M7824 Versus Pembrolizumab as a First-line (1L) Treatment in Participants With Programmed Death-ligand 1 (PD-L1) Expressing Advanced Non-small Cell Lung Cancer (NSCLC)

NCT ID: NCT03631706

Last Updated: 2025-04-08

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

304 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-10-01

Study Completion Date

2024-06-25

Brief Summary

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The purpose of the study is to evaluate the efficacy and safety of bintrafusp alfa (M7824) compared with pembrolizumab in participants with advanced NSCLC with high PD-L1-tumor expression, with no epidermal growth factor receptor (EGFR) mutation or anaplastic lymphoma kinase (ALK) translocation. The Phase III adaptive design allows for the option to recruit up to 584 patients based on pre-specified rules.

Detailed Description

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Conditions

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Non-small Cell Lung Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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M7824

Group Type EXPERIMENTAL

M7824

Intervention Type DRUG

Participants received intravenous infusion of M7824 at a dose of 1200 milligrams (mg) once every 2 weeks until confirmed progression of disease, death, unacceptable toxicity, or study withdrawal.

Pembrolizumab

Group Type ACTIVE_COMPARATOR

Pembrolizumab

Intervention Type DRUG

Pembrolizumab: Participants received intravenous infusion of Pembrolizumab at a dose of 200 milligrams (mg) once every 3 weeks until confirmed progression of disease, death, unacceptable toxicity, or study withdrawal.

Interventions

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M7824

Participants received intravenous infusion of M7824 at a dose of 1200 milligrams (mg) once every 2 weeks until confirmed progression of disease, death, unacceptable toxicity, or study withdrawal.

Intervention Type DRUG

Pembrolizumab

Pembrolizumab: Participants received intravenous infusion of Pembrolizumab at a dose of 200 milligrams (mg) once every 3 weeks until confirmed progression of disease, death, unacceptable toxicity, or study withdrawal.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Histologically confirmed diagnosis of advanced NSCLC
* Have not received prior systemic therapy treatment for their advanced/Stage four NSCLC. Completion of treatment with cytotoxic chemotherapy, biological therapy, and/or radiation as part of neoadjuvant/adjuvant therapy is allowed as long as therapy was completed at least 6 months prior to the diagnosis of metastatic disease. Confirmation of resolution of toxic effects of previous neoadjuvant/adjuvant chemotherapy therapy to Grade less than or equal to 1. For radiation toxicity or prior major surgeries, participants should have recovered from side effects and/or complications
* Have measurable disease based on RECIST 1.1
* Have a life expectancy of at least 3 months
* Availability of tumor tissue (less than 6 months old) before the first dose is mandatory to determine PD-L1 expression level prior to enrollment
* PD-L1 high status as determined by central testing

Exclusion Criteria

* Participants with nonsquamous NSCLC histologies whose tumor harbors any of the following molecular alterations and targeted therapy is locally approved: epidermal growth factor receptor (EGFR) sensitizing (activating) mutation, anaplastic lymphoma kinase (ALK) translocation, ROS1 rearrangement, or BRAF V600E mutation
* Has received major surgery within 4 weeks prior to the first dose of study intervention; received thoracic radiation therapy of greater than 30 units of gray (Gy) within 6 months prior to the first dose of study
* Known severe hypersensitivity to investigational products (M7824 or pembrolizumab), or any components in their formulations
* Previous malignant disease (other than the target malignancy to be investigated in this study) within the last 3 years
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck KGaA, Darmstadt, Germany

INDUSTRY

Sponsor Role collaborator

EMD Serono Research & Development Institute, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Responsible

Role: STUDY_DIRECTOR

Merck KGaA, Darmstadt, Germany

Locations

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Oncology Specialties, PC; Clearview Cancer Institute

Huntsville, Alabama, United States

Site Status

Cedars Sinai Medical Center - Inflammatory Bowel Disease Center (Clinic

Los Angeles, California, United States

Site Status

UC Irvine Medical Center

Orange, California, United States

Site Status

Kaiser Permanente - Harbor City

San Diego, California, United States

Site Status

Sansum Clinic - Santa Barbara

Santa Barbara, California, United States

Site Status

Rocky Mountain Cancer Centers - Colorado Springs, N. Nevada

Colorado Springs, Colorado, United States

Site Status

Eastern Connecticut Hematology/Oncology Assoc.

