CANTATA: CB-839 With Cabozantinib vs. Cabozantinib With Placebo in Patients With Metastatic Renal Cell Carcinoma

NCT ID: NCT03428217

Last Updated: 2023-03-20

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

444 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-04-24

Study Completion Date

2021-07-16

Brief Summary

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Tthe primary objective of this study is to compare blinded Independent Radiology Committee (IRC)-adjudicated progression free survival (PFS) of patients treated with CB-839 + cabozantinib (CB-Cabo) versus placebo + cabozantinib (Pbo-Cabo) for advanced or metastatic clear-cell RCC (ccRCC).

Detailed Description

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Conditions

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Advanced Renal Cell Carcinoma Metastatic Renal Cell Carcinoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

This is a double blinded placebo-controlled study where patients will be randomized 1:1 to either CB-839 (telaglenastat) plus cabozantinib or placebo plus cabozantinib
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Participants, care providers, investigators and outcomes assessors are blinded to treatment. Progression free survival (PFS) will be assessed by a blinded Independent Radiology Committee for the primary endpoint of the study.

Study Groups

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Pbo-Cabo

Placebo twice daily (BID) + cabozantinib (60 mg once daily \[QD\]) administered orally on Days 1 through 28 of each 28-day cycle until disease progression per Response Evaluation Criteria in Solid Tumors version 1.1 (RECIST v1.1) or unacceptable toxicity, whichever occurred first.

Group Type PLACEBO_COMPARATOR

Cabozantinib

Intervention Type DRUG

Oral receptor tyrosine kinase inhibitor

Placebo

Intervention Type DRUG

Placebo tablets

CB-Cabo

CB-839 800 mg BID + cabozantinib (60 mg QD) administered orally on Days 1 through 28 of each 28-day cycle until disease progression per RECIST v1.1 or unacceptable toxicity, whichever occurred first.

Group Type EXPERIMENTAL

CB-839

Intervention Type DRUG

Oral glutaminase inhibitor

Cabozantinib

Intervention Type DRUG

Oral receptor tyrosine kinase inhibitor

Interventions

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CB-839

Oral glutaminase inhibitor

Intervention Type DRUG

Cabozantinib

Oral receptor tyrosine kinase inhibitor

Intervention Type DRUG

Placebo

Placebo tablets

Intervention Type DRUG

Other Intervention Names

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telaglenastat Cabometyx Cabometriq

Eligibility Criteria

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Inclusion Criteria

1. Documented histological or cytological diagnosis of renal cell carcinoma with a clear-cell component
2. Adult patients
3. Karnofsky Performance Score (KPS) ≥ 70%
4. Measurable Disease per Response Evaluation Criteria in Solid Tumors version 1.1 (RECIST v1.1)
5. 1-2 lines of prior therapy for advanced or metastatic renal cell carcinoma (RCC) including one anti-angiogenic therapy (any vascular endothelial growth factor \[VEGF\] pathway-targeted agent used either as monotherapy or as a component of a combination regimen) OR the combination regimen of nivolumab + ipilimumab
6. Adequate hepatic, renal, cardiac and hematologic function

Exclusion Criteria

1. Prior treatment with cabozantinib (or other mesenchymal-epithelial transition \[MET\] inhibitor) or CB-839
2. Receipt of other anticancer therapy within 2-6 weeks, depending on the treatment
3. Untreated or active brain metastases or central nervous system cancer, as defined per protocol
4. Prior gastric surgery, small bowel resection, or other conditions that may impede adequate absorption of oral study drug
5. Known active infection with human immunodeficiency virus (HIV), Hepatitis B or C virus
6. Inability to discontinue proton-pump-inhibitor use before randomization
7. Patients who are pregnant or lactating
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Calithera Biosciences, Inc

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Sam Whiting, M.D., Ph.D.

