Anti-MUC1 CAR T Cells and PD-1 Knockout Engineered T Cells for NSCLC

NCT ID: NCT03525782

Last Updated: 2018-05-16

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

UNKNOWN

Clinical Phase

PHASE1/PHASE2

Total Enrollment

60 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-02-01

Study Completion Date

2022-01-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The study is to assess the safety and efficacy of the anti-MUC1 CAR T cells and /or PD-1 knockout engineered T cells for patients with advanced non-small cell lung cancer.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This is a combined phase 1 and 2 clinical study. The study is to assess the safety and efficacy of the anti-MUC1 CAR T cells and /or PD-1 knockout engineered T cells for patients with advanced non-small cell lung cancer. The treatment outcomes will be compared.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Lung Neoplasm Malignant Non-small Cell Lung Cancer

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

SINGLE

Participants

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

CAR-T

Anti-MUC1 CAR-T cells will be prepared ex vivo and infused back to the patients.

Group Type EXPERIMENTAL

CAR-T Cells

Intervention Type BIOLOGICAL

Using the T cells from the patients to produce anti-MUC1 CAR-T Cells and then the cells will be infused back to the patients.

CAR-T combining PD-1 knockout

Anti-MUC1 CAR-T cells and PD-1 knockout Engineered T cells will be prepared ex vivo and infused back to the patients.

Group Type EXPERIMENTAL

CAR-T Cells

Intervention Type BIOLOGICAL

Using the T cells from the patients to produce anti-MUC1 CAR-T Cells and then the cells will be infused back to the patients.

CAR-T combining PD-1 Knockout

Intervention Type COMBINATION_PRODUCT

Using the T cells from the patients to prepare anti-MUC1 CAR-T Cells and PD-1 knockout T cells, then the cells will be infused back to the patients

PD-1 knockout

Intervention Type BIOLOGICAL

Using the T cells from the patients to prepare PD-1 knockout T cells, then the cells will be infused back to the patients

PD-1 knockout

PD-1 knockout Engineered T cells will be prepared ex vivo and infused back to the patients.

Group Type EXPERIMENTAL

PD-1 knockout

Intervention Type BIOLOGICAL

Using the T cells from the patients to prepare PD-1 knockout T cells, then the cells will be infused back to the patients

PD-1 mAb

Patients will be treated with a FDA approved monoclonal antibody for an identical course of treatment. This group will serve as PD-1 antibody treated group.

Group Type ACTIVE_COMPARATOR

PD-1 mAb

Intervention Type DRUG

Patients will be treated with an identical course with a FDA approved monoclonal antibody against PD-1

Sham Control

Patient's T cells will be separate without genetic or engineered modification ex vivo and infused back to the patients.

Group Type PLACEBO_COMPARATOR

Sham control

Intervention Type OTHER

Patient's T cell will treated ex vivo with modification and then infused back in a similar time course.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

CAR-T Cells

Using the T cells from the patients to produce anti-MUC1 CAR-T Cells and then the cells will be infused back to the patients.

Intervention Type BIOLOGICAL

CAR-T combining PD-1 Knockout

Using the T cells from the patients to prepare anti-MUC1 CAR-T Cells and PD-1 knockout T cells, then the cells will be infused back to the patients

Intervention Type COMBINATION_PRODUCT

PD-1 knockout

Using the T cells from the patients to prepare PD-1 knockout T cells, then the cells will be infused back to the patients

Intervention Type BIOLOGICAL

PD-1 mAb

Patients will be treated with an identical course with a FDA approved monoclonal antibody against PD-1

Intervention Type DRUG

Sham control

Patient's T cell will treated ex vivo with modification and then infused back in a similar time course.

Intervention Type OTHER

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

Keytruda

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* MUC1 is expressed in malignancy tissues by immuno-histochemical (IHC).
* Eastern cooperative oncology group (ECOG) performance status of 0-1 or karnofsky performance status (KPS) score is higher than 60.
* Patients have a life expectancy \> 12 weeks.
* Adequate venous access for apheresis or venous sampling, and no other contraindications for leukapheresis.
* Negative pregnancy test for females of child-bearing potentials.
* Adequate bone marrow, liver and renal function as assessed by the following laboratory requirements: White blood cell count (WBC) ≥ 2500c/ml, Platelets ≥ 50×10\^9/L, Hb ≥ 9.0g/dL, lymphocyte (LY) ≥ 0.7×10\^9/L, LY% ≥ 15%, Alb ≥ 2.8g/dL, serum lipase and amylase \< 1.5×upper limit of normal, serum creatinine ≤ 2.5mg/dL, aspartate aminotransferase (AST) and alanine aminotransferase (ALT) ≤ 5×upper limit of normal, serum total bilirubin ≤ 2.0mg/dL. These tests must be conducted within 7 days prior to registration.
* Signed informed consent form.

Exclusion Criteria

* Number of T cells is less than 10% or the amplification of the T cells via artificial antigen presenting cell (aAPC) stimulation is less than 5 times.
* Patients with symptomatic central nervous system (CNS) involvement.
* Pregnant or nursing women.
* Known HIV infection.
* Serious illness or medical condition which would not permit the patient to be managed according to the protocol, including active uncontrolled infection, major cardiovascular, coagulation disorders, respiratory or immune system, myocardial infarction, cardiac arrhythmias, obstructive/restrictive pulmonary disease, or psychiatric or emotional disorders.
* History of severe immediate hypersensitivity to any of the agents including cyclophosphamide, fludarabine, or aldesleukin.
* Concurrent use of systemic steroids. Recent or current use of inhaled steroids is not exclusionary.
* Previously treatment with any gene therapy products.
* The existence of unstable or active ulcers or gastrointestinal bleeding. Patients with portal vein vascular invasion or extrahepatic, are excluded from this study.
* Patients with a history of organ transplantation or are waiting for organ transplantation.
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Guangzhou Anjie Biomedical Technology Co., Ltd.

INDUSTRY

Sponsor Role collaborator

University of Technology, Sydney

OTHER

Sponsor Role collaborator

The First Affiliated Hospital of Guangdong Pharmaceutical University

OTHER

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Size Chen

Professor

Responsibility Role PRINCIPAL_INVESTIGATOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

First Affiliated Hospital of Guangdong Pharmaceutical University

Guangzhou, Guangdong, China

Site Status RECRUITING

Professor Size Chen

Guangzhou, Guangdong, China

Site Status RECRUITING

Professor Size Chen

Guangzhou, Guangdong, China

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

China

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Guobiao Huang

Role: primary

86-20-39352064

Size Chen, MD,PhD

Role: primary

+8613720956393

Zhizhou Huang, MSc

Role: backup

+8613268258980

Size Chen, MD,PhD

Role: primary

+8613720956393

References

Explore related publications, articles, or registry entries linked to this study.

Barr T, Ma S, Li Z, Yu J. Recent advances and remaining challenges in lung cancer therapy. Chin Med J (Engl). 2024 Mar 5;137(5):533-546. doi: 10.1097/CM9.0000000000002991. Epub 2024 Feb 7.

Reference Type DERIVED
PMID: 38321811 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2018-006

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Antigen-specific T Cells Against Lung Cancer
NCT03356808 UNKNOWN PHASE1/PHASE2