Safety, Efficacy, PK and PD of CTAP101 (Calcifediol) ER Capsules for SHPT in HD Patients VDI

NCT ID: NCT03602261

Last Updated: 2025-03-30

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

44 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-07-09

Study Completion Date

2021-02-24

Brief Summary

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Safety, Efficacy, PK and PD of CTAP101 (calcifediol) ER Capsules for SHPT in HD Patients VDI

Detailed Description

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A Multi-Center, Randomized, Two-Cohort Phase 2 Study to Evaluate the Safety, Efficacy, Pharmacokinetics (PK) and Pharmacodynamics (PD) of CTAP101 (calcifediol) Extended-Release Capsules to Treat Secondary Hyperparathyroidism (SHPT) in Subjects with Vitamin D Insufficiency (VDI) and Chronic Kidney Disease Requiring Regular Hemodialysis.

Conditions

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Secondary Hyperparathyroidism Due to Renal Causes Chronic Kidney Diseases Vitamin D Deficiency Stage 5 Chronic Kidney Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

SINGLE

Participants

Study Groups

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CTAP101 Capsules 900mcg/weekly

CTAP101 Oral Capsules/Calcifediol, calcidiol, 25-hydroxyvitamin D3, 900mcg/weekly for 26 weeks

Group Type ACTIVE_COMPARATOR

Calcifediol Oral Capsule

Intervention Type DRUG

Capsule, weekly

Placebo Capsules weekly

Placebo Oral Capsules/weekly for 26 weeks

Group Type PLACEBO_COMPARATOR

Placebo oral capsule

Intervention Type DRUG

Capsule, weekly

Interventions

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Calcifediol Oral Capsule

Capsule, weekly

Intervention Type DRUG

Placebo oral capsule

Capsule, weekly

Intervention Type DRUG

Other Intervention Names

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CTAP101

Eligibility Criteria

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Inclusion Criteria

Each subject must meet the following criteria to be enrolled in this study:

1. Be at least 18 years of age.
2. Be diagnosed with CKD requiring in-center HD tiw for the preceding 6 months, as confirmed by medical history.
3. Be without any disease state or physical condition that might impair evaluation of safety or which, in the investigator's opinion, would interfere with study participation, including:

1. Serum albumin ≤ 3.0 g/dL; and,
2. Serum transaminase (alanine transaminase \[ALT\], glutamic pyruvic transaminase \[SGPT\], aspartate aminotransferase \[AST\] or glutamic oxaloacetic transaminase \[SGOT\]) \> 2.5 times the upper limit of normal at screening.
4. Be receiving calcimimetic therapy (either etelcalcetide or cinacalcet) and/or calcitriol or other 1α-hydroxylated vitamin D analog (paricalcitol or doxercalciferol) for at least 1 month at the time of screening for enrollment. Approximately 50% of enrolled subjects will have been receiving calcimimetic therapy.
5. Exhibit during the initial screening visit:

1. Plasma immunoreactive parathyroid hormone (iPTH) ≥150 pg/mL and \<600 pg/mL if receiving etelcalcetide, cinacalcet, calcitriol or other 1α-hydroxylated vitamin D analog (paricalcitol or doxercalciferol); or
2. Plasma iPTH ≥300 pg/mL and \<900 pg/mL if not receiving etelcalcetide, cinacalcet, calcitriol or other 1α-hydroxylated vitamin D analog; and,
3. Serum total 25-hydroxyvitamin D \<30 ng/mL if not receiving vitamin D supplementation.
6. When otherwise confirmed eligible at Visit 1, must forgo any further treatment with etelcalcetide and cinacalcet for the duration of the study and undergo an 8-week washout period.
7. When otherwise confirmed eligible at Visit 1, must forgo any further treatment with calcitriol or other 1α-hydroxylated vitamin D analogs or vitamin D supplements for the duration of the study and undergo an 8-week washout period.
8. Exhibit after the 8-week washout period (if required due to prior use of etelcalcetide, cinacalcet, calcitriol or other 1α-hydroxylated vitamin D analogs, or vitamin D supplementation):