Role: STUDY_DIRECTOR

Calithera Biosciences, Inc

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Mayo Clinic Cancer Center

Phoenix, Arizona, United States

Site Status

The University of Arizona Cancer Center

Tucson, Arizona, United States

Site Status

Cedars-Sinai Medical Center, Samuel Oschin Comprehensive Cancer Institute

Los Angeles, California, United States

Site Status

Stanford Cancer Center

Palo Alto, California, United States

Site Status

Salinas Valley Memorial Healthcare System

Salinas, California, United States

Site Status

St. Joseph Heritage Healthcare

Santa Rosa, California, United States

Site Status

Penrose Cancer Center, Research Department

Colorado Springs, Colorado, United States

Site Status

Georgetown University Medical Center

Washington D.C., District of Columbia, United States

Site Status

Florida Cancer Specialists

Fort Myers, Florida, United States

Site Status

University of Miami Sylvester Comprehensive Cancer Center

Miami, Florida, United States

Site Status

Florida Cancer Specialists

St. Petersburg, Florida, United States

Site Status

H.Lee Moffitt Cancer & Research Institute (Moffitt Cancer Center)

Tampa, Florida, United States

Site Status

Emory Winship Cancer Institute

Atlanta, Georgia, United States

Site Status

Georgia Cancer Center at Augusta University

Augusta, Georgia, United States

Site Status

Northwest Georgia Oncology Centers, PC

Marietta, Georgia, United States

Site Status

St. Luke's Mountain States Tumor Institute

Boise, Idaho, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

University of Chicago

Chicago, Illinois, United States

Site Status

NorthShore University HealthSystem

Evanston, Illinois, United States

Site Status

AMITA Health Cancer Institute & Outpatient Center

Hinsdale, Illinois, United States

Site Status

Orchard Healthcare Research, Inc.

Skokie, Illinois, United States

Site Status

Northwestern Medicine Cancer Center Warrenville

Warrenville, Illinois, United States

Site Status

Goshen Center for Cancer Care

Goshen, Indiana, United States

Site Status

East Jefferson General Hospital

Metairie, Louisiana, United States

Site Status

Ochsner Clinic Foundation

New Orleans, Louisiana, United States

Site Status

University of Maryland, Greenebaum Comprehensive Cancer Center

Baltimore, Maryland, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Karmanos Cancer Institute

Detroit, Michigan, United States

Site Status

HealthPartners Institute, Regions Cancer Care Center

Saint Paul, Minnesota, United States

Site Status

Hattiesburg Clinic Hematology/Oncology

Hattiesburg, Mississippi, United States

Site Status

University of Mississippi Medical Center

Jackson, Mississippi, United States

Site Status

Mercy Hospital

Joplin, Missouri, United States

Site Status

HCA Midwest Health

Kansas City, Missouri, United States

Site Status

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, United States

Site Status

San Juan Oncology Associates, PC

Farmington, New Mexico, United States

Site Status

Roswell Park Cancer Center

Buffalo, New York, United States

Site Status

North Shore Hematology Oncology Associates PC dba NY Cancer and Blood Specialists

East Setauket, New York, United States

Site Status

NYU Winthrop Hospital

Mineola, New York, United States

Site Status

Northern Westchester Hospital

Mount Kisco, New York, United States

Site Status

Stony Brook Cancer Center

Stony Brook, New York, United States

Site Status

Levine Cancer Institute

Charlotte, North Carolina, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

INTEGRIS Cancer Institute of Oklahoma Proton Campus

Oklahoma City, Oklahoma, United States

Site Status

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

Allegheny General Hospital

Pittsburgh, Pennsylvania, United States

Site Status

University of Pittsburgh Medical Center (UPMC) Hillman Cancer Center

Pittsburgh, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Saint Francis Hospital Cancer Center