Norwich, Connecticut, United States

Site Status

Cancer Specialists, LLC - Department of Clinical Research

Jacksonville, Florida, United States

Site Status

Woodlands Medical Specialists

Pensacola, Florida, United States

Site Status

The University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

Decatur Memorial Hospital - Clinical Research

Decatur, Illinois, United States

Site Status

Baptist Health Lexington Oncology Associates

Lexington, Kentucky, United States

Site Status

Norton Cancer Institute

Louisville, Kentucky, United States

Site Status

Henry Ford Medical Center

Detroit, Michigan, United States

Site Status

Health Midwest Ventures Group, Inc d/b/a HCA MidAmerica Division, LLC - Menorah Medical Center - Oncology Account

Kansas City, Missouri, United States

Site Status

Southeast Nebraska Cancer Center

Lincoln, Nebraska, United States

Site Status

The Valley Hospital - Luckow Pavilion

Paramus, New Jersey, United States

Site Status

University of Rochester Medical Center

Rochester, New York, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

UPMC Cancer Center

Pittsburgh, Pennsylvania, United States

Site Status

SCRI - Tennessee Oncology

Nashville, Tennessee, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Texas Oncology - Bedford

Bedford, Texas, United States

Site Status

Texas Oncology, P.A. - Sugarland

Sugar Land, Texas, United States

Site Status

Virginia Cancer Specialists, PC

Fairfax, Virginia, United States

Site Status

Centro de Oncologia e Investigacion Buenos Aires

Berazategui, , Argentina

Site Status

Instituto Medico Especializado Alexander Fleming

Ciudad Autonoma Buenos Aires, , Argentina

Site Status

Sanatorio Allende

Córdoba, , Argentina

Site Status

Instituto Medico Rio Cuarto

Río Cuarto, , Argentina

Site Status

Instituto de Oncología de Rosario

Rosario, , Argentina

Site Status

Centro Medico San Roque S.R.L.

San Miguel de Tucumán, , Argentina

Site Status

Universitair Ziekenhuis Brussel - Geriatrie

Brussels, , Belgium

Site Status

Jessa Ziekenhuis Hospital

Hasselt, , Belgium

Site Status

UZ Leuven

Pellenberg, , Belgium

Site Status

CHU Mont-Godinne

Yvoir, , Belgium

Site Status

Hospital de Câncer de Barretos - Fundação Pio XII

Barretos, , Brazil

Site Status

CRIO - Centro Regional Integrado de Oncologia

Fortaleza, , Brazil

Site Status

Hospital São Lucas da PUCRS

Porto Alegre, , Brazil

Site Status

INCA - Instituto Nacional de Câncer

Rio de Janeiro, , Brazil

Site Status

NOB - Núcleo de Oncologia da Bahia

Salvador, , Brazil

Site Status

CEPHO - Centro de Estudos e Pesquisas em Hematologia e Oncologia - Faculdade de Medicina do ABC

Santo André, , Brazil

Site Status

Saint John Regional Hospital

Saint John, New Brunswick, Canada

Site Status

Tom Baker Cancer Centre

Alberta, , Canada

Site Status

Stronach Regional Cancer Centre - at Southlake

Ontario, , Canada

Site Status

Peking University Cancer Hospital

Beijing, , China

Site Status

Guangdong General Hospital

Guangzhou, , China

Site Status

Shanghai Cancer Hospital, Fudan University

Shanghai, , China

Site Status

Groupe Hospitalier Sud - Hôpital Haut-Lévêque - Maison du Ha

Pessac, Gironde, France

Site Status

Centre Hospitalier Intercommunal de Créteil - Service de Pneumologie

Créteil, Val De Marne, France

Site Status

Hôpital Nord - AP-HM Marseille# - Service d'Oncologie Multidisciplinaire

Bouches-du-Rhône, , France

Site Status

Centre Léon Bérard

Lyon, , France

Site Status

CHU Rennes - Hopital Pontchaillou - service de pneumologie

Rennes, , France

Site Status

ICO - Site René Gauducheau

Saint-Herblain, , France

Site Status

CHU de Toulouse - Hôpital Larrey - Service de Pneumologie et Oncologie Pneumologique

