Study to Investigate LP352 in Subjects With Developmental and Epileptic Encephalopathies

NCT ID: NCT05364021

Last Updated: 2024-11-08

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

52 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-03-03

Study Completion Date

2023-11-20

Brief Summary

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The objective of this study is to assess the safety, tolerability, efficacy, and pharmacokinetics of adjunctive therapy of LP352 in adults and adolescents with developmental and epileptic encephalopathies.

Detailed Description

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This is a randomized, double-blind, parallel-group, dose-escalation, placebo-controlled study of LP352 in adults and adolescents with developmental and epileptic encephalopathies (DEE) with an average of ≥ 4 observed/countable motor seizures per 4-week period during the 12 weeks before screening while on stable antiseizure medicine (ASM).

Subjects will be randomized 4:1 to LP352 or placebo. The study will have a baseline period of 28 days, followed by a 15 day up-titration period during which time subjects will titrate up to their highest tolerated doses, and a 60-day maintenance period. After Day 75, subjects will be tapered down over a period of up to 15 days, with a follow-up visit 30 days after last dose. Enrolled subjects will be allowed to continue treatment with up to 4 concomitant ASMs at a stable dose.

Conditions

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Developmental and Epileptic Encephalopathy Dravet Syndrome Lennox Gastaut Syndrome

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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LP352

Subjects will be titrated up to highest tolerated dose of LP352 during a 15-day period, followed by a 60-day maintenance period and a 15-day taper/down titration period.

Group Type EXPERIMENTAL

LP352

Intervention Type DRUG

LP352 administered three times daily, orally or through G-tube

Placebo

Placebo for LP352

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching placebo for LP352 administered three times daily, orally or through G-tube

Interventions

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LP352

LP352 administered three times daily, orally or through G-tube

Intervention Type DRUG

Placebo

Matching placebo for LP352 administered three times daily, orally or through G-tube

Intervention Type DRUG

Other Intervention Names

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Placebo Comparator

Eligibility Criteria

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Inclusion Criteria

1. Male or non-pregnant, non-lactating female, age 12 to 65 years
2. Diagnosis of Dravet syndrome, Lennox-Gastaut syndrome, or other developmental and epileptic encephalopathy
3. Has a minimum number of seizures per 4-week period while taking 1 to 4 anti-seizure medications
4. All medications and epilepsy interventions must be stable for 4 weeks before screening and are expected to remain stable during the study
5. The patient/parent/caregiver is able and willing to attend study visits, complete the diary and take study drug as instructed

Exclusion Criteria

1. Current or past history of cardiovascular or cerebrovascular disease, such as cardiac valvulopathy, myocardial infarction, stroke, pulmonary arterial hypertension or abnormal blood pressure
2. Has glaucoma, renal impairment, liver disease or any other medical condition that would affect study participation or pose a risk to the subject
3. Current or recent history of moderate or severe depression, anorexia nervosa, bulimia or at risk of suicidal behavior
4. Currently taking anorectic agents, monoamine oxidase inhibitors; serotonin agonists or antagonists including fenfluramine, atomoxetine, vortioxetine, or other medications for weight loss
5. Positive test result on the drug screen, except tetrahydrocannabinol (THC) for patients taking prescribed cannabidiol
Minimum Eligible Age

12 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Longboard Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Dennis J Dlugos, MD

Role: PRINCIPAL_INVESTIGATOR

Children's Hospital of Philadelphia

Locations

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University of Arizona - Health Sciences Center

Tucson, Arizona, United States

Site Status

Arkansas Children's Hospital

Little Rock, Arkansas, United States

Site Status

Rancho Los Amigos National Rehabilitation Center (RLANRC)

Downey, California, United States

Site Status

Children's Hospital of Orange County

Orange, California, United States

Site Status

University of California San Francisco

San Francisco, California, United States

Site Status

Northwest Florida Clinical Research Group

Gulf Breeze, Florida, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

Advent Health Orlando

Orlando, Florida, United States

Site Status

Research Institute of Orlando

Orlando, Florida, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Hawaii Pacific Neuroscience

Honolulu, Hawaii, United States

Site Status

Consultants in Epilepsy and Neurology

Boise, Idaho, United States

Site Status

Northwestern University Feinberg School of Medicine

Chicago, Illinois, United States

Site Status

Mid-Atlantic Epilepsy and Sleep Center

Bethesda, Maryland, United States

Site Status

Spectrum Health

Grand Rapids, Michigan, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Boston Children's Health Physicians LLP

Hawthorne, New York, United States

Site Status

New York University Langone Hospital - Long Island

Mineola, New York, United States

Site Status

Northwell Health

New York, New York, United States

Site Status

Northeast Regional Epilepsy Group

Staten Island, New York, United States

Site Status

OnSite Clinical Solutions LLC

Charlotte, North Carolina, United States

Site Status

Wake Forest University School of Medicine

Winston-Salem, North Carolina, United States

Site Status

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status

Providence Neurological Specialties-East

Portland, Oregon, United States

Site Status

Child Neurology Consultants of Austin

Austin, Texas, United States

Site Status

Austin Epilepsy Care Center

Austin, Texas, United States

Site Status

University of Utah

Salt Lake City, Utah, United States

Site Status

University of Washington Valley Medical Center

Renton, Washington, United States

Site Status

Royal Brisbane Women's Hospital

Herston, Queensland, Australia

Site Status

Queensland Children's Hospital

South Brisbane, Queensland, Australia

Site Status

Monash Children's Hospital, Monash Health

Clayton, Victoria, Australia

Site Status

Austin Health

Heidelberg, Victoria, Australia

Site Status

Alfred Health

Melbourne, Victoria, Australia

Site Status

Countries

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United States Australia

Other Identifiers

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LP352-201

Identifier Type: -

Identifier Source: org_study_id

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