Greenville, South Carolina, United States

Site Status

West Cancer Center

Germantown, Tennessee, United States

Site Status

The Sarah Cannon Research Institute

Nashville, Tennessee, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

The Center for Cancer and Blood Disorders

Fort Worth, Texas, United States

Site Status

The University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status

University of Utah, Huntsman Cancer Institute

Salt Lake City, Utah, United States

Site Status

Kadlec Clinic Hematology and Oncology

Kennewick, Washington, United States

Site Status

Froedtert Hospital and the Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Southern Highlands Private Hospital (Cancer Centre)

Bowral, New South Wales, Australia

Site Status

Chris O'Brien Lifehouse

Camperdown, New South Wales, Australia

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MacQuarie University Hospital

North Ryde, New South Wales, Australia

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Liverpool Hospital

Sydney, New South Wales, Australia

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Tweed Hospital

Tweed Heads, New South Wales, Australia

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Pindara Private Hospital

Benowa, Queensland, Australia

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Cairns Hospital

Cairns, Queensland, Australia

Site Status

Mater Misericordiae Limited - Division of Cancer Services

South Brisbane, Queensland, Australia

Site Status

Princess Alexandra Hospital

Woolloongabba, Queensland, Australia

Site Status

Ballarat Health Services

Ballarat, Victoria, Australia

Site Status

Peninsula Private Hospital

Frankston, Victoria, Australia

Site Status

Cabrini Hospital

Malvern, Victoria, Australia

Site Status

Goulburn Valley Health

Shepparton, Victoria, Australia

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Hollywood Private Hospital

Nedlands, Western Australia, Australia

Site Status

Centre hospitalier régional universitaire (CHRU) de Besançon - Jean-Minjoz

Besançon, , France

Site Status

CHU de Bordeaux Hôpital Saint André

Bordeaux, , France

Site Status

Centre François Baclesse

Caen, , France

Site Status

Centre Jean Perrin

Clermont-Ferrand, , France

Site Status

Centre hospitalier universitaire (CHU) Henri-Mondor

Créteil, , France

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Centre Georges-François Leclerc

Dijon, , France

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Centre Léon Bérard

Lyon, , France

Site Status

Institut Paoli-Calmettes Service d'Urologie

Marseille, , France

Site Status

Institut de Cancérologie de Montpellier (ICM)

Montpellier, , France

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Centre Antoine Lacassagne

Nice, , France

Site Status

Hôpital Européen Georges-Pompidou (HEGP)

Paris, , France

Site Status

Institut de Cancérologie de l'Ouest (ICO) - Centre René Gauducheau

Saint-Herblain, , France

Site Status

CHU de Strasbourg (Les Hôpitaux Universitaires de Strasbourg)

Strasbourg, , France

Site Status

IUCTO Bureau des Essais Cliniques (Institut Claudius Regaud)

Toulouse, , France

Site Status

Institut de Cancérologie de Lorraine

Vandœuvre-lès-Nancy, , France

Site Status

Institut Gustave Roussy - Le département de Medecine oncologique

Villejuif, , France

Site Status

Medical University Heidelberg, NCT (National Center for Tumour Diseases), Medical Oncology

Heidelberg, Baden-Wurttemberg, Germany

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Technischen Universitat München - Urologische Klinik

München, Bavaria, Germany

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Charité Universitätsmedizin Berlin, Dept. of Interdisciplinary Urology

Berlin, , Germany

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Universitätsklinikum Carl Gustav Carus an der Technischen Universität Dresden, Klinik und Poliklinik

Dresden, , Germany

Site Status

Universitätsklinikum Essen (AöR) Westdeutsches Tumorzentrum

Essen, , Germany

Site Status

Medizinische Hochschule Hannover

Hanover, , Germany

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Universitätsklinikum Tübingen, Klinik für Urologie

Tübingen, , Germany

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Presidio Ospedaliero Antonio Perrino - U.O.C. Oncologia Medica

Brindisi, , Italy

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S.C. Oncologia - ASST Cremona P.O. Ospedale di Cremona

Cremona, , Italy

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Fondazione IRCCS Istituto Nazionale dei Tumori