Toulouse, , France

Site Status

Vivantes Klinikum Am Urban - Haematologie und Onkologie

Berlin, , Germany

Site Status

Asklepios Fachkliniken Muenchen-Gauting - Abteilung Internistische Onkologie

Gauting, , Germany

Site Status

LungenClinic Grosshansdorf

Großhansdorf, , Germany

Site Status

Medizinische Hochschule Hannover - Pneumologie

Hanover, , Germany

Site Status

Universitaetsklinikum Schleswig- Holstein Campus Luebeck

Lübeck, , Germany

Site Status

Universitaetsklinikum Regensburg - Klinik und Poliklinik fuer Innere Medizin II

Regensburg, , Germany

Site Status

251 General Air Force Hospital

Athens, , Greece

Site Status

General Hospital of Athens of Chest Disease "SOTIRIA"

Athens, , Greece

Site Status

University General Hospital of Heraklion "PAGNI"

Heraklion, , Greece

Site Status

General Hospital Papageorgiou-2nd Department of Dermatalogy

Thessaloniki, , Greece

Site Status

Princess Margaret Hospital

Hong Kong, , Hong Kong

Site Status

The University of Hong Kong

Hong Kong, , Hong Kong

Site Status

The Chinese University of Hong Kong - Emergency Medicine

Shatin, , Hong Kong

Site Status

Azienda Ospedaliera San Giuseppe Moscati - U.O Oncologia Medica

Avellino, , Italy

Site Status

IRCCS Centro di Riferimento Oncologico - Oncologia Medica A

Aviano, , Italy

Site Status

Azienda Ospedaliera Universitaria Policlinico Sant'Orsola Malpighi - Oncologia Medica

Bologna, , Italy

Site Status

Azienda Ospedaliera Univ. Policlinico Gaspare Rodolico - Unità Operativa di Oncologia

Catania, , Italy

Site Status

Azienda Ospedaliero Universitaria Mater Domini-Campus Universitario - Centro Oncologico

Catanzaro, , Italy

Site Status

Fondazione IRCCS Istituto Nazionale dei Tumori - Medicina Oncologica I

Milan, , Italy

Site Status

Università degli studi della Campania Luigi Vanvitelli - Dipartimento di Oncologia

Napoli, , Italy

Site Status

NHO Hokkaido Cancer Center - Dept of Respiratory Medicine

Sapporo, Hokkaido, Japan

Site Status

National Cancer Center Hospital - Dept of Respiratory Medicine

Chūōku, , Japan

Site Status

Saitama Medical University International Medical Center - Dept of Respiratory Medicine

Hidaka-shi, , Japan

Site Status

Saitama Cancer Center

Kitaadachigun, , Japan

Site Status

Cancer Institute Hospital of JFCR - Dept of Respiratory Medicine

Kōtoku, , Japan

Site Status

Kurume University Hospital

Kurume-shi, , Japan

Site Status

Osaka Medical Center for Cancer and Cardiovascular Diseases

Osaka, , Japan

Site Status

Kindai University Hospital

Osakasayama-sh, , Japan

Site Status

Antoni van Leeuwenhoek Ziekenhuis

Amsterdam, , Netherlands

Site Status

VU Medisch Centrum

Amsterdam, , Netherlands

Site Status

Universitair Medisch Centrum Groningen (UMCG) - Parent

Groningen, , Netherlands

Site Status

Maastricht University Medical Center - Dept of Medical Oncology

Maastricht, , Netherlands

Site Status

Erasmus Medisch Centrum

Rotterdam, , Netherlands

Site Status

St. Elisabeth Ziekenhuis - Parent

Tilburg, , Netherlands

Site Status

Seoul National University Bundang Hospital

Seongnam-si, Gyeonggi-do, South Korea

Site Status

Chungbuk National University Hospital

Cheongju-si, North Chungcheong, South Korea

Site Status

Gachon University Gil Medical Center

Incheon, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Hospital del Mar - Servicio de Oncologia

Barcelona, , Spain

Site Status

Hospital Universitari Quiron Dexeus - Servicio de Oncologia Medica

Barcelona, , Spain

Site Status

Hospital Universitari Vall d'Hebron - Dept of Oncology

Barcelona, , Spain

Site Status

ICO l´Hospitalet - Hospital Duran i Reynals - Servicio de Oncologia

L'Hospitalet de Llobregat, , Spain

Site Status

Hospital General Universitario Gregorio Marañon - Servicio de Oncologia Medica

Madrid, , Spain

Site Status

Hospital Universitario 12 de Octubre - Servicio de Oncologia

Madrid, , Spain

Site Status

Hospital Regional Universitario de Malaga

Málaga, , Spain

Site Status

Hospital Universitario Virgen Macarena - Servicio de Oncologia

Seville, , Spain

Site Status

Hospital Universitario Virgen del Rocio - Servicio de Oncologia

Seville, , Spain

Site Status

Hospital Universitari i Politecnic La Fe - Servicio de Oncologia Medica

Valencia, , Spain

Site Status

Taichung Veterans General Hospital

Taichung, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Tri-Service General Hospital

