holon, , Israel

Site Status

Schneider Children's Medical Center of Israel - Petah Tikvah - PIN

Petah Tikva, , Israel

Site Status

Sheba Medical Center - PPDS

Ramat Gan, , Israel

Site Status

Sheba Medical Center - PPDS

Ramat Gan, , Israel

Site Status

Tel Aviv Sourasky Medical Center PPDS

Tel Aviv, , Israel

Site Status

Szpital Kliniczny im. H.Swiecickiego Uniwersytetu Medycznego im. Karola Marcinkowskiego w Poznaniu

Poznan, Greater Poland Voivodeship, Poland

Site Status

Uniwersyteckie Centrum Kliniczne

Gdansk, Pomeranian Voivodeship, Poland

Site Status

Centrum Medyczne Plejady

Krakow, , Poland

Site Status

Samodzielny Publiczny Dzieciecy Szpital Kliniczny w Warszawie

Warsaw, , Poland

Site Status

NZOZ Centrum Neurologii Dzieciecej i Leczenia Padaczki

Kielce, Świętokrzyskie Voivodeship, Poland

Site Status

Centro Hospitalar Lisboa Central- Hospital Dona Estefania

Lisbon, , Portugal

Site Status

Centro Hospitalar Lisboa Norte, E.P.E. Hospital de Santa Maria

Lisbon, , Portugal

Site Status

Centro Hospitalar Lisboa Norte, E.P.E. Hospital de Santa Maria

Lisbon, , Portugal

Site Status

Hospital Ruber Internacional (Grupo Quironsalud)

Madrid, Madrid, Communidad Delaware, Spain

Site Status

Clinica Universidad Navarra

Pamplona, Navarre, Spain

Site Status

Hospital Vithas La Salud

Granada, , Spain

Site Status

Hospital Ruber Internacional (Grupo Quironsalud)

Madrid, , Spain

Site Status

Hospital Universitari i Politecnic La Fe de Valencia

Valencia, , Spain

Site Status

Countries

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United States Australia Canada China Israel Poland Portugal Spain

Related Links

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Other Identifiers

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U1111-1218-5515

Identifier Type: OTHER

Identifier Source: secondary_id

2018-002485-39

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2022-502801-13-00

Identifier Type: CTIS

Identifier Source: secondary_id

TAK-935-18-001

Identifier Type: -

Identifier Source: org_study_id

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