A Study of LY3002813 in Participants With Early Symptomatic Alzheimer's Disease (TRAILBLAZER-ALZ)

NCT ID: NCT03367403

Last Updated: 2022-10-13

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

272 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-12-18

Study Completion Date

2021-09-21

Brief Summary

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The purpose of this study is to evaluate the safety, tolerability and efficacy of LY3002813 in early symptomatic Alzheimer's disease.

Detailed Description

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Conditions

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Alzheimer Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Donanemab Monotherapy (Donanemab-M)

Participants received 700 milligram (mg) donanemab intravenously (IV) every 4 weeks (Q4W) x 3 doses, then 1400 mg donanemab IV Q4W for up to 72 weeks.

Group Type EXPERIMENTAL

Donanemab

Intervention Type DRUG

Administered IV

Placebo

Participants received placebo IV Q4W for up to 72 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered IV

Donanemab in Combination With LY3202626 (Donanemab-C)

Participants received 700 mg donanemab IV Q4W x 3 doses, then 1400 mg donanemab IV Q4W in combination with 12 mg of LY3202626 orally for up to 72 weeks.

As per protocol amendment (d) approved on Oct 9, 2018, donanemab in combination with LY3202626 (donanemab-C) arm discontinued as there was a low probability of identifying a statistically significant effect of 12mg of LY3202626 slowing cognitive decline.

Group Type EXPERIMENTAL

Donanemab

Intervention Type DRUG

Administered IV

LY3202626

Intervention Type DRUG

Administered orally

Interventions

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Donanemab

Administered IV

Intervention Type DRUG

Placebo

Administered IV

Intervention Type DRUG

LY3202626

Administered orally

Intervention Type DRUG

Other Intervention Names

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LY3002813

Eligibility Criteria

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Inclusion Criteria

* Gradual and progressive change in memory function reported by participants or informants for ≥ 6 months.
* MMSE score of 20 to 28 (inclusive) at baseline or an acceptable historical flortaucipir PET scan within 6 months prior to baseline that meets the central read criteria.
* Meet 18F flortaucipir PET scan eligibility criteria.
* Meet 18F florbetapir PET scan (central read) eligibility criteria.

Exclusion Criteria

* Have a history of long QT syndrome.
* Have received treatment with a stable dose of an acetylcholinesterase inhibitor (AChEI) and/or memantine for less than 2 months before randomization.
* Contraindication to MRI.
Minimum Eligible Age

60 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eli Lilly and Company

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 9 AM - 5 PM Eastern time (UTC/GMT - 5 hours, EST)

Role: STUDY_DIRECTOR

Eli Lilly and Company

Locations

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Banner Alzheimer's Institute

Phoenix, Arizona, United States

Site Status

Banner Sun Health Research Institute

Sun City, Arizona, United States

Site Status

Neurology Center of North Orange County

Fullerton, California, United States

Site Status

Irvine Clinical Research Center

Irvine, California, United States

Site Status

Institute for Memory Impairment & Neurological Disorders

Irvine, California, United States

Site Status

Pharmacology Research Institute

Newport Beach, California, United States

Site Status

Pacific Research Network Inc

San Diego, California, United States

Site Status

Sharp Mesa Vista Hospital

San Diego, California, United States

Site Status

Syrentis Clinical Research

Santa Ana, California, United States

Site Status

Associated Neurologists, PC - Danbury

Danbury, Connecticut, United States

Site Status

KI Health Partners, LLC d/b/a NE Inst. for Clin. Res.

Stamford, Connecticut, United States

Site Status

JEM Research Institute

Atlantis, Florida, United States

Site Status

Bradenton Research Center

Bradenton, Florida, United States

Site Status

Brain Matters Research

Delray Beach, Florida, United States

Site Status

Infinity Clinical Research, LLC

Hollywood, Florida, United States

Site Status

Jacksonville Center for Clinical Research

Jacksonville, Florida, United States

Site Status

Merritt Island Medical Research LLC

Merritt Island, Florida, United States

Site Status

Pharmax Research Clinic

Miami, Florida, United States

Site Status

Miami Jewish Health Systems

Miami, Florida, United States

Site Status

Suncoast Clinical Research

New Port Richey, Florida, United States

Site Status

Compass Research

Orlando, Florida, United States

Site Status

Palm Beach Neurological Group

Palm Beach Gardens, Florida, United States

Site Status

Quantum Laboratories

Pompano Beach, Florida, United States

Site Status

Progressive Medical Research

Port Orange, Florida, United States

Site Status

Intercoastal Medical Group

Sarasota, Florida, United States

Site Status

Axiom Research

Tampa, Florida, United States

Site Status

Stedman Clinical Trials

Tampa, Florida, United States

Site Status

Compass Research

The Villages, Florida, United States

Site Status

Great Lakes Clinical Trials

Chicago, Illinois, United States

Site Status

Alexian Brothers Medical Center

Elk Grove Village, Illinois, United States

Site Status

Indiana University School of Medicine

Indianapolis, Indiana, United States

Site Status

Josephson Wallack Munshower Neurology

Indianapolis, Indiana, United States

Site Status

University of Kansas Hospital

Fairway, Kansas, United States

Site Status

Cotton O'Neil Clinic

Topeka, Kansas, United States

Site Status

McLean Hospital

Belmont, Massachusetts, United States

Site Status

ActivMed Practices & Research, Inc

Methuen, Massachusetts, United States

Site Status

Boston Center for Memory

Newton, Massachusetts, United States

Site Status

Donald S Marks

Plymouth, Massachusetts, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

Las Vegas Medical Research

Las Vegas, Nevada, United States

Site Status

Advanced Memory Research Institute of New Jersey

Toms River, New Jersey, United States

Site Status

Behavioral Health Center Research

Charlotte, North Carolina, United States

Site Status

Guilford Neurologic Associates

Greensboro, North Carolina, United States

Site Status

Raleigh Neurology Associates

Raleigh, North Carolina, United States

Site Status

Piedmont Medical Research

Winston-Salem, North Carolina, United States

Site Status

Insight Clinical Trials

Beachwood, Ohio, United States

Site Status

Ohio State University Medical Center

Columbus, Ohio, United States

Site Status

Neurology Diagnostics, Inc.

