An Efficacy and Safety Study of APX001 in Non-Neutropenic Patients With Candidemia

NCT ID: NCT03604705

Last Updated: 2025-09-16

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

21 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-10-03

Study Completion Date

2020-07-02

Brief Summary

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This is a multicenter, open-label, non-comparative, single-arm study to evaluate the efficacy and safety of APX001 for the first-line treatment for candidemia including suspected or confirmed antifungal-resistant candidemia in non-neutropenic patients 18 yeas of age and older.

Suspicion of antifungal-resistant candidemia is sufficient (documented resistance is not required for enrollment). The Study Drug Treatment Period of APX001 will be a maximum of 14 days. After completion of 14 days study drug therapy, if further antifungal treatment is indicated to complete treatment of candidemia in accordance with standard practice guidelines, fluconazole (unless susceptibility results warrant alternative antifungal therapy) may commence for up to a further 7 days. There will be a Follow up Period of 4 weeks (+4 days) after EOT. The total duration of participation in the study is up to approximately 7.5 weeks.

This study will be conducted at approximately 20 sites in the United States and globally.

Detailed Description

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Conditions

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Candidemia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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APX001 Treatment

Group Type EXPERIMENTAL

APX001

Intervention Type DRUG

APX001

Interventions

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APX001

APX001

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Provision of written consent
* Adults ages 18 and above male or female
* New diagnosis of candidemia
* Able to have pre-existing intravascular catheters removed and replaced (as necessary)

Exclusion Criteria

* neutropenia
* deep-seated Candida-related infections
* hepatosplenic candidiasis
* received more than 2 days of prior systemic antifungal treatment for current candidemia episode
* severe hepatic impairment
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Basilea Pharmaceutica

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Marc Engelhardt

Role: STUDY_DIRECTOR

Basilea Pharmaceutica International Ltd, Allschwil

Locations

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University of Alabama at Birmingham School of Medicine

Birmingham, Alabama, United States

Site Status

University of Alabama at Birmingham (UAB)

Birmingham, Alabama, United States

Site Status

University of California, Davis

Davis, California, United States

Site Status

University of California-Davis Medical Center

Sacramento, California, United States

Site Status

Augusta University (Georgia Regents University)

Augusta, Georgia, United States

Site Status

University of Chicago

Chicago, Illinois, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

Duke University Hospital Medical Center

Durham, North Carolina, United States

Site Status

University of Texas- Health Science Center and Medical School at Houston

Houston, Texas, United States

Site Status

Institut Jules Bordet,Service De Microbiologie

Brussels, , Belgium

Site Status

Hopital Erasme

Brussels, , Belgium

Site Status

Institut Jules Bordet

Brussels, , Belgium

Site Status

Universite Libre de Bruxelles (ULB) - Hopital Erasme

Brussels, , Belgium

Site Status

CHU de Charleroi - Hopital Civil Marie Curie

Lodelinsart, , Belgium

Site Status

Mont-Godinne University Hospital

Yvoir, , Belgium

Site Status

University Hospital Mont-Godinne

Yvoir, , Belgium

Site Status

Klinik I fur Innere Medizin- Uniklinik Koln

Cologne, , Germany

Site Status

University Hospital Heidelberg

Heidelberg, , Germany

Site Status

Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz - III. Medizinische Klinik Haematologie/Onkologie

Mainz, , Germany

Site Status

Infectious Diseases Unit, Rambam Medical Center

Haifa, , Israel

Site Status

Rambam Medical Center

Haifa, , Israel

Site Status

Infectious Diseases Unit

Tel Aviv, , Israel

Site Status

Sourasky Medical Center

Tel Aviv, , Israel

Site Status

Infectious Diseases Unit,Sheba Medical Center

Tel Litwinsky, , Israel

Site Status

Sheba Medical Center

Tel Litwinsky, , Israel

Site Status

Hospital Universitario Mutua de Terrassa

Terrassa, Barcelona, Spain

Site Status

Hospital General Universitario de Alicante

Alicante, , Spain

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital VLL D Hebron

Barcelona, , Spain

Site Status

Countries

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United States Belgium Germany Israel Spain

References

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Pappas PG, Vazquez JA, Oren I, Rahav G, Aoun M, Bulpa P, Ben-Ami R, Ferrer R, Mccarty T, Thompson GR, Schlamm H, Bien PA, Barbat SH, Wedel P, Oborska I, Tawadrous M, Hodges MR. Clinical safety and efficacy of novel antifungal, fosmanogepix, for the treatment of candidaemia: results from a Phase 2 trial. J Antimicrob Chemother. 2023 Oct 3;78(10):2471-2480. doi: 10.1093/jac/dkad256.

Reference Type RESULT
PMID: 37596890 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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C4791009

Identifier Type: OTHER

Identifier Source: secondary_id

APX001-201

Identifier Type: -

Identifier Source: org_study_id

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