Taipei, , Taiwan

Site Status

Adana Numune Training and Research Hospital - Cardiology Department

Adana, , Turkey (Türkiye)

Site Status

Dr. Abdurrahman Yurtaslan Oncology Teaching and Research Hospital - Oncology Department

Ankara, , Turkey (Türkiye)

Site Status

Trakya University Medical Faculty - Medical Oncology

Edirne, , Turkey (Türkiye)

Site Status

Kocaeli University Research and Application Hospital

Kocaeli, , Turkey (Türkiye)

Site Status

CI Dnipropetrovsk CMCH #4 of Dnipropetrovsk RC Dept of Chemotherapy SI Dnipropetrovsk MA of MOHU - Ch of Oncology and MR

Dnipro, , Ukraine

Site Status

CI Transcarpathian Cl Onc Center Dep of Surgery#1 SHEI Ivano-Frankivsk NMU - Chair of Oncology

Ivano-Frankivsk, , Ukraine

Site Status

Communal Non-profit Enterprise Regional Center of Oncology - Parent

Kharkiv, , Ukraine

Site Status

Medical and Preventive Treatment Institution Volyn Regional Oncological Dispensary - Dept of Oncochemotherapy

Lutsk, , Ukraine

Site Status

CCCH City Oncological Center SHEI Uzhgorod NU - Ch of R&O of Faculty of PGE&PUT

Uzhhorod, , Ukraine

Site Status

Medical center "Oncolife"

Zaporizhzhia, , Ukraine

Site Status

Countries

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United States Argentina Belgium Brazil Canada China France Germany Greece Hong Kong Italy Japan Netherlands South Korea Spain Taiwan Turkey (Türkiye) Ukraine

References

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Brown T, Pilkington G, Bagust A, Boland A, Oyee J, Tudur-Smith C, Blundell M, Lai M, Martin Saborido C, Greenhalgh J, Dundar Y, Dickson R. Clinical effectiveness and cost-effectiveness of first-line chemotherapy for adult patients with locally advanced or metastatic non-small cell lung cancer: a systematic review and economic evaluation. Health Technol Assess. 2013 Jul;17(31):1-278. doi: 10.3310/hta17310.

Reference Type RESULT
PMID: 23886301 (View on PubMed)

Cho BC, Lee JS, Wu YL, Cicin I, Dols MC, Ahn MJ, Cuppens K, Veillon R, Nadal E, Dias JM, Martin C, Reck M, Garon EB, Felip E, Paz-Ares L, Mornex F, Vokes EE, Adjei AA, Robinson C, Sato M, Vugmeyster Y, Machl A, Audhuy F, Chaudhary S, Barlesi F. Bintrafusp Alfa Versus Pembrolizumab in Patients With Treatment-Naive, Programmed Death-Ligand 1-High Advanced NSCLC: A Randomized, Open-Label, Phase 3 Trial. J Thorac Oncol. 2023 Dec;18(12):1731-1742. doi: 10.1016/j.jtho.2023.08.018. Epub 2023 Aug 18.

Reference Type RESULT
PMID: 37597750 (View on PubMed)

Milenkovic-Grisic AM, Terranova N, Mould DR, Vugmeyster Y, Mrowiec T, Machl A, Girard P, Venkatakrishnan K, Khandelwal A. Tumor growth inhibition modeling in patients with second line biliary tract cancer and first line non-small cell lung cancer based on bintrafusp alfa trials. CPT Pharmacometrics Syst Pharmacol. 2024 Jan;13(1):143-153. doi: 10.1002/psp4.13068. Epub 2023 Dec 13.

Reference Type DERIVED
PMID: 38087967 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://medical.emdserono.com/en_US/home.html

US Medical Information website, Medical Resources

Other Identifiers

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2018-001517-32

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

MS200647_0037

Identifier Type: -

Identifier Source: org_study_id

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