Dayton, Ohio, United States

Site Status

Abington Neurological Associates

Willow Grove, Pennsylvania, United States

Site Status

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status

Butler Hospital

Providence, Rhode Island, United States

Site Status

Texas Neurology, PA

Dallas, Texas, United States

Site Status

Houston Methodist

Houston, Texas, United States

Site Status

The Memory Clinic

Bennington, Vermont, United States

Site Status

Cognition Health

Fairfax, Virginia, United States

Site Status

National Clinical Research - Richmond

Richmond, Virginia, United States

Site Status

Bruyere Research Institute

Ottawa, Ontario, Canada

Site Status

Kawartha Regional Memory Clinic

Peterborough, Ontario, Canada

Site Status

Toronto Memory Program

Toronto, Ontario, Canada

Site Status

Clinique de la Memoire de l'Outaouais

Gatineau, Quebec, Canada

Site Status

DIEX Recherche Sherbrooke, Inc

Sherbrooke, Quebec, Canada

Site Status

Countries

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United States Canada

References

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Chandler JM, Lansdall CJ, Ye W, McDougall F, Belger M, Toth B, Mi X, Sink KM, Atkins AS. The Alzheimer's Disease Cooperative Study - Activities of Daily Living dependence score: revision and validation of an algorithm evaluating patient dependence across the spectrum of AD severity. J Prev Alzheimers Dis. 2025 Sep;12(8):100261. doi: 10.1016/j.tjpad.2025.100261. Epub 2025 Jul 1.

Reference Type DERIVED
PMID: 40603145 (View on PubMed)

Zimmer JA, Ardayfio P, Wang H, Khanna R, Evans CD, Lu M, Sparks J, Andersen S, Lauzon S, Nery ESM, Battioui C, Engle SE, Biffi A, Svaldi D, Salloway S, Greenberg SM, Sperling RA, Mintun M, Brooks DA, Sims JR. Amyloid-Related Imaging Abnormalities With Donanemab in Early Symptomatic Alzheimer Disease: Secondary Analysis of the TRAILBLAZER-ALZ and ALZ 2 Randomized Clinical Trials. JAMA Neurol. 2025 May 1;82(5):461-469. doi: 10.1001/jamaneurol.2025.0065.

Reference Type DERIVED
PMID: 40063015 (View on PubMed)

Klein EG, Schroeder K, Wessels AM, Phipps A, Japha M, Schilling T, Zimmer JA. How donanemab data address the coverage with evidence development questions. Alzheimers Dement. 2024 Apr;20(4):3127-3140. doi: 10.1002/alz.13700. Epub 2024 Feb 7.

Reference Type DERIVED
PMID: 38323738 (View on PubMed)

Pontecorvo MJ, Lu M, Burnham SC, Schade AE, Dage JL, Shcherbinin S, Collins EC, Sims JR, Mintun MA. Association of Donanemab Treatment With Exploratory Plasma Biomarkers in Early Symptomatic Alzheimer Disease: A Secondary Analysis of the TRAILBLAZER-ALZ Randomized Clinical Trial. JAMA Neurol. 2022 Dec 1;79(12):1250-1259. doi: 10.1001/jamaneurol.2022.3392.

Reference Type DERIVED
PMID: 36251300 (View on PubMed)

Shcherbinin S, Evans CD, Lu M, Andersen SW, Pontecorvo MJ, Willis BA, Gueorguieva I, Hauck PM, Brooks DA, Mintun MA, Sims JR. Association of Amyloid Reduction After Donanemab Treatment With Tau Pathology and Clinical Outcomes: The TRAILBLAZER-ALZ Randomized Clinical Trial. JAMA Neurol. 2022 Oct 1;79(10):1015-1024. doi: 10.1001/jamaneurol.2022.2793.

Reference Type DERIVED
PMID: 36094645 (View on PubMed)

Mintun MA, Lo AC, Duggan Evans C, Wessels AM, Ardayfio PA, Andersen SW, Shcherbinin S, Sparks J, Sims JR, Brys M, Apostolova LG, Salloway SP, Skovronsky DM. Donanemab in Early Alzheimer's Disease. N Engl J Med. 2021 May 6;384(18):1691-1704. doi: 10.1056/NEJMoa2100708. Epub 2021 Mar 13.

Reference Type DERIVED
PMID: 33720637 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://trials.lillytrialguide.com/en-US/trial/4iGquIFHpuwam80Imyiukq

A Study of LY3002813 in Participants With Early Symptomatic Alzheimer's Disease

Other Identifiers

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I5T-MC-AACG

Identifier Type: OTHER

Identifier Source: secondary_id

16933

Identifier Type: -

Identifier Source: org_study_id

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