1. Plasma iPTH increased by at least 50%;
2. Plasma iPTH ≥300 pg/mL and \<1,200 pg/mL;
3. Corrected serum calcium \<9.8 mg/dL;
4. Serum total 25-hydroxyvitamin D \<50 ng/mL; and,
5. Serum phosphorus \<6.5 mg/dL.
9. When otherwise confirmed eligible at Visit 1, if taking more than 1,000 mg per day of elemental calcium, reduce calcium use (to ≤1,000 mg per day) and/or use non-calcium based phosphate binder therapies (as needed) for the duration of the study.
10. When otherwise confirmed eligible at Visit 1, if taking bone metabolism therapies that may interfere with study endpoints, must discontinue use of these agents for the duration of the study.
11. Willing and able to comply with study instructions and commit to all clinic visits for the duration of the study.
12. Female subjects of childbearing potential must be neither pregnant nor lactating and must have a negative serum beta-human chorionic gonadotropin (b-hCG) pregnancy test at the first screening visit and at other scheduled times.
13. All female subjects of childbearing potential and male subjects with female partners of childbearing potential must agree to use effective contraception (eg, implants, injectables, combined oral contraceptives, intrauterine device, sexual abstinence, vasectomy or vasectomized partner) for the duration of the study.
14. Be able to read, understand and sign the subject Informed Consent Form (ICF) or have a legal representative sign the ICF.

Exclusion Criteria

Subjects who meet any of the following criteria will be excluded from the study:

1. Scheduled kidney transplant or parathyroidectomy.
2. History (prior 2 months) of corrected serum calcium ≥9.8 mg/dL or serum phosphorus

≥6.5 mg/dL if not receiving calcitriol or other 1α-hydroxylated vitamin D analog.
3. Receipt of bisphosphonate therapy or other bone modifying treatment (eg, denosumab) within 6 months prior to enrollment.
4. Known previous or concomitant serious illness or medical condition, such as malignancy, human immunodeficiency virus, significant gastrointestinal or hepatic disease, intestinal malabsorption disorder, hepatitis or cardiovascular event that in the opinion of the investigator may worsen or reduce life expectancy, and/or interfere with participation in the study.
5. History of neurological/psychiatric disorder, including psychotic disorder or dementia, or any reason which, in the opinion of the investigator makes adherence to a treatment or follow-up schedule unlikely.
6. Known or suspected hypersensitivity to any of the constituents of the study drugs.
7. Currently participating in, or has participated in, an interventional/investigational study within 30 days prior to study screening.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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OPKO Health, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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AKDHC Medical Research Services

Peoria, Arizona, United States

Site Status

AKDHC Medical Research Services

Phoenix, Arizona, United States

Site Status

AKDHC Medical Research Services

Phoenix, Arizona, United States

Site Status

AKDHC Medical Research Services

Phoenix, Arizona, United States

Site Status

WCCT Global, Inc.

Cypress, California, United States

Site Status

Hacienda Dialysis Center

Hacienda Heights, California, United States

Site Status

California Institute of Renal Research CKD/Dialysis & Transplant Division

La Mesa, California, United States

Site Status

Long Beach Quest Dialysis Center

Long Beach, California, United States

Site Status

Ontario Dialysis Center

Ontario, California, United States

Site Status

North America Research Institute, Inc.

San Dimas, California, United States

Site Status

Laurel Canyon Dialysis, LLC

Sun Valley, California, United States

Site Status

University of Colorado Denver Anschutz Medical Campus

Aurora, Colorado, United States

Site Status

Research by Design, LLC

Chicago, Illinois, United States

Site Status

Northshore University Health

Evanston, Illinois, United States

Site Status

Renal and Transplant Associates of New England

Springfield, Massachusetts, United States

Site Status

Southwest MS Nephrology

McComb, Mississippi, United States

Site Status

Southwest Houston Research LTD

Houston, Texas, United States

Site Status

Kidney & Hypertension Specialists

San Antonio, Texas, United States

Site Status

Countries

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United States

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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CTAP101-CL-2010

Identifier Type: -

Identifier Source: org_study_id

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