Milan, , Italy

Site Status

Istituto Europeo di Oncologia - Divisione di Oncologia Medica Urogenitale e Cervico Facciale

Milan, , Italy

Site Status

U.O.C. ASST Santi Paolo e Carlo - Ospedale San Carlo Borromeo

Milan, , Italy

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University of Modena and Reggio Emilia (Azienda Ospedaliera-Universitaria Policlinico Modena)

Modena, , Italy

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Istituto Nazionale Tumori IRCCS "Fondazione G. Pascale"

Naples, , Italy

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Azienda Ospedaliero Universitaria San Luigi Gonzaga

Orbassano, , Italy

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Unità Operativa (UO) di Oncologia Medica - ICS Maugeri

Pavia, , Italy

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U.O. Oncologia Ospedale degli Infermi - Dipartimento di Oncologia ed Ematologia

Rimini, , Italy

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Policlinico Universitario A. Gemelli

Roma, , Italy

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Policlinico Universitario Campus Bio-Medico

Rome, , Italy

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Auckland City Hospital

Auckland, Grafton, New Zealand

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Christchurch Hospital

Christchurch, South Island, New Zealand

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Waikato Hospital

Hamilton, , New Zealand

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Wellington Regional Hospital

Wellington, , New Zealand

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Hospital Universitario Virgen del Rocío

Seville, Andalusia, Spain

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Hospital Universitari VHIO - Vall d'Hebron Departamento de Oncologia

Barcelona, , Spain

Site Status

El Hospital Clínic i Provincial de Barcelona (HCPB)

Barcelona, , Spain

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Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Institut Català d'Oncologia (ICO) L'Hospitalet

Barcelona, , Spain

Site Status

Institut Català d'Oncologia

Girona, , Spain

Site Status

HGU Gregorio Marañon

Madrid, , Spain

Site Status

MD Anderson Cancer Center Madrid

Madrid, , Spain

Site Status

El Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Centro Integral Oncologico Clara Campal (CIOCC) HM

Madrid, , Spain

Site Status

Hospital Parc Taulí de Sabadell

Sabadell, , Spain

Site Status

Hospital Universitario Virgen de Macarena

Seville, , Spain

Site Status

Fundación Instituto Valencia d'Oncología (IVO)

Valencia, , Spain

Site Status

The Christie NHS Foundation Trust

Manchester, Greater Manchester, United Kingdom

Site Status

Beatson West of Scotland Cancer Centre

Glasgow, Lanarkshire, United Kingdom

Site Status

Mount Vernon Cancer Centre

London, Middlesex, United Kingdom

Site Status

Nottingham University Hospitals NHS Trust - City Hospital Campus

Nottingham, Nottinghamshire, United Kingdom

Site Status

St. Bartholomew's Hospital, Barts Health NHS Trust

London, , United Kingdom

Site Status

The Royal Marsden NHS Foundation Trust

London, , United Kingdom

Site Status

Sarah Cannon Research Institute UK Limited

London, , United Kingdom

Site Status

Southampton General Hospital

Southampton, , United Kingdom

Site Status

Countries

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United States Australia France Germany Italy New Zealand Spain United Kingdom

References

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Tannir NM, Agarwal N, Porta C, Lawrence NJ, Motzer R, McGregor B, Lee RJ, Jain RK, Davis N, Appleman LJ, Goodman O Jr, Stadler WM, Gandhi S, Geynisman DM, Iacovelli R, Mellado B, Sepulveda Sanchez JM, Figlin R, Powles T, Akella L, Orford K, Escudier B. Efficacy and Safety of Telaglenastat Plus Cabozantinib vs Placebo Plus Cabozantinib in Patients With Advanced Renal Cell Carcinoma: The CANTATA Randomized Clinical Trial. JAMA Oncol. 2022 Oct 1;8(10):1411-1418. doi: 10.1001/jamaoncol.2022.3511.

Reference Type DERIVED
PMID: 36048457 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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CX-839-008

Identifier Type: -

Identifier Source: org_study_id

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